Clinical trial • Phase IV • Endocrinology

HYDROCORTISONE PH. EUR. for Adrenal hyperplasia | Primary adrenal insufficiency | Panhypopituitarism (secondary or tertiary adrenal insufficiency)

Phase IV trial of HYDROCORTISONE PH. EUR. for Adrenal hyperplasia | Primary adrenal insufficiency | Panhypopituitarism (secondary or tertiary adrenal insu…

Overview

Trial Therapeutic Area
Endocrinology
Trial Disease
Adrenal hyperplasia | Primary adrenal insufficiency | Panhypopituitarism (secondary or tertiary adrenal insufficiency)
Trial Stage
Phase IV
Drug Modality
Small molecule
Paediatric Trial
Yes

Key dates

Initial CTIS Submission Date
25-10-2024
First CTIS Authorization Date
31-10-2024

Trial design

HYDROCORTISONE PH. EUR. (oral). Dose unit: mg/m2; max daily dose 12 mg/m2; max total dose 1080 mg/m2; specific schedule not stated in available data.-controlled Phase IV trial across 1 site in Spain.

Comparator
HYDROCORTISONE PH. EUR. (oral). Dose unit: mg/m2; max daily dose 12 mg/m2; max total dose 1080 mg/m2; specific schedule not stated in available data.
Target Sample Size
35

Eligibility

Recruits 35 paediatric patients.

Vulnerable Population
Includes minors aged 6 to 17 years; informed consent must be signed by parent(s) or guardian(s) and/or patients (as stated in inclusion criteria). Subject information and informed consent forms for minor patients and for parents/legal representatives are provided (documents labelled _ESP indicate Spanish-language versions).

Inclusion criteria

  • {"criterion_text":"- Outpatients of both sexes, ≥ 6 years of age without swallowing problems and up to 17 years, at the time of signing the informed consent document by parent (s) or guardian (s) and / or patients.\n- Diagnosis of adrenal hyperplasia or isolated primary adrenal insufficiency or panhypopituitarism (secondary or tertiary adrenal insufficiency)."}

Exclusion criteria

  • {"criterion_text":"- Known hypersensitivity to any of the excipients in the hydrocortisone compounding.\n- Any disorder or situation (decompensation) that, in the opinion of the medical researcher, poses a risk of not complying with the treatment."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- The sensory acceptability of the formulation.","definition_or_measurement_approach":""}

Recruitment

Planned Sample Size
35
Recruitment Window Months
12
Consent Approach
Informed consent to be signed by parent(s) or legal guardian(s) and/or by the patients themselves as applicable (inclusion criterion states consent signing by parent(s) or guardian(s) and/or patients). Subject information and informed consent forms are available for minor patients and for parents/legal representatives (documents labeled with _ESP indicate Spanish-language versions).

Geography

Total Number Of Sites
1
Total Number Of Participants
35

Spain

Earliest CTIS Part Ii Submission Date
21-10-2024
Latest Decision Or Authorization Date
31-10-2024
Processing Time Days
10
Number Of Sites
1
Number Of Participants
35

Sites

Site Name
Hospital Universitari Vall D Hebron
Department Name
Pharmacy service
Contact Person Name
Carlos Javier Parramón
Number Of Participants
35

Sponsor

Primary sponsor

Full Name
Fundacio Hospital Universitari Vall D’Hebron Institut De Recerca
Organisation Type
Laboratory/Research/Testing facility
Country Of Registered Address
Spain

Investigational products

Investigational Product Name
HYDROCORTISONE PH. EUR.
Active Substance
HYDROCORTISONE PH. EUR.
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Maximum Dose
Max daily dose 12 mg/m2; max total dose 1080 mg/m2
Investigational Product Name
HYDROCORTISONE PH. EUR.
Active Substance
HYDROCORTISONE PH. EUR.
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Maximum Dose
Max daily dose 12 mg/m2; max total dose 1080 mg/m2

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