Clinical trial • Phase III • Cardiology

Epinephrine bitartrate for Out-of-hospital cardiac arrest | Cardiac arrest

Phase III trial of Epinephrine bitartrate for Out-of-hospital cardiac arrest | Cardiac arrest.

Overview

Trial Therapeutic Area
Cardiology
Trial Disease
Out-of-hospital cardiac arrest | Cardiac arrest
Trial Stage
Phase III
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
09-07-2025
First CTIS Authorization Date
08-10-2025

Trial design

Randomised, standard dose arm: adrenaline renaudin 1 mg/ml, solution injectable en ampoule — 1 mg epinephrine iv bolus every 3–5 minutes during cardiopulmonary resuscitation (cpr). test arm (low dose): adrenaline renaudin 0,50 mg/ml, solution injectable — 0.5 mg epinephrine iv bolus every 3–5 minutes during cpr.-controlled Phase III trial across 26 sites in France.

Randomised
Yes
Comparator
Standard dose arm: ADRENALINE RENAUDIN 1 mg/ml, solution injectable en ampoule — 1 mg epinephrine IV bolus every 3–5 minutes during cardiopulmonary resuscitation (CPR). Test arm (low dose): ADRENALINE RENAUDIN 0,50 mg/ml, solution injectable — 0.5 mg epinephrine IV bolus every 3–5 minutes during CPR.
Target Sample Size
4336
Trial Duration For Participant
28

Stratification factors

  • SMUR vehicle

Eligibility

Recruits 4336 Vulnerable populations are explicitly considered and partly excluded: the protocol excludes persons referred to in Articles 10, 31, 32, 33 and 34 of Regulation (EU) No 536/2014 (including pregnant, birthing or breastfeeding women; adults under legal protection measures such as guardianship or conservatorship; and individuals deprived of liberty). Subject information and informed consent documents (multiple L1 documents including adapted information for sequelae, deceased subjects and follow-up) are provided for participants; only adults (≥18 years) are eligible..

Pregnancy Exclusion
Individuals referred to in Articles 10, 31, 32, 33 and 34 of Regulation (EU) No 536/2014, including. ­ Pregnant women, birthing or breastfeeding mothers ­ Adults under legal protection measure (such as guardianship, conservatorship) ­ Individuals deprived of liberty due to judicial or administrative decision
Vulnerable Population
Vulnerable populations are explicitly considered and partly excluded: the protocol excludes persons referred to in Articles 10, 31, 32, 33 and 34 of Regulation (EU) No 536/2014 (including pregnant, birthing or breastfeeding women; adults under legal protection measures such as guardianship or conservatorship; and individuals deprived of liberty). Subject information and informed consent documents (multiple L1 documents including adapted information for sequelae, deceased subjects and follow-up) are provided for participants; only adults (≥18 years) are eligible.

Inclusion criteria

  • {"criterion_text":"- Male or female, aged ≥18 years."}
  • {"criterion_text":"- Out-of-hospital cardiac arrest for which resuscitation is decided by the SMUR team."}
  • {"criterion_text":"- Medical Out-of-hospital cardiac arrest."}
  • {"criterion_text":"- Affiliated with or beneficiary of a social security plan"}

Exclusion criteria

  • {"criterion_text":"- Non-medical OHCA (traumatic, drownings, electrocution, asphyxia, overdose, unknown cause)."}
  • {"criterion_text":"- out-of-hospital cardiac arrest without advanced life support (Do Not Attempt Resuscitation order, body finding, the decision not to attempt ALS is at the physician’s discretion)."}
  • {"criterion_text":"- Individuals referred to in Articles 10, 31, 32, 33 and 34 of Regulation (EU) No 536/2014, including. ­\tPregnant women, birthing or breastfeeding mothers ­\tAdults under legal protection measure (such as guardianship, conservatorship) ­\tIndividuals deprived of liberty due to judicial or administrative decision"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- 28-day survival with a favorable neurological function defined as a Modified Rankin Scale (mRS) of score 2 or less at 28-days.","definition_or_measurement_approach":"Defined as a Modified Rankin Scale (mRS) score of 2 or less measured at 28 days."}

Secondary endpoints

  • {"endpoint_text":"- Return of Spontaneous Circulation, assessed during cardiopulmonary resuscitation (CPR) and defined as a clinical assessment that shows signs of life, including palpable pulse or generating a blood pressure.","definition_or_measurement_approach":"Assessed during CPR; defined as clinical signs of life including a palpable pulse or measurable blood pressure."}
  • {"endpoint_text":"- Survival at hospital admission.","definition_or_measurement_approach":"Alive status at time of hospital admission (binary)."}
  • {"endpoint_text":"- 28-day survival.","definition_or_measurement_approach":"Survival status at 28 days after the cardiac arrest (binary)."}
  • {"endpoint_text":"- Modified Rankin Scale (mRS) score used as a continuous variable (in contrast with the use of the mRS scale in the primary outcome).","definition_or_measurement_approach":"mRS score evaluated at 28 days and analysed as a continuous variable."}

Recruitment

Planned Sample Size
4336
Recruitment Window Months
48
Consent Approach
Participants are adults (≥18 years). Subject information and informed consent forms are provided (multiple L1 documents listed, including adapted information for sequelae, deceased subjects, opposition and follow-up). The protocol lists subject information and ICF documents for use; explicit procedures for emergency/deferred consent are not detailed in the provided CTIS data.

Methods

  • Enrollment occurs in the out-of-hospital setting by SMUR (mobile medical team) personnel: eligible patients are identified during out-of-hospital cardiac arrest events for which resuscitation is decided by the SMUR team and randomized on scene.

Geography

Total Number Of Sites
26
Total Number Of Participants
4336

France

Earliest CTIS Part Ii Submission Date
29-09-2025
Latest Decision Or Authorization Date
08-10-2025
Processing Time Days
9
Number Of Sites
26
Number Of Participants
4336

Sites

Site Name
Centre Hospitalier De Colmar
Department Name
Pôle Urgence Pasteur
Principal Investigator Name
Yannick GOTTWALLES
Principal Investigator Email
yannick.gottwalles@ch-colmar.fr
Contact Person Name
Yannick GOTTWALLES
Site Name
Centre Hospitalier Universitaire De Nimes
Department Name
Service des urgences, SMUR
Principal Investigator Name
Fabien COISY
Principal Investigator Email
fabien.cosy@chu-nimes.fr
Contact Person Name
Fabien COISY
Contact Person Email
fabien.cosy@chu-nimes.fr
Site Name
Centre Hospitalier Universitaire De Nice
Department Name
Département hospitalo-universitaire de médecine d’urgence DHUMU
Principal Investigator Name
Julie CONTENTI
Principal Investigator Email
contenti.j@chu-nice.fr
Contact Person Name
Julie CONTENTI
Contact Person Email
contenti.j@chu-nice.fr
Site Name
Centre Hospitalier De La Cote Basque
Department Name
Urgences / SAMU/ SMUR
Principal Investigator Name
Xavier PEREIRA
Principal Investigator Email
x.perreira@ch-cotebasque.fr
Contact Person Name
Xavier PEREIRA
Contact Person Email
x.perreira@ch-cotebasque.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
SAMU 92 – SMUR Raymond Poincaré, Garches
Principal Investigator Name
Armelle SÉVERIN
Principal Investigator Email
armelle.severin@aphp.fr
Contact Person Name
Armelle SÉVERIN
Contact Person Email
armelle.severin@aphp.fr
Site Name
Centre Hospitalier Regional Universitaire De Tours
Department Name
Département des urgences
Principal Investigator Name
Alexandre JEZIORNY
Principal Investigator Email
a.jeziorny@chu-tours.fr
Contact Person Name
Alexandre JEZIORNY
Contact Person Email
a.jeziorny@chu-tours.fr
Site Name
Hopital Necker Enfants Malades
Department Name
SAMU de Paris – SMUR de NECKER
Principal Investigator Name
Alice HUTIN
Principal Investigator Email
alice.hutin@aphp.fr
Contact Person Name
Alice HUTIN
Contact Person Email
alice.hutin@aphp.fr
Site Name
Centre Hospitalier Regional Et Universitaire De Brest
Department Name
Urgences
Principal Investigator Name
Adrien BASSET
Principal Investigator Email
adrien.basset@chu-brest.fr
Contact Person Name
Adrien BASSET
Contact Person Email
adrien.basset@chu-brest.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Urgences
Principal Investigator Name
Anthony CHAUVIN
Principal Investigator Email
anthony.chauvin@aphp.fr
Contact Person Name
Anthony CHAUVIN
Contact Person Email
anthony.chauvin@aphp.fr
Site Name
Hopital Beaujon
Department Name
SMUR
Principal Investigator Name
Bénédicte DOUAY
Principal Investigator Email
benedicte.douay@aphp.fr
Contact Person Name
Bénédicte DOUAY
Contact Person Email
benedicte.douay@aphp.fr
Site Name
Centre Hospitalier Universitaire De Montpellier
Department Name
SAMU – SMUR CHU Lapeyronie
Principal Investigator Name
Thomas SANCHEZ
Principal Investigator Email
thomas-sanchez@chu-montpellier.fr
Contact Person Name
Thomas SANCHEZ
Site Name
Centre Hospitalier Universitaire De Poitiers
Department Name
Service Urgences SAMU SMUR 86
Principal Investigator Name
Nicolas MARJANOVIC
Principal Investigator Email
nicolas.marjanovic@chu-poitiers.fr
Contact Person Name
Nicolas MARJANOVIC
Site Name
Centre Hospitalier Universitaire De Rennes
Department Name
Urgences-SAMU35-SAS-SMUR-CESU
Principal Investigator Name
Nicolas PESCHANSKI
Principal Investigator Email
n-peschanski@live.fr
Contact Person Name
Nicolas PESCHANSKI
Contact Person Email
n-peschanski@live.fr
Site Name
Centre Hospitalier Annecy Genevois
Department Name
SMUR
Principal Investigator Name
Hugo SCHMIT
Principal Investigator Email
hschmit@ch-annecygenevois.fr
Contact Person Name
Hugo SCHMIT
Contact Person Email
hschmit@ch-annecygenevois.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Urgences générales
Principal Investigator Name
Clémentine CASSARD
Principal Investigator Email
clementine.cassard@aphp.fr
Contact Person Name
Clémentine CASSARD
Contact Person Email
clementine.cassard@aphp.fr
Site Name
Centre Hospitalier Universitaire Rouen
Department Name
Département de médecine d'urgence
Principal Investigator Name
Marie OZANNE
Principal Investigator Email
m.ozanne@chu-rouen.fr
Contact Person Name
Marie OZANNE
Contact Person Email
m.ozanne@chu-rouen.fr
Site Name
Centre hospitalier Annecy Genevois Site Julien en GENEVOIS
Department Name
SMUR
Principal Investigator Name
Arnaud RELLY
Principal Investigator Email
arelly@ch-annecygenevois.fr
Contact Person Name
Arnaud RELLY
Contact Person Email
arelly@ch-annecygenevois.fr
Site Name
CHU Besancon
Department Name
Médecine d'urgence et de réanimation
Principal Investigator Name
Abdo KHOURY
Principal Investigator Email
akhoury@chu-besancon.fr
Contact Person Name
Abdo KHOURY
Contact Person Email
akhoury@chu-besancon.fr
Site Name
Centre Hospitalier Universitaire Reims
Department Name
SAU Adultes et SAMU
Principal Investigator Name
Stéphane GENNAI
Principal Investigator Email
s.gennai@chu-reims.fr
Contact Person Name
Stéphane GENNAI
Contact Person Email
s.gennai@chu-reims.fr
Site Name
Brigade de Sapeurs-Pompiers de Paris
Department Name
Division Santé
Principal Investigator Name
Simon-Pierre CORCOSTEGUI
Principal Investigator Email
simon-pierre.corcostegui@pompiersparis.fr
Contact Person Name
Simon-Pierre CORCOSTEGUI
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
CHU PURPAN / SAMU 31-
Principal Investigator Name
Bertand GUIHARD
Principal Investigator Email
samu.secretariat@chu-toulouse.fr
Contact Person Name
Bertand GUIHARD
Site Name
Hospices Civils De Lyon
Department Name
SAMU/ SAU
Principal Investigator Name
Youri YORDANOV
Principal Investigator Email
youri.yordanov@chu-lyon.fr
Contact Person Name
Youri YORDANOV
Contact Person Email
youri.yordanov@chu-lyon.fr
Site Name
Centre Hospitalier Universitaire De Nantes
Department Name
Département des urgences SAMU
Principal Investigator Name
François JAVAUDIN
Principal Investigator Email
francois.javaudin@chu-nantes.fr
Contact Person Name
François JAVAUDIN
Site Name
CH SUD Francilien
Department Name
SAMU-SMUR 91
Principal Investigator Name
Romain BARDELAY
Principal Investigator Email
secretariat@samu91.org
Contact Person Name
Romain BARDELAY
Contact Person Email
secretariat@samu91.org
Site Name
Centre Hospitalier Universitaire Grenoble Alpes
Department Name
SAMU 38
Principal Investigator Name
Nicolas SEGOND
Principal Investigator Email
nsegond@chu.grenoble.fr
Contact Person Name
Nicolas SEGOND
Contact Person Email
nsegond@chu.grenoble.fr
Site Name
CHRU De Nancy
Department Name
Samu - Smur - Service des Urgences
Principal Investigator Name
Tahar CHOUIHED
Principal Investigator Email
T.CHOUIHEDMAHJOUB@chru-nancy.fr
Contact Person Name
Tahar CHOUIHED

Sponsor

Primary sponsor

Full Name
CHRU De Nancy
Organisation Type
Hospital/Clinic/Other health care facility
Country Of Registered Address
France

Investigational products

Investigational Product Name
ADRENALINE RENAUDIN 0,50 mg/ml, solution injectable
Active Substance
Epinephrine bitartrate
Modality
Small molecule
Routes Of Administration
INTRAVENOUS BOLUS INJECTION/IV INFUSION
Route
Intravenous bolus
Authorisation Status
Authorised (marketing authorisation available in FR)
Starting Dose
0.5 mg (IV bolus)
Dose Levels
0.5 mg
Frequency
Every 3–5 minutes during cardiopulmonary resuscitation (CPR)
Investigational Product Name
ADRENALINE RENAUDIN 1 mg/ml, solution injectable en ampoule
Active Substance
Epinephrine bitartrate
Modality
Small molecule
Routes Of Administration
INTRAVENOUS BOLUS USE
Route
Intravenous bolus
Authorisation Status
Authorised (marketing authorisation available in FR)
Starting Dose
1 mg (IV bolus)
Dose Levels
1 mg
Frequency
Every 3–5 minutes during cardiopulmonary resuscitation (CPR)

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