Clinical trial • Phase III|Phase IV • Immunology|Nephrology

IPTACOPAN for IgA nephropathy

Phase III|Phase IV trial of IPTACOPAN for IgA nephropathy. open-label. 440 participants.

Overview

Trial Therapeutic Area
Immunology|Nephrology
Trial Disease
IgA nephropathy
Trial Stage
Phase III|Phase IV
Drug Modality
Small molecule
Orphan Drug
Yes

Key dates

Initial CTIS Submission Date
26-03-2024
First CTIS Authorization Date
02-05-2024

Trial design

open-label Phase III|Phase IV trial in Italy, Netherlands, Czechia and others.

Open Label
Yes
Target Sample Size
440

Eligibility

Recruits 440 Vulnerable population selected (isVulnerablePopulationSelected=true). Signed informed consent must be obtained prior to participation in the REP; participants should be able to communicate well with the Investigator, understand and comply with the requirements of the study. ICF templates are provided for adults; a 'Parent Legal Guardian' ICF document is present for France. No paediatric assent documentation is referenced..

Pregnancy Exclusion
Pregnant or breastfeeding females, where pregnancy is confirmed by a positive Human Chorionic Gonadotrophin (HCG) test.
Vulnerable Population
Vulnerable population selected (isVulnerablePopulationSelected=true). Signed informed consent must be obtained prior to participation in the REP; participants should be able to communicate well with the Investigator, understand and comply with the requirements of the study. ICF templates are provided for adults; a 'Parent Legal Guardian' ICF document is present for France. No paediatric assent documentation is referenced.

Inclusion criteria

  • {"criterion_text":"- Signed informed consent must be obtained prior to participation in the REP; participants should be able to communicate well with the Investigator, understand and comply with the requirements of the study.\n- For CLNP023X2203, participants must have completed Part 1 or Part 2 of the trial. For other parent trials participants must have completed the entire parent trial duration defined by the respective protocol.\n- eGFR* ≥ 20 mL/min/1.73m2. *eGFR calculated using the CKD-EPI formula (or modified MDRD formula according to specific ethnic groups and local practice guidelines).\n- Per Investigator’s clinical judgment, the participant may benefit from receiving the open-label treatment of iptacopan 200 mg b.i.d.\n- Prior vaccination against Neisseria meningitidis, Streptococcus pneumoniae and Haemophilus influenzae infections should be up to date (i.e. any boosters required administered according to local regulations).\n- All participants must be on supportive care regimen of stable dose of ACEi or ARB* as per KDIGO guidelines (KDIGO 2021). * Participants with allergies or intolerance to ACEi and ARB are eligible for the study but the Investigator should clearly document the reasons for not being on maximal ACEi/ARB dose in the source documents."}

Exclusion criteria

  • {"criterion_text":"- Participants who are screen or baseline failed in any of the iptacopan parent studies in IgAN or who prematurely withdrew from iptacopan parent studies in IgAN for any reason.\n- Evidence of severe urinary obstruction or difficulty in voiding; any urinary tract disorder other than IgAN at screening and before dosing with iptacopan.\n- Current (within 4 weeks prior to study treatment administration in the REP) acute kidney injury (AKI) defined by AKIN criteria.\n- Presence of Rapidly Progressive Glomerulonephritis (RPGN) as defined by 50% decline in eGFR within the last 3 months.\n- Participants treated with immunosuppressive or other immunomodulatory agents such as but not limited to cyclophosphamide, rituximab, infliximab, eculizumab, canakinumab, mycophenolate mofetil (MMF) or mycophenolate sodium (MPS), cyclosporine, tacrolimus, sirolimus, everolimus and/or systemic corticosteroids exposure (>7.5 mg/d prednisone/prednisolone equivalent) within 90 days prior to first study drug administration. Rituximab requires 180 days wash out. Participants treated with endothelin (receptor) antagonists within 90 days prior to first study drug administration.\n- Use of other investigational drugs at the time of enrollment, or within 5 half-lives of enrollment or within 30 days whichever is longer\n- History of recurrent invasive infections caused by encapsulated organisms, such as Neisseria meningitidis, Streptococcus pneumoniae and Hemophilus influenzae.\n- All transplanted participants (any solid organ, or bone marrow transplantation).\n- Major concurrent comorbidities including but not limited to severe uncontrolled hypertension, other chronic kidney disease (with or without kidney failure), advanced cardiac disease (e.g., NYHA class IV), severe pulmonary disease (e.g., severe pulmonary hypertension (WHO class IV), or hepatic disease (e.g. active hepatitis) that in the opinion of the Investigator precludes participant's participation in the study.\n- Any medical condition deemed likely to interfere with the participant’s participation in the study.\n- Active systemic bacterial, viral (including COVID-19) or fungal infection within 14 days prior to study treatment administration.\n- Presence of fever ≥ 38°C (100.4°F) within 7 days prior to study treatment administration.\n- History of Human Immunodeficiency Virus (HIV) infection (known history of HIV or test positive for HIV antibody at Screening).\n- Liver disease or liver injury as indicated by abnormal liver function tests (LFT) at screening as defined below. ALT (SGPT), AST (SGOT), GGT, alkaline phosphatase and serum bilirubin will be tested. • Any single parameter of ALT, AST, GGT, alkaline phosphatase must not exceed 3 × upper limit of normal (ULN) • Serum bilirubin must not exceed 2 × ULN Participants from CLNP023X2203 study or any other parent study participants if required by local regulations will be additionally tested for HBsAg and HCV-RNA and are not eligible if the results are positive.\n- History of hypersensitivity to any of the study treatments or its excipients or to drugs of similar chemical classes or any participant who discontinued study treatment in the parent study due to a suspected treatment-related AE.\n- History of malignancy of any organ system (other than localized basal cell carcinoma of the skin or in situ cervical cancer treated with curative intent), treated or untreated, within the past 5 years, regardless of whether there is evidence of local recurrence or metastases.\n- Pregnant or breastfeeding females, where pregnancy is confirmed by a positive Human Chorionic Gonadotrophin (HCG) test."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Safety and tolerability endpoints (including but not limited to AEs/SAEs, safety laboratory parameters, vital signs).","definition_or_measurement_approach":"Assessment of adverse events (AEs/SAEs), safety laboratory parameters and vital signs as reported during the open-label treatment period."}

Secondary endpoints

  • {"endpoint_text":"- Annualized total eGFR slope.","definition_or_measurement_approach":"Change over time of estimated glomerular filtration rate expressed as an annualized slope."}
  • {"endpoint_text":"- Change from baseline in eGFR.","definition_or_measurement_approach":"Difference in eGFR measurements compared to baseline values."}
  • {"endpoint_text":"- Log transformed ratio to baseline in UPCR, UACR.","definition_or_measurement_approach":"Log-transformed ratio of urinary protein/creatinine (UPCR) and urine albumin/creatinine (UACR) compared to baseline."}

Recruitment

Planned Sample Size
440
Recruitment Window Months
144
Consent Approach
Signed informed consent must be obtained prior to participation in the REP. Consent is provided by the participant (adult). Country-specific ICFs are available (examples in the submission include English, Italian, Dutch, Czech, German, Norwegian, Hungarian, Spanish, Swedish, French, Slovak, Slovenian, Danish). A 'Parent Legal Guardian' ICF document is available for France.

Geography

Total Number Of Sites
38
Total Number Of Participants
100

Italy

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
29-05-2024
Processing Time Days
37
Number Of Sites
2
Number Of Participants
9

Sites

Site Name
Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
Department Name
5703: UOC Nefrologia, Dialisi e trapianto
Principal Investigator Name
Gaetano La Manna
Principal Investigator Email
gaetano.lamanna@unibo.it
Contact Person Name
Gaetano La Manna
Contact Person Email
gaetano.lamanna@unibo.it
Site Name
Azienda Ospedaliera Universitaria Federico II Di Napoli
Department Name
5702: Cattedra di Nefrologia
Principal Investigator Name
Antonio Pisani
Principal Investigator Email
antonio.pisani13@gmail.com
Contact Person Name
Antonio Pisani
Contact Person Email
antonio.pisani13@gmail.com

Netherlands

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
02-05-2024
Processing Time Days
10
Number Of Sites
1
Number Of Participants
2

Sites

Site Name
Universitair Medisch Centrum Groningen
Department Name
6100: Nephrology
Principal Investigator Name
Mark Eijgelsheim
Principal Investigator Email
m.eijgelsheim@umcg.nl
Contact Person Name
Mark Eijgelsheim
Contact Person Email
m.eijgelsheim@umcg.nl

Czechia

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
06-05-2024
Processing Time Days
14
Number Of Sites
1
Number Of Participants
10

Sites

Site Name
Vseobecna Fakultni Nemocnice V Praze
Department Name
4800: Klinika nefrologie
Principal Investigator Name
Vladimir Tesar
Principal Investigator Email
vladimir.tesar@vfn.cz
Contact Person Name
Vladimir Tesar
Contact Person Email
vladimir.tesar@vfn.cz

Germany

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
06-05-2024
Processing Time Days
14
Number Of Sites
12
Number Of Participants
21

Sites

Site Name
Charite Universitaetsmedizin Berlin KöR
Department Name
5204: Medizinische Klinik mit Schwerpunkt Nephrologie und Intensivmedizin
Principal Investigator Name
Adrian Schreiber
Principal Investigator Email
Adrian.schreiber@charite.de
Contact Person Name
Adrian Schreiber
Contact Person Email
Adrian.schreiber@charite.de
Site Name
Medical Center - University Of Freiburg
Department Name
5209: Abteilung für Innere Medizin IV
Principal Investigator Name
Wibke Bechtel-Walz
Principal Investigator Email
Wibke.bechtelr@uniklinik-freiburg.de
Contact Person Name
Wibke Bechtel-Walz
Site Name
Eberhard Karls Universitaet Tuebingen
Department Name
5207: Medizinische Klinik IV, Diabetologie, Endokrinologie, Nephrologie
Principal Investigator Name
Ferruh Artunc
Principal Investigator Email
ferruh.artunc@med.uni-tuebingen.de
Contact Person Name
Ferruh Artunc
Site Name
Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz KöR
Department Name
5212: I. Medizinische Klinik und Poliklinik
Principal Investigator Name
Julia Weinmann-Menke
Principal Investigator Email
Julia.weinmann-menke@unimedizin-mainz.de
Contact Person Name
Julia Weinmann-Menke
Site Name
Medizinische Hochschule Hannover
Department Name
5210: Studienzentrum für Nieren- und Hochdruckerkrankungen
Principal Investigator Name
Kai Schmidt-Ott
Principal Investigator Email
schmidt-ott.kai@mh-hannover.de
Contact Person Name
Kai Schmidt-Ott
Contact Person Email
schmidt-ott.kai@mh-hannover.de
Site Name
Universitaetsklinikum Schleswig-Holstein AöR
Department Name
5224: Klinik für Innere Medizin IV
Principal Investigator Name
Kevin Schulte
Principal Investigator Email
Kevin.Schulte@uksh.de
Contact Person Name
Kevin Schulte
Contact Person Email
Kevin.Schulte@uksh.de
Site Name
Universitaetsklinikum Aachen AöR
Department Name
5220: Medizinische Klinik III
Principal Investigator Name
Markus Moeller
Principal Investigator Email
mmoeller@ukaachen.de
Contact Person Name
Markus Moeller
Contact Person Email
mmoeller@ukaachen.de
Site Name
Universitaetsklinikum Carl Gustav Carus Dresden an der Technischen Universitaet Dresden AöR
Department Name
5208: Medizinische Klinik und Poliklinik III
Principal Investigator Name
Christian Hugo
Principal Investigator Email
Christian.hugo@uniklinikum-dresden.de
Contact Person Name
Christian Hugo
Site Name
Robert Bosch Krankenhaus GmbH
Department Name
5223: Abteilung für Allgemeine Innere Medizin und Nephrologie
Principal Investigator Name
Markus Ketteler
Principal Investigator Email
Markus.ketteler@rbk.de
Contact Person Name
Markus Ketteler
Contact Person Email
Markus.ketteler@rbk.de
Site Name
Universitaetsklinikum Magdeburg AöR
Department Name
5216: Klinik für Nieren u. Hochdruckkrankheiten, Diabetologie und Endokrinologie
Principal Investigator Name
Peter Mertens
Principal Investigator Email
Peter.mertens@med.ovgu.de
Contact Person Name
Peter Mertens
Contact Person Email
Peter.mertens@med.ovgu.de
Site Name
Universitaetsklinikum Essen AöR
Department Name
5201: Klinik für Nephrologie
Principal Investigator Name
Anja Gäckler
Principal Investigator Email
Anja.gaeckler@uk-essen.de
Contact Person Name
Anja Gäckler
Contact Person Email
Anja.gaeckler@uk-essen.de
Site Name
Universitaetsklinikum Ulm AöR
Department Name
5215: Klinik für Innere Medizin I, Sektion Nephrologie
Principal Investigator Name
Lena Schulte-Kemna
Principal Investigator Email
Lena.Schulte-Kemna@uniklinik-ulm.de
Contact Person Name
Lena Schulte-Kemna

Norway

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
03-05-2024
Processing Time Days
11
Number Of Sites
2
Number Of Participants
4

Sites

Site Name
Helse Bergen HF
Department Name
6201: Nefrologisk seksjon
Principal Investigator Name
Rannveig Skrunes
Principal Investigator Email
rannveig.skrunes@helse-bergen.no
Contact Person Name
Rannveig Skrunes
Site Name
Akershus University Hospital
Department Name
6202: Avdeling for nyresykdommer
Principal Investigator Name
Bartlomiej J. Witczak
Principal Investigator Email
Bartlomiej.J.Witczak@ahus.no
Contact Person Name
Bartlomiej J. Witczak
Contact Person Email
Bartlomiej.J.Witczak@ahus.no

Hungary

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
03-05-2024
Processing Time Days
11
Number Of Sites
3
Number Of Participants
4

Sites

Site Name
University Of Pecs
Department Name
5402: II. sz Belgyógyászati Klinika és Nephrológiai Centrum
Principal Investigator Name
Tibor Kovács
Principal Investigator Email
kovacs.tibor.jozsef@pte.hu
Contact Person Name
Tibor Kovács
Contact Person Email
kovacs.tibor.jozsef@pte.hu
Site Name
University Of Szeged
Department Name
5403: Belgyogyaszati Klinika
Principal Investigator Name
László Bitó
Principal Investigator Email
bito.laszlo.zsolt@med.u-szeged.hu
Contact Person Name
László Bitó
Site Name
University Of Debrecen
Department Name
5401: Belgyógyászati Klinika, Nephrológiai Osztály
Principal Investigator Name
János Mátyus
Principal Investigator Email
matyus@belklinika.com
Contact Person Name
János Mátyus
Contact Person Email
matyus@belklinika.com

Spain

Earliest CTIS Part Ii Submission Date
31-05-2024
Latest Decision Or Authorization Date
31-07-2024
Processing Time Days
61
Number Of Sites
3
Number Of Participants
7

Sites

Site Name
Hospital Universitario De Salamanca
Department Name
3408: Nefrology
Principal Investigator Name
Maria Pilar Fraile Gomez
Principal Investigator Email
pilarfg@usal.es
Contact Person Name
Maria Pilar Fraile Gomez
Contact Person Email
pilarfg@usal.es
Site Name
Hospital Clinic De Barcelona
Department Name
3404: Nefrology
Principal Investigator Name
Luis Fernando Quintana Porras
Principal Investigator Email
lfquinta@clinic.cat
Contact Person Name
Luis Fernando Quintana Porras
Contact Person Email
lfquinta@clinic.cat
Site Name
Clinica Universidad De Navarra
Department Name
3405: Unidad de Ensayos Clinicos
Principal Investigator Name
Nuria Garcia Fernandez
Principal Investigator Email
nrgarcia@unav.es
Contact Person Name
Nuria Garcia Fernandez
Contact Person Email
nrgarcia@unav.es

Sweden

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
02-05-2024
Processing Time Days
10
Number Of Sites
1
Number Of Participants
2

Sites

Site Name
Karolinska University Hospital
Department Name
6700: Forskningsmottagningen Njurmedicin M87
Principal Investigator Name
Olof Heimbürger
Principal Investigator Email
olof.heimburger@regionstockholm.se
Contact Person Name
Olof Heimbürger

France

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
06-05-2024
Processing Time Days
14
Number Of Sites
3
Number Of Participants
4

Sites

Site Name
Centre Hospitalier Regional De Marseille
Department Name
5103: Centre de Néphrologie et de Transplantation rénale
Principal Investigator Name
Bertrand DUSSOL
Principal Investigator Email
bertrand.dussol@ap-hm.fr
Contact Person Name
Bertrand DUSSOL
Contact Person Email
bertrand.dussol@ap-hm.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
5101: Service de Néphrologie
Principal Investigator Name
Alexandre KARRAS
Principal Investigator Email
alexandre.karras@aphp.fr
Contact Person Name
Alexandre KARRAS
Contact Person Email
alexandre.karras@aphp.fr
Site Name
Centre Hospitalier Universitaire De Montpellier
Department Name
5100: Néphrologie, Soins intensifs, Dialyse et transplantation
Principal Investigator Name
Moglie LE QUINTREC-DONNETTE
Principal Investigator Email
m-lequintrec-donnette@chu-montpellier.fr
Contact Person Name
Moglie LE QUINTREC-DONNETTE

Belgium

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
15-05-2024
Processing Time Days
23
Number Of Sites
3
Number Of Participants
18

Sites

Site Name
Antwerp University Hospital
Department Name
4302: Nefrology
Principal Investigator Name
Rowena Vleut
Principal Investigator Email
rowena.vleut@uza.be
Contact Person Name
Rowena Vleut
Contact Person Email
rowena.vleut@uza.be
Site Name
Algemeen Ziekenhuis Delta
Department Name
4301: Nefrology
Principal Investigator Name
An Vanacker
Principal Investigator Email
an.vanacker@azdelta.be
Contact Person Name
An Vanacker
Contact Person Email
an.vanacker@azdelta.be
Site Name
UZ Leuven
Department Name
4300: Nefrology
Principal Investigator Name
Kathleen Claes
Principal Investigator Email
kathleen.claes@uzleuven.be
Contact Person Name
Kathleen Claes
Contact Person Email
kathleen.claes@uzleuven.be

Slovakia

Earliest CTIS Part Ii Submission Date
07-08-2024
Latest Decision Or Authorization Date
16-08-2024
Processing Time Days
9
Number Of Sites
1
Number Of Participants
1

Sites

Site Name
FMC dialyzacne sluzby s.r.o.
Department Name
#3600: Nefrologická ambulancia
Principal Investigator Name
Jaroslav Rosenberger
Contact Person Name
Jaroslav Rosenberger

Slovenia

Earliest CTIS Part Ii Submission Date
31-05-2024
Latest Decision Or Authorization Date
13-08-2024
Processing Time Days
74
Number Of Sites
2
Number Of Participants
6

Sites

Site Name
University Medical Center Ljubljana
Department Name
3500: Division of Internal Medicine, Department of Nephrology
Principal Investigator Name
Andreja Ales Rigler
Principal Investigator Email
andreja.ales@kclj.si
Contact Person Name
Andreja Ales Rigler
Contact Person Email
andreja.ales@kclj.si
Site Name
UNIVERZITETNI KLINICNI CENTER MARIBOR
Department Name
3501: Division of Internal medicine, Department of Nephrology
Principal Investigator Name
Sebastjan Bevc
Principal Investigator Email
sebastjan.bevc@ukc-mb.si
Contact Person Name
Sebastjan Bevc
Contact Person Email
sebastjan.bevc@ukc-mb.si

Denmark

Earliest CTIS Part Ii Submission Date
22-04-2024
Latest Decision Or Authorization Date
02-05-2024
Processing Time Days
10
Number Of Sites
4
Number Of Participants
12

Sites

Site Name
Aalborg University Hospital
Department Name
4901: Dialysen 3.Ø
Principal Investigator Name
Jon Waarst Gregersen
Principal Investigator Email
jon.gregersen@rn.dk
Contact Person Name
Jon Waarst Gregersen
Contact Person Email
jon.gregersen@rn.dk
Site Name
Rigshospitalet
Department Name
4903: Nefrologisk Klinik P
Principal Investigator Name
Mads Hornum
Principal Investigator Email
Mads.hornum@regonh.dk
Contact Person Name
Mads Hornum
Contact Person Email
Mads.hornum@regonh.dk
Site Name
Odense University Hospital
Department Name
4902: Klinisk Forskningsenhed, Nyremedicinsk Afdeling Y
Principal Investigator Name
Ann-Maria Gramkow
Principal Investigator Email
Ann-Maria.Gramkow@rsyd.dk
Contact Person Name
Ann-Maria Gramkow
Contact Person Email
Ann-Maria.Gramkow@rsyd.dk
Site Name
Aarhus Universitetshospital
Department Name
4900: Nyremedicinsk Forskning, Nyresygdomme
Principal Investigator Name
Per Ramløv Ivarsen
Principal Investigator Email
perivars@rm.dk
Contact Person Name
Per Ramløv Ivarsen
Contact Person Email
perivars@rm.dk

Sponsor

Primary sponsor

Full Name
Novartis Pharma AG
Organisation Type
Pharmaceutical company
Country Of Registered Address
Switzerland

Contract research organisations

Name
IQVIA Limited
Responsibilities
sponsorDuties: [{"id":980439,"code":"1"},{"id":980440,"code":"3"}], contact eu_clinical_trials_information@iqvia.com
Name
Parexel International (IRL) Limited
Responsibilities
sponsorDuties: [{"id":980453,"code":"12"}], contact Clinicaltrial.Enquiries@parexel.com
Name
Syneos Health Inc.
Responsibilities
sponsorDuties: [{"id":980447,"code":"1"}], contact sm_ctis@syneoshealth.com
Name
Icon Clinical Research Limited
Responsibilities
sponsorDuties: [{"id":980443,"code":"1"}], contact Triona.PriceSmith1@docsglobal.com
Name
Medidata Solutions Inc.
Responsibilities
sponsorDuties: [{"id":980451,"code":"6"},{"id":980452,"code":"7"}], contact info@medidata.com

Third parties

  • {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"sponsorDuties: [{\"id\":980439,\"code\":\"1\"},{\"id\":980440,\"code\":\"3\"}]","organisation_type":"Pharmaceutical company"}
  • {"country":"Norway","full_name":"Freja Transport & Logistics AS","duties_or_roles":"Drug destruction and re-labelling (sponsorDuties code 15)","organisation_type":"Pharmaceutical company"}
  • {"country":"Hungary","full_name":"ADR Logistics Kft.","duties_or_roles":"sponsorDuties: [{\"id\":980441,\"code\":\"14\"},{\"id\":980442,\"code\":\"15\",\"value\":\"Destruction of IMP Locally purchased drug storage, distribution, and destruction\"}]","organisation_type":"Pharmaceutical company"}
  • {"country":"Ireland","full_name":"Parexel International (IRL) Limited","duties_or_roles":"sponsorDuties: [{\"id\":980453,\"code\":\"12\"}]","organisation_type":"Pharmaceutical company"}
  • {"country":"Hungary","full_name":"Opt-X-Pense Kft.","duties_or_roles":"patient reimbursement (sponsorDuties code 15)","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Illingworth Research Group Limited","duties_or_roles":"sponsorDuties: [{\"id\":980446,\"code\":\"13\"}]","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"United Kingdom","full_name":"Q Squared Solutions Limited","duties_or_roles":"sponsorDuties: [{\"id\":980445,\"code\":\"4\"}]","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Syneos Health Inc.","duties_or_roles":"sponsorDuties: [{\"id\":980447,\"code\":\"1\"}]","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Medidata Solutions Inc.","duties_or_roles":"sponsorDuties: [{\"id\":980451,\"code\":\"6\"},{\"id\":980452,\"code\":\"7\"}]","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"Italy","full_name":"Mipharm S.p.A.","duties_or_roles":"Local drug supply Local equipment storage (sponsorDuties code 15)","organisation_type":"Pharmaceutical company"}
  • {"country":"Sweden","full_name":"Oriola Sweden AB","duties_or_roles":"sponsorDuties: [{\"id\":980449,\"code\":\"14\"}]","organisation_type":"Pharmaceutical company"}
  • {"country":"Denmark","full_name":"Specific Pharma A/S","duties_or_roles":"Country depot services, drug distribution, return and destruction and relabeling (sponsorDuties codes 14,15)","organisation_type":"Pharmaceutical company"}
  • {"country":"Germany","full_name":"Winicker-Norimed Medizinische Forschung GmbH","duties_or_roles":"Upload Study documentation to document management System CREDI (sponsorDuties code 15)","organisation_type":"Pharmaceutical company"}
  • {"country":"Ireland","full_name":"Icon Clinical Research Limited","duties_or_roles":"sponsorDuties: [{\"id\":980443,\"code\":\"1\"}]","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
IPTACOPAN
Active Substance
IPTACOPAN
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Authorisation Status
Authorised (prodAuthStatus=1)
Orphan Designation
Yes
Starting Dose
200 mg b.i.d.
Frequency
b.i.d.
Maximum Dose
400 mg per day

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