Clinical trial • Phase II/III • Oncology

LENVATINIB for Ewing sarcoma | Recurrent Ewing sarcoma | Primary refractory Ewing sarcoma

Phase II/III trial of LENVATINIB for Ewing sarcoma | Recurrent Ewing sarcoma | Primary refractory Ewing sarcoma.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Ewing sarcoma | Recurrent Ewing sarcoma | Primary refractory Ewing sarcoma
Trial Stage
Phase II/III
Drug Modality
Small molecule
Paediatric Trial
Yes

Key dates

Initial CTIS Submission Date
15-10-2024
First CTIS Authorization Date
29-11-2024

Trial design

Randomised, open-label, arms referenced include ce, ifos and ifos-l (arm names referenced in protocol/endpoints); specific drug composition, doses and schedules per comparator arm are not specified in the provided json.-controlled Phase II/III trial in Austria, Belgium, Czechia and others.

Randomised
Yes
Open Label
Yes
Comparator
Arms referenced include CE, IFOS and IFOS-L (arm names referenced in protocol/endpoints); specific drug composition, doses and schedules per comparator arm are not specified in the provided JSON.
Target Sample Size
276

Eligibility

Recruits 276 paediatric patients.

Pregnancy Exclusion
Pregnant or breastfeeding women.
Vulnerable Population
Vulnerable populations (children/adolescents) are included. The protocol requires "Written informed consent from the patient and/or parent/legal guardian." Age-specific patient information sheets and consent/assent forms are provided (children, adolescents, parents/guardians and adults) and country-specific versions are available per site/documents.

Inclusion criteria

  • {"criterion_text":"- Histologically confirmed Ewing or Ewing-like sarcoma of the bone or soft tissues. Histological confirmation either at initial diagnosis or disease progression.\n- Patient agrees to use effective contraception during therapy and for 12 months after last trial treatment, where applicable.\n- For IFOS/IFOS-L randomisation only: Adequate liver function: bilirubin <3 x ULN and ALT or AST < 5 x ULN.\n- For IFOS/IFOS-L randomisation only: Left ventricular ejection fraction ≥50% at baseline as determined by echocardiography.\n- For IFOS/IFOS-L randomisation only: Adequately controlled blood pressure (BP) with or without antihypertensive medications, defined as: a. BP <95th percentile for sex, age, and height. Subjects >18 years of age should have BP ≤150/90 mm Hg at screening.\n- For IFOS/IFOS-L randomisation only: Urine dipstick <2+ for proteinuria. If ≥2+ proteinuria on dipstick, a spot urine protein:creatinine ratio test must be < CTCAE grade 2 Proteinuria.\n- Written informed consent from the patient and/or parent/legal guardian.\n- Radiological evidence of disease progression during or after completion of first or any subsequent line of treatment.\n- Age ≥ 2 years (* Trial sites in Austria will only recruit patients aged ≥2 years<30 years due to the conditional approval issued by their ethics committee).\n- Eligible for randomisation between at least two open study arms.\n- Adequate renal function defined as GFR ≥60 ml/min/1.73m2. If GFR is calculated and is <90 ml/min/1.73m2, an isotopic GFR should be performed to confirm adequate renal function.\n- Patient assessed as medically fit to receive trial treatment.\n- Date of planned randomisation within 4 weeks of baseline imaging.\n- Documented negative pregnancy test for female patients of childbearing potential."}

Exclusion criteria

  • {"criterion_text":"- Absolute Neutrophil Count (ANC) <1.0 x 109/L or platelets <75 x 109/L.\n- Pre-existing medical condition that would necessitate a dose modification during cycle 1 as described in section 7 of the protocol.\n- Any central neurotoxicity with previous ifosfamide treatment.\n- For CE randomisation only: Carboplatin is contraindicated in patients with actively bleeding tumours. Therefore, patients with actively bleeding tumours are not eligible for the CE randomisation.\n- For IFOS/IFOS-L randomisation only: Clinically significant ECG abnormality, including a marked baseline prolonged QT or QTc interval (eg, a repeated demonstration of a QTc interval >480 msec).\n- For IFOS/IFOS-L randomisation only: History of aneurysm.\n- For IFOS/IFOS-L randomisation only: Arterial Thromboembolism in previous 6 months.\n- For IFOS/IFOS-L randomisation only: Gastrointestinal or non-gastrointestinal fistula.\n- For IFOS/IFOS-L randomisation only: Gastrointestinal bleeding or active haemoptysis within previous 3 weeks.\n- For IFOS/IFOS-L randomisation only: Major surgery within previous 3 weeks.\n- For IFOS/IFOS-L randomisation only: Previous treatment with tyrosine kinase inhibitors.\n- Clinical evidence of nephrotic syndrome.\n- For IFOS/IFOS-L randomisation only: Radiographic evidence of intratumoral cavitation, encasement, or invasion of a major blood vessel, or proximity to major blood vessels with potential risk of severe haemorrhage associated with tumor shrinkage/necrosis after lenvatinib therapy.\n- Follow-up not possible due to social, geographic or psychological reasons.\n- Previous randomisation into the rEECur trial.\n- Patients with a contraindication or hypersensitivity to any IMP may not be randomised to receive an arm that contains the contraindicated IMP.\n- Patients who have previously received one of the trial regimens off-trial may not be randomised to receive that regimen again. Patients who have had ifosfamide during first line therapy may receive the IFOS or IFOS-L arm. There is no requirement for a minimum time between receiving first line ifosfamide and entry to rEECur.\n- Cytotoxic chemotherapy or other investigational medicinal product (IMP) within previous two weeks.\n- Radiotherapy to target lesion within previous six weeks.\n- Pregnant or breastfeeding women."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Event-free survival time (EFS)","definition_or_measurement_approach":""}

Secondary endpoints

  • {"endpoint_text":"- Objective imaging response (OR) according to RECIST 1.1 criteria after 2, 4, and 6 cycles for CE and after 2 and 4 cycles for IFOS and IFOS-L, and at the end of trial treatment for all arms","definition_or_measurement_approach":"Measured using RECIST 1.1 criteria at specified cycle timepoints (after 2, 4, 6 cycles as specified per arm and at end of treatment)."}
  • {"endpoint_text":"- Progression-free survival time (PFS)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Overall survival time (OS)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Toxicity, defined by National Cancer Institute Common Terminology Criteria for Adverse Events (CTCAE) v4.0 (see Appendix 2 of protocol)","definition_or_measurement_approach":"Adverse events graded using NCI CTCAE v4.0."}
  • {"endpoint_text":"- PET-CT response after 4 cycles","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Quality of life (QoL)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Days spent in hospital","definition_or_measurement_approach":""}

Recruitment

Planned Sample Size
276
Recruitment Window Months
194
Consent Approach
Written informed consent from the patient and/or parent/legal guardian is required. Age-specific information and consent/assent documents are provided (children, adolescents, parents/guardians, adults). Country/language-specific ICF/PIS documents are listed (examples: Austria - DE; Belgium - FR/NL; Czechia - CS; Denmark - DA; Finland - FI; France - FR; Italy - IT; Spain - ES; Netherlands - NL; Norway - NO).

Geography

Total Number Of Sites
57
Total Number Of Participants
436

Austria

Earliest CTIS Part Ii Submission Date
30-10-2024
Latest Decision Or Authorization Date
02-12-2024
Processing Time Days
33
Number Of Sites
5
Number Of Participants
10

Sites

Site Name
Medical University Of Graz
Department Name
Klinische Abteilung für Pädiatrische Hämatologie/Onkologie
Principal Investigator Name
Martin Benesch
Principal Investigator Email
martin.benesch@medunigraz.at
Contact Person Name
Martin Benesch
Contact Person Email
martin.benesch@medunigraz.at
Site Name
Johannes Kepler University Linz
Department Name
Med Campus IV
Principal Investigator Name
Renate Steiner
Principal Investigator Email
renate.steiner@kepleruniklinikum.at
Contact Person Name
Renate Steiner
Site Name
Medizinische Universitaet Innsbruck
Department Name
Pädiatrie I Department für Kinder- und Jugendheilkunde
Principal Investigator Name
Roman Crazzolara
Principal Investigator Email
roman.crazzolara@i-med.ac.at
Contact Person Name
Roman Crazzolara
Contact Person Email
roman.crazzolara@i-med.ac.at
Site Name
Gemeinnuetzige Salzburger Landeskliniken Betriebsgesellschaft mbH
Department Name
Kinderspital / Abteilung für Kinderund Jugendheilkunde
Principal Investigator Name
Gabriele Dobrovoljski
Principal Investigator Email
gabriele.dobrovoljski@salk.at
Contact Person Name
Gabriele Dobrovoljski
Contact Person Email
gabriele.dobrovoljski@salk.at
Site Name
St. Anna Kinderspital GmbH
Department Name
Hämato/Onkologie
Principal Investigator Name
Caroline Hutter
Principal Investigator Email
Caroline.hutter@stanna.at
Contact Person Name
Caroline Hutter
Contact Person Email
Caroline.hutter@stanna.at

Belgium

Earliest CTIS Part Ii Submission Date
30-10-2024
Latest Decision Or Authorization Date
29-11-2024
Processing Time Days
30
Number Of Sites
1
Number Of Participants
8

Sites

Site Name
Cliniques Universitaires Saint-Luc
Department Name
Hematologie Pediatrique
Principal Investigator Name
Benedicte Brichard
Principal Investigator Email
benedicte.brichard@uclouvain.be
Contact Person Name
Benedicte Brichard

Czechia

Earliest CTIS Part Ii Submission Date
30-10-2024
Latest Decision Or Authorization Date
03-12-2024
Processing Time Days
34
Number Of Sites
1
Number Of Participants
7

Sites

Site Name
Fakultni Nemocnice V Motole
Department Name
Department of Oncology and Radiotherapy
Principal Investigator Name
Katerina Kopeckova
Principal Investigator Email
katerina.kopeckova@fnmotol.cz
Contact Person Name
Katerina Kopeckova
Contact Person Email
katerina.kopeckova@fnmotol.cz

Denmark

Earliest CTIS Part Ii Submission Date
30-10-2024
Latest Decision Or Authorization Date
29-11-2024
Processing Time Days
30
Number Of Sites
4
Number Of Participants
20

Sites

Site Name
Region Hovedstaden
Department Name
Department of Oncology
Principal Investigator Name
Bodil Engelmann
Principal Investigator Email
bodil.elisabeth.engelmann@regionh.dk
Contact Person Name
Bodil Engelmann
Site Name
Region Midtjylland
Department Name
Department of Paediatrics and Adolescent Medicine
Principal Investigator Name
Henrik Hasle
Principal Investigator Email
henrik.hasle@skejby.rm.dk
Contact Person Name
Henrik Hasle
Contact Person Email
henrik.hasle@skejby.rm.dk
Site Name
Rigshospitalet
Department Name
Department of Paediatrics and Adolescent Medicine
Principal Investigator Name
Karsten Nysom
Principal Investigator Email
Karsten.nysom@regionh.dk
Contact Person Name
Karsten Nysom
Contact Person Email
Karsten.nysom@regionh.dk
Site Name
Region Midtjylland
Department Name
Department of Oncology
Principal Investigator Name
Ninna Aggerholm-Pedersen
Principal Investigator Email
ninnpede@rm.dk
Contact Person Name
Ninna Aggerholm-Pedersen
Contact Person Email
ninnpede@rm.dk

Finland

Earliest CTIS Part Ii Submission Date
30-10-2024
Latest Decision Or Authorization Date
02-12-2024
Processing Time Days
33
Number Of Sites
5
Number Of Participants
20

Sites

Site Name
University Of Oulu
Department Name
Pediatrics
Principal Investigator Name
Elli-Maija Ukonmaanaho
Principal Investigator Email
elli-maija.ukonmaanaho@pohde.fi
Contact Person Name
Elli-Maija Ukonmaanaho
Site Name
HUS-Yhtymae
Department Name
Ped hem-onc
Principal Investigator Name
Jukka Kanerva
Principal Investigator Email
jukka.kanerva@hus.fi
Contact Person Name
Jukka Kanerva
Contact Person Email
jukka.kanerva@hus.fi
Site Name
HUS-Yhtymae
Department Name
Cancer Center
Principal Investigator Name
Susanna Mannisto
Principal Investigator Email
susanna.mannisto@hus.fi
Contact Person Name
Susanna Mannisto
Contact Person Email
susanna.mannisto@hus.fi
Site Name
Varsinais-Suomen hyvinvointialue
Department Name
Pediatrics
Principal Investigator Name
Anu Huurre
Principal Investigator Email
anu.huurre@varha.fi
Contact Person Name
Anu Huurre
Contact Person Email
anu.huurre@varha.fi
Site Name
Pirkanmaan hyvinvointialue
Department Name
Peditrics
Principal Investigator Name
Susanna Vuorenoja
Principal Investigator Email
susanna.vuorenoja@pirha.fi
Contact Person Name
Susanna Vuorenoja
Contact Person Email
susanna.vuorenoja@pirha.fi

France

Earliest CTIS Part Ii Submission Date
30-10-2024
Latest Decision Or Authorization Date
02-12-2024
Processing Time Days
33
Number Of Sites
7
Number Of Participants
88

Sites

Site Name
Institut Gustave Roussy
Department Name
nt de cancérologie de l’enfant et l’adolescent
Principal Investigator Name
Nathalie Gaspar
Principal Investigator Email
nathalie.gaspar@gustaveroussy.fr
Contact Person Name
Nathalie Gaspar
Site Name
Les Hopitaux Universitaires De Strasbourg
Department Name
Onco-hématologie pédiatrique
Principal Investigator Name
Natacha Entz-Werlé
Principal Investigator Email
Natacha.Entz-Werle@chru-strasbourg.fr
Contact Person Name
Natacha Entz-Werlé
Site Name
Centre Leon Berard
Department Name
Paediatric oncology
Principal Investigator Name
Perrine Marec-Berard
Principal Investigator Email
perrine.marec-berard@ihope.fr
Contact Person Name
Perrine Marec-Berard
Contact Person Email
perrine.marec-berard@ihope.fr
Site Name
Centre Hospitalier Regional De Marseille
Department Name
Service d’immunologie, hématologie et oncologie pédiatrique
Principal Investigator Name
Andre Nicolas
Principal Investigator Email
nicolas.andre@ap-hm.fr
Contact Person Name
Andre Nicolas
Contact Person Email
nicolas.andre@ap-hm.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Service d'Hématologie et oncologie pédiatrique
Principal Investigator Name
Marie-Dominique Tabone
Principal Investigator Email
marie-dominique.tabone@trs.ap-hop-paris.fr
Contact Person Name
Marie-Dominique Tabone
Site Name
Hopital Des Enfants
Department Name
Pediatric oncology
Principal Investigator Name
Marie-Pierre Castex
Principal Investigator Email
castex.mp@chu-toulouse.fr
Contact Person Name
Marie-Pierre Castex
Contact Person Email
castex.mp@chu-toulouse.fr
Site Name
CHU Besancon
Department Name
Hématologie oncologie pédiatrique
Principal Investigator Name
Natacha Entz-Werle
Principal Investigator Email
Natacha.Entz-Werle@chru-strasbourg.fr
Contact Person Name
Natacha Entz-Werle

Italy

Earliest CTIS Part Ii Submission Date
30-10-2024
Latest Decision Or Authorization Date
04-12-2024
Processing Time Days
35
Number Of Sites
10
Number Of Participants
102

Sites

Site Name
Istituto Ortopedico Rizzoli
Department Name
SC Osteoncology Unit
Principal Investigator Name
Toni Ibrahim
Principal Investigator Email
toni.ibrahim@ior.it
Contact Person Name
Toni Ibrahim
Contact Person Email
toni.ibrahim@ior.it
Site Name
Fondazione IRCCS Istituto Nazionale Dei Tumori
Department Name
SC Oncologia Medica dei Tumori Mesenchimali dell’Adulto
Principal Investigator Name
Rossella Bertulli
Principal Investigator Email
rossella.bertulli@istitutotumori.mi.it
Contact Person Name
Rossella Bertulli
Site Name
I.F.O. Istituti Fisioterapici Ospitalieri
Department Name
UOSD Sarcomi e Tumori Rari
Principal Investigator Name
Virginia Ferraresi
Principal Investigator Email
virginia.ferraresi@ifo.it
Contact Person Name
Virginia Ferraresi
Contact Person Email
virginia.ferraresi@ifo.it
Site Name
Ospedale Pediatrico Bambino Gesu
Department Name
Dipartimento di Oncoematologia e Terapia
Principal Investigator Name
Giuseppe Maria Milano
Principal Investigator Email
Giuseppemaria.milano@opbg.net
Contact Person Name
Giuseppe Maria Milano
Contact Person Email
Giuseppemaria.milano@opbg.net
Site Name
Azienda Ospedaliera Universitaria Citta Della Salute E Della Scienza Di Torino
Department Name
SC oncoematologia pediatrica
Principal Investigator Name
Franca Fagioli
Principal Investigator Email
franca.fagioli@unito.it
Contact Person Name
Franca Fagioli
Contact Person Email
franca.fagioli@unito.it
Site Name
Azienda Ospedaliera Universitaria Meyer IRCCS
Department Name
Dipartimento di Oncoematologia Pediatrica e Cure Domiciliari
Principal Investigator Name
Angela Tamburini
Principal Investigator Email
angela.tamburini@meyer.it
Contact Person Name
Angela Tamburini
Contact Person Email
angela.tamburini@meyer.it
Site Name
Azienda Ospedaliero Universitaria Pisana
Department Name
Pediatric Onco-Hematology Unit
Principal Investigator Name
Luca Coccoli
Principal Investigator Email
l.coccoli@ao-pisa.toscana.it
Contact Person Name
Luca Coccoli
Contact Person Email
l.coccoli@ao-pisa.toscana.it
Site Name
Fondazione IRCCS Istituto Nazionale Dei Tumori
Department Name
SC pediatria Oncologica
Principal Investigator Name
Roberto Luksch
Principal Investigator Email
roberto.Luksch@istitutotumori.mi.it
Contact Person Name
Roberto Luksch
Site Name
Azienda Ospedaliera Santobono Pausilipon
Department Name
Department of Oncology, Hematology and Cell Therapies
Principal Investigator Name
Massimo Eraldo Abate
Principal Investigator Email
massimoeraldo.abate@santobonopausilipon.it
Contact Person Name
Massimo Eraldo Abate
Site Name
Azienda Ospedaliera di Padova
Department Name
UOC Oncoematologia Pediatrica
Principal Investigator Name
Marta Pierobon
Principal Investigator Email
marta.pierobon@aopd.veneto.it
Contact Person Name
Marta Pierobon
Contact Person Email
marta.pierobon@aopd.veneto.it

Spain

Earliest CTIS Part Ii Submission Date
30-10-2024
Latest Decision Or Authorization Date
03-12-2024
Processing Time Days
34
Number Of Sites
18
Number Of Participants
150

Sites

Site Name
Hospital Universitario Central De Asturias
Department Name
Medical Oncology
Principal Investigator Name
Pilar Blay
Principal Investigator Email
pilarblayalbors@gmail.com
Contact Person Name
Pilar Blay
Contact Person Email
pilarblayalbors@gmail.com
Site Name
Hospital Universitario Regional De Malaga
Department Name
Paediatric Oncology
Principal Investigator Name
Laura García Hidalgo
Principal Investigator Email
laura_garcia_hidalgo@hotmail.com
Contact Person Name
Laura García Hidalgo
Site Name
Hospital General Universitario Gregorio Maranon
Department Name
Medical Oncology
Principal Investigator Name
Rosa Álvarez
Principal Investigator Email
rosa.alvarez.al@gmail.com
Contact Person Name
Rosa Álvarez
Contact Person Email
rosa.alvarez.al@gmail.com
Site Name
Hospital Universitario Fundacion Jimenez Diaz
Department Name
Medical Oncology
Principal Investigator Name
Javier Martin
Principal Investigator Email
jmartin@atbsarc.org
Contact Person Name
Javier Martin
Contact Person Email
jmartin@atbsarc.org
Site Name
Hospital Universitari Vall D Hebron
Department Name
Medical Oncology
Principal Investigator Name
Claudia Valverde
Principal Investigator Email
cvalverde@vhio.net
Contact Person Name
Claudia Valverde
Contact Person Email
cvalverde@vhio.net
Site Name
Hospital Infantil Universitario Nino Jesus
Department Name
Medical Oncology
Principal Investigator Name
Alba Rubio
Principal Investigator Email
alba.rubio@salud.madrid.org
Contact Person Name
Alba Rubio
Contact Person Email
alba.rubio@salud.madrid.org
Site Name
Hospital Universitario Ramon Y Cajal
Department Name
Medical Oncology
Principal Investigator Name
María Ángeles Vaz
Principal Investigator Email
mavaz4@gmail.com
Contact Person Name
María Ángeles Vaz
Contact Person Email
mavaz4@gmail.com
Site Name
Hospital Universitario Miguel Servet
Department Name
Medical Oncology
Principal Investigator Name
Javier Martínez Trufero
Principal Investigator Email
oncojmt@gmail.com
Contact Person Name
Javier Martínez Trufero
Contact Person Email
oncojmt@gmail.com
Site Name
Hospital Universitario De Canarias
Department Name
Medical Oncology
Principal Investigator Name
Josefina Cruz
Principal Investigator Email
jcruzjurado@gmail.com
Contact Person Name
Josefina Cruz
Contact Person Email
jcruzjurado@gmail.com
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Medical Oncology
Principal Investigator Name
Pilar Sancho
Principal Investigator Email
mariap.sancho.sspa@juntadeandalucia.es
Contact Person Name
Pilar Sancho
Site Name
University Hospital Son Espases
Department Name
Medical Oncology
Principal Investigator Name
Pablo Luna
Principal Investigator Email
pablo.luna@ssib.es
Contact Person Name
Pablo Luna
Contact Person Email
pablo.luna@ssib.es
Site Name
Hospital Universitario Y Politecnico La Fe
Department Name
Medical Oncology
Principal Investigator Name
Roberto Díaz-Beveridge
Principal Investigator Email
robertdiazbeveridge@gmail.com
Contact Person Name
Roberto Díaz-Beveridge
Contact Person Email
robertdiazbeveridge@gmail.com
Site Name
Institut Catala D'oncologia
Department Name
Medical Oncology
Principal Investigator Name
Xavier García del Muro
Principal Investigator Email
garciadelmuro@iconcologia.net
Contact Person Name
Xavier García del Muro
Contact Person Email
garciadelmuro@iconcologia.net
Site Name
Hospital De La Santa Creu I Sant Pau
Department Name
Medical Oncology
Principal Investigator Name
Raúl Terés
Principal Investigator Email
rteres@santpau.cat
Contact Person Name
Raúl Terés
Contact Person Email
rteres@santpau.cat
Site Name
Hospital Universitario La Paz
Department Name
Medical Oncology
Principal Investigator Name
Andrés Redondo
Principal Investigator Email
aredondo@gmail.com
Contact Person Name
Andrés Redondo
Contact Person Email
aredondo@gmail.com
Site Name
Hospital Universitario Virgen De La Victoria
Department Name
Medical Oncology
Principal Investigator Name
Isabel Sevilla
Principal Investigator Email
isevilla02@yahoo.es
Contact Person Name
Isabel Sevilla
Contact Person Email
isevilla02@yahoo.es
Site Name
Hospital Universitario De Cruces
Department Name
Medical Oncology
Principal Investigator Name
Natalia Fuente
Principal Investigator Email
NATALIA.FUENTEFERNANDEZ@osakidetza.eus
Contact Person Name
Natalia Fuente
Site Name
Hospital Sant Joan De Deu Barcelona
Department Name
Paediatric Oncology
Principal Investigator Name
Jaume Mora
Principal Investigator Email
Jmora@hsjdbcn.es
Contact Person Name
Jaume Mora
Contact Person Email
Jmora@hsjdbcn.es

Netherlands

Earliest CTIS Part Ii Submission Date
30-10-2024
Latest Decision Or Authorization Date
04-12-2024
Processing Time Days
35
Number Of Sites
2
Number Of Participants
11

Sites

Site Name
Radboud universitair medisch centrum Stichting
Department Name
Department of Medical Oncology
Principal Investigator Name
Suzanne Kaal
Principal Investigator Email
Suzanne.Kaal@radboudumc.nl
Contact Person Name
Suzanne Kaal
Contact Person Email
Suzanne.Kaal@radboudumc.nl
Site Name
Prinses Maxima Centrum voor Kinderoncologie B.V.
Department Name
Solid Tumours
Principal Investigator Name
Hans Merks
Principal Investigator Email
J.H.M.Merks@prinsesmaximacentrum.nl
Contact Person Name
Hans Merks

Norway

Earliest CTIS Part Ii Submission Date
30-10-2024
Latest Decision Or Authorization Date
29-11-2024
Processing Time Days
30
Number Of Sites
4
Number Of Participants
20

Sites

Site Name
Universitetssykehuset Nord-Norge HF
Department Name
Department of Oncology
Principal Investigator Name
Eivind Smeland
Principal Investigator Email
Eivind.smeland@unn.no
Contact Person Name
Eivind Smeland
Contact Person Email
Eivind.smeland@unn.no
Site Name
St. Olavs Hospital HF
Department Name
Oncology department
Principal Investigator Name
Heidi Knobel
Principal Investigator Email
Heidi.Knobel@stolav.no
Contact Person Name
Heidi Knobel
Contact Person Email
Heidi.Knobel@stolav.no
Site Name
Helse Bergen HF
Department Name
Department of Oncology
Principal Investigator Name
Dorota Malgorzata Wojcik
Principal Investigator Email
Dorota.malgorzata.wojcik@helse-bergen.no
Contact Person Name
Dorota Malgorzata Wojcik
Site Name
Oslo University Hospital HF
Department Name
Oncology Department
Principal Investigator Name
Kjetil Boye
Principal Investigator Email
pkb@ous-hf.no
Contact Person Name
Kjetil Boye
Contact Person Email
pkb@ous-hf.no

Sponsor

Primary sponsor

Full Name
The University Of Birmingham
Organisation Type
Educational Institution
Country Of Registered Address
United Kingdom

Third parties

  • {"country":"Denmark","full_name":"Frederiksberg Hospital","duties_or_roles":"code:1","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"United Kingdom","full_name":"St James's University Hospital","duties_or_roles":"codes:15 (Biobank), 4","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"United Kingdom","full_name":"The Christie NHS Foundation Trust","duties_or_roles":"codes:15 (Biobank), 4","organisation_type":"Hospital/Clinic/Other health care facility"}

Investigational products

Investigational Product Name
LENVIMA 4 mg hard capsules
Active Substance
LENVATINIB
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
ORAL
Authorisation Status
Marketing authorisation EU/1/15/1002/001
Maximum Dose
24 mg
Investigational Product Name
LENVIMA 10 mg hard capsules
Active Substance
LENVATINIB
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
ORAL
Authorisation Status
Marketing authorisation EU/1/15/1002/002
Maximum Dose
24 mg
Investigational Product Name
GEMCITABINE
Active Substance
GEMCITABINE
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Authorisation Status
Not authorised (marketingAuthNumber: -)
Maximum Dose
900 mg/m2
Investigational Product Name
TEMOZOLOMIDE
Active Substance
TEMOZOLOMIDE
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
ORAL
Authorisation Status
Not authorised (marketingAuthNumber: -)
Maximum Dose
100 mg/m2
Investigational Product Name
IFOSFAMIDE
Active Substance
IFOSFAMIDE
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Authorisation Status
Not authorised (marketingAuthNumber: -)
Maximum Dose
3 gm/m2
Investigational Product Name
CARBOPLATIN
Active Substance
CARBOPLATIN
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Authorisation Status
Not authorised (marketingAuthNumber: -)
Maximum Dose
400 mg/m2
Investigational Product Name
ETOPOSIDE PHOSPHATE
Active Substance
ETOPOSIDE PHOSPHATE
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Authorisation Status
Not authorised (marketingAuthNumber: -)
Maximum Dose
136.32 mg/m2
Investigational Product Name
ETOPOSIDE
Active Substance
ETOPOSIDE
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Authorisation Status
Not authorised (marketingAuthNumber: -)
Maximum Dose
120 mg/m2
Investigational Product Name
IRINOTECAN
Active Substance
IRINOTECAN
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Authorisation Status
Not authorised (marketingAuthNumber: -)
Maximum Dose
50 mg/m2
Investigational Product Name
TOPOTECAN
Active Substance
TOPOTECAN
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Authorisation Status
Not authorised (marketingAuthNumber: -)
Maximum Dose
0.75 mg/m2
Investigational Product Name
DOCETAXEL / ANHYDROUS DOCETAXEL
Active Substance
DOCETAXEL
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Authorisation Status
Not authorised (marketingAuthNumber: -)
Maximum Dose
80 mg/m2
Investigational Product Name
CYCLOPHOSPHAMIDE
Active Substance
CYCLOPHOSPHAMIDE
Modality
Small molecule
Routes Of Administration
INTRAVENOUS
Route
INTRAVENOUS
Authorisation Status
Not authorised (marketingAuthNumber: -)
Maximum Dose
250 mg/m2
Combination Treatment
Yes

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