Clinical trial • Phase III • Immunology|Nephrology

obinutuzumab for Primary membranous nephropathy|Membranous nephropathy

Phase III trial of obinutuzumab for Primary membranous nephropathy|Membranous nephropathy.

Overview

Trial Therapeutic Area
Immunology|Nephrology
Trial Disease
Primary membranous nephropathy|Membranous nephropathy
Trial Stage
Phase III
Drug Modality
Monoclonal antibody|Small molecule

Key dates

Initial CTIS Submission Date
29-01-2024
First CTIS Authorization Date
05-03-2024

Trial design

Randomised, open-label, arm 1: obinutuzumab — infusions of obinutuzumab 1000 mg iv at week 0 (day 1), week 2, week 24, and week 26; premedication with methylprednisolone 80 mg iv, oral or iv antihistamine, and analgesic. arm 2 (comparator): tacrolimus — starting oral dose 0.05 mg per kilogram per day, divided into two doses given at 12-hour intervals.-controlled Phase III trial in France, Spain, Poland and others.

Randomised
Yes
Open Label
Yes
Comparator
Arm 1: Obinutuzumab — infusions of obinutuzumab 1000 mg IV at Week 0 (Day 1), Week 2, Week 24, and Week 26; premedication with methylprednisolone 80 mg IV, oral or IV antihistamine, and analgesic. Arm 2 (Comparator): Tacrolimus — starting oral dose 0.05 mg per kilogram per day, divided into two doses given at 12-hour intervals.
Biomarker Stratified
True, anti-PLA2R autoantibody titer (strata: high titer >175 RU/mL vs non-high titer <175 RU/mL)
Target Sample Size
88
Trial Duration For Participant
728

Stratification factors

  • Region: North America (United States and Canada) and Europe vs. rest of world (ROW)
  • Anti-PLA2R autoantibody titer: high titer (> 175 RU/mL) vs. non-high titer (< 175 RU/mL)

Eligibility

Recruits 88 Vulnerable population selected (isVulnerablePopulationSelected = true). The registry indicates vulnerable population selection but no detailed description of consent/assent handling or parental consent is provided in the available CTIS data..

Vulnerable Population
Vulnerable population selected (isVulnerablePopulationSelected = true). The registry indicates vulnerable population selection but no detailed description of consent/assent handling or parental consent is provided in the available CTIS data.

Inclusion criteria

  • {"criterion_text":"- Ability to comply with the study protocol, in the investigator's judgment"}
  • {"criterion_text":"- Diagnosis of pMN according to renal biopsy prior to or during screening"}
  • {"criterion_text":"- Screening urinary protein-to-creatinine ratio (UPCR) >= 5 g/g from 24-hour urine collection after best supportive care for >= 3 months prior to screening or screening UPCR >= 4 g/g after best supportive care for >= 6 months prior to screening"}
  • {"criterion_text":"- eGFR >= 40 mL/min/1.73m2 or qualified endogenous creatinine clearance >= 40 mL/min/1.73m2 based on 24-hour urine collection during screening"}
  • {"criterion_text":"- Patients who previously responded to calcineurin inhibitor (CNIs), rituximab, or alkylating agents with either a CR or partial remission and subsequently relapsed are eligible but require discontinuation of CNIs or alkylating agents for >= 6 months and rituximab for >= 9 months prior to screening"}
  • {"criterion_text":"- For patients enrolled in the extended China enrollment phase at China’s sites: current resident of mainland China and of Chinese ancestry"}
  • {"criterion_text":"- (Implicit) Patients classified in clinical trial group: Patients"}

Exclusion criteria

  • {"criterion_text":"- Uncontrolled blood pressure, in the opinion of the investigator, during 3 months prior to screening"}
  • {"criterion_text":"- Evidence of >= 50% reduction in proteinuria during the previous 6 months prior to randomization"}
  • {"criterion_text":"- Receipt of renal replacement therapy"}
  • {"criterion_text":"- Type 1 or 2 diabetes mellitus"}
  • {"criterion_text":"- Receipt of previous therapies as follows: - Treatment with MMF or oral, intramuscular, or intravenous corticosteroids within 1 month prior to or during screening - Any B-cell depleting therapy such as rituximab, ocrelizumab, or ofatumumab within 9 months prior to or during screening - Treatment with cyclophosphamide or CNI within 6 months prior to or during screening - Treatment with any biologic therapy such as belimumab, ustekinumab, or anifrolumab within 6 months prior to or during screening - Treatment with an inhibitor of Janus-associated kinase, Bruton’s tyrosine kinase, or tyrosine kinase 2, including but not limited to tofacitinib, baricitinib, upadacitinib, filgotinib, ibrutinib, or fenebrutinib within 3 months prior to or during screening - Treatment with any investigational agent within 28 days of screening or 5 drug-elimination half-lives of the investigational drug, whichever is longer - Receipt of a live vaccine within 28 days prior to screening or during screening"}
  • {"criterion_text":"- Patients with a secondary cause of MN (e.g., hepatitis B, SLE, medications, malignancies)"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- 1. The proportion of patients who achieve a CR at Week 104","definition_or_measurement_approach":"Proportion of patients who achieve a complete remission (CR) at Week 104; no further operational definition or measurement thresholds for CR provided in the available CTIS fields."}

Secondary endpoints

  • {"endpoint_text":"- 1. The proportion of patients who achieve an overall remission at Week 104","definition_or_measurement_approach":""}
  • {"endpoint_text":"- 2. The proportion of patients who achieve CR at Week 76","definition_or_measurement_approach":""}
  • {"endpoint_text":"- 3. Time to treatment failure, meeting escape criteria, or relapse after complete or partial remission","definition_or_measurement_approach":""}
  • {"endpoint_text":"- 4. Time to a sustained reduction of eGFR >= 30% from baseline","definition_or_measurement_approach":""}
  • {"endpoint_text":"- 5. Mean change in T-score from baseline in the Patient-Reported Outcomes Measurement Information System (PROMIS) Fatigue scale at Week 104","definition_or_measurement_approach":""}
  • {"endpoint_text":"- 6. Duration of CR","definition_or_measurement_approach":""}
  • {"endpoint_text":"- 7. Change in anti-PLA2R autoantibody titer from Baseline to Week 52","definition_or_measurement_approach":""}
  • {"endpoint_text":"- 8. Mean change from baseline in the Patient-Reported Outcomes Measurement Information System (PROMIS) Global Assessment of Physical Health scale at Week 104","definition_or_measurement_approach":""}
  • {"endpoint_text":"- 9. Incidence and severity of adverse events, with severity determined according to National Cancer Institute Common Terminology Criteria for Adverse Events version 5.0","definition_or_measurement_approach":"Severity determined according to NCI CTCAE v5.0"}
  • {"endpoint_text":"- 10. Characterization of adverse events of special interest","definition_or_measurement_approach":""}
  • {"endpoint_text":"- 11. Change from baseline in targeted vital signs","definition_or_measurement_approach":""}
  • {"endpoint_text":"- 12. Change from baseline in targeted clinical laboratory test results","definition_or_measurement_approach":""}
  • {"endpoint_text":"- 13. Serum concentrations of obinutuzumab at specified timepoints","definition_or_measurement_approach":""}
  • {"endpoint_text":"- 14. Peripheral B-cell counts at specified timepoints","definition_or_measurement_approach":""}
  • {"endpoint_text":"- 15. Prevalence of anti-drug antibodies (ADAs) to obinutuzumab at baseline and incidence of ADAs during the study","definition_or_measurement_approach":""}

Recruitment

Planned Sample Size
88
Recruitment Window Months
81
Consent Approach
Informed consent is required prior to screening: 'Consenting patients will enter a screening period...' Subject information and informed consent forms are listed among trial documents (multiple ICF/SIS documents). No detailed text on assent or parental consent for minors is provided in the available CTIS fields.

Geography

Total Number Of Sites
18
Total Number Of Participants
52

France

Earliest CTIS Part Ii Submission Date
12-02-2024
Latest Decision Or Authorization Date
05-03-2024
Processing Time Days
22
Number Of Sites
3
Number Of Participants
10

Sites

Site Name
Assistance Publique Hopitaux De Paris
Department Name
Nephrology
Principal Investigator Name
Jean-Jacques BOFFA
Principal Investigator Email
jean-jacques.boffa@aphp.fr
Contact Person Name
Jean-Jacques BOFFA
Contact Person Email
jean-jacques.boffa@aphp.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Nephrology
Principal Investigator Name
Dil SAHALI
Principal Investigator Email
dil.sahali@inserm.fr
Contact Person Name
Dil SAHALI
Contact Person Email
dil.sahali@inserm.fr
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
Nephrology and Organ Transplantation
Principal Investigator Name
Dominique CHAUVEAU
Principal Investigator Email
chauveau.d@chu-toulouse.fr
Contact Person Name
Dominique CHAUVEAU
Contact Person Email
chauveau.d@chu-toulouse.fr

Spain

Earliest CTIS Part Ii Submission Date
12-02-2024
Latest Decision Or Authorization Date
05-03-2024
Processing Time Days
22
Number Of Sites
5
Number Of Participants
12

Sites

Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Nephrology
Principal Investigator Name
Miguel Angel Perez Valdivia
Principal Investigator Email
miguelangelperezvaldivia@gmail.com
Contact Person Name
Miguel Angel Perez Valdivia
Site Name
Hospital Universitari Vall D Hebron
Department Name
Nephrology
Principal Investigator Name
irene Agraz Pamplona
Principal Investigator Email
irene.agraz@vallhebron.cat
Contact Person Name
irene Agraz Pamplona
Contact Person Email
irene.agraz@vallhebron.cat
Site Name
Bellvitge University Hospital
Department Name
Nephrology
Principal Investigator Name
Xavier Fulladosa Oliveras
Principal Investigator Email
xfulladosa@bellvitgehospital.cat
Contact Person Name
Xavier Fulladosa Oliveras
Site Name
Hospital Clinic De Barcelona
Department Name
Nephrology
Principal Investigator Name
Luis F. Quintana Porras
Principal Investigator Email
mmr@clinic.cat
Contact Person Name
Luis F. Quintana Porras
Contact Person Email
mmr@clinic.cat
Site Name
Hospital Universitario 12 De Octubre
Department Name
Nephrology
Principal Investigator Name
Enrique Morales Ruiz
Principal Investigator Email
emoralesr@senefro.org
Contact Person Name
Enrique Morales Ruiz
Contact Person Email
emoralesr@senefro.org

Poland

Earliest CTIS Part Ii Submission Date
12-02-2024
Latest Decision Or Authorization Date
07-03-2024
Processing Time Days
24
Number Of Sites
5
Number Of Participants
18

Sites

Site Name
Samodzielny Publiczny Zaklad Opieki Zdrowotnej Centralny Szpital Kliniczny Uniwersytetu Medycznego W Lodzi
Department Name
Klinika Nefrologii, Hipertensjologii, Transpolantologii i Chorób Wewnętrznych
Principal Investigator Name
Michał Nowicki
Principal Investigator Email
nefro@wp.pl
Contact Person Name
Michał Nowicki
Contact Person Email
nefro@wp.pl
Site Name
Uniwersytecki Szpital Kliniczny W Bialymstoku
Department Name
II Klinika Nefrologii, Hipertensjologii i Chorób Wewnętrznych z Ośrodkiem Dializ
Principal Investigator Name
Tomasz Hryszko
Principal Investigator Email
tomasz.hryszko@umb.edu.pl
Contact Person Name
Tomasz Hryszko
Contact Person Email
tomasz.hryszko@umb.edu.pl
Site Name
Samodzielny Publiczny Zaklad Opieki Zdrowotnej Uniwersytecki Szpital Kliniczny Nr 1 Im. Norberta Barlickiego Uniwersytetu Medycznego W Lodzi
Department Name
Oddział Kliniczny Nefrologii i Chorób Wewnętrznych
Principal Investigator Name
Ilona Kurnatowska
Principal Investigator Email
ilona.kurnatowska@umed.lodz.pl
Contact Person Name
Ilona Kurnatowska
Contact Person Email
ilona.kurnatowska@umed.lodz.pl
Site Name
Szpital Uniwersytecki Nr 1 Im. Dr. A. Jurasza W Bydgoszczy
Department Name
Klinika Nefrologii, Nadciśnienia Tętniczego i Chorób Wewnętrznych
Principal Investigator Name
Mariusz Flisinski
Principal Investigator Email
nefrologia@jurasza.pl
Contact Person Name
Mariusz Flisinski
Contact Person Email
nefrologia@jurasza.pl
Site Name
Uniwersytecki Szpital Kliniczny Im. Jana Mikulicza-Radeckiego We Wroclawiu
Department Name
Klinika Nefrologii, Medycyny Transplantacyjnej i Chorób Wewnętrznych
Principal Investigator Name
Mirosław Banasik
Principal Investigator Email
badaniakliniczne@usk.wroc.pl
Contact Person Name
Mirosław Banasik
Contact Person Email
badaniakliniczne@usk.wroc.pl

Italy

Earliest CTIS Part Ii Submission Date
12-02-2024
Latest Decision Or Authorization Date
02-04-2024
Processing Time Days
50
Number Of Sites
5
Number Of Participants
12

Sites

Site Name
Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia
Department Name
UO Nefrologia
Principal Investigator Name
Federico Alberici
Principal Investigator Email
federico.alberici@unibs.it
Contact Person Name
Federico Alberici
Contact Person Email
federico.alberici@unibs.it
Site Name
Universita' Degli Studi Di Napoli Federico II
Department Name
UO Nefrologia
Principal Investigator Name
Antonio Pisani
Principal Investigator Email
antonio.pisani@unina.it
Contact Person Name
Antonio Pisani
Contact Person Email
antonio.pisani@unina.it
Site Name
Ospedale San Giovanni Bosco
Department Name
UO Nefrologia
Principal Investigator Name
Savino Sciascia
Principal Investigator Email
savino.sciascia@unito.it
Contact Person Name
Savino Sciascia
Contact Person Email
savino.sciascia@unito.it
Site Name
University Hospital Consorziale Policlinico
Department Name
Nefrologia
Principal Investigator Name
Loreto Gesualdo
Principal Investigator Email
loreto.gesualdo@uniba.it
Contact Person Name
Loreto Gesualdo
Contact Person Email
loreto.gesualdo@uniba.it
Site Name
Fondazione IRCCS San Gerardo Dei Tintori
Department Name
UO Nefrologia
Principal Investigator Name
Federico Umberto Pieruzzi
Principal Investigator Email
federico.pieruzzi@unimib.it
Contact Person Name
Federico Umberto Pieruzzi
Contact Person Email
federico.pieruzzi@unimib.it

Sponsor

Primary sponsor

Full Name
F. Hoffmann-La Roche AG
Organisation Type
Pharmaceutical company
Country Of Registered Address
Switzerland

Contract research organisations

Name
IQVIA Limited
Responsibilities
sponsorDuties codes: 1; contact eu_clinical_trials_information@iqvia.com
Name
Labcorp Central Laboratory Services SARL
Responsibilities
sponsorDuties codes: 4; laboratory services (contact ctasubmissions@labcorp.com)
Name
Fortrea Inc.
Responsibilities
sponsorDuties code 15; Mobile Nursing (contact roche-pm@fortrea.com)
Name
Perceptive Eclinical Limited
Responsibilities
sponsorDuties codes: 14, 3; eClinical/platform activities (contact martin.preis@calyx.ai)

Third parties

  • {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"sponsorDuties codes: 1","organisation_type":"Pharmaceutical company"}
  • {"country":"Switzerland","full_name":"Labcorp Central Laboratory Services SARL","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Fortrea Inc.","duties_or_roles":"Mobile Nursing (sponsorDuties code 15)","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Perceptive Eclinical Limited","duties_or_roles":"sponsorDuties codes: 14, 3","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Gazyvaro (obinutuzumab)
Active Substance
obinutuzumab
Modality
Monoclonal antibody
Routes Of Administration
IV INFUSION
Route
IV infusion
Authorisation Status
Authorised
Starting Dose
1000 mg IV (Week 0, Day 1)
Dose Levels
1000 mg IV at Week 0 (Day 1), Week 2, Week 24, and Week 26
Frequency
Doses at Week 0 (Day 1), Week 2, Week 24, Week 26
Maximum Dose
1000 mg per infusion; max total dose noted in product data: 4 g
Investigational Product Name
Prograf (tacrolimus)
Active Substance
tacrolimus
Modality
Small molecule
Routes Of Administration
ORAL
Route
Oral
Authorisation Status
Authorised
Starting Dose
0.05 mg/kg/day, divided into two doses given at 12-hour intervals (oral)
Dose Levels
Starting 0.05 mg/kg/day (divided BID); per product info maxDailyDoseAmount = 0.05 mg/Kg
Frequency
Twice daily (divided doses every 12 hours)

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