Clinical trial • Phase II/III • Neurology
dextromethorphan; deramciclane fumarate for Agitation in Alzheimer's disease dementia
Phase II/III trial of dextromethorphan; deramciclane fumarate for Agitation in Alzheimer's disease dementia.
Overview
- Trial Therapeutic Area
- Neurology
- Trial Disease
- Agitation in Alzheimer's disease dementia
- Trial Stage
- Phase II/III
- Drug Modality
- Small molecule
Key dates
- Initial CTIS Submission Date
- 18-12-2025
- First CTIS Authorization Date
- 28-04-2026
Trial design
Randomised, active investigational arms: exv-802 and exv-801; comparator: matching placebo. dose/schedule not specified in the provided data (exv-801 max daily dose reported as 60 mg in product data; exv-802 dose details not specified).-controlled Phase II/III trial across 38 sites in Czechia, Spain, Poland and others.
- Randomised
- Yes
- Comparator
- Active investigational arms: EXV-802 and EXV-801; Comparator: Matching Placebo. Dose/schedule not specified in the provided data (EXV-801 max daily dose reported as 60 mg in product data; EXV-802 dose details not specified).
- Target Sample Size
- 102
- Trial Duration For Participant
- 42
Eligibility
Recruits 102 Vulnerable population selected: participants with Alzheimer's disease dementia (isVulnerablePopulationSelected = true). Informed consent materials include Main ICF and Caregiver ICF documents and privacy notices; provisions for legally authorised representatives (LAR) are documented (e.g. 'Main ICF for participant_LAR' in country-specific materials). Caregiver information and caregiver-specific consent/ICF materials are provided. Materials are available in multiple country languages (EN, ES, PL, SK, IT, DE, CZ) as indicated by language-specific ICF and SIS documents..
- Vulnerable Population
- Vulnerable population selected: participants with Alzheimer's disease dementia (isVulnerablePopulationSelected = true). Informed consent materials include Main ICF and Caregiver ICF documents and privacy notices; provisions for legally authorised representatives (LAR) are documented (e.g. 'Main ICF for participant_LAR' in country-specific materials). Caregiver information and caregiver-specific consent/ICF materials are provided. Materials are available in multiple country languages (EN, ES, PL, SK, IT, DE, CZ) as indicated by language-specific ICF and SIS documents.
Inclusion criteria
- {"criterion_text":"- The participant is an adult male or female between the ages of 55 to 90 years inclusively, who can move around by themselves, with a walker, or with a wheelchair.\n- A previously established diagnosis of AD dementia.\n- The participant meets definition for agitation which require treatment with medicines.\n- The severity of agitation is at least moderate."}
Exclusion criteria
- {"criterion_text":"- The participant has a confirmed primary diagnosis of a dementia-related disease other than AD dementia.\n- The participant has symptoms of agitation that are due to psychiatric conditions other than AD dementia.\n- The participant has a history of uncontrolled seizures or a history of epilepsy.\n- The participant lacks a caregiver or support person who attends regularly to the participants’ needs."}
Endpoints
Primary endpoints
- {"endpoint_text":"- Difference between active and placebo as measured by changes from baseline to endpoint (Week 6) in the Cohen-Mansfield Agitation Inventory total score","definition_or_measurement_approach":"Change from baseline to endpoint (Week 6) in the Cohen-Mansfield Agitation Inventory (CMAI) total score; comparison of active vs placebo."}
Secondary endpoints
- {"endpoint_text":"- EXV-802: Difference between active and placebo as measured by changes from baseline to endpoint (Week 6) in the Clinical Global Impression of Severity of Illness (CGI-S) score, as related to symptoms of agitation.","definition_or_measurement_approach":"Change from baseline to Week 6 in CGI-S score related to agitation; comparison EXV-802 vs placebo."}
- {"endpoint_text":"- EXV-802: Difference between active and placebo as measured by changes from baseline to endpoint (Week 6) in the NPI-C Caregiver Distress total score for agitation and aggression.","definition_or_measurement_approach":"Change from baseline to Week 6 in NPI-C Caregiver Distress total score for agitation/aggression; comparison EXV-802 vs placebo."}
- {"endpoint_text":"- EXV-802: Difference between active and placebo as measured by changes from baseline to endpoint (Week 6) in the NPI-C Irritability / Lability score.","definition_or_measurement_approach":"Change from baseline to Week 6 in NPI-C Irritability/Lability score; comparison EXV-802 vs placebo."}
- {"endpoint_text":"- EXV-802: Difference between active and placebo as measured by changes from baseline to endpoint (Week 6) in the NPI-C Sleep Disorders score.","definition_or_measurement_approach":"Change from baseline to Week 6 in NPI-C Sleep Disorders score; comparison EXV-802 vs placebo."}
- {"endpoint_text":"- EXV-802: Difference between active and placebo in frequency and severity of adverse events and clinically relevant changes in relevant safety endpoints e.g.: •\tMini‐Mental State Examination (MMSE) •\tColumbia Suicide Severity Rating Scale (C-SSRS) score •\tClinical laboratory values •\tVital signs •\tElectrocardiograms (ECGs) •\tPhysical examination findings","definition_or_measurement_approach":"Frequency and severity of adverse events and changes in safety measures (MMSE, C-SSRS, labs, vital signs, ECGs, physical exam) compared between EXV-802 and placebo."}
- {"endpoint_text":"- EXV-801: Difference between active and placebo as measured by changes from baseline to endpoint (Week 6) in CMAI, CGI-S, NPI-C, exploratory PD markers (BDNF), and blood-based biomarkers (analysis limited to descriptive statistics, including the effect size).","definition_or_measurement_approach":"Change from baseline to Week 6 in CMAI, CGI-S, NPI-C; exploratory PD marker BDNF and blood-based biomarkers assessed descriptively (including effect size) for EXV-801 vs placebo."}
- {"endpoint_text":"- EXV-801: Difference between active and placebo in frequency and severity of adverse events and clinically relevant changes in relevant safety endpoints e.g.: •\tMini‐Mental State Examination (MMSE) •\tColumbia Suicide Severity Rating Scale (C-SSRS) score •\tClinical laboratory values •\tVital signs •\tElectrocardiograms (ECGs) •\tPhysical examination findings","definition_or_measurement_approach":"Frequency and severity of adverse events and changes in safety measures (MMSE, C-SSRS, labs, vital signs, ECGs, physical exam) compared between EXV-801 and placebo."}
Recruitment
- Registry Or Advocacy Recruitment
- True, Amsterdam UMC Stichting (listed as Patient organisation/association) is included among third parties.
- Digital Remote Recruitment
- True, PatientGO app and associated digital materials (PatientGO App, PatientGO Data Consent Form, PatientGO EULA, PatientGO Privacy Policy, PatientGO Patient Info Sheet) are present and used for recruitment and participant communications.
- Planned Sample Size
- 222
- Recruitment Window Months
- 32
- Consent Approach
- Informed consent obtained using Main ICF documents; separate Caregiver ICF and SIS (subject information sheet) materials are provided. Provision for consent by a legally authorised representative (LAR) is indicated (e.g. 'Main ICF for participant_LAR' country-specific documents). Privacy notices and data consent forms are provided. Consent materials are available in multiple languages specific to participating countries (English, Spanish, Polish, Slovak, Italian, German, Czech as indicated by language-tagged documents).
Methods
- Posters and flyers placed in clinics and public spaces (country-specific poster/flyer recruitment materials listed per member state).
- Patient/caregiver brochures and flowcharts distributed to potential participants and caregivers (country-specific patient/caregiver brochures and flowcharts listed).
- GP/clinician referral letters (GP letter available in recruitment materials).
- PatientGO digital app-based recruitment and study information (PatientGO App, PatientGO Patient Info Sheet, PatientGO Privacy Policy, PatientGO Data Consent Form present in multiple countries).
- Visit reminder cards and study visit guides for caregivers to support retention and scheduling.
Geography
- Total Number Of Sites
- 38
- Total Number Of Participants
- 222
Czechia
- Earliest CTIS Part Ii Submission Date
- 23-03-2026
- Latest Decision Or Authorization Date
- 28-04-2026
- Processing Time Days
- 36
- Number Of Sites
- 5
- Number Of Participants
- 24
Sites
- Site Name
- Gerontologické centrum
- Contact Person Name
- Iva Holmerová
- Contact Person Email
- clinical.trials@gerontocentrum.cz
- Site Name
- NeuropsychiatrieHK s.r.o.
- Contact Person Name
- Martin Vališ
- Contact Person Email
- valismar@seznam.cz
- Site Name
- Psychiatrie-ambulance s.r.o.
- Contact Person Name
- Veronika Sýkorová
- Contact Person Email
- veronikasykora@centrum.cz
- Site Name
- Brain-Soultherapy s.r.o.
- Contact Person Name
- Klaudia Vocičková Borzová
- Contact Person Email
- brain-soultherapy@seznam.cz
- Site Name
- Fakultni Nemocnice U Sv Anny V Brne
- Department Name
- Neurologie/Neurology
- Contact Person Name
- Lenka Krajčovičová
- Contact Person Email
- lenka.krajcovicova@fnusa.cz
Spain
- Earliest CTIS Part Ii Submission Date
- 23-03-2026
- Latest Decision Or Authorization Date
- 04-05-2026
- Processing Time Days
- 42
- Number Of Sites
- 5
- Number Of Participants
- 30
Sites
- Site Name
- Hospital Universitario Rio Hortega
- Department Name
- Psychiatry
- Contact Person Name
- Juan Luis Muñoz Sanchez
- Contact Person Email
- jlmusa@icloud.com
- Site Name
- Hospital Germans Trias I Pujol
- Department Name
- Neurologia
- Contact Person Name
- Pau Pastor Muñoz
- Contact Person Email
- paupastorm.germanstrias@gencat.cat
- Site Name
- Hospital Clinico San Carlos
- Department Name
- Neurology/Institute of Neuroscience
- Contact Person Name
- Jordi Matias-Guiu
- Contact Person Email
- jordimatiasguiu@hotmail.com
- Site Name
- Complejo Asistencial De Zamora Hospital Provincial De Zamora
- Department Name
- Psychiatry
- Contact Person Name
- Manuel Angel Franco Martin
- Contact Person Email
- mfrancom@saludcastillayleon.es
- Site Name
- Hospital San Juan de Dios De Sevilla
- Department Name
- Instituto Neurológico Andaluz (INA)
- Contact Person Name
- Felix Viñuela Fernandez
- Contact Person Email
- Felix.vinuela@institutoneurologicoandaluz.es
Poland
- Earliest CTIS Part Ii Submission Date
- 23-03-2026
- Latest Decision Or Authorization Date
- 30-04-2026
- Processing Time Days
- 38
- Number Of Sites
- 10
- Number Of Participants
- 60
Sites
- Site Name
- Clinhouse Sp. z o.o.
- Contact Person Name
- Klaudiusz Kumor
- Contact Person Email
- klaudiusz.kumor@cmclinhouse.pl
- Site Name
- Centrum Medyczne Hcp Sp. z o.o.
- Contact Person Name
- Przemysław Osip
- Contact Person Email
- Przemyslaw.osip@cmhcp.pl
- Site Name
- Futuremeds Sp. z o.o.
- Contact Person Name
- Aleksandra Herrera-Sokołowska
- Contact Person Email
- aleksandra.herrera@futuremeds.com
- Site Name
- Velocity Nova Sp. z o.o.
- Contact Person Name
- Monika Wrona
- Contact Person Email
- mwrona@velocityclinical.com
- Site Name
- Rcmed Oddzial Sochaczew
- Contact Person Name
- Małgorzata Fengler-Czeczko
- Contact Person Email
- Malgorzata.fenglerczeczko@rcmed.com.pl
- Site Name
- Krakowska Akademia Neurologii Sp. z o.o.
- Contact Person Name
- Monika Rudzińska-Bar
- Contact Person Email
- mrudzinska-bar@uafm.edu.pl
- Site Name
- NZOZ Wroclawskie Centrum Alzheimerowskie
- Contact Person Name
- Katarzyna Okopien
- Contact Person Email
- katarzyna.okopien@gmail.com
- Site Name
- Silmedic Sp. z o.o.
- Contact Person Name
- Ilona Palka-Kisielowska
- Contact Person Email
- ikisielowska@silmedic.pl
- Site Name
- Niepubliczny Zaklad Opieki Zdrowotnej Neuromed M. I M. Nastaj. sp.p.
- Contact Person Name
- Marcin Nastaj
- Contact Person Email
- marcinnastaj@gmail.com
- Site Name
- Etg Neuroscience Sp. z o.o.
- Contact Person Name
- Aleksandra Karbowniczek
- Contact Person Email
- a.karbowniczek@neuroscience.com.pl
Slovakia
- Earliest CTIS Part Ii Submission Date
- 23-03-2026
- Latest Decision Or Authorization Date
- 29-04-2026
- Processing Time Days
- 37
- Number Of Sites
- 6
- Number Of Participants
- 36
Sites
- Site Name
- Crystal Comfort s.r.o.
- Department Name
- Psychiatricka ambulancia
- Contact Person Name
- Dagmar Breznoscakova
- Contact Person Email
- dbreznoscakova@gmail.com
- Site Name
- Epamed s.r.o.
- Department Name
- Psychiatricka ambulancia
- Contact Person Name
- Eva Palova
- Contact Person Email
- palovae@hotmail.com
- Site Name
- University Hospital Bratislava
- Department Name
- Psychiatricka klinika
- Contact Person Name
- Maria Kralova
- Contact Person Email
- macula.kocuro@gmail.com
- Site Name
- MUDr. Beata Dupejova neurologicka ambulancia s.r.o.
- Department Name
- Neurologicka ambulancia
- Contact Person Name
- Beata Dupejova
- Contact Person Email
- dupejova@gmail.com
- Site Name
- Konzilium s.r.o.
- Department Name
- Neurologicka ambulancia
- Contact Person Name
- Magdalena Perichtova
- Contact Person Email
- perichtova.md@gmail.com
- Site Name
- Klinika AuraMedica
- Department Name
- Neurologicka ambulancia
- Contact Person Name
- Stanislav Sutovsky
- Contact Person Email
- nilusuto@gmail.com
Germany
- Earliest CTIS Part Ii Submission Date
- 23-03-2026
- Latest Decision Or Authorization Date
- 30-04-2026
- Processing Time Days
- 38
- Number Of Sites
- 6
- Number Of Participants
- 36
Sites
- Site Name
- curiositas ad sanum Studien und Beratungs GmbH
- Contact Person Name
- Johannes Schwarz
- Contact Person Email
- j.schwarz@curiositas-ad-sanum.de
- Site Name
- Praxis Dr. med. Kirsten Hahn
- Contact Person Name
- Kirsten Hahn
- Contact Person Email
- neurol.studien@gmail.com
- Site Name
- Pharmakologisches Studienzentrum Chemnitz GmbH
- Contact Person Name
- Ralf Bodenschatz
- Contact Person Email
- ralf.bodenschatz.sz@studienzentrum-chemnitz.de
- Site Name
- Studienzentrum Dr. Bischof GmbH
- Contact Person Name
- Felix Bischof
- Contact Person Email
- felix.bischof@studienzentrum-boeblingen.de
- Site Name
- Zentrum für Psychiatrie Emmendingen
- Contact Person Name
- Michael Hüll
- Contact Person Email
- m.huell@zfp-emmendingen.de
- Site Name
- Klinikum der Technischen Universitaet Muenchen (TUM Klinikum)
- Department Name
- Neurologische Klinik, Ambulanz für neurokognitive Erkrankungen
- Contact Person Name
- Timo Grimmer
- Contact Person Email
- t.grimmer@tum.de
Italy
- Earliest CTIS Part Ii Submission Date
- 23-03-2026
- Latest Decision Or Authorization Date
- 28-04-2026
- Processing Time Days
- 36
- Number Of Sites
- 6
- Number Of Participants
- 36
Sites
- Site Name
- Azienda Ospedaliero-Universitaria Sant Andre
- Department Name
- UOC Neurologia
- Contact Person Name
- Franco Giubilei
- Contact Person Email
- franco.giubilei@uniroma1.it
- Site Name
- Azienda Ospedaliera Universitaria Policlinico Paolo Giaccone
- Department Name
- Department of Medical Care (DAI Medico)
- Contact Person Name
- Mario Barbagallo
- Contact Person Email
- mario.barbagallo@unipa.it
- Site Name
- Provincia Lombardo Veneta Dell’Ordine Ospedaliero Di San Giovanni Di Dio Fatebenefratelli
- Department Name
- Dementia and Rehabilitation Unit
- Contact Person Name
- Barbara Borroni
- Contact Person Email
- bborroni@fatebenefratelli.eu
- Site Name
- Pia Fondazione Di Culto E Religione Card G Panico
- Department Name
- UOC Malattie Neurodegenerative
- Contact Person Name
- Daniele Urso
- Contact Person Email
- d.urso@piafondazionepanico.it
- Site Name
- Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico
- Department Name
- SSD Neurologia - Malattie Neurodegenerative
- Contact Person Name
- Andrea Arighi
- Contact Person Email
- andrea.arighi@policlinico.mi.it
- Site Name
- Azienda Ospedaliera Policlinico Universitario Tor Vergata
- Contact Person Name
- Alessandro Martorana
- Contact Person Email
- martorana@med.uniroma2.it
Sponsor
Primary sponsor
- Full Name
- Exciva GmbH
- Organisation Type
- Pharmaceutical company
- Country Of Registered Address
- Germany
Contract research organisations
- Name
- Syneos Health Inc.
- Responsibilities
- sponsorDuties codes: 4
- Name
- Syneos Health Germany GmbH
- Responsibilities
- sponsorDuties codes: 1,10,11,12,15,2,5,6; includes EC applications, Patient concierge services and patient reimbursement, Safety reporting to CIRB for Unanticipated Problems
Third parties
- {"country":"Switzerland","full_name":"Maxia Strategies GmbH","duties_or_roles":"sponsorDuties codes: 12, 5","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Syneos Health Inc.","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"Acm Global Central Laboratory Limited","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Laboratory/Research/Testing facility"}
- {"country":"Netherlands","full_name":"Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Hospital/Clinic/Other health care facility"}
- {"country":"Germany","full_name":"Syneos Health Germany GmbH","duties_or_roles":"sponsorDuties codes: 1,10,11,12,15,2,5,6; code 15 description: EC applications, Patient concierge services and patient reimbursement, Safety reporting to CIRB for Unanticipated Problems","organisation_type":"Pharmaceutical company"}
- {"country":"Netherlands","full_name":"Amsterdam UMC Stichting","duties_or_roles":"sponsorDuties codes: 4","organisation_type":"Patient organisation/association"}
Investigational products
- Investigational Product Name
- EXV-802
- Active Substance
- dextromethorphan; deramciclane fumarate
- Modality
- Small molecule
- Routes Of Administration
- ORAL
- Route
- ORAL
- Authorisation Status
- 1
- Investigational Product Name
- EXV-801
- Active Substance
- deramciclane
- Modality
- Small molecule
- Routes Of Administration
- ORAL
- Route
- ORAL
- Authorisation Status
- 1
- Maximum Dose
- 60 mg
- Investigational Product Name
- Matching Placebo
- Modality
- Other
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