Clinical trial • Phase I/II • Oncology
DISITAMAB VEDOTIN for HER2 expressing advanced breast cancer
Phase I/II trial of DISITAMAB VEDOTIN for HER2 expressing advanced breast cancer. open-label. 64 participants.
Overview
- Trial Therapeutic Area
- Oncology
- Trial Disease
- HER2 expressing advanced breast cancer
- Trial Stage
- Phase I/II
- Drug Modality
- ADC
Key dates
- Initial CTIS Submission Date
- 30-07-2025
- First CTIS Authorization Date
- 18-11-2025
Trial design
open-label Phase I/II trial across 21 sites in Germany, Italy, Spain.
- Open Label
- Yes
- Biomarker Stratified
- True; HER2 (HER2+, HER2-low, HER2-ultralow) and HR (HR+, HR-)
- Target Sample Size
- 64
Eligibility
Recruits 64 No vulnerable populations selected; trial includes adults only; subject information and informed consent forms are present for participants (multiple language versions available). No assent procedures for minors are indicated..
- Vulnerable Population
- No vulnerable populations selected; trial includes adults only; subject information and informed consent forms are present for participants (multiple language versions available). No assent procedures for minors are indicated.
Inclusion criteria
- {"criterion_text":"- Histologically or cytologically confirmed diagnosis of locally-advanced, unresectable, or metastatic breast carcinoma.\n- HER2 and HR status appropriate for enrollment in cohort.\n- HER2 status determined by most recent local assessment based on American Society of Clinical Oncology (ASCO) and College of American Pathologists (CAP) guidelines for assessment of HER2 in BC for interpretation of HER2 expression and amplification.\n- HR+ disease is determined as either estrogen receptor (ER) and/or progesterone receptor (PgR) positive [ER or PgR ≥1%]) and HR negative disease is determined as both ER and PR negative [ER and PgR <1%]) per ASCO/CAP guidelines in the advanced disease setting. If a patient has had multiple ER/PgR results for advanced disease, the most recent test result will be used to confirm eligibility."}
Exclusion criteria
- {"criterion_text":"- Known hypersensitivity to any excipient contained in the drug formulation of disitamab vedotin.\n- Central nervous system (CNS) and/or leptomeningeal metastasis.\n- Participants with a history of other invasive malignancy within 3 years before the Cycle 1 Day 1 (C1D1) of study intervention, or any evidence of residual disease from a previously diagnosed malignancy.\n- Prior therapy with ADCs with MMAE payload.\n- Participants who have received prior systemic anticancer treatment or radiotherapy within 2 weeks, or 5 half-lives, whichever is shorter, prior to C1D1 of study intervention."}
Endpoints
Primary endpoints
- {"endpoint_text":"- Objective response (OR) (confirmed complete response [CR] and confirmed partial response [PR]) per Response Evaluation Criteria in Solid Tumors version 1.1 (RECIST v1.1) by investigator assessment.","definition_or_measurement_approach":"Measured by investigator assessment per RECIST v1.1; OR defined as confirmed CR or confirmed PR."}
Secondary endpoints
- {"endpoint_text":"- Duration of response (DOR) per RECIST v1.1 by investigator assessment.","definition_or_measurement_approach":"Measured per RECIST v1.1 by investigator assessment; duration from first documented response until progression or death."}
- {"endpoint_text":"- Disease control rate (DCR) (confirmed CR, confirmed PR, and stable disease) per RECIST v1.1 by investigator assessment.","definition_or_measurement_approach":"Measured per RECIST v1.1 by investigator assessment; DCR includes confirmed CR, confirmed PR, and stable disease."}
- {"endpoint_text":"- Progression-free survival (PFS) per RECIST v1.1 by investigator assessment.","definition_or_measurement_approach":"Time from randomization/enrollment to disease progression per RECIST v1.1 or death, assessed by investigator."}
- {"endpoint_text":"- Overall survival (OS).","definition_or_measurement_approach":"Time from randomization/enrollment to death from any cause."}
- {"endpoint_text":"- Estimates of selected PK parameters of disitamab vedotin, total antibody, and unconjugated MMAE.","definition_or_measurement_approach":"Pharmacokinetic sampling and analysis to estimate standard PK parameters for disitamab vedotin, total antibody, and unconjugated MMAE."}
- {"endpoint_text":"- Incidence of anti-drug antibodies (ADA) against disitamab vedotin.","definition_or_measurement_approach":"Immunogenicity assays to detect and report incidence of ADA."}
- {"endpoint_text":"- Safety (type, incidence, severity, seriousness, and relatedness of adverse events [AEs]. Type, incidence, and severity of laboratory abnormalities as well as significant changes from baseline. Frequency of treatment interruptions, dose reductions, and treatment discontinuation due to AEs).","definition_or_measurement_approach":"Adverse event reporting, laboratory monitoring and recording of treatment modifications and discontinuations due to AEs."}
Recruitment
- Digital Remote Recruitment
- True; recruitment materials explicitly include paid search keywords, Facebook page, landing page, study page, image library, patient digital media board and homepage tiles; country-specific versions available (DE, IT, ES, and OUS/EN variants).
- Planned Sample Size
- 64
- Recruitment Window Months
- 29
- Consent Approach
- Informed consent obtained from participants (adults). Subject information and informed consent forms (Main ICD and optional procedure ICDs) are present and available in multiple language versions (German, Italian, Spanish and English versions of documents are listed). Recruitment informed consent procedure documents are provided per country. No assent procedures for minors are indicated.
Methods
- Study-specific web pages / study landing pages (Study Page, Landing Page) — digital study pages for participant information (materials available in DE, EN, IT, ES and OUS variants).
- Paid search keywords / patient paid search — paid search advertising to reach potential participants.
- Social media (OUS Facebook Page) — use of Facebook pages for outreach and recruitment.
- Patient digital media and image libraries / homepage tiles — digital media assets for websites and online adverts.
- Patient digital media board and digital advertising materials — patient-facing digital content for outreach.
- Printed recruitment material and participant-facing recruitment material (creation, printing and shipping) — vendor-supported physical materials.
Geography
- Total Number Of Sites
- 21
- Total Number Of Participants
- 26
Germany
- Earliest CTIS Part Ii Submission Date
- 24-10-2025
- Latest Decision Or Authorization Date
- 29-04-2026
- Processing Time Days
- 187
- Number Of Sites
- 5
- Number Of Participants
- 8
Sites
- Site Name
- Universitaetsklinikum Leipzig AöR
- Department Name
- Universitäres Krebszentrum Leipzig (UCCL)
- Contact Person Name
- Dirk Forstmeyer
- Contact Person Email
- forstmeyer.studienmails@medizin.uni-leipzig.de
- Site Name
- Charite Universitaetsmedizin Berlin KöR
- Department Name
- Campus Mitte, Klinik fuer Gynaekologie m. S. Senologie
- Contact Person Name
- Verena Kiver
- Contact Person Email
- verena.kiver@charite.de
- Site Name
- KEM I Evang. Kliniken Essen-Mitte gGmbH
- Department Name
- Kliniken Essen-Mitte, Evangelische Huyssens-Stiftung, Klinik für Senologie/ Brustzentrum
- Contact Person Name
- Sherko Kümmel
- Contact Person Email
- s.kuemmel@kem-med.com
- Site Name
- Universitaetsklinikum Carl Gustav Carus Dresden an der Technischen Universitaet Dresden AöR
- Department Name
- Klinik und Poliklinik für Frauenheilkunde und Geburtshilfe
- Contact Person Name
- Theresa Link
- Contact Person Email
- Theresa.link@uniklinikum-dresden.de
- Site Name
- Universitaetsklinikum Heidelberg AöR
- Contact Person Name
- Carlo Fremd
- Contact Person Email
- carlo.fremd@med.uni-heidelberg.de
Italy
- Earliest CTIS Part Ii Submission Date
- 01-10-2025
- Latest Decision Or Authorization Date
- 22-04-2026
- Processing Time Days
- 203
- Number Of Sites
- 8
- Number Of Participants
- 10
Sites
- Site Name
- Fondazione IRCCS San Gerardo Dei Tintori
- Department Name
- Centro Ricerca Fase 1
- Contact Person Name
- Maria Elena Cazzaniga
- Contact Person Email
- marinaelena.cazzaniga@irccs-sangerardo.it
- Site Name
- Universita Cattolica Del Sacro Cuore
- Department Name
- Unità operativa semplice di dipartimento Medicina di Precisione in Senologia
- Contact Person Name
- Alessandra Fabi
- Contact Person Email
- alessandra.fabi@policlinicogemelli.it
- Site Name
- Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
- Department Name
- Medical Oncology and Haematology
- Contact Person Name
- Claudio Zamagni
- Contact Person Email
- claudio.zamagni@aosp.bo.it
- Site Name
- Centro Di Riferimento Oncologico Di Aviano
- Department Name
- +390434659253
- Contact Person Name
- Fabio Puglisi
- Contact Person Email
- fabio.puglisi@cro.it
- Site Name
- IRCCS Istituto Nazionale Tumori Fondazione Pascale
- Department Name
- S.C. Oncologia Clinica Sperimentale di Senologia
- Contact Person Name
- Michelino De Laurentiis
- Contact Person Email
- delauren@breastunit.org
- Site Name
- Istituto Romagnolo Per Lo Studio Dei Tumori Dino Amadori IRST S.r.l.
- Department Name
- Complex Structure in Medical Oncology
- Contact Person Name
- Antonino Musolino
- Contact Person Email
- antonino.musolino@irst.emr.it
- Site Name
- Azienda Unita' Sanitaria Locale Toscana Nord Ovest
- Department Name
- UOC Oncologia Medica di Livorno
- Contact Person Name
- Giacomo Allegrini
- Contact Person Email
- giacomo.allegrini@uslnordovest.toscana.it
- Site Name
- Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
- Department Name
- Medical Oncology and Haematology
- Contact Person Name
- Claudio Zamagni
- Contact Person Email
- claudio.zamagni@aosp.bo.it
Spain
- Earliest CTIS Part Ii Submission Date
- 24-10-2025
- Latest Decision Or Authorization Date
- 29-04-2026
- Processing Time Days
- 187
- Number Of Sites
- 8
- Number Of Participants
- 8
Sites
- Site Name
- Hospital Universitario Virgen De La Victoria
- Department Name
- Oncology
- Contact Person Name
- Ana Godoy Ortiz
- Contact Person Email
- anagodort@gmail.com
- Site Name
- Hospital Del Mar
- Department Name
- Oncology
- Contact Person Name
- Sònia Servitja Tormo
- Contact Person Email
- sservitja@parcdesalutmar.cat
- Site Name
- Hospital Universitari Vall D Hebron
- Department Name
- Oncology
- Contact Person Name
- Cristina Saura
- Contact Person Email
- Csaura@vhio.net
- Site Name
- Hospital Universitario La Paz
- Department Name
- Oncology
- Contact Person Name
- Virginia Martinez Marin
- Contact Person Email
- virgimarin9@hotmail.com
- Site Name
- Hospital Beata Maria Ana
- Department Name
- Oncology
- Contact Person Name
- Javier Cortes Castán
- Contact Person Email
- Javier.cortes@maj3.health
- Site Name
- Hospital Clinico Universitario De Valencia
- Department Name
- Oncology
- Contact Person Name
- Begoña Bermejo de las Heras
- Contact Person Email
- begobermejo@gmail.com
- Site Name
- Hospital Universitario Virgen De Las Nieves
- Department Name
- Oncology
- Contact Person Name
- Encarnacion Gonzalez Flores
- Contact Person Email
- encarnagonzalezflores@gmail.com
- Site Name
- Hospital Universitario La Paz
- Department Name
- Oncology
- Contact Person Name
- Virginia Martinez Marin
- Contact Person Email
- virgimarin9@hotmail.com
Sponsor
Primary sponsor
- Full Name
- Pfizer Inc.
- Organisation Type
- Pharmaceutical company
- Country Of Registered Address
- United States
Contract research organisations
- Name
- Icon Clinical Research Limited
- Responsibilities
- training
- Name
- PPD Development LP / PPD Global Central Labs
- Responsibilities
- lab samples reception and storage; other trial support
Third parties
- {"country":"Ireland","full_name":"Icon Clinical Research Limited","duties_or_roles":"training","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Professional Case Management Clinical Trials LLC","duties_or_roles":"home health services","organisation_type":"Laboratory/Research/Testing facility"}
- {"country":"Belgium","full_name":"PPD Global Central Labs","duties_or_roles":"lab samples reception and storage","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Frontage Laboratories Inc.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Q Squared Solutions Holdings LLC","duties_or_roles":"","organisation_type":"Laboratory/Research/Testing facility"}
- {"country":"Belgium","full_name":"CellCarta","duties_or_roles":"","organisation_type":"Laboratory/Research/Testing facility"}
- {"country":"United Kingdom (Northern Ireland)","full_name":"Almac Clinical Services Limited","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"WCG Clinical Inc.","duties_or_roles":"CRC support","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Guardant Health Inc.","duties_or_roles":"","organisation_type":"Laboratory/Research/Testing facility"}
- {"country":"United States","full_name":"PPD Development LP","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Medidata Solutions Inc.","duties_or_roles":"","organisation_type":"Non-Pharmaceutical company"}
- {"country":"United States","full_name":"Azenta US Inc.","duties_or_roles":"lab sample biobank","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"Innovative Trials Limited","duties_or_roles":"printing and shipping of participant and site facing recruitment material","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Scout Clinical","duties_or_roles":"participant reimbursement vendor","organisation_type":"Hospital/Clinic/Other health care facility"}
- {"country":"United States","full_name":"Stark Raving LLC","duties_or_roles":"creation of participant and site facing recruitment material","organisation_type":"Non-Pharmaceutical company"}
Investigational products
- Investigational Product Name
- Disitamab Vedotin
- Active Substance
- DISITAMAB VEDOTIN
- Modality
- ADC
- Routes Of Administration
- INTRAVENOUS
- Route
- INTRAVENOUS
Related trials
Other published trials that may interest you.
- GDC-9545 for Locally advanced or metastatic estrogen receptor-positive breast cancer
- Abemaciclib for Stage IV lung cancer | Breast cancer
- BGB-43395 for Advanced or metastatic solid tumors | Hormone receptor positive HER2 negative breast cancer
- AZD9833 for Estrogen receptor-positive HER2-negative advanced breast cancer
- Pembrolizumab for Classical Hodgkin lymphoma | Melanoma | Solid tumours (MSI-H/dMMR) | Solid tumours (TMB-H)