Clinical trial • Phase II • Immunology|Dermatology

ENPATORAN for Subacute cutaneous lupus erythematosus | Discoid lupus erythematosus | Systemic lupus erythematosus

Phase II trial of ENPATORAN for Subacute cutaneous lupus erythematosus | Discoid lupus erythematosus | Systemic lupus erythematosus.

Overview

Trial Therapeutic Area
Immunology|Dermatology
Trial Disease
Subacute cutaneous lupus erythematosus | Discoid lupus erythematosus | Systemic lupus erythematosus
Trial Stage
Phase II
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
10-05-2024
First CTIS Authorization Date
17-07-2024

Trial design

Randomised, enpatoran (active) and enpatoran placebo (placebo comparator); dose and schedule not specified in provided documents-controlled Phase II trial across 13 sites in Poland, Bulgaria, Romania and others.

Randomised
Yes
Comparator
Enpatoran (active) and Enpatoran Placebo (placebo comparator); dose and schedule not specified in provided documents
Target Sample Size
202

Eligibility

Recruits 202 No vulnerable populations selected (isVulnerablePopulationSelected: false); participants are adults (≥18). Informed consent is required and subject information / ICF documents are provided..

Vulnerable Population
No vulnerable populations selected (isVulnerablePopulationSelected: false); participants are adults (≥18). Informed consent is required and subject information / ICF documents are provided.

Inclusion criteria

  • {"criterion_text":"- Are ≥ 18 and ≤ 76 years of age at the time of signing the informed consent"}
  • {"criterion_text":"- Are active SCLE, DLE and/or SLE that have completed the 24 week Treatment of the Willow Study"}
  • {"criterion_text":"- Have a Body Mass Index (BMI) within the greater than or equal to (>=) 40 kilograms per meter square (inclusive) at Screening"}
  • {"criterion_text":"- Participants who had successfully completed Week 48 of the Part 1 will have the opportunity to participate in the LTE Part 2. In exceptional cases and after Sponsor review, participants who have completed the Week 48 visit of the Part 1 within the previous 4-weeks may be considered for Part 2 participation based on eligibility review. Previous 4-weeks will be calculated from the Week 48 visit of Part 1"}
  • {"criterion_text":"- Other protocol defined inclusion criteria could apply"}

Exclusion criteria

  • {"criterion_text":"- Participants who experienced serious event(s) related to the study intervention during the WILLOW study - Other severe acute or chronic medical or psychiatric condition or laboratory abnormality that may increase the risk associated with Long Term Extension (LTE) study participation"}
  • {"criterion_text":"- Ongoing or active clinically significant viral (including Severe acute arespiratory syndrome coronavirus 2 [(SARS‑CoV‑2)], bacterial or fungal infection, or any major episode of infection requiring hospitalization"}
  • {"criterion_text":"- Received LTE prohibited medication during the WILLOW study or after the WILLOW study Week 24"}
  • {"criterion_text":"- Participation in any other investigational drug study after the WILLOW study Week 24"}
  • {"criterion_text":"- Other protocol defined exclusion criteria could apply"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Part 1: Safety Profile as Assessed by Incidence of Treatment-Emergent Adverse Events (TEAEs), Serious Adverse Events (SAEs), Adverse Event of Special Interest (AESIs)","definition_or_measurement_approach":"Measured by incidence counts of TEAEs, SAEs and AESIs in Part 1"}
  • {"endpoint_text":"- Part 2: Safety Profile as Assessed by Incidence of Treatment-Emergent Adverse Events (TEAEs), Serious Adverse Events (SAEs), Adverse Event of Special Interest (AESIs)","definition_or_measurement_approach":"Measured by incidence counts of TEAEs, SAEs and AESIs in Part 2"}

Secondary endpoints

  • {"endpoint_text":"- Part 1 and Part 2: Number of Participants with Abnormalities in Laboratory Parameters and QT Interval Corrected","definition_or_measurement_approach":"Number/proportion of participants with laboratory parameter abnormalities and with abnormal corrected QT interval (QTc) as assessed by scheduled laboratory and ECG assessments"}

Recruitment

Planned Sample Size
202
Recruitment Window Months
67
Consent Approach
Informed consent required from participants (participants are adults ≥18). Subject information and informed consent forms (ICFs) available in multiple language versions (examples in documents list: EN, BG, EL, PL, ES, RO) and both Part 1 and Part 2 ICF versions are provided; consent provided by participant (no paediatric assent procedures required).

Geography

Total Number Of Sites
13
Total Number Of Participants
65

Poland

Earliest CTIS Part Ii Submission Date
27-05-2024
Latest Decision Or Authorization Date
08-05-2026
Processing Time Days
711
Number Of Sites
1
Number Of Participants
15

Sites

Site Name
Centrum Medyczne Plejady Magdalena Celinska Loewenhoff Michal Zolnowski sp.k.
Department Name
Not applicable
Principal Investigator Name
Magdalena Celinska-Lowenhoff
Principal Investigator Email
magdalena.lowenhoff@gmail.com
Contact Person Name
Magdalena Celinska-Lowenhoff
Contact Person Email
magdalena.lowenhoff@gmail.com

Bulgaria

Earliest CTIS Part Ii Submission Date
27-05-2024
Latest Decision Or Authorization Date
11-05-2026
Processing Time Days
714
Number Of Sites
3
Number Of Participants
26

Sites

Site Name
Dkc Fokus-5 Lzip OOD
Department Name
Not applicable
Principal Investigator Name
Grisha Mateev
Principal Investigator Email
grisha_mateev@yahoo.com
Contact Person Name
Grisha Mateev
Contact Person Email
grisha_mateev@yahoo.com
Site Name
University Multiprofile Hospital For Active Treatment St. Ivan Rilski EAD
Department Name
Clinic of rheumatology
Principal Investigator Name
Rasho Rashkov
Principal Investigator Email
proff_rashkov@yahoo.com
Contact Person Name
Rasho Rashkov
Contact Person Email
proff_rashkov@yahoo.com
Site Name
Diagnostics And Consultancy Center Sveti Georgi EOOD
Department Name
Not applicable
Principal Investigator Name
Irida Vasileva
Principal Investigator Email
iridavasileva@gmail.com
Contact Person Name
Irida Vasileva
Contact Person Email
iridavasileva@gmail.com

Romania

Earliest CTIS Part Ii Submission Date
27-05-2024
Latest Decision Or Authorization Date
11-05-2026
Processing Time Days
714
Number Of Sites
5
Number Of Participants
4

Sites

Site Name
Saint Maria Hospital
Department Name
Rheumatology
Principal Investigator Name
Andra-Rodica Balanescu
Principal Investigator Email
balanescu.andra@gmail.com
Contact Person Name
Andra-Rodica Balanescu
Contact Person Email
balanescu.andra@gmail.com
Site Name
Arensia Clinics S.R.L.
Department Name
Rheumatology
Principal Investigator Name
Mihai Abobului
Principal Investigator Email
mihai.abobului.ext@arensia-em.com
Contact Person Name
Mihai Abobului
Site Name
Delta Health Care S.R.L.
Department Name
Rheumatology
Principal Investigator Name
Bogdan Horia Chicos
Principal Investigator Email
b_chicos@yahoo.com
Contact Person Name
Bogdan Horia Chicos
Contact Person Email
b_chicos@yahoo.com
Site Name
Spitalul Clinic Colentina Bucuresti
Department Name
Rheumatology
Principal Investigator Name
Razvan Adrian Ionescu
Principal Investigator Email
mihai.abobului.ext@arensia-em.com
Contact Person Name
Razvan Adrian Ionescu
Site Name
Saint Maria Hospital
Department Name
Rheumatology
Principal Investigator Name
Florian Berghea
Principal Investigator Email
berghea1@gmail.com
Contact Person Name
Florian Berghea
Contact Person Email
berghea1@gmail.com

Greece

Earliest CTIS Part Ii Submission Date
23-07-2024
Latest Decision Or Authorization Date
07-05-2026
Processing Time Days
653
Number Of Sites
2
Number Of Participants
13

Sites

Site Name
Laiko General Hospital Of Athens
Department Name
1st Pre-educational Pathology Clinic & Rheumatology Unit
Principal Investigator Name
Petros Sfikakis
Principal Investigator Email
psfikakis@med.uoa.gr
Contact Person Name
Petros Sfikakis
Contact Person Email
psfikakis@med.uoa.gr
Site Name
General Hospital Of Thessaloniki Papageorgiou
Department Name
B’ Dermatology Clinic
Principal Investigator Name
Elisavet Lazaridou
Principal Investigator Email
bethlaz@auth.gr
Contact Person Name
Elisavet Lazaridou
Contact Person Email
bethlaz@auth.gr

Spain

Earliest CTIS Part Ii Submission Date
27-05-2024
Latest Decision Or Authorization Date
10-05-2026
Processing Time Days
713
Number Of Sites
2
Number Of Participants
7

Sites

Site Name
Hospital Universitario Regional De Malaga
Department Name
Rheumatology
Principal Investigator Name
Antonio Fernandez Nebro
Principal Investigator Email
afernandezn@gmail.com
Contact Person Name
Antonio Fernandez Nebro
Contact Person Email
afernandezn@gmail.com
Site Name
Complexo Hospitalario Universitario A Coruna
Department Name
Rheumatology
Principal Investigator Name
Francisco Javier Blanco García
Principal Investigator Email
fblagar@sergas.es
Contact Person Name
Francisco Javier Blanco García
Contact Person Email
fblagar@sergas.es

Sponsor

Primary sponsor

Full Name
Merck Healthcare KGaA
Organisation Type
Pharmaceutical company
Country Of Registered Address
Germany

Contract research organisations

Name
IQVIA Limited
Responsibilities
sponsorDuties codes: 1,10,11,12,15 (value: 'Site contracts. Centralized ECG Services. Provide the software functionality for data collection per protocol requirements. Also supply device'),2,3,6,8
Name
IQVIA RDS Hellas Single Member S.A.
Responsibilities
sponsorDuties codes: 1,12,5,8
Name
Iqvia Laboratories Limited
Responsibilities
sponsorDuties code: 4

Third parties

  • {"country":"United Kingdom","full_name":"Iqvia Laboratories Limited","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"Germany","full_name":"Fisher Clinical Services GmbH","duties_or_roles":"sponsorDuties codes: 14","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"sponsorDuties codes: 1,10,11,12,15 (value: 'Site contracts. Centralized ECG Services. Provide the software functionality for data collection per protocol requirements. Also supply device'),2,3,6,8","organisation_type":"Pharmaceutical company"}
  • {"country":"Greece","full_name":"IQVIA RDS Hellas Single Member S.A.","duties_or_roles":"sponsorDuties codes: 1,12,5,8","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"Switzerland","full_name":"Fisher Clinical Services GmbH (Switzerland address)","duties_or_roles":"sponsorDuties codes: 14","organisation_type":"Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Medical Equipment Supplies And Management Limited","duties_or_roles":"sponsorDuties code: 15 (value: 'Medical Equipment Supplies and Management')","organisation_type":"Pharmaceutical company"}
  • {"country":"Germany","full_name":"Nuvisan GmbH","duties_or_roles":"sponsorDuties code: 15 (value: 'PK Analysis')","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Oracle America Inc.","duties_or_roles":"sponsorDuties code: 7","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Enpatoran
Active Substance
ENPATORAN
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
ORAL
Authorisation Status
prodAuthStatus: 1; MIA number: DE_HE_01_MIA_2023-0007
Investigational Product Name
Enpatoran Placebo
Modality
Other

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