Clinical trial • Phase III • Immunology|Gastroenterology

GUSELKUMAB for Ulcerative colitis|Moderately to severely active ulcerative colitis

Phase III trial of GUSELKUMAB for Ulcerative colitis|Moderately to severely active ulcerative colitis.

Overview

Trial Therapeutic Area
Immunology|Gastroenterology
Trial Disease
Ulcerative colitis|Moderately to severely active ulcerative colitis
Trial Stage
Phase III
Drug Modality
Monoclonal antibody

Key dates

Initial CTIS Submission Date
14-05-2024
First CTIS Authorization Date
18-06-2024

Trial design

Randomised, placebo arms (guselkumab 1 ml pfs placebo; guselkumab 2 ml pfs placebo) compared with guselkumab (investigational product listed as guselkumab; product listing includes 'guselkumab - solution for injection in pre-filled syringe - 100 mg/ml'). specific dose and schedule details are not provided in the json.-controlled Phase III trial across 33 sites in Slovakia, Czechia, Bulgaria and others.

Randomised
Yes
Comparator
Placebo arms (Guselkumab 1 mL PFS Placebo; Guselkumab 2 mL PFS Placebo) compared with Guselkumab (investigational product listed as Guselkumab; product listing includes 'Guselkumab - solution for injection in pre-filled syringe - 100 mg/mL'). Specific dose and schedule details are not provided in the JSON.
Target Sample Size
174

Eligibility

Recruits 174 Vulnerable population selection indicated (populationOfTrialSubjects.isVulnerablePopulationSelected = true). Country-specific subject information and informed consent forms are listed in the documentation, including documents titled for Pregnant Partner and 12 months infant follow-up (e.g., "REDACTED_L1_SIS and ICF Pregnant Partner", "REDACTED_L1_SIS and ICF 12 months infant follow-up"). Informed consent appears to be obtained via country-specific SIS/ICF documents in multiple languages; partner/infant follow-up ICFs are provided, indicating additional consent processes for partners/infant follow-up where applicable..

Vulnerable Population
Vulnerable population selection indicated (populationOfTrialSubjects.isVulnerablePopulationSelected = true). Country-specific subject information and informed consent forms are listed in the documentation, including documents titled for Pregnant Partner and 12 months infant follow-up (e.g., "REDACTED_L1_SIS and ICF Pregnant Partner", "REDACTED_L1_SIS and ICF 12 months infant follow-up"). Informed consent appears to be obtained via country-specific SIS/ICF documents in multiple languages; partner/infant follow-up ICFs are provided, indicating additional consent processes for partners/infant follow-up where applicable.

Inclusion criteria

  • {"criterion_text":"- Documented diagnosis of ulcerative colitis (UC) for at least 3 months prior to baseline.\n- Moderately to severely active UC as assessed by the modified mayo score\n- Demonstraed inadequate response to or intolerance of conventional (ie, 6-MP, AZA, or corticosteroids) or advanced therapy (ADT; ie, TNFα antagonists, vedolizumab, ozanimod, or approved JAK inhibitors)."}

Exclusion criteria

  • {"criterion_text":"- 1.Has severe extensive colitis as defined in the protocol\n- 2.Extent of inflammatory disease limited to the rectum\n- 3.Participants with current diagnosis of indeterminate colitis, microscopic colitis, ischemic colitis, or crohn's disease (CD)\n- 4.Has a history of, or ongoing, chronic or recurrent infectious disease\n- 5.Currently has a malignancy or a history of malignancy within 5 years before screening (with the exception of nonmelanoma skin cancer or cervical carcinoma in situ that has been treated with no evidence of recurrence within 12 weeks prior to first dose of study intervention)"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Clinical remission (at week 12)","definition_or_measurement_approach":"Assessed at week 12. Disease activity in the trial is evaluated using the modified Mayo score (modified mayo score referenced elsewhere in eligibility criteria); no further formal definition of 'clinical remission' is provided in the JSON."}

Recruitment

Planned Sample Size
174
Recruitment Window Months
62
Consent Approach
Informed consent is managed via country-specific Subject Information Sheets and Informed Consent Forms (numerous SIS/ICF documents are listed by country and language). There are ICF documents for main consent, pregnant partner ICFs, and 12-month infant follow-up ICFs, indicating age- or role-specific consent documents. Multiple language versions are available (document titles include language identifiers such as EN, CZ, BG, DE, ES, PL, FR, HU). CTIS public/scientific contact for the sponsor is provided (functionalName 'CTIS Point of Contact', email CTISadmin@its.jnj.com).

Geography

Total Number Of Sites
33
Total Number Of Participants
143

Slovakia

Latest Decision Or Authorization Date
28-02-2025
Number Of Sites
2
Number Of Participants
2

Sites

Site Name
Endomed s.r.o.
Department Name
Gastroenterologicka ambulancia
Principal Investigator Name
Miroslav Fedurco
Principal Investigator Email
fedurco@endomed.sk
Contact Person Name
Miroslav Fedurco
Contact Person Email
fedurco@endomed.sk
Site Name
Cliniq s.r.o.
Department Name
Gastroenterologicka ambulancia
Principal Investigator Name
Tibor Hlavaty
Principal Investigator Email
tibor.hlavaty2@gmail.com
Contact Person Name
Tibor Hlavaty
Contact Person Email
tibor.hlavaty2@gmail.com

Czechia

Latest Decision Or Authorization Date
09-09-2025
Number Of Sites
3
Number Of Participants
12

Sites

Site Name
Gastroenterologie s.r.o.
Principal Investigator Name
Milan Široký
Principal Investigator Email
gastro@gastroenterologie-hk.cz
Contact Person Name
Milan Široký
Contact Person Email
gastro@gastroenterologie-hk.cz
Site Name
Nemocnice Ceske Budejovice a.s.
Department Name
Gastroenterologické oddělení
Principal Investigator Name
Martin Bortlík
Principal Investigator Email
borlik.martin@nemcb.cz
Contact Person Name
Martin Bortlík
Contact Person Email
borlik.martin@nemcb.cz
Site Name
Axon Clinical s.r.o.
Principal Investigator Name
Jan Matouš
Principal Investigator Email
jan.matous@axon-clinical.com
Contact Person Name
Jan Matouš
Contact Person Email
jan.matous@axon-clinical.com

Bulgaria

Latest Decision Or Authorization Date
15-09-2025
Number Of Sites
2
Number Of Participants
3

Sites

Site Name
Medical center Asclepion humane medicine researches EOOD
Principal Investigator Name
Rayna Draganova
Principal Investigator Email
drdraganova@abv.bg
Contact Person Name
Rayna Draganova
Contact Person Email
drdraganova@abv.bg
Site Name
Diagnostics And Consultation Center Convex Ltd.
Principal Investigator Name
Ludmila Tankova
Principal Investigator Email
drtankova@abv.bg
Contact Person Name
Ludmila Tankova
Contact Person Email
drtankova@abv.bg

Germany

Latest Decision Or Authorization Date
09-09-2025
Number Of Sites
2
Number Of Participants
5

Sites

Site Name
Medizinisches Versorgungszentrum (MVZ) Dachau
Department Name
Medizinisches Versorgungszentrum (MVZ) Dachau
Principal Investigator Name
Wilfred Landry
Principal Investigator Email
kontakt@dachau-med.de
Contact Person Name
Wilfred Landry
Contact Person Email
kontakt@dachau-med.de
Site Name
Medizinische Hochschule Hannover
Department Name
Klinik fur Gastroenterologie, Hepatologie und Endokrinologie
Principal Investigator Name
Ursula Seidler
Principal Investigator Email
seidler.ursula@mh-hannover.de
Contact Person Name
Ursula Seidler
Contact Person Email
seidler.ursula@mh-hannover.de

Spain

Latest Decision Or Authorization Date
09-09-2025
Number Of Sites
2
Number Of Participants
6

Sites

Site Name
Hospital Universitario Virgen De La Macarena
Department Name
Gastroenterology Service
Principal Investigator Name
Federico Arguelles Arias
Principal Investigator Email
farguelles@telefonica.net
Contact Person Name
Federico Arguelles Arias
Contact Person Email
farguelles@telefonica.net
Site Name
Hospital Marina Baixa De La Vila Joiosa
Department Name
Gastroenterology Service
Principal Investigator Name
Antonio García Herola
Principal Investigator Email
agherola@gmail.com
Contact Person Name
Antonio García Herola
Contact Person Email
agherola@gmail.com

Poland

Latest Decision Or Authorization Date
12-09-2025
Number Of Sites
13
Number Of Participants
93

Sites

Site Name
Gastromed Sp. z o.o.
Department Name
Gastromed Sp. z o.o.
Principal Investigator Name
Adam Kopon
Principal Investigator Email
gastromedtorun@gmail.com
Contact Person Name
Adam Kopon
Contact Person Email
gastromedtorun@gmail.com
Site Name
Twoja Przychodnia Szczecinskie Centrum Medyczne Sp. z o.o.
Department Name
Twoja Przychodnia - SCM
Principal Investigator Name
Beata Gawdis-Wojnarska
Principal Investigator Email
scm@twojaprzychodnia.com
Contact Person Name
Beata Gawdis-Wojnarska
Contact Person Email
scm@twojaprzychodnia.com
Site Name
Medical Network Sp. z o.o.
Department Name
Medical Network Spolka z o.o. WIP Warsaw IBD Point Profesor Kierkus
Principal Investigator Name
Jaroslaw Kierkus
Principal Investigator Email
wip@wip.waw.pl
Contact Person Name
Jaroslaw Kierkus
Contact Person Email
wip@wip.waw.pl
Site Name
Centrum Medyczne Lukamed Sp. z o.o.
Department Name
Centrum Medyczne LukaMed
Principal Investigator Name
Artur Soltysiak
Principal Investigator Email
joannaluka@lukamed.com
Contact Person Name
Artur Soltysiak
Contact Person Email
joannaluka@lukamed.com
Site Name
Centrum Medyczne Lukamed Sp. z o.o.
Department Name
Centrum Medyczne LukaMed
Principal Investigator Name
Dariusz Gajda
Principal Investigator Email
dariuszgajda@lukamed.com
Contact Person Name
Dariusz Gajda
Contact Person Email
dariuszgajda@lukamed.com
Site Name
Bodyclinic Sp. z o.o. sp.k.
Department Name
Bodyclinic Sp. z o.o. Sp. k.
Principal Investigator Name
Piotr Gietka
Principal Investigator Email
kontakt@bodyclinic.pl
Contact Person Name
Piotr Gietka
Contact Person Email
kontakt@bodyclinic.pl
Site Name
Melita Medical Sp. z o.o.
Department Name
Centrum Medyczne MELITA MEDICAL
Principal Investigator Name
Jaroslaw Leszczyszyn
Principal Investigator Email
b.lapuszynski@melitamedical.pl
Contact Person Name
Jaroslaw Leszczyszyn
Contact Person Email
b.lapuszynski@melitamedical.pl
Site Name
Gastromed Kralisz Romatowski Stachurska Sp. j.
Department Name
Gastromed Kralisz Romatowski Stachurska Sp. j.
Principal Investigator Name
Jacek Romatowski
Principal Investigator Email
biuro@gastromed.info
Contact Person Name
Jacek Romatowski
Contact Person Email
biuro@gastromed.info
Site Name
Pro Life Medica Sp. z o.o.
Department Name
Pro Life Medica Sp z o o ETG Zamosc
Principal Investigator Name
Katarzyna Wojcik
Principal Investigator Email
zamosc@etg-network.com
Contact Person Name
Katarzyna Wojcik
Contact Person Email
zamosc@etg-network.com
Site Name
Centrum Medyczne Plejady Magdalena Celinska Loewenhoff Michal Zolnowski sp.k.
Department Name
Centrum Medyczne Plejady
Principal Investigator Name
Monika Augustyn
Principal Investigator Email
trials@plejady.com.pl
Contact Person Name
Monika Augustyn
Contact Person Email
trials@plejady.com.pl
Site Name
Promed P.Lach R.Glowacki Sp. j.
Department Name
Centrum Medyczne PROMED
Principal Investigator Name
Danuta Owczarek
Principal Investigator Email
badania.kliniczne@cmpromed.pl
Contact Person Name
Danuta Owczarek
Contact Person Email
badania.kliniczne@cmpromed.pl
Site Name
Centrum Medyczne Medyk Sp. z o.o. S.K.
Department Name
Centrum Medyczne Medyk
Principal Investigator Name
Rafal Filip
Principal Investigator Email
badaniakliniczne.rejtana@medyk.rzeszow.pl
Contact Person Name
Rafal Filip
Site Name
Vistamed & Vertigo Sp. z o.o.
Department Name
Vistamed & Vertigo Sp. z o.o.
Principal Investigator Name
Bernadeta Frysna
Principal Investigator Email
m.szewczuk@vistamed.pl
Contact Person Name
Bernadeta Frysna
Contact Person Email
m.szewczuk@vistamed.pl

Belgium

Latest Decision Or Authorization Date
08-09-2025
Number Of Sites
1
Number Of Participants
2

Sites

Site Name
CHU Saint Pierre
Department Name
Hépato-Gastro-Entérologie
Principal Investigator Name
Vinciane Muls
Principal Investigator Email
vinciane.muls@stpierre-bru.be
Contact Person Name
Vinciane Muls
Contact Person Email
vinciane.muls@stpierre-bru.be

France

Latest Decision Or Authorization Date
03-10-2025
Number Of Sites
5
Number Of Participants
12

Sites

Site Name
Centre Hospitalier Universitaire De Bordeaux
Department Name
Hepato Gastroenterology Department
Principal Investigator Name
David LAHARIE
Principal Investigator Email
david.laharie@chu-bordeaux.fr
Contact Person Name
David LAHARIE
Contact Person Email
david.laharie@chu-bordeaux.fr
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
Hepato Gastroenterology Department
Principal Investigator Name
Cyrielle GILLETTA DE SAINT-JOSEPH
Principal Investigator Email
gilletta.c@chu-toulouse.fr
Contact Person Name
Cyrielle GILLETTA DE SAINT-JOSEPH
Contact Person Email
gilletta.c@chu-toulouse.fr
Site Name
Nouvelles Cliniques Nimoises
Department Name
Hepato Gastroenterology Department
Principal Investigator Name
Florent GONZALEZ
Principal Investigator Email
secretariat@gastromeridien.fr
Contact Person Name
Florent GONZALEZ
Contact Person Email
secretariat@gastromeridien.fr
Site Name
CHRU De Nancy
Department Name
Hepato Gastroenterology Department
Principal Investigator Name
Benedicte CARON
Principal Investigator Email
b.caron@chru-nancy.fr
Contact Person Name
Benedicte CARON
Contact Person Email
b.caron@chru-nancy.fr
Site Name
Centre Medico Chirurgical Ambroise Pare Hartmann
Department Name
Institut des MICI
Principal Investigator Name
Yoram BOUHNIK
Principal Investigator Email
yoram.bouhnik@institutdesmici.fr
Contact Person Name
Yoram BOUHNIK

Hungary

Latest Decision Or Authorization Date
09-10-2025
Number Of Sites
3
Number Of Participants
8

Sites

Site Name
Semmelweis University
Department Name
Gasztroenterológia
Principal Investigator Name
Pál Miheller
Principal Investigator Email
pmiheller@gmail.com
Contact Person Name
Pál Miheller
Contact Person Email
pmiheller@gmail.com
Site Name
Vasutegeszseguegyi Nonprofit Koezhasznu Kft.
Department Name
Gasztroenterológia
Principal Investigator Name
Gyula G.Kiss
Principal Investigator Email
gkissgyula@gmail.com
Contact Person Name
Gyula G.Kiss
Contact Person Email
gkissgyula@gmail.com
Site Name
Semmelweis University
Department Name
Gasztroenterológia
Principal Investigator Name
Emese Mihály
Principal Investigator Email
emesemihaly@hotmail.com
Contact Person Name
Emese Mihály
Contact Person Email
emesemihaly@hotmail.com

Sponsor

Primary sponsor

Full Name
Janssen - Cilag International
Organisation Type
Pharmaceutical company
Country Of Registered Address
Belgium

Contract research organisations

Name
Parexel International (IRL) Limited
Name
Iqvia Rds Inc.
Responsibilities
Country level study set-up, country and site management, local regulatory submissions
Name
Almac Clinical Technologies LLC
Responsibilities
Treatment randomisation

Third parties

  • {"country":"Canada","full_name":"Alimentiv Inc.","duties_or_roles":"Histopathology","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Bioclinica Inc.","duties_or_roles":"Imaging Vendor","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Ireland","full_name":"Parexel International (IRL) Limited","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Labcorp Central Laboratory Services LP","duties_or_roles":"Sample management sercies and forwarding shipment to other labs/Janssen facilities","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Almac Clinical Technologies LLC","duties_or_roles":"Treatment randomisation","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Yprime LLC","duties_or_roles":"eCOA","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Iqvia Rds Inc.","duties_or_roles":"Country level study set-up, country and site management, local regulatory submissions","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Guselkumab
Active Substance
GUSELKUMAB
Modality
Monoclonal antibody
Routes Of Administration
SUBCUTANEOUS USE
Route
Subcutaneous
Authorisation Status
1
Investigational Product Name
Guselkumab - solution for injection in pre-filled syringe - 100 mg/mL
Active Substance
GUSELKUMAB
Modality
Monoclonal antibody
Routes Of Administration
SUBCUTANEOUS USE
Route
Subcutaneous
Authorisation Status
1
Investigational Product Name
Guselkumab 1 mL PFS Placebo
Modality
Other
Investigational Product Name
Guselkumab 2 mL PFS Placebo
Modality
Other

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