Clinical trial • Phase III • Oncology

NAVTEMADLIN for Myelofibrosis | Primary myelofibrosis | Secondary myelofibrosis

Phase III trial of NAVTEMADLIN for Myelofibrosis | Primary myelofibrosis | Secondary myelofibrosis.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Myelofibrosis | Primary myelofibrosis | Secondary myelofibrosis
Trial Stage
Phase III
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
24-05-2024
First CTIS Authorization Date
17-09-2024

Trial design

Randomised, navtemadlin (oral tablet formulations including navtemadlin 25-30, navtemadlin 25-60, navtemadlin 25-120, navtemadlin 25-180) as add-on therapy to continuous ruxolitinib versus matching placebo as add-on therapy to continuous ruxolitinib.-controlled Phase III trial in Belgium, Croatia, Germany and others.

Randomised
Yes
Comparator
Navtemadlin (oral tablet formulations including Navtemadlin 25-30, Navtemadlin 25-60, Navtemadlin 25-120, Navtemadlin 25-180) as add-on therapy to continuous ruxolitinib versus matching placebo as add-on therapy to continuous ruxolitinib.
Biomarker Stratified
True, TP53 (TP53 wild-type (TP53WT) required by central testing)
Target Sample Size
57
Trial Duration For Participant
168

Eligibility

Recruits 57 Vulnerable population flag is selected in the application. The trial population is limited to adults (Adults ≥ 18 years of age able to provide informed consent). Informed consent must be provided by the participant (adult). No assent procedures for minors are provided because the trial excludes participants <18..

Vulnerable Population
Vulnerable population flag is selected in the application. The trial population is limited to adults (Adults ≥ 18 years of age able to provide informed consent). Informed consent must be provided by the participant (adult). No assent procedures for minors are provided because the trial excludes participants <18.

Inclusion criteria

  • {"criterion_text":"- Ruxolitinib Run-In Period: 1.\tAdults ≥ 18 years of age able to provide informed consent."}
  • {"criterion_text":"- Ruxolitinib Run-In Period: 2. Confirmed diagnosis of PMF, post-PV MF, or post-ET MF, as assessed by the treating physician according to the World Health Organization (WHO) criteria"}
  • {"criterion_text":"- Ruxolitinib Run-In Period: 3.\tHigh, Intermediate-1, Intermediate-2 risk category International Prognosis System Score (IPSS)"}
  • {"criterion_text":"- Ruxolitinib Run-In Period: 4. Eastern Cooperative Oncology Group (ECOG) performance status of 0 to 2."}
  • {"criterion_text":"- Ruxolitinib Run-In Period: 5. JAK-inhibitor treatment naive"}
  • {"criterion_text":"- Randomized Add-on Period: 1.\tPMF, post-PV MF, or post-ET MF that is TP53WT as assessed by central testing."}
  • {"criterion_text":"- Randomized Add-on Period: 2. ECOG performance status of 0 to 2."}
  • {"criterion_text":"- Randomized Add-on Period: 3.\tTreatment with a stable dose of ruxolitinib"}
  • {"criterion_text":"- Randomized Add-on Period: 4.\t Suboptimal response to run-in ruxolitinib therapy"}

Exclusion criteria

  • {"criterion_text":"- Ruxolitinib Run-In Period: 1.\tPrior Splenectomy"}
  • {"criterion_text":"- Ruxolitinib Run-In Period: 2. Splenic irradiation within 3 months prior to the first dose"}
  • {"criterion_text":"- Ruxolitinib Run-In Period: 3. Prior BCL-XL, BET, MDM2, PI3K, PIM, or XPO1 inhibitors therapy or p53- directed therapy"}
  • {"criterion_text":"- Ruxolitinib Run-In Period: 4. Eligible for Bone Marrow Transplant"}
  • {"criterion_text":"- Ruxolitinib Run-In Period: 5. Peripheral blood or bone marrow blast count ≥ 10%"}
  • {"criterion_text":"- Randomized Period: 1. Peripheral blood or bone marrow blast count ≥ 10%"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- SVR will be evaluated 24 weeks after randomized treatment begins by MRI/CT scan (central review).","definition_or_measurement_approach":"Spleen volume reduction (SVR) evaluated 24 weeks after randomization by MRI or CT scan with central review."}
  • {"endpoint_text":"- TSS reduction will be evaluated 24 weeks after randomized treatment begins using the Myelofibrosis Symptom Assessment Form (MFSAF) v4.0.","definition_or_measurement_approach":"Total Symptom Score (TSS) reduction measured at 24 weeks using the Myelofibrosis Symptom Assessment Form (MFSAF) version 4.0."}

Secondary endpoints

  • {"endpoint_text":"- The proportion of patients who have spleen volume reduction between Arm 1 and Arm 2","definition_or_measurement_approach":"Proportion of patients achieving spleen volume reduction comparing Arm 1 vs Arm 2 (measurement method as per SVR; imaging-based assessment)."}
  • {"endpoint_text":"- The proportion of patients who have TSS reduction between Arm 1 and Arm 2","definition_or_measurement_approach":"Proportion of patients with reduction in Total Symptom Score (TSS) between Arm 1 and Arm 2 measured using MFSAF v4.0."}
  • {"endpoint_text":"- Time to death from any cause in patients randomized to each arm","definition_or_measurement_approach":"Overall survival (time from randomization to death from any cause)."}
  • {"endpoint_text":"- Time to progression or death from any cause in patients randomized to each arm","definition_or_measurement_approach":"Time to disease progression or death (composite endpoint) measured from randomization."}
  • {"endpoint_text":"- Analyses of the safety endpoints will include the following measurements or assessments: physical examinations, laboratory tests, adverse events (AEs), serious AEs (SAEs), electrocardiograms (ECGs), and vital signs","definition_or_measurement_approach":"Safety and tolerability assessed via physical exams, laboratory tests, AE/SAE reporting, ECGs and vital signs according to study schedule."}
  • {"endpoint_text":"- Change in SVR 24 weeks after the randomized treatment begins","definition_or_measurement_approach":"Change in spleen volume reduction from baseline to 24 weeks (imaging assessment)."}
  • {"endpoint_text":"- Change in TSS 24 weeks after the randomized treatment begins","definition_or_measurement_approach":"Change in Total Symptom Score from baseline to 24 weeks measured by MFSAF v4.0."}

Recruitment

Digital Remote Recruitment
True, recruitment materials include website content (POIESIS), online study materials for HCP and non-HCP, and electronic patient-reported outcome (ePRO) systems (ePRO vendor listed among third parties).
Planned Sample Size
57
Recruitment Window Months
56
Consent Approach
Informed consent is obtained from the participant (adults ≥18 years). Subject information sheets and informed consent forms are provided; documents are available in multiple languages (English and country-specific languages as per uploaded documents, e.g., BE-FR, BE-NL, AT-DE, FR, ES, IT, PL, PT, HU, HR, CZ, RO and others). Specific pregnancy-related information/ICFs are provided (separate pregnancy ICF documents are included).

Methods

  • Referral letters to physicians (Dr-to-Dr / referral letter) — documented in recruitment materials (e.g., 'Referral Letter' PDFs).
  • POIESIS website content for healthcare professionals (HCP) and non-HCP (patient/caregiver) — documented in recruitment materials (POIESIS Website HCP / Non HCP PDFs).
  • Study flyers and postcards for patient/caregiver outreach (Advertisement Study Flyer Print; Schema Postcard).
  • Study webpage postings and online materials (country-specific recruitment materials and website content PDFs).
  • HCP-targeted communications (materials labelled Website HCP, HCP referral materials).

Geography

Total Number Of Sites
123
Total Number Of Participants
126

Belgium

Earliest CTIS Part Ii Submission Date
20-08-2024
Latest Decision Or Authorization Date
17-09-2024
Processing Time Days
28
Number Of Sites
5
Number Of Participants
5

Sites

Site Name
Centre Hospitalier Universitaire Dinant Godinne Sainte-Elisabeth-UCL-Namur
Department Name
Hematology
Principal Investigator Name
Julien Devreux
Principal Investigator Email
julien.devreux@chuuclnamur.uclouvain.be
Contact Person Name
Julien Devreux
Site Name
UZ Leuven
Department Name
Hematology
Principal Investigator Name
Timothy Devos
Principal Investigator Email
timothy.devos@uzleuven.be
Contact Person Name
Timothy Devos
Contact Person Email
timothy.devos@uzleuven.be
Site Name
Algemeen Ziekenhuis Delta
Department Name
Hematology
Principal Investigator Name
Lien Deleu
Principal Investigator Email
lien.deleu@azdelta.be
Contact Person Name
Lien Deleu
Contact Person Email
lien.deleu@azdelta.be
Site Name
Het Ziekenhuisnetwerk Antwerpen
Department Name
Hematology
Principal Investigator Name
Nikki Granacher
Principal Investigator Email
nikki.granacher@zna.be
Contact Person Name
Nikki Granacher
Contact Person Email
nikki.granacher@zna.be
Site Name
Centre hospitalier universitaire de Liege
Department Name
Hematology
Principal Investigator Name
Gaelle Vertenoeil
Principal Investigator Email
gaelle.vertenoeil@chuliege.be
Contact Person Name
Gaelle Vertenoeil
Contact Person Email
gaelle.vertenoeil@chuliege.be

Croatia

Earliest CTIS Part Ii Submission Date
27-08-2024
Latest Decision Or Authorization Date
22-09-2024
Processing Time Days
26
Number Of Sites
8
Number Of Participants
7

Sites

Site Name
Clinical Hospital Dubrava
Department Name
Hematology
Principal Investigator Name
Marko Lucijanic
Principal Investigator Email
markolucijanic@yahoo.com
Contact Person Name
Marko Lucijanic
Contact Person Email
markolucijanic@yahoo.com
Site Name
Klinicka bolnica Merkur
Department Name
Hematology
Principal Investigator Name
Marko Martinovic
Principal Investigator Email
Marko.Martinovic@kb-merkur.hr
Contact Person Name
Marko Martinovic
Contact Person Email
Marko.Martinovic@kb-merkur.hr
Site Name
General Hospital Sibenik
Department Name
Hematology
Principal Investigator Name
Ivan Krecak
Principal Investigator Email
krecak.ivan@gmail.com
Contact Person Name
Ivan Krecak
Contact Person Email
krecak.ivan@gmail.com
Site Name
University Hospital Centre Zagreb
Department Name
Hematology
Principal Investigator Name
Pavle Roncevic
Principal Investigator Email
kronac@gmail.com
Contact Person Name
Pavle Roncevic
Contact Person Email
kronac@gmail.com
Site Name
KBC Split
Department Name
Hematology
Principal Investigator Name
Davor Galusic
Principal Investigator Email
davorgalusic@net.hr
Contact Person Name
Davor Galusic
Contact Person Email
davorgalusic@net.hr
Site Name
Poliklinika Solmed d.o.o.
Department Name
Hematology
Principal Investigator Name
Goran Rincic
Principal Investigator Email
grincic@yahoo.com
Contact Person Name
Goran Rincic
Contact Person Email
grincic@yahoo.com
Site Name
Clinical Hospital Centre Rijeka
Department Name
Hematology
Principal Investigator Name
Dragana Grohovac
Principal Investigator Email
dzdrijeka@gmail.com
Contact Person Name
Dragana Grohovac
Contact Person Email
dzdrijeka@gmail.com
Site Name
Clinical Hospital Dubrava (additional site listing) or duplicate entries

Germany

Earliest CTIS Part Ii Submission Date
23-08-2024
Latest Decision Or Authorization Date
18-09-2024
Processing Time Days
26
Number Of Sites
13
Number Of Participants
15

Sites

Site Name
Universitaetsklinikum Jena KöR
Department Name
Clinic for Internal Medicine II. Department of Haematology and Oncology
Principal Investigator Name
Carl Crodel
Principal Investigator Email
Carl.Crodel@med.uni-jena.de
Contact Person Name
Carl Crodel
Contact Person Email
Carl.Crodel@med.uni-jena.de
Site Name
Marien Hospital Duesseldorf GmbH
Department Name
Clinic for Oncology, Haematology and Palliative Medicine
Principal Investigator Name
Stefanie Groepper
Principal Investigator Email
stefanie.groepper@vkkd-kliniken.de
Contact Person Name
Stefanie Groepper
Site Name
Martin-Luther-Universitaet Halle-Wittenberg
Department Name
Internal Medicine IV (Haematology and Oncology)
Principal Investigator Name
Haifa Kathrin Al-Ali
Principal Investigator Email
haifa.al-ali@uk-halle.de
Contact Person Name
Haifa Kathrin Al-Ali
Contact Person Email
haifa.al-ali@uk-halle.de
Site Name
Kliniken Ostalb
Department Name
Oncology Center
Principal Investigator Name
Holger Hebart
Principal Investigator Email
holger.hebart@kliniken-ostalb.de
Contact Person Name
Holger Hebart
Site Name
Robert Bosch Krankenhaus GmbH
Department Name
Haemotology, Oncology and Palliative Medicine
Principal Investigator Name
Martin Kaufmann
Principal Investigator Email
martin.kaufmann@rbk.de
Contact Person Name
Martin Kaufmann
Contact Person Email
martin.kaufmann@rbk.de
Site Name
Klinikum rechts der Isar der TU Muenchen AöR
Department Name
III. Medical Department
Principal Investigator Name
Peter Herhaus
Principal Investigator Email
peter.herhaus@mri.tum.de
Contact Person Name
Peter Herhaus
Contact Person Email
peter.herhaus@mri.tum.de
Site Name
University Medical Center Hamburg-Eppendorf
Department Name
II. Medical Clinic and Polyclinic
Principal Investigator Name
Philippe Schafhausen
Principal Investigator Email
schafhausen@uke.de
Contact Person Name
Philippe Schafhausen
Contact Person Email
schafhausen@uke.de
Site Name
Medizinische Hochschule Hannover
Department Name
Clinic for Haematology, Haemostaseology, Oncology and Stem Cell Transplantation
Principal Investigator Name
Susanne Isfort
Principal Investigator Email
isfort.susanne@mh-hannover.de
Contact Person Name
Susanne Isfort
Contact Person Email
isfort.susanne@mh-hannover.de
Site Name
Medical Center - University Of Freiburg
Department Name
Clinic for Internal Medicine I Haematology, Oncology and Stell Cell Transplantation
Principal Investigator Name
Heiko Becker
Principal Investigator Email
heiko.becker@uniklinik-freiburg.de
Contact Person Name
Heiko Becker
Site Name
MVZ Leipzig Mitte
Department Name
Onkology, Haematology, Palliative Medicine
Principal Investigator Name
Baerbel Schaedlich
Principal Investigator Email
b.schaedlich@mvz-mitte-leipzig.de
Contact Person Name
Baerbel Schaedlich
Site Name
Universitaetsklinikum Heidelberg AöR
Department Name
Centre for Internal Medicine (Krehl Clinic), Department of Haematology, Oncology, Rheumatology
Principal Investigator Name
Tim Sauer
Principal Investigator Email
tim.sauer@med.uni-heidelberg.de
Contact Person Name
Tim Sauer
Site Name
Universitaetsklinikum Ulm AöR
Department Name
Clinic for Internal Medicine III Medical Clinic (oberer Eselsberg)
Principal Investigator Name
Konstanze Doehner
Principal Investigator Email
konstanze.doehner@uniklinik-ulm.de
Contact Person Name
Konstanze Doehner
Site Name
Klinikum Nuernberg
Department Name
Clinic for Internal Medicine V
Principal Investigator Name
Stefan Knop
Principal Investigator Email
stefan.knop@klinikum-nuernberg.de
Contact Person Name
Stefan Knop

Greece

Earliest CTIS Part Ii Submission Date
06-09-2024
Latest Decision Or Authorization Date
18-09-2024
Processing Time Days
12
Number Of Sites
5
Number Of Participants
5

Sites

Site Name
Geniko Nosokomeio Thessalonikis George Papanikolaou
Department Name
Haematology Clinic
Principal Investigator Name
Damianos Sotiropoulos
Principal Investigator Email
dsotiro@otenet.gr
Contact Person Name
Damianos Sotiropoulos
Contact Person Email
dsotiro@otenet.gr
Site Name
General University Hospital Of Patras
Department Name
Haematology Department
Principal Investigator Name
Alexandros Spyridonidis
Principal Investigator Email
spyridonidis@upatras.gr
Contact Person Name
Alexandros Spyridonidis
Contact Person Email
spyridonidis@upatras.gr
Site Name
University General Hospital Of Ioannina
Department Name
Department of Haematology
Principal Investigator Name
Eleftheria Hatzimichael
Principal Investigator Email
ehatzim@uoi.gr
Contact Person Name
Eleftheria Hatzimichael
Contact Person Email
ehatzim@uoi.gr
Site Name
University General Hospital Attikon General Hospital Of West Attica H Agia Varvara
Department Name
2nd Department of Propaedeutic Internal Medicine
Principal Investigator Name
Panagiotis Tsirigotis
Principal Investigator Email
panagtsirigotis@gmail.com
Contact Person Name
Panagiotis Tsirigotis
Contact Person Email
panagtsirigotis@gmail.com
Site Name
Laiko General Hospital Of Athens
Department Name
Haematology Clinic
Principal Investigator Name
Panayiotis Panayiotidis
Principal Investigator Email
ppanayi@med.uoa.gr
Contact Person Name
Panayiotis Panayiotidis
Contact Person Email
ppanayi@med.uoa.gr

Poland

Earliest CTIS Part Ii Submission Date
19-08-2024
Latest Decision Or Authorization Date
22-09-2024
Processing Time Days
34
Number Of Sites
18
Number Of Participants
18

Sites

Site Name
Szpital Uniwersytecki Nr 2 Im Dr Jana Biziela W Bydgoszczy
Department Name
Department of Hematology
Principal Investigator Name
Marta Sobas
Principal Investigator Email
marta.sobas@gmail.com
Contact Person Name
Marta Sobas
Contact Person Email
marta.sobas@gmail.com
Site Name
Szpital Kliniczny Ministerstwa Spraw Wewnetrznych I Administracji Z Warminsko-Mazurskim Centrum Onkologii W Olsztynie
Department Name
Oddział Kliniczny Hematologii i Chorób Wewnętrznych z Ośrodkiem Transplantacji Szpiku
Principal Investigator Name
Janusz Hałka
Principal Investigator Email
janusz.halka@poliklinika.net
Contact Person Name
Janusz Hałka
Contact Person Email
janusz.halka@poliklinika.net
Site Name
Pratia Hematologia Sp. z o.o.
Department Name
Pratia Onkologia Katowice
Principal Investigator Name
Sebastian Grosicki
Principal Investigator Email
kontakt.onkologia@pratia.com
Contact Person Name
Sebastian Grosicki
Contact Person Email
kontakt.onkologia@pratia.com
Site Name
"InterHem" Katarzyna Mazgajska-Barczyk, Marek Milewski, Jarosław Piszcz, Piotr Radziwon Sp. j
Department Name
Oddział Hematologiczny Nowotworów Krwi
Principal Investigator Name
Jarosław Piszcz
Principal Investigator Email
jaroslaw.piszcz@gmail.com
Contact Person Name
Jarosław Piszcz
Contact Person Email
jaroslaw.piszcz@gmail.com
Site Name
Szpital Specjalistyczny Im. Jedrzeja Sniadeckiego W Nowym Saczu SPZOZ
Department Name
Oddział Hematologiczny
Principal Investigator Name
Szymon Fornagiel
Principal Investigator Email
szf@wp.pl
Contact Person Name
Szymon Fornagiel
Contact Person Email
szf@wp.pl
Site Name
Clinical Best Solutions Sp. z o.o. S.K.
Principal Investigator Name
Joanna Barankiewicz
Principal Investigator Email
Joanna.barankiewicz@gmail.com
Contact Person Name
Joanna Barankiewicz
Contact Person Email
Joanna.barankiewicz@gmail.com
Site Name
Specjalistyczny Szpital Im. Dra Alfreda Sokolowskiego
Department Name
Oddział Hematologiczny
Principal Investigator Name
Aleksandra Butrym
Principal Investigator Email
aleksandra.butrym@zdrowie.walbrzych.pl
Contact Person Name
Aleksandra Butrym
Site Name
Samodzielny Publiczny Zaklad Opieki Zdrowotnej Szpital Uniwersytecki W Krakowie
Department Name
Poradnia Hematologiczna
Principal Investigator Name
Tomasz Sacha
Principal Investigator Email
sachatom@gmail.com
Contact Person Name
Tomasz Sacha
Contact Person Email
sachatom@gmail.com
Site Name
Uniwersyteckie Centrum Kliniczne
Department Name
Klinika Hematologii, Transplantologii i Terapii Komórkowych
Principal Investigator Name
Witold Prejzner
Principal Investigator Email
wpre@gumed.edu.pl
Contact Person Name
Witold Prejzner
Contact Person Email
wpre@gumed.edu.pl
Site Name
Wojewodzki Szpital Zespolony Im.L.Rydygiera W Toruniu
Department Name
Oddział Hematologii
Principal Investigator Name
Magdalena Szczepańska
Principal Investigator Email
magzal@vp.pl
Contact Person Name
Magdalena Szczepańska
Contact Person Email
magzal@vp.pl
Site Name
Centrum Medyczne Damiana Holding Sp. z o.o.
Department Name
DOM LEKARSKI - AMBULATORIUM STRUGA
Principal Investigator Name
Marcin Flont
Principal Investigator Email
marcin.flont@domlekarski.pl
Contact Person Name
Marcin Flont
Contact Person Email
marcin.flont@domlekarski.pl
Site Name
Uniwersytecki Szpital Kliniczny Im. Jana Mikulicza-Radeckiego We Wroclawiu
Department Name
Klinika Hematologii, Terapii Komórkowych i Chorób Wewnętrznych
Principal Investigator Name
Tomasz Wróbel
Principal Investigator Email
tomasz_wrobel@wp.pl
Contact Person Name
Tomasz Wróbel
Contact Person Email
tomasz_wrobel@wp.pl
Site Name
Aidport Sp. z o.o.
Department Name
AIDPORT
Principal Investigator Name
Łukasz Pruchniewski
Principal Investigator Email
lukasz.pruchniewski@aidport.pl
Contact Person Name
Łukasz Pruchniewski
Contact Person Email
lukasz.pruchniewski@aidport.pl
Site Name
Wojewodzki Szpital Specjalistyczny Im. Janusza Korczaka W Slupsku Sp. z o.o.
Department Name
Oddział hematologiczny
Principal Investigator Name
Wojciech Homenda
Principal Investigator Email
wojhom@sl.home.pl
Contact Person Name
Wojciech Homenda
Contact Person Email
wojhom@sl.home.pl
Site Name
Wojewodzkie Wielospecjalistyczne Centrum Onkologii I Traumatologii Im M.Kopernika W Lodzi
Department Name
Oddział Hematoonkologii i Chorób Wewnętrznych z Pododdziałem Chemioterapii Dziennej
Principal Investigator Name
Joanna Góra-Tybor
Principal Investigator Email
joannagora@op.pl
Contact Person Name
Joanna Góra-Tybor
Contact Person Email
joannagora@op.pl
Site Name
Other Poland listed sites (multiple)

Romania

Earliest CTIS Part Ii Submission Date
07-06-2024
Latest Decision Or Authorization Date
23-09-2024
Processing Time Days
108
Number Of Sites
5
Number Of Participants
7

Sites

Site Name
Institute Of Oncology Prof. Dr. Ion Chiricuta Cluj-Napoca
Department Name
Hematology
Principal Investigator Name
Ionut-Ciprian Tomuleasa
Principal Investigator Email
ciprian.tomuleasa@gmail.com
Contact Person Name
Ionut-Ciprian Tomuleasa
Contact Person Email
ciprian.tomuleasa@gmail.com
Site Name
Onco Card S.R.L.
Department Name
Hematology
Principal Investigator Name
Mihaela Cornelia Lazaroiu
Principal Investigator Email
mihaela.c.lazaroiu@gmail.com
Contact Person Name
Mihaela Cornelia Lazaroiu
Contact Person Email
mihaela.c.lazaroiu@gmail.com
Site Name
Spitalul Clinic Colentina Bucuresti
Department Name
Hematology
Principal Investigator Name
Viola Maria Popov
Principal Investigator Email
violamariap@gmail.com
Contact Person Name
Viola Maria Popov
Contact Person Email
violamariap@gmail.com
Site Name
Spitalul Clinic Judetean De Urgenta Bihor
Department Name
Hematology
Principal Investigator Name
Cristian Marcian Burca
Principal Investigator Email
cristian.burca@gmail.com
Contact Person Name
Cristian Marcian Burca
Contact Person Email
cristian.burca@gmail.com
Site Name
Spitalul Clinic Judetean De Urgenta Targu Mures
Department Name
Hematology
Principal Investigator Name
Ioan Macarie
Principal Investigator Email
macarie.ioan07@gmail.com
Contact Person Name
Ioan Macarie
Contact Person Email
macarie.ioan07@gmail.com

Italy

Earliest CTIS Part Ii Submission Date
07-06-2024
Latest Decision Or Authorization Date
18-09-2024
Processing Time Days
103
Number Of Sites
19
Number Of Participants
19

Sites

Site Name
Azienda Ospedaliera Ospedali Riuniti Marche Nord
Department Name
Hematology and Stem Cell Transplant Centre
Principal Investigator Name
Alessandro Isidori
Principal Investigator Email
alessandro.isidori@ospedalimarchenord.it
Contact Person Name
Alessandro Isidori
Site Name
Azienda Ospedaliero-Universitaria San Luigi Gonzaga
Department Name
Department of clinical and biological sciences
Principal Investigator Name
Alessandro Morotti
Principal Investigator Email
alessandro.morotti@unito.it
Contact Person Name
Alessandro Morotti
Contact Person Email
alessandro.morotti@unito.it
Site Name
Careggi University Hospital
Department Name
Department of Medical oncology
Principal Investigator Name
Alessandro Vannucchi
Principal Investigator Email
amvannucchi@unifi.it
Contact Person Name
Alessandro Vannucchi
Contact Person Email
amvannucchi@unifi.it
Site Name
Azienda Ospedaliero Universitaria Policlinico G Rodolico San Marco Di Catania
Department Name
Hematology with bone marrow transplantation
Principal Investigator Name
Giuseppe Palumbo
Principal Investigator Email
na.na@na.com
Contact Person Name
Giuseppe Palumbo
Contact Person Email
na.na@na.com
Site Name
Istituto Europeo Di Oncologia S.r.l.
Department Name
Onco-Hematology
Principal Investigator Name
Federica Gigli
Principal Investigator Email
federica.gigli@ieo.it
Contact Person Name
Federica Gigli
Contact Person Email
federica.gigli@ieo.it
Site Name
Azienda Sanitaria Locale Roma 2
Department Name
UOC Hematology
Principal Investigator Name
Elisabetta Abruzzese
Principal Investigator Email
ufficio.sperimentazioni@aslroma2.it
Contact Person Name
Elisabetta Abruzzese
Site Name
Azienda Unita Sanitaria Locale Della Romagna
Department Name
Oncology and Hematology Department
Principal Investigator Name
Arbana Dizdari
Principal Investigator Email
Dizdari.Arbana@auslromagna.it
Contact Person Name
Arbana Dizdari
Contact Person Email
Dizdari.Arbana@auslromagna.it
Site Name
Azienda Socio Sanitaria Territoriale Dei Sette Laghi
Department Name
Haematology Department
Principal Investigator Name
Marco Brociner
Principal Investigator Email
marco.brociner@asst-settelaghi.it
Contact Person Name
Marco Brociner
Site Name
Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
Department Name
SSD Medical Oncology Addarii
Principal Investigator Name
Francesca Palandri
Principal Investigator Email
francesca.palandri@unibo.it
Contact Person Name
Francesca Palandri
Contact Person Email
francesca.palandri@unibo.it
Site Name
Azienda Ospedaliera Ordine Mauriziano Di Torino
Department Name
SCDU Ematologia e Terapie cellulari
Principal Investigator Name
Elisabetta Rumi
Principal Investigator Email
s.rumi@smatteo.pv.it
Contact Person Name
Elisabetta Rumi
Contact Person Email
s.rumi@smatteo.pv.it
Site Name
Fondazione IRCCS Policlinico San Matteo
Department Name
Oncohematology, Operative Unit of Hematology
Principal Investigator Name
Elisabetta Rumi
Principal Investigator Email
s.rumi@smatteo.pv.it
Contact Person Name
Elisabetta Rumi
Contact Person Email
s.rumi@smatteo.pv.it
Site Name
Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia
Department Name
Hematology
Principal Investigator Name
Alessandra Tucci
Principal Investigator Email
alessandra.tucci@asst-spedalicivili.it
Contact Person Name
Alessandra Tucci
Site Name
Azienda Ospedaliero-Universitaria Maggiore Della Carita
Department Name
SCDU Ematology
Principal Investigator Name
Andrea Patriarca
Principal Investigator Email
andrea.patriarca@unipo.it
Contact Person Name
Andrea Patriarca
Contact Person Email
andrea.patriarca@unipo.it
Site Name
Azienda Ospedaliero-Universitaria Ss Antonio E Biagio E Cesare Arrigo
Department Name
Hematology Department
Principal Investigator Name
Monia Marchetti
Principal Investigator Email
monia.marchetti@ospedale.al.it
Contact Person Name
Monia Marchetti
Contact Person Email
monia.marchetti@ospedale.al.it
Site Name
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico
Department Name
Hematology
Principal Investigator Name
Francesco Passamonti
Principal Investigator Email
francesco.passamonti@policlinico.mi.it
Contact Person Name
Francesco Passamonti
Site Name
Azienda Ospedaliera Universitaria Policlinico Paolo Giaccone
Department Name
Hematology
Principal Investigator Name
Marco Santoro
Principal Investigator Email
marco.santoro1@policlinico.pa.it
Contact Person Name
Marco Santoro
Site Name
Istituto Romagnolo Per Lo Studio Dei Tumori Dino Amadori IRST S.r.l.
Department Name
Complex Structure of Clinical and Experimental Oncology in Innovative and High-Dose Thera
Principal Investigator Name
Alessandro Lucchesi
Principal Investigator Email
alessandro.lucchesi@irst.emr.it
Contact Person Name
Alessandro Lucchesi
Site Name
Azienda Ospedaliera Universitaria Citta Della Salute E Della Scienza Di Torino
Department Name
Hematology
Principal Investigator Name
Giulia Benevolo
Principal Investigator Email
gbenevolo@cittadellasalute.to.it
Contact Person Name
Giulia Benevolo

Hungary

Earliest CTIS Part Ii Submission Date
22-08-2024
Latest Decision Or Authorization Date
17-09-2024
Processing Time Days
26
Number Of Sites
5
Number Of Participants
5

Sites

Site Name
Tolna Varmegyei Balassa Janos Korhaz
Department Name
Department of Hematology
Principal Investigator Name
Renata Csalodi
Principal Investigator Email
csalodi.renata@tmkorhaz.hu
Contact Person Name
Renata Csalodi
Contact Person Email
csalodi.renata@tmkorhaz.hu
Site Name
Fejer Varmegyei Szent Gyoergy Egyetemi Oktato Korhaz
Department Name
Department of Internal Medicine III, Hematology
Principal Investigator Name
Arpad Szomor
Principal Investigator Email
info@mail.fmkorhaz.hu
Contact Person Name
Arpad Szomor
Contact Person Email
info@mail.fmkorhaz.hu
Site Name
Szabolcs-Szatmar-Bereg Varmegyei Oktatokorhaz
Department Name
Department of Hematology
Principal Investigator Name
Laszlo Rejto
Principal Investigator Email
lrejto@med.unideb.hu
Contact Person Name
Laszlo Rejto
Contact Person Email
lrejto@med.unideb.hu
Site Name
Semmelweis University
Department Name
Department of Internal Medicine and Haematology, Division of Hematology
Principal Investigator Name
Zsolt Nagy
Principal Investigator Email
nagy.zsolt@med.semmelweis-univ.hu
Contact Person Name
Zsolt Nagy
Site Name
Other Hungary listed sites

Austria

Earliest CTIS Part Ii Submission Date
07-06-2024
Latest Decision Or Authorization Date
22-09-2024
Processing Time Days
107
Number Of Sites
7
Number Of Participants
7

Sites

Site Name
Johannes Kepler University Linz
Department Name
Kepler University Hospital, Clinical Department of Internal Medicine III, Hematology and Oncology
Principal Investigator Name
Clemens Schmitt
Principal Investigator Email
c.schmitt@kepleruniklinikum.at
Contact Person Name
Clemens Schmitt
Contact Person Email
c.schmitt@kepleruniklinikum.at
Site Name
Medical University Of Graz
Department Name
Department of Internal Medicine Clinical Department of Hematology
Principal Investigator Name
Albert Woelfler
Principal Investigator Email
albert.woelfler@medunigraz.at
Contact Person Name
Albert Woelfler
Contact Person Email
albert.woelfler@medunigraz.at
Site Name
Medizinische Universitaet Innsbruck
Department Name
Medical University Innsbruck, Department of Internal Medicine V (Hematology and Oncology)
Principal Investigator Name
Dominik Wolf
Principal Investigator Email
dominik.wolf@i-med.ac.at
Contact Person Name
Dominik Wolf
Contact Person Email
dominik.wolf@i-med.ac.at
Site Name
Stadt Wien Wiener Gesundheitsverbund
Department Name
Hospital Ottakring, Department of Internal Medicine I
Principal Investigator Name
Frédéric Hermann Witte
Principal Investigator Email
Frederic.Witte@gesundheitsverbund.at
Contact Person Name
Frédéric Hermann Witte
Site Name
Steiermaerkische Krankenanstalten Ges.m.b.H.
Department Name
LKH Hochsteiermark, Department of Internal Medicine, Hematology and Internal Oncology
Principal Investigator Name
Thamer Sliwa
Principal Investigator Email
Thamer.Sliwa@kages.at
Contact Person Name
Thamer Sliwa
Contact Person Email
Thamer.Sliwa@kages.at
Site Name
Medical University Of Vienna
Department Name
Department of Internal Medicine I, Clinical Department of Hematology and Hemostaseology
Principal Investigator Name
Maria-Theresa Krauth
Principal Investigator Email
maria.krauth@meduniwien.ac.at
Contact Person Name
Maria-Theresa Krauth
Contact Person Email
maria.krauth@meduniwien.ac.at
Site Name
Ordensklinikum Linz GmbH
Department Name
Department of Internal Medicine I, Hemostaseology and Medical Oncology
Principal Investigator Name
Veronika Buxhofer-Ausch
Principal Investigator Email
veronika.buxhofer-ausch@ordensklinikum.at
Contact Person Name
Veronika Buxhofer-Ausch

France

Earliest CTIS Part Ii Submission Date
21-08-2024
Latest Decision Or Authorization Date
17-09-2024
Processing Time Days
27
Number Of Sites
12
Number Of Participants
12

Sites

Site Name
Centre Hospitalier Universitaire Amiens Picardie
Department Name
Hématologie Clinique et Thérapie Cellulaire
Principal Investigator Name
Etienne Paubelle
Principal Investigator Email
paubelle.etienne@chu-amiens.fr
Contact Person Name
Etienne Paubelle
Contact Person Email
paubelle.etienne@chu-amiens.fr
Site Name
Les Hopitaux Universitaires De Strasbourg
Department Name
Hématologie
Principal Investigator Name
Shanti Amé
Principal Investigator Email
s.ame@icans.eu
Contact Person Name
Shanti Amé
Contact Person Email
s.ame@icans.eu
Site Name
Centre Hospitalier Universitaire De Nantes
Department Name
Hématologie
Principal Investigator Name
Viviane Dubruille
Principal Investigator Email
viviane.dubruille@chu-nantes.fr
Contact Person Name
Viviane Dubruille
Site Name
Institut Universitaire Du Cancer Toulouse-Oncopole
Department Name
Hématologie
Principal Investigator Name
Suzanne Tavitian
Principal Investigator Email
tavitian.suzanne@iuct-oncopole.fr
Contact Person Name
Suzanne Tavitian
Site Name
Centre Leon Berard
Department Name
Oncologie Médicale
Principal Investigator Name
Franck-Emmanuel Nicolini
Principal Investigator Email
franck-emmanuel.nicolini@lyon.unicancer.fr
Contact Person Name
Franck-Emmanuel Nicolini
Site Name
Centre Hospitalier Regional Universitaire De Tours
Department Name
Hématologie et Thérapie Cellulaire, Hôpital Bretonneau
Principal Investigator Name
Antoine Machet
Principal Investigator Email
a.machet@chu-tours.fr
Contact Person Name
Antoine Machet
Contact Person Email
a.machet@chu-tours.fr
Site Name
Centre Hospitalier Universitaire D'Angers
Department Name
Maladies du sang
Principal Investigator Name
Françoise Boyer
Principal Investigator Email
frboyer-perrard@chu-angers.fr
Contact Person Name
Françoise Boyer
Contact Person Email
frboyer-perrard@chu-angers.fr
Site Name
Centre Hospitalier Universitaire De Nimes
Department Name
Institut de Cancérologie du Gard
Principal Investigator Name
Stefan Wickenhauser
Principal Investigator Email
stefan.wickenhauser@chu-nimes.fr
Contact Person Name
Stefan Wickenhauser
Site Name
Centre Hospitalier Universitaire De Poitiers
Department Name
Oncologie Hématologique et Thérapie Cellulaire
Principal Investigator Name
Jose Miguel Torregrosa-Diaz
Contact Person Name
Jose Miguel Torregrosa-Diaz
Site Name
Centre Hospitalier Universitaire De Lille
Department Name
Maladie du Sang, Hôpital Claude Huriez
Principal Investigator Name
Mathieu Wemeau
Principal Investigator Email
mathieu.wemeau@chu-lille.fr
Contact Person Name
Mathieu Wemeau
Contact Person Email
mathieu.wemeau@chu-lille.fr
Site Name
Centre Hospitalier Universitaire De Nice
Department Name
Hématologie, Hôpital Archet 1
Principal Investigator Name
Michael Loschi
Principal Investigator Email
loschi.m@chu-nice.fr
Contact Person Name
Michael Loschi
Contact Person Email
loschi.m@chu-nice.fr
Site Name
Centre Hospitalier Universitaire De Bordeaux
Department Name
Hématologie, Hôpital Haut Lévêque
Principal Investigator Name
Clémence Mediavilla
Principal Investigator Email
cIemence.mediavilla@chu-bordeaux.fr
Contact Person Name
Clémence Mediavilla

Czechia

Earliest CTIS Part Ii Submission Date
21-08-2024
Latest Decision Or Authorization Date
19-09-2024
Processing Time Days
29
Number Of Sites
5
Number Of Participants
5

Sites

Site Name
Fakultni Nemocnice Ostrava
Department Name
Klinika hematologie
Principal Investigator Name
Lukáš Stejskal
Principal Investigator Email
lukas.stejskal@fno.cz
Contact Person Name
Lukáš Stejskal
Contact Person Email
lukas.stejskal@fno.cz
Site Name
Fakultni Nemocnice Brno
Department Name
Interní hematologická a onkologická klinika
Principal Investigator Name
Jiří Mayer
Principal Investigator Email
mayer.jiri@fnbrno.cz
Contact Person Name
Jiří Mayer
Contact Person Email
mayer.jiri@fnbrno.cz
Site Name
Fakultni Nemocnice Hradec Kralove
Department Name
IV. Interní klinica hematologie
Principal Investigator Name
Petra Bělohlávková
Principal Investigator Email
petra.belohlavkova@fnhk.cz
Contact Person Name
Petra Bělohlávková
Contact Person Email
petra.belohlavkova@fnhk.cz
Site Name
Institute Of Hematology And Blood Transfusion
Department Name
Ústav hematologie a krevní transfuze
Principal Investigator Name
Jacqueline Soukupová Maaloufová
Principal Investigator Email
jacqueline.maaloufova@uhkt.cz
Contact Person Name
Jacqueline Soukupová Maaloufová
Contact Person Email
jacqueline.maaloufova@uhkt.cz
Site Name
Fakultni Nemocnice Kralovske Vinohrady
Department Name
Interní hematologická klinika
Principal Investigator Name
Olga Černá
Principal Investigator Email
olga.cerna@fnkv.cz
Contact Person Name
Olga Černá
Contact Person Email
olga.cerna@fnkv.cz

Spain

Earliest CTIS Part Ii Submission Date
30-08-2024
Latest Decision Or Authorization Date
23-09-2024
Processing Time Days
24
Number Of Sites
15
Number Of Participants
15

Sites

Site Name
Hospital Universitario Y Politecnico La Fe
Department Name
Hematology
Principal Investigator Name
Elvira Mora Castera
Principal Investigator Email
mora_elv@gva.es
Contact Person Name
Elvira Mora Castera
Contact Person Email
mora_elv@gva.es
Site Name
Hospital Universitario De Salamanca
Department Name
Hematology
Principal Investigator Name
Jesús María Hernández Rivas
Principal Investigator Email
jmhr@usal.es
Contact Person Name
Jesús María Hernández Rivas
Contact Person Email
jmhr@usal.es
Site Name
Hospital Del Mar
Department Name
Hematology
Principal Investigator Name
Alicia Senin Magan
Principal Investigator Email
msenin@psmar.cat
Contact Person Name
Alicia Senin Magan
Contact Person Email
msenin@psmar.cat
Site Name
Hospital Universitari Vall D Hebron
Department Name
Hematology
Principal Investigator Name
Maria Laura Fox
Principal Investigator Email
mlfox@vhio.net
Contact Person Name
Maria Laura Fox
Contact Person Email
mlfox@vhio.net
Site Name
Hospital Clinico Universitario De Valencia
Department Name
Hematology
Principal Investigator Name
Juan Carlos Hernández Boluda
Principal Investigator Email
hernandez_jca@gva.es
Contact Person Name
Juan Carlos Hernández Boluda
Contact Person Email
hernandez_jca@gva.es
Site Name
Hospital Universitario Virgen De La Victoria
Department Name
Hematology
Principal Investigator Name
Regina García Delgado
Principal Investigator Email
reginagarciadel@yahoo.es
Contact Person Name
Regina García Delgado
Contact Person Email
reginagarciadel@yahoo.es
Site Name
Hospital Universitario Ramon Y Cajal
Department Name
Hematology
Principal Investigator Name
José Valentín García Gutiérrez
Principal Investigator Email
jvalentingg@gmail.com
Contact Person Name
José Valentín García Gutiérrez
Contact Person Email
jvalentingg@gmail.com
Site Name
University Hospital Son Espases
Department Name
Hematology and Hemotherapy
Principal Investigator Name
Sara Montolío Chiva
Principal Investigator Email
sara.montolio@ssib.es
Contact Person Name
Sara Montolío Chiva
Contact Person Email
sara.montolio@ssib.es
Site Name
Institut Catala D'oncologia (Badalona)
Department Name
Hematology
Principal Investigator Name
Blanca Xicoy Cirici
Principal Investigator Email
bxicoy@iconcologia.net
Contact Person Name
Blanca Xicoy Cirici
Contact Person Email
bxicoy@iconcologia.net
Site Name
Hospital Universitario 12 De Octubre
Department Name
Hematology
Principal Investigator Name
Rosa Ayala Díaz
Principal Investigator Email
rayaladiaz12@gmail.com
Contact Person Name
Rosa Ayala Díaz
Contact Person Email
rayaladiaz12@gmail.com
Site Name
El Hospital Universitario De Gran Canaria Dr. Negrin
Department Name
Hematology
Principal Investigator Name
Adrián Segura Díaz
Principal Investigator Email
adsegura@hotmail.es
Contact Person Name
Adrián Segura Díaz
Contact Person Email
adsegura@hotmail.es
Site Name
Institut Catala D'oncologia (L'Hospitalet)
Department Name
Hematology
Principal Investigator Name
Carolina Martínez Gómez
Principal Investigator Email
carolinamariamartinez@iconcologia.net
Contact Person Name
Carolina Martínez Gómez
Site Name
Hospital Quironsalud Zaragoza
Department Name
Hematology
Principal Investigator Name
Pilar Giraldo Castellano
Principal Investigator Email
giraldocastellano@gmail.com
Contact Person Name
Pilar Giraldo Castellano
Contact Person Email
giraldocastellano@gmail.com
Site Name
Hospital Universitario De Salamanca (additional listings)

Portugal

Earliest CTIS Part Ii Submission Date
23-08-2024
Latest Decision Or Authorization Date
23-09-2024
Processing Time Days
31
Number Of Sites
6
Number Of Participants
6

Sites

Site Name
CCAB Centro Clinico Academico Braga Associacao
Department Name
Oncology
Principal Investigator Name
Marco Dias
Principal Investigator Email
marco.dias@hb.min-saude.pt
Contact Person Name
Marco Dias
Contact Person Email
marco.dias@hb.min-saude.pt
Site Name
Unidade Local De Saude Da Regiao De Aveiro E.P.E.
Department Name
Hematology
Principal Investigator Name
Fernando Silva
Principal Investigator Email
fernando.silva.70836@chbv.min-saude.pt
Contact Person Name
Fernando Silva
Site Name
Unidade Local De Saude De Gaia/Espinho E.P.E.
Department Name
Hematolgy
Principal Investigator Name
Marcio Tavares
Principal Investigator Email
marcio.tavares@chvng.min-saude.pt
Contact Person Name
Marcio Tavares
Site Name
Unidade Local De Saude De Lisboa Ocidental E.P.E.
Department Name
Hematology
Principal Investigator Name
Celina Afonso
Principal Investigator Email
ccafonso@chlo.min-saude.pt
Contact Person Name
Celina Afonso
Contact Person Email
ccafonso@chlo.min-saude.pt
Site Name
Unidade Local De Saude Do Alto Minho E.P.E.
Department Name
Hematology
Principal Investigator Name
Mafalda Pimenta de Castro
Principal Investigator Email
mafalda.pimenta.castro@ulsam.min-saude.pt
Contact Person Name
Mafalda Pimenta de Castro
Site Name
Unidade Local De Saude De Santa Maria E.P.E.
Department Name
Hematolgy
Principal Investigator Name
Maria Blanca Polo Guerrero
Principal Investigator Email
maria.guerrero@chln.min-saude.pt
Contact Person Name
Maria Blanca Polo Guerrero

Sponsor

Primary sponsor

Full Name
Kartos Therapeutics Inc.
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Contract research organisations

Name
Psi CRO Greece
Responsibilities
Operational CRO responsibilities (listed sponsor duties include administrative and operational support)
Name
Psi Cro AG
Responsibilities
Operational CRO responsibilities (multiple sponsor duties listed)
Name
Ppd Inc.
Responsibilities
Vendor services (assay services)
Name
IQVIA Laboratories
Responsibilities
Laboratory/genetic testing support

Third parties

  • {"country":"United States","full_name":"EPL Pathology Archives LLC","duties_or_roles":"Storage of the samples for future testing","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Germany","full_name":"Fisher Clinical Services GmbH","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Ppd Inc.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Flagship Biosciences Inc.","duties_or_roles":"Genetic testing","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Aperio Clinical Outcomes LLC","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"IQVIA Laboratories","duties_or_roles":"Genetic Testing","organisation_type":"Industry"}
  • {"country":"Ireland","full_name":"Signant Health Global Solutions Limited","duties_or_roles":"ePRO","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Myriad RBM Inc.","duties_or_roles":"","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Greece","full_name":"Psi CRO Greece","duties_or_roles":"Multiple sponsor duties (administrative/operational roles as listed)","organisation_type":"Pharmaceutical company / CRO"}
  • {"country":"Switzerland","full_name":"Psi Cro AG","duties_or_roles":"Multiple sponsor duties (administrative/operational roles as listed)","organisation_type":"Pharmaceutical company / CRO"}
  • {"country":"United States","full_name":"Celerion Inc.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"Germany","full_name":"PrimeVigilance GmbH","duties_or_roles":"Pharmacovigilance","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Suvoda LLC","duties_or_roles":"","organisation_type":"Non-Pharmaceutical company (Vendor)"}
  • {"country":"United States","full_name":"Eurofins Central Laboratory LLC","duties_or_roles":"","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Perceptive Informatics Inc.","duties_or_roles":"Central imaging","organisation_type":"Pharmaceutical company / vendor"}

Investigational products

Investigational Product Name
Navtemadlin (KRT-232) / Navtemadlin 25-120 / Navtemadlin 25-60 / Navtemadlin 25-30 / Navtemadlin 25-180
Active Substance
NAVTEMADLIN
Modality
Small molecule
Routes Of Administration
ORAL
Route
Oral tablet
Authorisation Status
Investigational (product entries indicate PRD numbers; not standard marketing authorisation)
Dose Levels
Available tablet strengths referenced: 25-30 mg, 25-60 mg, 25-120 mg, 25-180 mg (product names indicate strength ranges)
Maximum Dose
240 mg (max daily dose amount listed)
Investigational Product Name
RUXOLITINIB
Active Substance
RUXOLITINIB
Modality
Small molecule
Routes Of Administration
ORAL
Route
Oral tablet
Authorisation Status
Authorised (product entry shows market authorisation status code indicating authorised product record)
Maximum Dose
50 mg (max daily dose amount listed)
Investigational Product Name
ONDANSETRON (auxiliary antiemetic)
Active Substance
ONDANSETRON
Modality
Small molecule
Routes Of Administration
ORAL
Route
Oral tablet/capsule
Authorisation Status
Authorised (marketing product record present)
Maximum Dose
16 mg (max daily dose amount listed)
Investigational Product Name
LOPERAMIDE (auxiliary)
Active Substance
LOPERAMIDE HYDROCHLORIDE
Modality
Small molecule
Routes Of Administration
ORAL
Route
Oral tablet/capsule
Authorisation Status
Authorised (marketing product record present)
Dose Levels
2 mg tablet formulation referenced
Maximum Dose
16 mg (max daily dose amount listed)
Combination Treatment
Yes

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