Clinical trial • Phase III • Oncology

NIVOLUMAB for Urothelial carcinoma (unresectable or metastatic)

Phase III trial of NIVOLUMAB for Urothelial carcinoma (unresectable or metastatic).

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Urothelial carcinoma (unresectable or metastatic)
Trial Stage
Phase III
Drug Modality
Monoclonal antibody | Small molecule

Key dates

Initial CTIS Submission Date
01-02-2024
First CTIS Authorization Date
08-03-2024

Trial design

Randomised, open-label, comparator: standard of care chemotherapy arms including gemcitabine products (gemci-cell® 38 mg/ml; gemcitabine 1 g powder for solution for infusion; gemcitabine 38 mg/ml concentrate for solution for infusion) with platinum agents cisplatin (cisplatin neocorp 1 mg/ml; cisplatin teva® 1 mg/ml; cisplatin-ebewe 1 mg/ml; max daily dose listed 70 mg/m2) or carboplatin products (carbo-cell® 10 mg/ml; carboplatin bendalis 10 mg/ml; carbomedac® 10 mg/ml; max daily dose listed as 5 [unit listed as 'other']). specific administration schedules are not specified in the ctis data provided.-controlled Phase III trial in Germany, Romania, Norway and others.

Randomised
Yes
Open Label
Yes
Comparator
Comparator: Standard of care chemotherapy arms including gemcitabine products (GEMCI-cell® 38 mg/ml; Gemcitabine 1 g Powder for Solution for Infusion; Gemcitabine 38 mg/ml Concentrate for Solution for Infusion) with platinum agents Cisplatin (Cisplatin NeoCorp 1 mg/ml; Cisplatin Teva® 1 mg/ml; CISPLATIN-EBEWE 1 mg/ml; max daily dose listed 70 mg/m2) or Carboplatin products (CARBO-cell® 10 mg/ml; Carboplatin Bendalis 10 mg/ml; Carbomedac® 10 mg/ml; max daily dose listed as 5 [unit listed as 'Other']). Specific administration schedules are not specified in the CTIS data provided.
Biomarker Stratified
True, PD-L1 (>=1% vs <1%)
Target Sample Size
1076

Eligibility

Recruits 1076 No vulnerable populations selected. Population listed as adult patients (no paediatric subjects). Informed consent is obtained from participants; no assent/child consent procedures are described in the available CTIS data..

Vulnerable Population
No vulnerable populations selected. Population listed as adult patients (no paediatric subjects). Informed consent is obtained from participants; no assent/child consent procedures are described in the available CTIS data.

Inclusion criteria

  • {"criterion_text":"- Metastatic or inoperable urothelial cancer\n- Must have at least 1 lesion with measurable disease\n- Must have full activity or, if limited, must be able to walk and carry out light activities such as light house work or office work\n- No prior systemic chemotherapy treatment in the metastatic setting"}

Exclusion criteria

  • {"criterion_text":"- Patients with ECOG PS >= 2\n- Patients with disease that is suitable for local therapy administered with curative intent\n- Patients with active brain metastases or leptomeningeal metastases\n- Patients with active, known or suspected autoimmune disease\n- Prior treatment with an anti-PD-1, anti-PD-L1, anti-PD-L2, anti-CD137, or anti-CTLA-4 antibody, or any other antibody or drug specifically targeting T-cell co-stimulation or checkpoint pathways\n- Participants may not have received live/attenuated vaccines within 30 days prior to first study treatment."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Primary endpoint of OS in cisplatin-ineligible randomized participants","definition_or_measurement_approach":"Overall Survival (OS)"}
  • {"endpoint_text":"- Primary endpoint of OS in PD-L1 positive (>= 1%) randomized participants by immunohistochemistry (IHC)","definition_or_measurement_approach":"Overall Survival (OS) in PD-L1 positive (>= 1%) randomized participants assessed by immunohistochemistry (IHC)"}

Secondary endpoints

  • {"endpoint_text":"- OS in all randomized participants","definition_or_measurement_approach":"Overall Survival (OS)"}
  • {"endpoint_text":"- PFS by blinded independent central review (BICR) (using RECIST 1.1) in cisplatin-ineligible randomized participants, in PD-L1 positive (>=1%) randomized participants and in all randomized participants","definition_or_measurement_approach":"Progression-Free Survival (PFS) assessed by blinded independent central review (BICR) using RECIST 1.1"}
  • {"endpoint_text":"- European Organisation for Research and Treatment of Care (EORTC) QLQ-C30 Global Health Status score in all randomized participants","definition_or_measurement_approach":"EORTC QLQ-C30 Global Health Status score (health-related quality of life measure)"}

Recruitment

Planned Sample Size
1076
Recruitment Window Months
102
Consent Approach
Informed consent obtained from adult participants. Subject information sheets and informed consent forms (L1_SIS and ICF) are provided and available in multiple country/language versions (examples in the public documents include Polish (PL), Greek (GR), Czech (CZ), Spanish (ES), French (FR), Dutch (NL), Italian (IT) and others). No assent/child consent procedures are described in the CTIS data.

Geography

Total Number Of Sites
42
Total Number Of Participants
701

Germany

Earliest CTIS Part Ii Submission Date
19-02-2024
Latest Decision Or Authorization Date
13-03-2024
Processing Time Days
23
Number Of Sites
8
Number Of Participants
92

Sites

Site Name
Medical Center - University Of Freiburg
Department Name
Klinik f. Innere Medizin I
Contact Person Name
Cornelius Waller
Site Name
Klinikum Nuernberg
Department Name
Medizinische Klinik 5
Contact Person Name
Marinela Augustin
Site Name
Universitaetsklinikum Tuebingen AöR
Department Name
Universitaetsklinik fuer Urologie
Contact Person Name
Steffen Rausch
Site Name
Asklepios Kliniken Hamburg GmbH
Department Name
Klinik f. Urologie
Contact Person Name
christian Wuelfing
Contact Person Email
c.wuelfing@asklepios.com
Site Name
Medizinische Hochschule Hannover
Department Name
Klinik f Urologie und Urologische Onkologie
Contact Person Name
Christoph von Klot
Contact Person Email
klot.christoph@mh-hannover.de
Site Name
Universitaetsklinikum Jena KöR
Department Name
Studienbuero Urologie
Contact Person Name
Marc-Oliver Grimm
Site Name
Universitaetsklinikum Wuerzburg AöR
Department Name
Interdisziplinäres Studienzentrum (ISZ) mit ECTU (Haus C16)
Contact Person Name
Hubert Kuebler
Contact Person Email
kuebler_h@ukw.de
Site Name
Universitat Heidelberg
Department Name
Urologische Klinik
Contact Person Name
Frederik Wessels

Romania

Earliest CTIS Part Ii Submission Date
19-02-2024
Latest Decision Or Authorization Date
21-03-2024
Processing Time Days
31
Number Of Sites
2
Number Of Participants
75

Sites

Site Name
Institute Of Oncology Prof. Dr. Ion Chiricuta Cluj-Napoca
Department Name
Oncology
Contact Person Name
Tudor Ciuleanu
Contact Person Email
office@iocn.ro
Site Name
Centrul De Oncologie SF Nectarie S.R.L.
Department Name
Oncology
Contact Person Name
Michael Schenker
Contact Person Email
centruldeoncologie@yahoo.com

Norway

Earliest CTIS Part Ii Submission Date
19-02-2024
Latest Decision Or Authorization Date
08-03-2024
Processing Time Days
18
Number Of Sites
1
Number Of Participants
8

Sites

Site Name
Akershus University Hospital
Department Name
Department of Oncology
Contact Person Name
Jan Oldenburg
Contact Person Email
Jan.oldenburg@medisin.uio.no

Denmark

Earliest CTIS Part Ii Submission Date
19-02-2024
Latest Decision Or Authorization Date
11-03-2024
Processing Time Days
21
Number Of Sites
2
Number Of Participants
13

Sites

Site Name
Herlev Hospital
Department Name
Oncology
Principal Investigator Name
Lene Sonne Mouritsen
Principal Investigator Email
lene.sonne.mouritsen@regionh.dk
Contact Person Name
Lene Sonne Mouritsen
Site Name
Aalborg University Hospital
Department Name
Oncology
Principal Investigator Name
Andreas Carus
Principal Investigator Email
andreas.carus@rn.dk
Contact Person Name
Andreas Carus
Contact Person Email
andreas.carus@rn.dk

Poland

Earliest CTIS Part Ii Submission Date
14-05-2024
Latest Decision Or Authorization Date
20-03-2024
Number Of Sites
1
Number Of Participants
35

Sites

Site Name
Szpital Wojewodzki Im. Mikolaja Kopernika W Koszalinie
Department Name
Oddział Dzienny Chemioterapii
Contact Person Name
Mariusz Kwiatkowski
Contact Person Email
szpital@swk.med.pl

Greece

Earliest CTIS Part Ii Submission Date
19-02-2024
Latest Decision Or Authorization Date
22-04-2024
Processing Time Days
63
Number Of Sites
2
Number Of Participants
70

Sites

Site Name
University General Hospital Of Ioannina
Department Name
Oncology Clinic
Contact Person Name
Davide Mauri
Contact Person Email
dvd.mauri@gmail.com
Site Name
Alexandra Hospital
Department Name
Department of Clinical Therapeutics
Contact Person Name
Michalis Liontos
Contact Person Email
mliontos@gmail.gr

Netherlands

Earliest CTIS Part Ii Submission Date
19-02-2024
Latest Decision Or Authorization Date
11-03-2024
Processing Time Days
21
Number Of Sites
3
Number Of Participants
70

Sites

Site Name
Medisch Centrum Leeuwarden B.V.
Department Name
Medische Oncologie
Contact Person Name
Marco-Ben Polée
Contact Person Email
Wetenschap@mclacademie.nl
Site Name
Universitair Medisch Centrum Groningen
Department Name
Medische Oncologie
Contact Person Name
Sjoukje Oosting
Site Name
Het Nederlands Kanker Instituut-Antoni van Leeuwenhoek Ziekenhuis Stichting
Department Name
Medische Oncologie
Contact Person Name
Michiel van der Heijden
Contact Person Email
communicatie@nki.nl

Czechia

Earliest CTIS Part Ii Submission Date
19-02-2024
Latest Decision Or Authorization Date
11-03-2024
Processing Time Days
21
Number Of Sites
2
Number Of Participants
20

Sites

Site Name
Fakultni Nemocnice Hradec Kralove
Department Name
Klinika onkologie a radioterapie
Contact Person Name
Jindrich Kopecky
Contact Person Email
jindrich.kopecky@fnhk.cz
Site Name
Masarykuv Onkologicky Ustav
Department Name
Klinika komplexni onkologicke pece
Contact Person Name
Alexandr Poprach
Contact Person Email
poprach@mou.cz

Spain

Earliest CTIS Part Ii Submission Date
19-02-2024
Latest Decision Or Authorization Date
11-03-2024
Processing Time Days
21
Number Of Sites
7
Number Of Participants
85

Sites

Site Name
Hospital Universitario Ramon Y Cajal
Department Name
Oncologia
Contact Person Name
Teresa Alonso
Contact Person Email
talonso@oncologiahrc.com
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Oncologia Medica
Contact Person Name
Begoña Perez Valderrama
Contact Person Email
bpvalderrama@gmail.com
Site Name
Fundacion Instituto Valenciano De Oncologia
Department Name
Unidad Investigacion Clinica
Contact Person Name
Miguel Angel Climent
Contact Person Email
macliment@fivo.org
Site Name
Complejo Hospitalario Universitario Juan Canalejo
Department Name
Oncologia
Contact Person Name
Aurea Molina Diaz
Contact Person Email
aurea.molina.diaz@sergas.es
Site Name
Hospital Universitario Marques De Valdecilla
Department Name
Oncologia Medica
Contact Person Name
Ignacio Duran
Contact Person Email
ignaciojose.duran@scsalud.es
Site Name
Hospital Universitario 12 De Octubre
Department Name
Oncologia
Contact Person Name
Daniel Castellano
Contact Person Email
cdanicas@hotmail.com
Site Name
Hospital De La Santa Creu I Sant Pau
Department Name
Genitourinari Oncologia Medica
Contact Person Name
Jose Pablo Maroto
Contact Person Email
jmaroto@santpau.cat

France

Earliest CTIS Part Ii Submission Date
19-02-2024
Latest Decision Or Authorization Date
12-03-2024
Processing Time Days
22
Number Of Sites
7
Number Of Participants
144

Sites

Site Name
Hospital Foch
Department Name
Medical Oncology
Contact Person Name
Christine Abraham
Contact Person Email
c.abraham@hopital-foch.com
Site Name
Centre Hospitalier Universitaire De Saint Etienne
Department Name
Oncology
Contact Person Name
Pierre Cornillon
Contact Person Email
pierre.cornillon@chuse.fr
Site Name
Centre Oscar Lambret
Department Name
Urological and Digestive Oncology
Contact Person Name
Aurélien Carnot
Contact Person Email
a-carnot@o-lambret.fr
Site Name
Centre Hospitalier Universitaire De Nimes
Department Name
Medical Oncology
Contact Person Name
Nadine Houédé
Contact Person Email
Nadine.houede@chu-nimes.fr
Site Name
Institut Gustave Roussy
Department Name
Medical Oncology
Contact Person Name
Loriot Yohann
Contact Person Email
yohann.loriot@gustaveroussy.fr
Site Name
Institut Paoli-Calmettes
Department Name
Medical Oncology
Contact Person Name
Gwenaëlle Gravis
Contact Person Email
gravisg@ipc.unicancer.fr
Site Name
Centre Hospitalier Regional Universitaire De Tours
Department Name
Oncology
Contact Person Name
Bérengère Narciso

Italy

Earliest CTIS Part Ii Submission Date
19-02-2024
Latest Decision Or Authorization Date
21-03-2024
Processing Time Days
31
Number Of Sites
7
Number Of Participants
89

Sites

Site Name
Azienda Unita Sanitaria Locale Della Romagna
Department Name
U.O di Oncologia
Contact Person Name
Francesco Carrozza
Site Name
Fondazione IRCCS Istituto Nazionale Dei Tumori
Department Name
Oncologia medica genitourinaria
Contact Person Name
Melanie Claps
Site Name
Azienda USL Toscana Sud Est
Department Name
U.O.C Oncologia Medica 1
Contact Person Name
Alketa Hamzaj
Site Name
Azienda Unita Sanitaria Locale Della Romagna
Department Name
U.O di Oncologia
Contact Person Name
Francesco Carrozza
Site Name
Istituto Romagnolo Per Lo Studio Dei Tumori Dino Amadori IRST S.r.l.
Department Name
Oncologia Medica
Contact Person Name
Giuseppe Schepisi
Contact Person Email
giuseppe.schepisi@irst.emr.it
Site Name
Azienda Unita Sanitaria Locale Della Romagna
Department Name
U.O di Oncologia
Contact Person Name
Francesco Carrozza
Site Name
Azienda Unita Sanitaria Locale Della Romagna
Department Name
U.O di Oncologia
Contact Person Name
Francesco Carrozza

Sponsor

Primary sponsor

Full Name
Bristol-Myers Squibb Services Unlimited Company
Organisation Type
Pharmaceutical company
Country Of Registered Address
Ireland

Contract research organisations

Name
Icon (Lr) Limited
Responsibilities
Routine clin pathology test,Clin chemistry,Clin haematol,Clin microbiol,Histopathol,Serol/endocrinol,Analytical chemistry,Primary/surrogate endpoint test,spl mgmt,kit-supply provision,storage & distri for anal,pathology report receipt,PBMC processing
Name
PAREXEL INTERNATIONAL (IRL) Limited
Responsibilities
Subject Number assignment, Treatment/Arm assignment, Drug (re)supplies assignment
Name
PPD Development LP
Responsibilities
Serum PK and serum immunogenicity analysis
Name
Bioclinica Inc.
Responsibilities
Collection of de-identified images; Imaging doc development; Independent reader training;...

Third parties

  • {"country":"Ireland","full_name":"Icon (Lr) Limited","duties_or_roles":"Routine clin pathology test,Clin chemistry,Clin haematol,Clin microbiol,Histopathol,Serol/endocrinol,Analytical chemistry,Primary/surrogate endpoint test,spl mgmt,kit-supply provision,storage & distri for anal,pathology report receipt,PBMC processing","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Cellcarta Fremont LLC","duties_or_roles":"Myeloid Derived Suppressor Cells (MDSCs) analysis","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Myriad RBM Inc.","duties_or_roles":"Specialty Biomarker Laboratory, Exploratory Serum Biomarker analysis","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"PPD Development LP","duties_or_roles":"Serum PK and serum immunogenicity analysis","organisation_type":"Pharmaceutical company"}
  • {"country":"India","full_name":"Accenture Solutions Private Limited","duties_or_roles":"Various operational support (codes referenced in CTIS data)","organisation_type":"Pharmaceutical company"}
  • {"country":"Ireland","full_name":"PAREXEL INTERNATIONAL (IRL) Limited","duties_or_roles":"Subject Number assignment, Treatment/Arm assignment, Drug (re)supplies assignment","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Bioclinica Inc.","duties_or_roles":"Collection of de-identified images; Imaging doc development; Independent reader training;...","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Icon Laboratories Inc.","duties_or_roles":"Data entry of Local Laboratory Values","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Mosaic Laboratories LLC","duties_or_roles":"Specialty Biomarker Laboratory,IHC Biomarker expression analysis (PD-L1)","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
OPDIVO 10 mg/mL concentrate for solution for infusion.
Active Substance
NIVOLUMAB
Modality
Monoclonal antibody
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS USE
Authorisation Status
Authorised (prodAuthStatus=2)
Maximum Dose
max daily dose 480 mg (max total dose 4080 mg)
Investigational Product Name
YERVOY 5 mg/ml concentrate for solution for infusion
Active Substance
IPILIMUMAB
Modality
Monoclonal antibody
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS USE
Authorisation Status
Authorised (prodAuthStatus=2)
Maximum Dose
max daily dose 3 mg/Kg (max total dose 12 mg/Kg)
Investigational Product Name
GEMCI-cell® 38 mg/ml Konzentrat zur Herstellung einer Infusionslösung / Gemcitabine products
Active Substance
GEMCITABINE
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS USE
Authorisation Status
Authorised (prodAuthStatus=2)
Maximum Dose
max daily dose 1000 mg/m2 (max total dose 12000 mg/m2)
Investigational Product Name
Cisplatin products (Cisplatin NeoCorp / Cisplatin Teva® / CISPLATIN-EBEWE)
Active Substance
CISPLATIN
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS USE
Authorisation Status
Authorised (prodAuthStatus=2)
Maximum Dose
max daily dose 70 mg/m2 (max total dose 420 mg/m2)
Investigational Product Name
Carboplatin products (CARBO-cell® / Carboplatin Bendalis / Carbomedac®)
Active Substance
CARBOPLATIN
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS USE
Authorisation Status
Authorised (prodAuthStatus=2)
Maximum Dose
max daily dose 5 (unit listed as 'Other')
Combination Treatment
Yes

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