Clinical trial • Phase II • Oncology
Epcoritamab for Diffuse large B-cell lymphoma
Phase II trial of Epcoritamab for Diffuse large B-cell lymphoma.
Overview
- Trial Therapeutic Area
- Oncology
- Trial Disease
- Diffuse large B-cell lymphoma
- Trial Stage
- Phase II
- Drug Modality
- Bispecific antibody | Small molecule
- Orphan Drug
- Yes
Key dates
- Initial CTIS Submission Date
- 06-12-2023
- First CTIS Authorization Date
- 18-01-2024
Trial design
Randomised, open-label, arm 1: epcoritamab monotherapy (subcutaneous formulation, product listing shows maximum daily dose amount 48 mg). arm 2: epcoritamab plus lenalidomide (oral lenalidomide listed with max daily dose amount 20 mg).-controlled Phase II trial in Austria, Belgium, Czechia and others.
- Randomised
- Yes
- Open Label
- Yes
- Comparator
- Arm 1: Epcoritamab monotherapy (subcutaneous formulation, product listing shows maximum daily dose amount 48 mg). Arm 2: Epcoritamab plus Lenalidomide (oral lenalidomide listed with max daily dose amount 20 mg).
- Target Sample Size
- 38
Eligibility
Recruits 38 Vulnerable population not selected (isVulnerablePopulationSelected=false). Informed consent is obtained from adult participants via provided subject information and informed consent forms (multiple ICF versions present); eConsent/remote consent materials are available. Additional ICFs for pregnant partners and baby data collection are present in the document list..
- Vulnerable Population
- Vulnerable population not selected (isVulnerablePopulationSelected=false). Informed consent is obtained from adult participants via provided subject information and informed consent forms (multiple ICF versions present); eConsent/remote consent materials are available. Additional ICFs for pregnant partners and baby data collection are present in the document list.
Inclusion criteria
- {"criterion_text":"- Must have newly diagnosed CD20+ large cell lymphoma."}
- {"criterion_text":"- Is ineligible for anthracycline-based therapy/cytotoxic chemotherapy due to: oBeing age ≥80 years; AND/OR oBeing age ≥75 years and having important comorbid condition(s), which are likely to have a negative impact on tolerability of anthracycline-based therapy/cytotoxic chemotherapy, Have Immune Effector Cell-Associated Encephalopathy (ICE) score of at least 8 out of 10."}
- {"criterion_text":"- Have Ann Arbor Stage II-IV disease."}
- {"criterion_text":"- Have ECOG PS of 0, 1, or 2; (ECOG PS of 3 may be considered if impairment is attributed to current lymphoma/DLBCL and if pre-phase treatment during the screening phase results in an improvement of ECOG PS to ≤2 prior to enrollment.)"}
- {"criterion_text":"- Have measurable disease as per Lugano criteria."}
- {"criterion_text":"- Have acceptable organ function based on baseline bloodwork."}
- {"criterion_text":"- Must have fresh (preferred) or archival biopsy material at screening."}
Exclusion criteria
- {"criterion_text":"- Has known active, clinically significant bacterial, viral, fungal, mycobacterial, parasitic, or other infection at trial enrollment, including COVID-19 infection."}
- {"criterion_text":"- Has suspected active or inadequately treated latent tuberculosis."}
- {"criterion_text":"- Has a known history of seropositivity for HIV. Note: HIV testing is required at screening only if required per local health authorities or institutional standards."}
- {"criterion_text":"- Has severe cardiovascular disease (other than those eligibility criteria that preclude the subject from receiving anthracycline-based therapy/cytotoxic chemotherapy)."}
- {"criterion_text":"- Has been exposed to/received any of the following prior therapies, treatments, or procedures within the specified timeframes: oMajor surgery within 4 weeks prior to the first dose of epcoritamab; oNon-investigational antineoplastic agents or any investigational drug within 4 weeks or 5 half-lives, whichever is shorter, prior to the first dose of epcoritamab; oAutologous hematopoietic stem cell transplantation (HSCT), CAR-T, allogeneic stem cell transplantation, or solid organ transplantation; oLive, attenuated vaccines within 30 days prior to initiation of epcoritamab; oInvestigational vaccines within 28 days before the planned first dose of epcoritamab (ie, experimental and/or non-authorized SARS-CoV-2 vaccinations and therapies are not allowed); oInvasive investigational medical device use within 28 days before the planned first dose of epcoritamab."}
- {"criterion_text":"- Has primary central nervous system (CNS) tumor or known CNS involvement or intracranial involvement as confirmed by mandatory brain magnetic resonance imaging/computed tomography (MRI/CT) scan at screening and, if clinically indicated, by lumbar puncture."}
- {"criterion_text":"- Has a seizure disorder requiring anti-epileptic therapy or experienced a seizure within 6 months of signing an informed consent form."}
- {"criterion_text":"- Has known past or current malignancy other than inclusion diagnosis, with exceptions as stated in protocol."}
- {"criterion_text":"- Has known or suspected allergies, hypersensitivity, or intolerance to either of the trial treatments or has known or suspected contraindication to the use of all locally available anti-cytokine therapies per local guidelines for management of cytokine release syndrome (CRS)."}
- {"criterion_text":"- Has active hepatitis B virus (HBV) (DNA polymerase chain reaction [PCR]-positive) or hepatitis C virus (HCV) (RNA PCR-positive) infection, current alcohol abuse, or cirrhosis."}
- {"criterion_text":"- Has active cytomegalovirus (CMV) infection (DNA PCR-positive) requiring treatment."}
Endpoints
Primary endpoints
- {"endpoint_text":"- Complete response (CR) rate determined by Lugano criteria","definition_or_measurement_approach":"Determined by Lugano criteria"}
Secondary endpoints
- {"endpoint_text":"- Duration of response (DOR) determined by Lugano criteria","definition_or_measurement_approach":"Determined by Lugano criteria"}
- {"endpoint_text":"- Duration of complete response (DOCR) determined by Lugano criteria","definition_or_measurement_approach":"Determined by Lugano criteria"}
- {"endpoint_text":"- Time to response (TTR) determined by Lugano criteria","definition_or_measurement_approach":"Determined by Lugano criteria"}
- {"endpoint_text":"- Overall response rate (ORR) determined by Lugano criteria","definition_or_measurement_approach":"Determined by Lugano criteria"}
- {"endpoint_text":"- Progression-free survival (PFS) determined by Lugano criteria","definition_or_measurement_approach":"Determined by Lugano criteria"}
- {"endpoint_text":"- Time to next (anti-lymphoma) therapy (TTNT).","definition_or_measurement_approach":""}
- {"endpoint_text":"- Rate and duration of minimal residual disease (MRD) negative status","definition_or_measurement_approach":""}
- {"endpoint_text":"- Overall survival (OS)","definition_or_measurement_approach":""}
- {"endpoint_text":"- Incidence of dose-limiting toxicities (DLTs)","definition_or_measurement_approach":""}
- {"endpoint_text":"- Incidence and severity of adverse events (AEs)","definition_or_measurement_approach":""}
- {"endpoint_text":"- Incidence and severity of changes in laboratory values","definition_or_measurement_approach":""}
- {"endpoint_text":"- Incidence of antidrug antibodies (ADAs) to epcoritamab","definition_or_measurement_approach":""}
- {"endpoint_text":"- PK parameters (clearance, volume of distribution, area under-the- concentration-time curve [AUC0-last and AUC0-∞], maximum concentration [Cmax], time of Cmax [Tmax], predose values, and halflife [t½])","definition_or_measurement_approach":"Standard PK parameter assessment (AUC0-last, AUC0-∞, Cmax, Tmax, clearance, volume of distribution, predose values, t½)"}
- {"endpoint_text":"- Changes in lymphoma symptoms as measured by the Functional Assessment of Cancer Therapy – Lymphoma (FACT-Lym)","definition_or_measurement_approach":"Patient-reported outcomes measured using FACT-Lym instrument"}
Recruitment
- Digital Remote Recruitment
- Yes
- Planned Sample Size
- 38
- Recruitment Window Months
- 57
- Consent Approach
- Informed consent obtained from adult participants via provided subject information sheets and formal informed consent forms (multiple ICF versions listed). eConsent/remote consent platform is available (eConsent submission letter, video storyboard, system email screenshots, remote consent screenshots). Additional documents include Pregnant Partner and Baby data collection ICFs. Consent materials available in multiple languages as indicated by document filenames (EN, FR, PL, DE, ES, IT, CZ, NL).
Methods
- Physician referral letters (documents titled 'Referral letter' and 'Physician Referral Letter' present) — targets referring physicians and clinical sites.
- Site website / patient-facing landing pages (documents titled 'Site ... Website information' and 'Patient facing landing page') — targets potential patients searching site-specific information.
- Social media scripts (document 'Social Media Script') — digital outreach to potential patients.
- eConsent / remote consent procedures (documents: eConsent Submission Letter, eConsent Video Storyboard, eConsent System Email Screenshots, Remote Consent Screenshots) — remote/digital consenting for participants.
- Patient-facing recruitment materials (patient ID cards, information leaflets, Lenalidomide information sheets) — direct-to-patient informational materials at sites.
Geography
- Total Number Of Sites
- 41
- Total Number Of Participants
- 102
Austria
- Earliest CTIS Part Ii Submission Date
- 21-12-2023
- Latest Decision Or Authorization Date
- 27-03-2026
- Processing Time Days
- 827
- Number Of Sites
- 2
- Number Of Participants
- 7
Sites
- Site Name
- Klinikum Wels-Grieskirchen GmbH
- Department Name
- Abteilung für Innere Medizin IV
- Contact Person Name
- Sonja Heibl
- Contact Person Email
- sonja.heibl@klinikum-wegr.at
- Site Name
- SCRI CCCIT Ges.m.b.H.
- Department Name
- Universitätsklinik für Innere Medizin III der PMU
- Contact Person Name
- Thomas Melchardt
- Contact Person Email
- t.melchardt@salk.at
Belgium
- Earliest CTIS Part Ii Submission Date
- 21-12-2023
- Latest Decision Or Authorization Date
- 25-03-2026
- Processing Time Days
- 825
- Number Of Sites
- 5
- Number Of Participants
- 17
Sites
- Site Name
- Ziekenhuis Aan De Stroom
- Department Name
- Hematology
- Contact Person Name
- Ka Lung Wu
- Contact Person Email
- kalung.wu@zna.be
- Site Name
- UZ Brussel
- Department Name
- Hematology
- Contact Person Name
- Veerle Beckers
- Contact Person Email
- veerle.beckers@uzbrussel.be
- Site Name
- UZ Leuven
- Department Name
- General Medical Oncology
- Contact Person Name
- Sherida Woei-A-Jin
- Contact Person Email
- sherida.woei-a-jin@uzleuven.be
- Site Name
- Algemeen Ziekenhuis Delta
- Department Name
- Hematology
- Contact Person Name
- Caressa Meert
- Contact Person Email
- caressa.meert@azdelta.be
- Site Name
- Institut Jules Bordet
- Department Name
- Clinical Hematology
- Contact Person Name
- Fulvio Massaro
- Contact Person Email
- fulvio.massaro@hubruxelles.be
Czechia
- Earliest CTIS Part Ii Submission Date
- 21-12-2023
- Latest Decision Or Authorization Date
- 27-03-2026
- Processing Time Days
- 827
- Number Of Sites
- 1
- Number Of Participants
- 5
Sites
- Site Name
- Fakultni Nemocnice Hradec Kralove
- Department Name
- IV. interní hematologická klinika
- Contact Person Name
- David Belada
- Contact Person Email
- david.belada@fnhk.cz
France
- Earliest CTIS Part Ii Submission Date
- 21-12-2023
- Latest Decision Or Authorization Date
- 30-03-2026
- Processing Time Days
- 830
- Number Of Sites
- 11
- Number Of Participants
- 24
Sites
- Site Name
- Centre Hospitalier Universitaire Amiens Picardie
- Department Name
- Hématologie
- Contact Person Name
- Pierre MOREL
- Contact Person Email
- morel.pierre@chu-amiens.fr
- Site Name
- Centre Hospitalier Regional Universitaire De Tours
- Department Name
- Hématologie
- Contact Person Name
- Emmanuel Gyan
- Contact Person Email
- emmanuel.gyan@univ-tours.fr
- Site Name
- Assistance Publique Hopitaux De Paris
- Department Name
- Onco-hématologie
- Contact Person Name
- Catherine Thieblemont
- Contact Person Email
- catherine.thieblemont@aphp.fr
- Site Name
- Assistance Publique Hopitaux De Paris
- Department Name
- Hématologie
- Contact Person Name
- Nicolas Stocker
- Contact Person Email
- nicolas.stocker@aphp.fr
- Site Name
- Assistance Publique Hopitaux De Marseille
- Department Name
- Hématologie
- Contact Person Name
- Régis Costello
- Contact Person Email
- regis.costello@ap-hm.fr
- Site Name
- Centre Hospitalier Universitaire D'Angers
- Department Name
- Hématologie
- Contact Person Name
- Jérôme Paillassa
- Contact Person Email
- jerome.paillassa@chu-angers.fr
- Site Name
- Centre Hospitalier Universitaire De Nantes
- Department Name
- Hématologie
- Contact Person Name
- Thomas Gastinne
- Contact Person Email
- thomas.gastinne@chu-nantes.fr
- Site Name
- Centre Hospitalier Universitaire De Lille
- Department Name
- Hématologie
- Contact Person Name
- Franck Morschhauser
- Contact Person Email
- franck.morschhauser@chru-lille.fr
- Site Name
- Assistance Publique Hopitaux De Paris
- Department Name
- Hématologie
- Contact Person Name
- David Sibon
- Contact Person Email
- david.sibon@aphp.fr
- Site Name
- Centre Hospitalier Universitaire De Bordeaux
- Department Name
- Hématologie
- Contact Person Name
- François-Xavier Gros
- Contact Person Email
- fracois-xavier.gros@chu-bordeaux.fr
- Site Name
- Centre Hospitalier Universitaire De Pessac (Bordeaux region)
- Department Name
- Hématologie
Germany
- Earliest CTIS Part Ii Submission Date
- 21-12-2023
- Latest Decision Or Authorization Date
- 30-03-2026
- Processing Time Days
- 830
- Number Of Sites
- 6
- Number Of Participants
- 7
Sites
- Site Name
- Universitaetsklinikum Augsburg
- Department Name
- II. Medizinische Klinik
- Contact Person Name
- Mathias Lutz
- Contact Person Email
- mathias.lutz@uk-augsburg.de
- Site Name
- Universitaetsklinikum Wuerzburg AöR
- Department Name
- Med. Klinik und Poliklinik II, Zentrum für Innere Medizin
- Contact Person Name
- Johannes Düll
- Contact Person Email
- Duell_J@ukw.de
- Site Name
- Vivantes Netzwerk fuer Gesundheit GmbH
- Department Name
- Fachbereich Hämatologie, Onkologie und Palliativmedizin
- Contact Person Name
- Maike de Wit
- Contact Person Email
- maike.dewit@vivantes.de
- Site Name
- Klinikum Chemnitz gGmbH
- Department Name
- Zentrum für klinische Studien
- Contact Person Name
- Mathias Hänel
- Contact Person Email
- m.haenel@skc.de
- Site Name
- Medical Center - University Of Freiburg
- Department Name
- Innere Medizin I - Hämatologie und Onkologie
- Contact Person Name
- Reinhard Marks
- Contact Person Email
- reinhard.marks@uniklinik-freiburg.de
- Site Name
- Universitaetsklinikum Aachen AöR
- Department Name
- Medizinische Klinik IV Onkologie, Haematologie
- Contact Person Name
- Mareike Tometten
- Contact Person Email
- mtometten@ukaachen.de
Italy
- Earliest CTIS Part Ii Submission Date
- 21-12-2023
- Latest Decision Or Authorization Date
- 30-03-2026
- Processing Time Days
- 830
- Number Of Sites
- 5
- Number Of Participants
- 16
Sites
- Site Name
- Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia
- Department Name
- UO Ematologia
- Contact Person Name
- Alessandra Tucci
- Contact Person Email
- alessandra.tucci@asst-spedalicivili.it
- Site Name
- Istituto Di Candiolo Fondazione Del Piemonte Per Loncologia IRCCS
- Department Name
- Oncologia Medica
- Contact Person Name
- Umberto Vitolo
- Contact Person Email
- umberto.vitolo@ircc.it
- Site Name
- European Institute Of Oncology S.r.l.
- Department Name
- Divisione di Oncoematologia e Trapianto di cellule staminali
- Contact Person Name
- Enrico Derenzini
- Contact Person Email
- enrico.derenzini@ieo.it
- Site Name
- Azienda Sanitaria Universitaria Giuliano Isontina
- Department Name
- SC Ematologia
- Contact Person Name
- Francesco Zaja
- Contact Person Email
- francesco.zaja@asugi.sanita.fvg.it
- Site Name
- Azienda Unita Sanitaria Locale Di Piacenza
- Department Name
- Ematologia
- Contact Person Name
- Annalisa Arcari
- Contact Person Email
- a.arcari@ausl.pc.it
Spain
- Earliest CTIS Part Ii Submission Date
- 21-12-2023
- Latest Decision Or Authorization Date
- 27-03-2026
- Processing Time Days
- 827
- Number Of Sites
- 9
- Number Of Participants
- 21
Sites
- Site Name
- Hospital San Pedro De Alcantara
- Department Name
- Haematology
- Contact Person Name
- Juan Miguel Bergua Burgues
- Contact Person Email
- jmberguaburg@gmail.com
- Site Name
- Institut Catala D'oncologia
- Department Name
- Oncology
- Contact Person Name
- Juan Manuel Sancho Cia
- Contact Person Email
- jsancho@iconcologia.net
- Site Name
- Hospital Universitario Fundacion Jimenez Diaz
- Department Name
- Haematology
- Contact Person Name
- Sergio Ramos Cillan
- Contact Person Email
- sergio.ramosc@quironsalud.es
- Site Name
- Hospital General Universitario Gregorio Maranon
- Department Name
- Haematology
- Contact Person Name
- Mariana Bastos Oreiro
- Contact Person Email
- bastosmariana@yahoo.com
- Site Name
- Hospital Universitario Ramon Y Cajal
- Department Name
- Haematology
- Contact Person Name
- Javier Lopez Jimenez
- Contact Person Email
- jljimenez@salud.madrid.org
- Site Name
- Hospital Clinic De Barcelona
- Department Name
- Haematology
- Contact Person Name
- Eva Giné Soca
- Contact Person Email
- EGINE@clinic.cat
- Site Name
- Hospital Universitario Virgen De Valme
- Department Name
- Haematology
- Contact Person Name
- Eduardo Rios Herranz
- Contact Person Email
- eduardo.rios.sspa@juntadeandalucia.es
- Site Name
- Institut Catala D'oncologia (L'hospitalet De Llobregat)
- Department Name
- Haematology
- Contact Person Name
- Anna Sureda Balari
- Contact Person Email
- asureda@iconcologia.net
- Site Name
- Hospital Universitario Virgen De La Macarena
- Department Name
- Hematology
- Contact Person Name
- Sergio Ortegon Alcaide
- Contact Person Email
- sortegonalcaide@gmail.com
Poland
- Earliest CTIS Part Ii Submission Date
- 21-12-2023
- Latest Decision Or Authorization Date
- 27-03-2026
- Processing Time Days
- 827
- Number Of Sites
- 2
- Number Of Participants
- 5
Sites
- Site Name
- Pratia S.A.
- Department Name
- Pratia MCM Krakow
- Contact Person Name
- Wojciech Jurczak
- Contact Person Email
- wojciech.jurczak@pratia.com
- Site Name
- Aidport Sp. z o.o.
- Contact Person Name
- Michał Kwiatek
- Contact Person Email
- michal.kwiatek@aidport.pl
Sponsor
Primary sponsor
- Full Name
- Genmab A/S
- Organisation Type
- Pharmaceutical company
- Country Of Registered Address
- Denmark
Contract research organisations
- Name
- Fortrea Development Limited
- Name
- Tigermed-Bdm Inc.
- Responsibilities
- Programming/Biostatistics
- Name
- Icon Laboratory Services Inc.
- Responsibilities
- Pharmacokinetics and antidrug antibody analysis. Central Repository and Review of local lab reports
- Name
- Clinipace Inc.
- Name
- Q Squared Solutions Limited
- Name
- Endpoint Clinical Inc.
- Name
- CellCarta
- Responsibilities
- Immunohistochemistry
- Name
- Adaptive Biotechnologies Corp.
- Responsibilities
- MRD analysis.
- Name
- Eresearchtechnology Inc.
- Responsibilities
- ePROs and ECG analysis
- Name
- Perceptive Eclinical Limited
- Responsibilities
- Medical image analysis.
- Name
- IQVIA Limited
- Responsibilities
- Project management, expedited and aggregate safety reporting to investigators, and ECs. DNA sequencing.
Third parties
- {"country":"United Kingdom","full_name":"Fortrea Development Limited","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Tigermed-Bdm Inc.","duties_or_roles":"Programming/Biostatistics","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Icon Laboratory Services Inc.","duties_or_roles":"Pharmacokinetics and antidrug antibody analysis. Central Repository and Review of local lab reports","organisation_type":"Laboratory/Research/Testing facility"}
- {"country":"United States","full_name":"Clinipace Inc.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"Q Squared Solutions Limited","duties_or_roles":"","organisation_type":"Non-Pharmaceutical company"}
- {"country":"United States","full_name":"Endpoint Clinical Inc.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
- {"country":"Belgium","full_name":"CellCarta","duties_or_roles":"Immunohistochemistry","organisation_type":"Laboratory/Research/Testing facility"}
- {"country":"United States","full_name":"Adaptive Biotechnologies Corp.","duties_or_roles":"MRD analysis.","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Eresearchtechnology Inc.","duties_or_roles":"ePROs and ECG analysis","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Genmab US Inc.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"Perceptive Eclinical Limited","duties_or_roles":"Medical image analysis.","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"Project management, expedited and aggregate safety reporting to investigators, and ECs. DNA sequencing.","organisation_type":"Pharmaceutical company"}
Investigational products
- Investigational Product Name
- Epcoritamab
- Active Substance
- Epcoritamab
- Modality
- Bispecific antibody
- Routes Of Administration
- Subcutaneous
- Route
- Subcutaneous
- Orphan Designation
- Yes
- Maximum Dose
- 48 mg
- Investigational Product Name
- Lenalidomide
- Active Substance
- Lenalidomide
- Modality
- Small molecule
- Routes Of Administration
- Oral
- Route
- Oral
- Maximum Dose
- 20 mg
- Combination Treatment
- Yes
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