Clinical trial • Phase IV • Endocrinology | Cardiology

Estradiol for Turner syndrome

Phase IV trial of Estradiol for Turner syndrome.

Overview

Trial Therapeutic Area
Endocrinology | Cardiology
Trial Disease
Turner syndrome
Trial Stage
Phase IV
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
01-10-2024
First CTIS Authorization Date
23-10-2024

Trial design

Estrofem (oral estradiol) versus Divigel 1 mg gel (transdermal estradiol); specific doses/schedules not specified in the record-controlled Phase IV trial across 1 site in Denmark.

Comparator
Estrofem (oral estradiol) versus Divigel 1 mg gel (transdermal estradiol); specific doses/schedules not specified in the record
Target Sample Size
50

Eligibility

Recruits 50 No vulnerable population selected; participants are adults aged 18-50. Consent obtained from adult participants; assent/parental consent not applicable..

Pregnancy Exclusion
Pregnancy
Vulnerable Population
No vulnerable population selected; participants are adults aged 18-50. Consent obtained from adult participants; assent/parental consent not applicable.

Inclusion criteria

  • {"criterion_text":"- Diagnosis of Turner syndrome regardless of karyotype (Turner syndrome)\n- Age 18-50 years (Turner syndrome and healthy controls)\n- Already receiving estrogen treatment (Turner syndrome)\n- Female (healthy controls)\n- Previously healthy (healthy controls)\n- Not receiving any medication (healthy controls)\n- Not using any kind of contraceptive pills (healthy controls)\n- No mental or psychiatric disorders (healthy controls)"}

Exclusion criteria

  • {"criterion_text":"- Active systemic chronic diseases\n- Known or suspected breast cancer\n- Known or suspected estradiol-dependent tumors (endometrial cancer or similar)\n- Untreated endometrial hyperplasia\n- Current or previous venous thromboembolism\n- Acute or previous liver disease where liver enzymes are still elevated by a factor 3 or more\n- Known hypersensitivity to the medications used\n- Pregnancy\n- Menopause (healthy controls only)"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Equipotency: Levels of luthenizing hormone and follicle stimulating hormone are measured at different doses","definition_or_measurement_approach":"Levels of luteinizing hormone (LH) and follicle stimulating hormone (FSH) measured at different estradiol doses to determine equipotency (using estradiol-dependent surrogate markers)."}

Recruitment

Planned Sample Size
50
Recruitment Window Months
59
Consent Approach
Informed consent obtained from adult participants. Subject information and informed consent forms are listed (documents L1_SIS, L1_ICF, L1_ICF_biobank). No assent or parental consent required. Documents include Danish translations.

Geography

Total Number Of Sites
1
Total Number Of Participants
50

Denmark

Earliest CTIS Part Ii Submission Date
17-10-2024
Latest Decision Or Authorization Date
23-10-2024
Processing Time Days
6
Number Of Sites
1
Number Of Participants
50

Sites

Site Name
Department of Endocrinology and Internal Medicine, Aarhus University Hospital
Department Name
Endocrinology and Internal Medicine
Contact Person Name
Camilla Mains Balle
Contact Person Email
camibl@clin.au.dk

Sponsor

Primary sponsor

Full Name
Region Midtjylland
Organisation Type
Hospital/Clinic/Other health care facility
Country Of Registered Address
Denmark

Third parties

  • {"country":"Denmark","full_name":"Aarhus Universitet","duties_or_roles":"Sponsor duty code 1","organisation_type":"Educational Institution"}

Investigational products

Investigational Product Name
Estrofem, filmovertrukne tabletter
Active Substance
Estradiol
Modality
Small molecule
Routes Of Administration
Oral
Route
Oral
Authorisation Status
Authorised (marketing authorisation number 06697)
Maximum Dose
10 mg per day (max total 140 mg)
Investigational Product Name
Divigel 1 mg gel
Active Substance
Estradiol
Modality
Small molecule
Routes Of Administration
Transdermal
Route
Transdermal
Authorisation Status
Authorised (marketing authorisation number 13296)
Maximum Dose
10 mg per day (max total 140 mg)

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