Clinical trial • Phase IV • Cardiology

Evolocumab for Acute myocardial infarction

Phase IV trial of Evolocumab for Acute myocardial infarction.

Overview

Trial Therapeutic Area
Cardiology
Trial Disease
Acute myocardial infarction
Trial Stage
Phase IV
Drug Modality
Monoclonal antibody

Key dates

Initial CTIS Submission Date
14-10-2024
First CTIS Authorization Date
11-11-2024

Trial design

Randomised, evolocumab (repatha 140 mg solution for injection in pre-filled pen) subcutaneous versus standard of care / "normal strategies" to reach guideline ldl objectives. specific dosing schedule not specified in the ctis summary.-controlled Phase IV trial in Spain, Poland, Germany and others.

Randomised
Yes
Comparator
Evolocumab (Repatha 140 mg solution for injection in pre-filled pen) subcutaneous versus standard of care / "normal strategies" to reach guideline LDL objectives. Specific dosing schedule not specified in the CTIS summary.
Real World Control
Yes
Target Sample Size
433
Trial Duration For Participant
365

Eligibility

Recruits 433 Vulnerable population not selected. The trial enrols adults; informed consent is required: "Inform consent obtained in writing at enrolment in the trial". No assent/parental consent procedures or paediatric consent arrangements are described..

Pregnancy Exclusion
Pregnant (with a positive pregnancy test at inclusion), breast-feeding or planning to have children or breast-feed during treatment and for a period of 17 weeks after the end of treatment in the trial.
Vulnerable Population
Vulnerable population not selected. The trial enrols adults; informed consent is required: "Inform consent obtained in writing at enrolment in the trial". No assent/parental consent procedures or paediatric consent arrangements are described.

Inclusion criteria

  • {"criterion_text":"- Male or female\n- Diagnosis of STEMI defined as: symptoms of acute MI of at least 30 min AND within the previous 24 hours with new persistent ST-segment elevation ≥1 mm in ≥2 continuous ECG leads AND an indication for primary PCI AND > 55 years reported by the patient\n- or, with a non-ST-segment elevation myocardial infarction (NSTEMI) defined by : Angiography performed within 72 hours, AND Indication for percutaneous coronary intervention, AND Presenting at least one of the following risk factors: Diabetes, Peripheral arterial disease, Multitruncular disease (≥ 2 or common trunk) confirmed by angiography, Previous myocardial infarction or stroke without sequelae prior to randomisation, eGFR creatinine clearance: 15 to 45 mL/min/1.73 m² calculated according to the MDRD formula at randomisation.\n- Statin at the maximum tolerated dose as part of standard management, i.e. intention to treat with a statin as soon as possible at randomisation\n- Inform consent obtained in writing at enrolment in the trial"}

Exclusion criteria

  • {"criterion_text":"- Fibrinolytic treatment\n- Participating in another clinical trial with other investigational treatments or devices within 30 days prior to inclusion in this trial, or already included in a trial.\n- Unavailable and/or non-compliant to attend follow-up visits and to follow all procedures required by the trial.\n- Scheduled bypass\n- Current haemodynamic instability defined by either : Killip III or IV, Symptomatic and/or sustained hypotension (systolic pressure <80 mmHg), Known left ventricular ejection fraction < 30%.\n- Evidence of severe hepatobiliary disease: active liver dysfunction or active biliary obstruction, decompensated cirrhosis or infectious/inflammatory hepatitis.\n- Active cancer\n- Comorbidity limiting life expectancy to less than 12 months\n- Previous or ongoing evolocumab or other anti-PCSK9 therapy\n- Known hypersensitivity to any component of the trial treatment\n- Pregnant (with a positive pregnancy test at inclusion), breast-feeding or planning to have children or breast-feed during treatment and for a period of 17 weeks after the end of treatment in the trial."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- The primary endpoint is a reduction in LDL-C levels ≥ 50% from baseline and an LDL-C level < 1.4 mmol/L at 12 months follow-up.","definition_or_measurement_approach":"LDL-C measured and compared to baseline at 12 months follow-up to assess ≥50% reduction and absolute LDL-C < 1.4 mmol/L."}
  • {"endpoint_text":"- LDL-C levels will be assessed at follow-up visits at 6 and 22 weeks and 12 months after randomisation. (At 38 weeks, 16, 20, 28 and 32 months post-randomisation, only if data are available).","definition_or_measurement_approach":"Scheduled LDL-C assessments at 6 weeks, 22 weeks and 12 months post-randomisation (and at additional later timepoints if data available) to evaluate lipid outcomes."}
  • {"endpoint_text":"- The primary clinical endpoint is the composite endpoint of death (any cause) or any unplanned hospitalization for a CV reason at 12 months","definition_or_measurement_approach":"Composite clinical outcome (all-cause death OR any unplanned cardiovascular hospitalization) assessed at 12 months post-randomisation."}

Secondary endpoints

  • {"endpoint_text":"- LDL-C<40, mg/dL at 12 months follow-up","definition_or_measurement_approach":"LDL-C measured at 12 months; assessment of whether LDL-C <40 mg/dL."}
  • {"endpoint_text":"- Composite of death (any cause), myocardial infarction, stroke, unplanned revascularization at 12 months follow-up","definition_or_measurement_approach":"Composite clinical outcome assessed at 12 months post-randomisation."}
  • {"endpoint_text":"- Composite of death (any cause) or myocardial infarction at 12 months follow-up","definition_or_measurement_approach":"Composite (all-cause death OR myocardial infarction) assessed at 12 months."}
  • {"endpoint_text":"- Death (any cause) at 12 months follow-up","definition_or_measurement_approach":"All-cause mortality status assessed at 12 months."}
  • {"endpoint_text":"- Death (cardiovascular) at 12 months follow-up","definition_or_measurement_approach":"Cardiovascular-specific mortality assessed at 12 months."}
  • {"endpoint_text":"- Composite of death (any cause), myocardial infarction, stroke at 12 months follow-up","definition_or_measurement_approach":"Composite outcome of death, MI, or stroke assessed at 12 months."}

Recruitment

Planned Sample Size
433
Recruitment Window Months
78
Consent Approach
Informed consent obtained in writing at enrolment from participants (adults). Subject information and informed consent form (L1) available for adults; protocol and ICF materials available in multiple languages (English, French, Polish, German, Italian as indicated by protocol synopses and ICF documents). No assent or minor-specific consent procedures described.

Geography

Total Number Of Sites
55
Total Number Of Participants
433

Spain

Earliest CTIS Part Ii Submission Date
06-11-2024
Latest Decision Or Authorization Date
23-05-2025
Processing Time Days
198
Number Of Sites
7
Number Of Participants
433

Sites

Site Name
Hospital Universitario Central De Asturias
Department Name
Cardiology
Principal Investigator Name
Alberto Alperi Garcia
Principal Investigator Email
alberto.alperi.garcia@hotmail.com
Contact Person Name
Alberto Alperi Garcia
Site Name
Bellvitge University Hospital
Department Name
Cardiology
Principal Investigator Name
Angel Cequier
Principal Investigator Email
acequier@bellvitgehospital.cat
Contact Person Name
Angel Cequier
Contact Person Email
acequier@bellvitgehospital.cat
Site Name
Hospital General Universitario De Alicante
Department Name
Cardiology
Principal Investigator Name
Juan Miguel Ruiz Nodar
Principal Investigator Email
Ruiz_jmi@gva.es
Contact Person Name
Juan Miguel Ruiz Nodar
Contact Person Email
Ruiz_jmi@gva.es
Site Name
Hospital Universitario Marques De Valdecilla
Department Name
Cardiology
Principal Investigator Name
Natalia Royuela Martinez
Principal Investigator Email
natalia.royuela@scsalud.es
Contact Person Name
Natalia Royuela Martinez
Contact Person Email
natalia.royuela@scsalud.es
Site Name
Hospital San Pedro
Department Name
Cardiology
Principal Investigator Name
Luis Javier Alonso Perez
Principal Investigator Email
lalonso@riojasalud.es
Contact Person Name
Luis Javier Alonso Perez
Contact Person Email
lalonso@riojasalud.es
Site Name
Hospital Alvaro Cunqueiro
Department Name
Cardiology
Principal Investigator Name
Victor Alfonso Jimenez Diaz
Principal Investigator Email
victor.alfonso.jimenez.diaz@sergas.es
Contact Person Name
Victor Alfonso Jimenez Diaz
Site Name
Hospital De La Santa Creu I Sant Pau
Department Name
Cardiology
Principal Investigator Name
Xavier Garcia-Moll Marimon
Principal Investigator Email
xgarcia-moll@santpau.cat
Contact Person Name
Xavier Garcia-Moll Marimon
Contact Person Email
xgarcia-moll@santpau.cat

Poland

Earliest CTIS Part Ii Submission Date
06-11-2024
Latest Decision Or Authorization Date
19-05-2025
Processing Time Days
194
Number Of Sites
9
Number Of Participants
433

Sites

Site Name
Krakowski Szpital Specjalistyczny IM. Jana Pawla II
Department Name
Cardiology
Principal Investigator Name
Jacek Legutko
Principal Investigator Email
jacek.legutko@uj.edu.pl
Contact Person Name
Jacek Legutko
Contact Person Email
jacek.legutko@uj.edu.pl
Site Name
Slaskie Centrum Chorob Serca W Zabrzu
Department Name
Cardiology
Principal Investigator Name
Zbiniew Kalarus
Principal Investigator Email
Sek.KD1@sccs.pl
Contact Person Name
Zbiniew Kalarus
Contact Person Email
Sek.KD1@sccs.pl
Site Name
Uniwersytecki Szpital Kliniczny W Poznaniu
Department Name
Cardiology
Principal Investigator Name
Maciej Lesiak
Principal Investigator Email
maciej.lesiak@skpp.edu.pl
Contact Person Name
Maciej Lesiak
Contact Person Email
maciej.lesiak@skpp.edu.pl
Site Name
Szpital Uniwersytecki W Krakowie
Department Name
Cardiology
Principal Investigator Name
Stanislaw Bartus
Principal Investigator Email
mbbartus@cyfronet.pl
Contact Person Name
Stanislaw Bartus
Contact Person Email
mbbartus@cyfronet.pl
Site Name
Uniwersyteckie Centrum Kliniczne Warszawskiego Uniwersytetu Medycznego
Department Name
Cardiology
Principal Investigator Name
Marcin Grabowski
Principal Investigator Email
marcin.grabowski@wum.edu.pl
Contact Person Name
Marcin Grabowski
Contact Person Email
marcin.grabowski@wum.edu.pl
Site Name
Uniwersytecki Szpital Kliniczny W Opolu
Department Name
Cardiology
Principal Investigator Name
Marek Gierlotka
Principal Investigator Email
marek.gierlotka@usk.opole.pl
Contact Person Name
Marek Gierlotka
Contact Person Email
marek.gierlotka@usk.opole.pl
Site Name
Wojewódzki Szpital Specjalistyczny we Wrocławiu Ośrodek Badawczo-Rozwojowy
Department Name
Cardiology
Principal Investigator Name
Tomasz Roleder
Principal Investigator Email
tomaszroleder@gmail.com
Contact Person Name
Tomasz Roleder
Contact Person Email
tomaszroleder@gmail.com
Site Name
Szpital Uniwersytecki Nr 1 Im. Dr. A. Jurasza W Bydgoszczy
Department Name
Cardiology
Principal Investigator Name
Jacek Kubica
Principal Investigator Email
jkubica@cm.umk.pl
Contact Person Name
Jacek Kubica
Contact Person Email
jkubica@cm.umk.pl
Site Name
Uniwersytecki Szpital Kliniczny (other Polish site)
Department Name
Cardiology

Germany

Earliest CTIS Part Ii Submission Date
06-11-2024
Latest Decision Or Authorization Date
05-06-2025
Processing Time Days
211
Number Of Sites
4
Number Of Participants
433

Sites

Site Name
Otto Von Guericke Universitaet Magdeburg
Department Name
Cardiology, Angiology
Principal Investigator Name
Rüdiger Braun-Dullaeus
Principal Investigator Email
r.braun-dullaeus@med.ovgu.de
Contact Person Name
Rüdiger Braun-Dullaeus
Contact Person Email
r.braun-dullaeus@med.ovgu.de
Site Name
Universitaetsklinikum Schleswig-Holstein AöR
Department Name
Medical Clinic II
Principal Investigator Name
Ingo Eitel
Principal Investigator Email
ingo.eitel@uksh.de
Contact Person Name
Ingo Eitel
Contact Person Email
ingo.eitel@uksh.de
Site Name
Universitaetsklinikum Jena KöR
Department Name
Interne Medizin I
Principal Investigator Name
Oliver Weingärtner
Principal Investigator Email
oliver.weingartner@med.uni-jena.de
Contact Person Name
Oliver Weingärtner
Site Name
Herzzentrum Leipzig GmbH
Department Name
Internal Medicine/Cardiology
Principal Investigator Name
Holger Thiele
Principal Investigator Email
holger.thiele@medizin.uni-leipzig.de
Contact Person Name
Holger Thiele

France

Earliest CTIS Part Ii Submission Date
06-11-2024
Latest Decision Or Authorization Date
18-11-2025
Processing Time Days
377
Number Of Sites
27
Number Of Participants
434

Sites

Site Name
Centre Hospitalier Yves Le Foll
Department Name
Service de Cardiologie
Principal Investigator Name
Laurent PAYOT
Principal Investigator Email
laurent.payot@ch-stbrieuc.fr
Contact Person Name
Laurent PAYOT
Contact Person Email
laurent.payot@ch-stbrieuc.fr
Site Name
Centre Hospitalier De Versailles
Department Name
Service de cardiologie
Principal Investigator Name
Guillaume GODEAU
Principal Investigator Email
ggodeau@ch-versailles.fr
Contact Person Name
Guillaume GODEAU
Contact Person Email
ggodeau@ch-versailles.fr
Site Name
Centre Hospitalier Universitaire D'Angers
Department Name
Service de cardiologie
Principal Investigator Name
Fabrice PRUNIER
Principal Investigator Email
FaPrunier@chu-angers.fr
Contact Person Name
Fabrice PRUNIER
Contact Person Email
FaPrunier@chu-angers.fr
Site Name
Clinique Du Pont De Chaume
Department Name
Service de cardiologie
Principal Investigator Name
Thibaut PETRONI
Principal Investigator Email
petroni.cardio@gmail.com
Contact Person Name
Thibaut PETRONI
Contact Person Email
petroni.cardio@gmail.com
Site Name
Centre Hospitalier Metropole Savoie
Department Name
Service de Cardiologie
Principal Investigator Name
Laure BATIAS-MOREAU
Principal Investigator Email
Laure.Batias@ch-metropole-savoie.fr
Contact Person Name
Laure BATIAS-MOREAU
Site Name
Centre Hospitalier Universitaire De Nimes
Department Name
Service de Cardiologie
Principal Investigator Name
Guillaume CAYLA
Principal Investigator Email
guillaumecayla@free.fr
Contact Person Name
Guillaume CAYLA
Contact Person Email
guillaumecayla@free.fr
Site Name
Centre Hospitalier Universitaire De Poitiers
Department Name
Service de cardiologie
Principal Investigator Name
Claire BOULETI
Principal Investigator Email
claire.bouleti@chu-poitiers.fr
Contact Person Name
Claire BOULETI
Contact Person Email
claire.bouleti@chu-poitiers.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Service de cardiologie
Principal Investigator Name
Jean-Guillaume DILLINGER
Principal Investigator Email
jean-guillaume.dillinger@aphp.fr
Contact Person Name
Jean-Guillaume DILLINGER
Site Name
Centre Hospitalier De Pau
Department Name
Service de cardiologie
Principal Investigator Name
Pierre POUSTIS
Principal Investigator Email
pierre.poustis@ch-pau.fr
Contact Person Name
Pierre POUSTIS
Contact Person Email
pierre.poustis@ch-pau.fr
Site Name
Assistance Publique Hopitaux De Paris (Institut de Cardiologie)
Department Name
Institut de Cardiologie
Principal Investigator Name
Gilles MONTALESCOT
Principal Investigator Email
gilles.montalescot@aphp.fr
Contact Person Name
Gilles MONTALESCOT
Contact Person Email
gilles.montalescot@aphp.fr
Site Name
CHRU De Nancy
Department Name
Service de cardiologie
Principal Investigator Name
Batric POPOVIC
Principal Investigator Email
b.popovic@chru-nancy.fr
Contact Person Name
Batric POPOVIC
Contact Person Email
b.popovic@chru-nancy.fr
Site Name
Hopital NOVO
Department Name
Service cardiologie
Principal Investigator Name
Véronique DECALF
Principal Investigator Email
veronique.decalf@ght-novo.fr
Contact Person Name
Véronique DECALF
Contact Person Email
veronique.decalf@ght-novo.fr
Site Name
Centre Hospitalier D'Antibes Juan Les Pins
Department Name
Service de Cardiologie, USIC
Principal Investigator Name
Anne BELLEMAIN-APPAIX
Principal Investigator Email
anne.bellemain-appaix@ch-antibes.fr
Contact Person Name
Anne BELLEMAIN-APPAIX
Site Name
Les Hopitaux Universitaires De Strasbourg
Department Name
Service de cardiologie Interventionnelle
Principal Investigator Name
Patrick OHLMANN
Principal Investigator Email
patrick.Ohlmann@chru-strasbourg.fr
Contact Person Name
Patrick OHLMANN
Site Name
University Hospital Of Clermont-Ferrand
Department Name
DépartemCardiologie et Maladies Vasculaires
Principal Investigator Name
Géraud SOUTEYRAND
Principal Investigator Email
gsouteyrand@chu-clermontferrand.fr
Contact Person Name
Géraud SOUTEYRAND
Site Name
CHU Besancon
Department Name
Service de cardiologie - Pôle Cœur-Poumons
Principal Investigator Name
François SCHIELE
Principal Investigator Email
francois.schiele@univ-fcomte.fr
Contact Person Name
François SCHIELE
Site Name
Centre Hospitalier De Haguenau
Department Name
Service de cardiologie interventionnelle et USIC
Principal Investigator Name
Sabrina UHRY
Principal Investigator Email
sabrina.uhry@ch-haguenau.fr
Contact Person Name
Sabrina UHRY
Contact Person Email
sabrina.uhry@ch-haguenau.fr
Site Name
Centre Hospitalier De Colmar
Department Name
Service de Cardiologie
Principal Investigator Name
Laszlo LEVAI
Principal Investigator Email
doclevai@calixo.net
Contact Person Name
Laszlo LEVAI
Contact Person Email
doclevai@calixo.net
Site Name
Centre Hospitalier Universitaire De Nice
Department Name
Service de Cardiologie
Principal Investigator Name
Emilie FERRARI
Principal Investigator Email
ferrari.e@chu-nice.fr
Contact Person Name
Emilie FERRARI
Contact Person Email
ferrari.e@chu-nice.fr
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
Service de Cardiologie
Principal Investigator Name
Meyer ELBAZ
Principal Investigator Email
elbaz.m@chu-toulouse.fr
Contact Person Name
Meyer ELBAZ
Contact Person Email
elbaz.m@chu-toulouse.fr
Site Name
Centre Hospitalier Universitaire De Lille
Department Name
Cardio Vasculaire et Pulmonaire
Principal Investigator Name
Eric VAN BELLE
Principal Investigator Email
e-vanbelle@chru-lille.fr
Contact Person Name
Eric VAN BELLE
Contact Person Email
e-vanbelle@chru-lille.fr
Site Name
Les Hopitaux De Chartres
Department Name
Service de Cardiologie
Principal Investigator Name
Gregoire RANGE
Principal Investigator Email
grange@ch-chartres.f
Contact Person Name
Gregoire RANGE
Contact Person Email
grange@ch-chartres.f
Site Name
Centre Hospitalier Departemental Vendee
Department Name
Service de Cardiologie
Principal Investigator Name
Jacques CHANPENG
Principal Investigator Email
jacques.chan-peng@ght85.fr
Contact Person Name
Jacques CHANPENG
Contact Person Email
jacques.chan-peng@ght85.fr
Site Name
Centre Hospitalier Universitaire De Nantes
Department Name
Institut du thorax
Principal Investigator Name
Julien PLESSIS
Principal Investigator Email
Julien.PLESSIS@chu-nantes.fr
Contact Person Name
Julien PLESSIS
Contact Person Email
Julien.PLESSIS@chu-nantes.fr
Site Name
Centre Hospitalier De La Cote Basque
Department Name
Service de cardiologie
Principal Investigator Name
Jean Noel LABEQUE
Principal Investigator Email
dr.jnlabeque@gmail.com
Contact Person Name
Jean Noel LABEQUE
Contact Person Email
dr.jnlabeque@gmail.com
Site Name
Centre Hospitalier Regional Universitaire De Tours
Department Name
Soins Intensifs et Cardiologie Interventionnelle
Principal Investigator Name
Denis ANGOULVANT
Principal Investigator Email
d.angoulvant@chu-tours.fr
Contact Person Name
Denis ANGOULVANT
Contact Person Email
d.angoulvant@chu-tours.fr
Site Name
Centre Hospitalier Universitaire De Caen Normandie
Department Name
Service de Cardiologie et Pathologie Vasculaire
Principal Investigator Name
Farzin BEYGUI
Principal Investigator Email
beygui-f@chu-caen.fr
Contact Person Name
Farzin BEYGUI
Contact Person Email
beygui-f@chu-caen.fr

Italy

Earliest CTIS Part Ii Submission Date
06-11-2024
Latest Decision Or Authorization Date
05-12-2025
Processing Time Days
394
Number Of Sites
8
Number Of Participants
433

Sites

Site Name
Sant'Andrea Hospital, La Spezia, ASL5 Liguria
Department Name
Cardiology
Principal Investigator Name
Alberto Menozzi
Principal Investigator Email
albemenozzi@gmail.com
Contact Person Name
Alberto Menozzi
Contact Person Email
albemenozzi@gmail.com
Site Name
Azienda Ospedaliero-Universitaria Sant'Anna
Department Name
Cardiology
Principal Investigator Name
Gianluca Campo
Principal Investigator Email
cmpglc@unife.it
Contact Person Name
Gianluca Campo
Contact Person Email
cmpglc@unife.it
Site Name
Azienda Sanitaria Locale Di Pescara
Department Name
Cardiology
Principal Investigator Name
Leonardo Paloscia
Principal Investigator Email
leonardo.paloscia@ausl.pe.it
Contact Person Name
Leonardo Paloscia
Contact Person Email
leonardo.paloscia@ausl.pe.it
Site Name
Azienda Unita' Sanitaria Locale Toscana Sud Est
Department Name
Cardiology
Principal Investigator Name
Andrea Picchi
Principal Investigator Email
andra.picchi@uslsudest.toscana.it
Contact Person Name
Andrea Picchi
Site Name
Federico II University of Naples
Department Name
Cardiology
Principal Investigator Name
Giovanni Esposito
Principal Investigator Email
giovanni.esposito2@unina.it
Contact Person Name
Giovanni Esposito
Contact Person Email
giovanni.esposito2@unina.it
Site Name
Azienda Ospedaliero-Universitaria Maggiore Della Carita
Department Name
Cardiology
Principal Investigator Name
Giuseppe Patti
Principal Investigator Email
giuseppe.patti@uniupo.it
Contact Person Name
Giuseppe Patti
Contact Person Email
giuseppe.patti@uniupo.it
Site Name
Azienda Sanitaria Locale TO3
Department Name
Cardiology
Principal Investigator Name
Giulio Piedimonte
Principal Investigator Email
giulio.piedimonte@gmail.com
Contact Person Name
Giulio Piedimonte
Contact Person Email
giulio.piedimonte@gmail.com
Site Name
Ospedale San Donato
Department Name
Cardiology
Principal Investigator Name
Maurizio Chioccioli
Principal Investigator Email
maurizio.chioccioli@uslsudest.toscana.it
Contact Person Name
Maurizio Chioccioli

Sponsor

Primary sponsor

Full Name
Assistance Publique Hopitaux De Paris
Organisation Type
Hospital/Clinic/Other health care facility
Country Of Registered Address
France

Third parties

  • {"country":"","full_name":"AMGEN","duties_or_roles":"Source of monetary support","organisation_type":""}

Investigational products

Investigational Product Name
Repatha 140 mg solution for injection in pre-filled pen
Active Substance
Evolocumab
Modality
Monoclonal antibody
Routes Of Administration
Subcutaneous
Route
Subcutaneous
Authorisation Status
Authorised (marketing authorisation EU/1/15/1016/002)
Maximum Dose
Max daily dose 140 mg; max total dose 11060 mg

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