Clinical trial • Phase III • Neurology

ozanimod hydrochloride for Relapsing-remitting multiple sclerosis

Phase III trial of ozanimod hydrochloride for Relapsing-remitting multiple sclerosis.

Overview

Trial Therapeutic Area
Neurology
Trial Disease
Relapsing-remitting multiple sclerosis
Trial Stage
Phase III
Drug Modality
Small molecule
Paediatric Trial
Yes

Key dates

Initial CTIS Submission Date
24-05-2024
First CTIS Authorization Date
11-09-2024

Trial design

Randomised, fingolimod (oral). product entries list fingolimod strengths (fingolimod 0.25 mg capsule, fingolimod 0.5 mg capsule); fingolimod is over-encapsulated to blind vs placebo. (no detailed schedule provided in the available data.)-controlled Phase III trial across 15 sites in Poland, Portugal, Spain and others.

Randomised
Yes
Comparator
Fingolimod (oral). Product entries list fingolimod strengths (Fingolimod 0.25 mg capsule, Fingolimod 0.5 mg capsule); fingolimod is over-encapsulated to blind vs placebo. (No detailed schedule provided in the available data.)
Target Sample Size
40
Trial Duration For Participant
730

Eligibility

Recruits 40 paediatric patients.

Pregnancy Exclusion
Core and Extension Phase: Pregnant or breastfeeding females
Vulnerable Population
Vulnerable population includes children and adolescents. Age-specific assent and consent procedures are provided: assent and information sheets for minors (documents for 10-11 yrs, 12-15 yrs, 13-17 yrs), parent/guardian consent forms, and age-of-majority consent documents; subject information and informed consent forms available in country/language-specific versions.

Inclusion criteria

  • {"criterion_text":"- Core Phase: Diagnosis of MS with a RRMS\n- Core Phase: 1 MS relapse in the previous year or 2 MS relapse in past 2 years or evidence of 1 or more growth in MRI within 6 months\n- Core Phase: 0 - 5.5 Expanded Disability Status Scale (EDSS)\n- Core Phase: Must be able to swallow capsule\n- Extension Phase: Completion of core phase"}

Exclusion criteria

  • {"criterion_text":"- Core and Extension phase: Diagnosis of progressive form of MS\n- Core and Extension Phase: Active or chronic disease of the immune system\n- Core and Extension Phase: Any cardiovascular, liver, neurological, endocrine, or other major body disease or history or presence of malignancy\n- Core and Extension Phase: History of any type of epileptic seizures, substance abuse, progressive neurological disorder, or history of suicide attempt\n- Core and Extension Phase: Pregnant or breastfeeding females\n- Core and Extension Phase: Previous treatment with certain lymphocyte-depleting therapies or other immunosuppressants\n- Core and Extension Phase: Discontinued treatment with fingolimod or similar modulator, due to the medication not working"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Core phase: To assess rate of Multiple Sclerosis (MS) relapse over 2 years","definition_or_measurement_approach":"Assess rate of Multiple Sclerosis (MS) relapse over a 2-year period (as stated: 'To assess rate of Multiple Sclerosis (MS) relapse over 2 years')."}

Secondary endpoints

  • {"endpoint_text":"- Core and Extension Phase: proportion of the participants who have worsening or improving RRMS","definition_or_measurement_approach":"Proportion of participants with worsening or improvement in RRMS (verbatim as listed)."}
  • {"endpoint_text":"- Core and Extension Phase: occurrence of adverse events (type, severity and relationship to the study drug)","definition_or_measurement_approach":"Occurrence of adverse events characterized by type, severity and relationship to study drug (verbatim as listed)."}
  • {"endpoint_text":"- Core and Extension Phase: early study discontinuation","definition_or_measurement_approach":"Monitoring of early study discontinuation (verbatim as listed)."}
  • {"endpoint_text":"- Core and Extension Phase: measurements of the amount of ozanimod in a participant’s body","definition_or_measurement_approach":"Pharmacokinetic measurements of ozanimod levels in participants (verbatim: 'measurements of the amount of ozanimod in a participant’s body')."}

Recruitment

Planned Sample Size
40
Recruitment Window Months
142
Consent Approach
Informed consent and assent procedures are age-specific: parent/guardian consent required for minors; assent documents provided for younger participants (documents for 10-11 yrs, 12-15 yrs, 13-17 yrs are listed). Age-of-majority consent documents and parent information/consent templates are available. Subject information and informed consent forms are provided in multiple country/language versions (examples in Polish, Portuguese, Spanish, Italian and English-language materials are present in the document list).

Geography

Total Number Of Sites
15
Total Number Of Participants
38

Poland

Earliest CTIS Part Ii Submission Date
03-09-2024
Latest Decision Or Authorization Date
07-11-2025
Processing Time Days
430
Number Of Sites
1
Number Of Participants
6

Sites

Site Name
Uniwersytecki Szpital Kliniczny W Poznaniu
Department Name
Oddział Kliniczny Neurologii Dzieci i Młodzieży
Principal Investigator Name
Barbara Steinborn
Contact Person Name
Barbara Steinborn
Contact Person Email
bstein@ump.edu.pl

Portugal

Earliest CTIS Part Ii Submission Date
20-08-2024
Latest Decision Or Authorization Date
04-11-2025
Processing Time Days
441
Number Of Sites
4
Number Of Participants
5

Sites

Site Name
Unidade Local De Saude De Sao Jose E.P.E.
Department Name
Centro de Responsabilidade Integrado de Esclerose Múltipla da ULS São José
Principal Investigator Name
João Sequeira
Contact Person Name
João Sequeira
Contact Person Email
joaopfsequeira@gmail.com
Site Name
Unidade Local De Saude De Coimbra E.P.E.
Department Name
Centro de Desenvolvimento da Criança - Neuropediatria
Principal Investigator Name
Filipe Palavra
Contact Person Name
Filipe Palavra
Contact Person Email
filipepalavra@gmail.com
Site Name
Unidade Local de Saude de Sao Joao E.P.E.
Department Name
Neuropediatria
Principal Investigator Name
Mafalda Sampaio
Contact Person Name
Mafalda Sampaio
Site Name
CCAB Centro Clinico Academico Braga Associacao
Department Name
Neurologia
Principal Investigator Name
João Cerqueira
Contact Person Name
João Cerqueira
Contact Person Email
jcerqueira@med.uminho.pt

Spain

Earliest CTIS Part Ii Submission Date
19-08-2024
Latest Decision Or Authorization Date
04-11-2025
Processing Time Days
442
Number Of Sites
5
Number Of Participants
7

Sites

Site Name
Sant Joan De Deu Barcelona Hospital
Department Name
Neurología
Principal Investigator Name
Thais Armangue
Contact Person Name
Thais Armangue
Contact Person Email
thais.armangue@sjd.es
Site Name
Hospital Universitario Virgen De La Macarena
Department Name
Neurología
Principal Investigator Name
Sara Eichau Madueño
Contact Person Name
Sara Eichau Madueño
Contact Person Email
saraeichau@gmail.com
Site Name
Hospital Alvaro Cunqueiro
Department Name
NEUROLOFÍA
Principal Investigator Name
ELENA Álvarez
Contact Person Name
ELENA Álvarez
Contact Person Email
elenaar86@hotmail.com
Site Name
Hospital Universitario Y Politecnico La Fe
Department Name
Neuroinmunología
Principal Investigator Name
Francisco Carlos Pérez Miralles
Contact Person Name
Francisco Carlos Pérez Miralles
Contact Person Email
fcomiralles.neuro@gmail.com
Site Name
Hospital Unviersitario Miguel Servet
Department Name
Neurología
Principal Investigator Name
JESUS Martin Martinez
Contact Person Name
JESUS Martin Martinez
Contact Person Email
jesmartin58@gmail.com

Italy

Earliest CTIS Part Ii Submission Date
07-06-2024
Latest Decision Or Authorization Date
03-11-2025
Processing Time Days
514
Number Of Sites
3
Number Of Participants
8

Sites

Site Name
Azienda Ospedaliera Universitaria Federico II Di Napoli
Department Name
Dipartimento di Neuroscienze, Scienze Riproduttive ed Odontostomatologiche
Principal Investigator Name
Vincenzo Brescia Morra
Contact Person Name
Vincenzo Brescia Morra
Contact Person Email
vincenzo.bresciamorra@unina.it
Site Name
Ospedale San Raffaele S.r.l.
Department Name
Neurologia
Principal Investigator Name
Massimo Filippi
Contact Person Name
Massimo Filippi
Contact Person Email
filippi.massimo@hsr.it
Site Name
Neurological Centre Of Latium Istituto Di Neuroscienze O In Breve N.C.L. Istituto Di Neuroscienze S.r.l.
Department Name
Neurologia Sperimentazioni Cliniche
Principal Investigator Name
Carlo Pozzilli
Contact Person Name
Carlo Pozzilli
Contact Person Email
carlo.pozzilli@uniroma1.it

Romania

Earliest CTIS Part Ii Submission Date
07-06-2024
Latest Decision Or Authorization Date
03-02-2026
Processing Time Days
606
Number Of Sites
2
Number Of Participants
12

Sites

Site Name
Spitalul Clinic De Psihiatrie Prof.Dr.Alexandru Obregia
Department Name
Neurology
Principal Investigator Name
Cristina Pomeran
Contact Person Name
Cristina Pomeran
Contact Person Email
secretariat@spital-obregia.ro
Site Name
Dr. Victor Gomoiu Clinical Children Hospital
Department Name
Pediatric Neurology
Principal Investigator Name
Raluca Ioana Teleanu
Contact Person Name
Raluca Ioana Teleanu
Contact Person Email
xyz@gmail.com

Sponsor

Primary sponsor

Full Name
Bristol-Myers Squibb Services Unlimited Company
Organisation Type
Pharmaceutical company
Country Of Registered Address
Ireland

Contract research organisations

Name
Frontage Laboratories (Shanghai) Co. Ltd.
Responsibilities
PK testing and reporting
Name
Endpoint Clinical Inc.
Responsibilities
Treatment/Arm Assignment; Drug (re) Supplies Assignment; IVRS-treatment
Name
Accenture Solutions Private Limited
Responsibilities
Operational support (codes/roles listed: 6, 'embarc operations')
Name
Clario
Responsibilities
Cardiac Safety Analysis; additional data services
Name
Signant Health Global LLC
Responsibilities
Treatment/Arm assignment; IVRS – treatment randomisation; Drug (re)supplies assignment; Subject Number assignment; PRO/COA

Third parties

  • {"country":"China","full_name":"Frontage Laboratories (Shanghai) Co. Ltd.","duties_or_roles":"PK testing and reporting","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Endpoint Clinical Inc.","duties_or_roles":"Treatment/Arm Assignment; Drug (re) Supplies Assignment; IVRS-treatment","organisation_type":"Pharmaceutical company"}
  • {"country":"India","full_name":"Accenture Solutions Private Limited","duties_or_roles":"Code 6 (role code present in record)","organisation_type":"Pharmaceutical company"}
  • {"country":"India","full_name":"Accenture Solutions Private Limited","duties_or_roles":"embarc operations; Code 6","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Clario","duties_or_roles":"Cardiac Safety Analysis; additional roles (codes 6 and 7 present)","organisation_type":"Industry"}
  • {"country":"United States","full_name":"Signant Health Global LLC","duties_or_roles":"Treatment/Arm assignment; IVRS – treatment randomisation; Drug (re)supplies assignment; Subject Number assignment; PRO/COA","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Ozanimod HCl
Active Substance
ozanimod hydrochloride
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
oral
Authorisation Status
prodAuthStatus=1
Dose Levels
Ozanimod HCl 0.23 mg, Ozanimod HCl 1 mg, Ozanimod HCl 0.0575 mg, Ozanimod HCl 0.25 mg
Investigational Product Name
Fingolimod
Active Substance
fingolimod
Modality
Small molecule
Routes Of Administration
ORAL
Route
oral
Authorisation Status
prodAuthStatus=2
Dose Levels
Fingolimod 0.25 mg capsule, Fingolimod 0.5 mg capsule

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