Clinical trial • Phase III • Oncology

DURVALUMAB for Biliary tract cancer | Cholangiocarcinoma | Gallbladder carcinoma

Phase III trial of DURVALUMAB for Biliary tract cancer | Cholangiocarcinoma | Gallbladder carcinoma.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Biliary tract cancer | Cholangiocarcinoma | Gallbladder carcinoma
Trial Stage
Phase III
Drug Modality
Monoclonal antibody | Small molecule

Key dates

Initial CTIS Submission Date
05-04-2024
First CTIS Authorization Date
05-06-2024

Trial design

Randomised, placebo plus gemcitabine/cisplatin (arm b) versus durvalumab plus gemcitabine/cisplatin (arm a); specific doses and schedules not specified in the provided record-controlled Phase III trial in Poland, Italy, France and others.

Randomised
Yes
Comparator
Placebo plus gemcitabine/cisplatin (Arm B) versus Durvalumab plus gemcitabine/cisplatin (Arm A); specific doses and schedules not specified in the provided record
Target Sample Size
685

Eligibility

Recruits 685 Vulnerable population not selected (isVulnerablePopulationSelected=false). Consent expected from adult participants only; no vulnerable/paediatric population indicated in record..

Vulnerable Population
Vulnerable population not selected (isVulnerablePopulationSelected=false). Consent expected from adult participants only; no vulnerable/paediatric population indicated in record.

Inclusion criteria

  • {"criterion_text":"- Histologically confirmed, unresectable advanced or metastatic biliary tract, including cholangiocarcinoma (intrahepatic or extrahepatic) and gallbladder carcinoma."}
  • {"criterion_text":"- Previously untreated disease if unresectable or metastatic at initial diagnosis"}
  • {"criterion_text":"- Recurrent disease >6 months after curative surgery or >6 months after the completion of adjuvant therapy (chemotherapy and/or radiation)"}
  • {"criterion_text":"- WHO/ECOG PS of 0 or 1"}

Exclusion criteria

  • {"criterion_text":"- History of another primary malignancy"}
  • {"criterion_text":"- Brain metastases or spinal cord compression"}
  • {"criterion_text":"- Uncontrolled intercurrent illness"}
  • {"criterion_text":"- Major surgical procedure within 28 days prior to the first dose of IP."}
  • {"criterion_text":"- Prior locoregional therapy such as radioembolization"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Overall survival","definition_or_measurement_approach":""}

Secondary endpoints

  • {"endpoint_text":"- Progression-free survival (PFS), ORR (Objective response rate) , and Duration of response (DoR) according to RECIST 1.1using Investigator assessments","definition_or_measurement_approach":"According to RECIST 1.1 using Investigator assessments (as stated)"}
  • {"endpoint_text":"- ORR and DoR according to RECIST 1.1 using BICR assessments","definition_or_measurement_approach":"According to RECIST 1.1 using Blinded Independent Central Review (BICR) (as stated)"}
  • {"endpoint_text":"- EORTC QLQ-C30: Global health status/QoL and impacts (eg, physical function); multi-term symptoms (eg, fatigue); and single items (eg, appetite loss, insomnia). EORTC QLQ-BIL21: Single-item symptoms (eg, abdominal pain [item 42], pruritus [item 36], jaundice [item 35])","definition_or_measurement_approach":"Patient-reported outcomes using EORTC QLQ-C30 and EORTC QLQ-BIL21 instruments (as stated)"}
  • {"endpoint_text":"- Association of PD-L1 expression level with PFS, ORR, DoR, and DCR (Disease control rate) according to RECIST 1.1 using Investigator assessments and OS (Overall survival)","definition_or_measurement_approach":"Subgroup analyses by PD-L1 expression level; endpoints assessed per RECIST 1.1 and OS (as stated)"}
  • {"endpoint_text":"- Serum concentration of durvalumab (peak and trough concentrations)","definition_or_measurement_approach":"Pharmacokinetic measurements: serum peak and trough concentrations (as stated)"}
  • {"endpoint_text":"- Presence of ADAs for durvalumab (confirmatory results: positive or negative)","definition_or_measurement_approach":"Immunogenicity testing for anti-drug antibodies (ADA) with confirmatory positive/negative results (as stated)"}

Recruitment

Planned Sample Size
685
Recruitment Window Months
11
Consent Approach
Informed consent obtained from adult participants. Subject information and informed consent forms available (country/language-specific documents present in record, e.g. 'L1_ SIS and ICF Main _Redacted_EU CTR', 'L1_ SIS and ICF Adult PL_Redacted', and other country-specific SIS/ICF documents). No paediatric assent process indicated.

Geography

Total Number Of Sites
15
Total Number Of Participants
125

Poland

Earliest CTIS Part Ii Submission Date
18-04-2024
Latest Decision Or Authorization Date
18-12-2024
Processing Time Days
244
Number Of Sites
2
Number Of Participants
34

Sites

Site Name
Uniwersyteckie Centrum Kliniczne
Department Name
Klinika Onkologii i Radioterapii
Contact Person Name
Renata Zaucha
Contact Person Email
rzaucha@gumed.edu.pl
Site Name
Wojewodzkie Wielospecjalistyczne Centrum Onkologii I Traumatologii Im M.Kopernika W Lodzi
Department Name
Oddzial Chemioterapii Nowotworów z Pododzialem Nowotworow Jednego Dnia
Contact Person Name
Rafał Czyżykowski
Contact Person Email
rafal.czyzykowski@wp.pl

Italy

Earliest CTIS Part Ii Submission Date
18-04-2024
Latest Decision Or Authorization Date
16-12-2024
Processing Time Days
242
Number Of Sites
4
Number Of Participants
31

Sites

Site Name
Careggi University Hospital
Department Name
Oncologia Medica
Contact Person Name
Lorenzo Antonuzzo
Contact Person Email
lorenzo.antonuzzo@unifi.it
Site Name
Azienda Ospedaliera Universitaria Integrata Verona
Department Name
Oncologia Medica
Contact Person Name
Michele Milella
Contact Person Email
michele.milella@univr.it
Site Name
Azienda Unita Sanitaria Locale Della Romagna
Department Name
Oncologia
Contact Person Name
Stefano Tamberi
Contact Person Email
ste.tamberi@gmail.com
Site Name
IRCCS Istituto Nazionale Tumori Fondazione Pascale
Department Name
Struttura Complessa di Oncologia Medica Addominale
Contact Person Name
Antonio Avallone

France

Earliest CTIS Part Ii Submission Date
18-04-2024
Latest Decision Or Authorization Date
17-12-2024
Processing Time Days
243
Number Of Sites
7
Number Of Participants
47

Sites

Site Name
Assistance Publique Hopitaux De Paris
Department Name
department of digestive oncology
Contact Person Name
Marie Lequoy
Contact Person Email
marie.lequoy@aphp.fr
Site Name
Centre Hospitalier Universitaire De Montpellier
Department Name
department of digestive oncology
Contact Person Name
Eric Assenat
Contact Person Email
e-assenat@chu-montpellier.fr
Site Name
Centre Hospitalier Universitaire De Poitiers
Department Name
department of digestive oncology
Contact Person Name
David Tougeron
Contact Person Email
david.tougeron@chu-poitiers.fr
Site Name
Centre Hospitalier Universitaire De Dijon
Department Name
department of digestive oncology
Contact Person Name
Sylvain Manfredi
Contact Person Email
sylvain.manfredi@chu-dijon.fr
Site Name
Hopital Beaujon
Department Name
department of digestive oncology
Contact Person Name
Mohamed Bouattour
Contact Person Email
Mohamed.bouattour@bjn.aphp.fr
Site Name
University Hospital Of Bordeaux
Department Name
oncology / digestive consultations
Contact Person Name
Jean-Frédéric Blanc
Site Name
Centre Hospitalier Universitaire De ??? (duplicate entry details in record)

Bulgaria

Earliest CTIS Part Ii Submission Date
18-04-2024
Latest Decision Or Authorization Date
13-02-2025
Processing Time Days
301
Number Of Sites
2
Number Of Participants
13

Sites

Site Name
Medical Center Nadezhda Clinikal EOOD
Department Name
Clinic of medical oncology
Contact Person Name
Mila Petrova
Contact Person Email
milllapetrova@gmail.com
Site Name
Acibadem City Clinic Tokuda University Hospital EAD
Department Name
Department of medical oncology
Contact Person Name
Jeliazko Arabadjiev
Contact Person Email
tcrc@acibademcityclinic.bg

Sponsor

Primary sponsor

Full Name
Astrazeneca AB
Organisation Type
Pharmaceutical company
Country Of Registered Address
Sweden

Investigational products

Investigational Product Name
IMFINZI 50 mg/mL concentrate for solution for infusion.
Active Substance
DURVALUMAB
Modality
Monoclonal antibody
Routes Of Administration
INTRAVENOUS
Route
INTRAVENOUS
Authorisation Status
Authorised (EU/1/18/1322/001)
Maximum Dose
1500 mg
Investigational Product Name
CISPLATIN
Active Substance
CISPLATIN
Modality
Small molecule
Routes Of Administration
INTRAVENOUS
Route
INTRAVENOUS
Investigational Product Name
GEMCITABINE
Active Substance
GEMCITABINE
Modality
Small molecule
Routes Of Administration
INTRAVENOUS
Route
INTRAVENOUS
Investigational Product Name
MYCOPHENOLATE MOFETIL
Active Substance
MYCOPHENOLATE MOFETIL
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Investigational Product Name
INFLIXIMAB
Active Substance
INFLIXIMAB
Modality
Monoclonal antibody
Routes Of Administration
INTRAVENOUS
Route
INTRAVENOUS
Combination Treatment
Yes

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