Clinical trial • Phase III • Cardiology

Colchicine for Peripheral arterial disease | Intermittent claudication

Phase III trial of Colchicine for Peripheral arterial disease | Intermittent claudication.

Overview

Trial Therapeutic Area
Cardiology
Trial Disease
Peripheral arterial disease | Intermittent claudication
Trial Stage
Phase III
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
25-10-2024
First CTIS Authorization Date
26-02-2025

Trial design

Randomised, active arm: colchicine 0.5 mg daily; control arm: placebo matching tiofarma colchicine 500 mcg tablets, daily Phase III trial across 19 sites in Belgium, Italy, Netherlands and others.

Randomised
Yes
Comparator
Active arm: Colchicine 0.5 mg daily; Control arm: Placebo matching Tiofarma colchicine 500 mcg tablets, daily
Target Sample Size
5852

Eligibility

Recruits 5852 Vulnerable population not selected; written informed consent from the patient is required. No assent or guardian consent provisions are specified in the available documentation..

Pregnancy Exclusion
Woman who is pregnant, or breast-feeding or of child-bearing potential not protected by reliable contraception or is planning conception during the study
Vulnerable Population
Vulnerable population not selected; written informed consent from the patient is required. No assent or guardian consent provisions are specified in the available documentation.

Inclusion criteria

  • {"criterion_text":"- Age > 18 years"}
  • {"criterion_text":"- Symptomatic atherosclerotic LE PAD fulfilling at least one of the following: a. Intermittent claudication with ankle/arm blood pressure ratio* (ABI ≤ 0.90) or artery stenosis ≥ 50% plus one of i. >1 vascular bed affected by atherosclerosis ii. Diabetes iii. Heart failure iv. Chronic kidney disease (eGFR < 60 mL/min/1.73 m2); b. Rest pain (mostly in foot) OR necrosis of limb OR gangrene of limb (corresponding to either Fontaine stages 3 or 4 OR Rutherford Classification categories 4 to 6). All must have an ankle/arm blood pressure ratio* (ABI ≤ 0.90) OR artery stenosis ≥ 50%. * In cases of incompressible ankle arteries, the presence of toe pressure ≤ 60 mm Hg or toe-brachial index ≤ 0.70 is acceptable; c. Revascularization defined as limb bypass surgery or endovascular revascularization procedures (irrespective of the specific device used), including percutaneous transluminal angioplasty/stent of iliac or infra-inguinal arteries or extra-anatomical bypass surgery; or d. Leg or foot amputation for arterial vascular indications"}
  • {"criterion_text":"- Written informed consent from the patient"}

Exclusion criteria

  • {"criterion_text":"- Contraindication to colchicine (including hypersensitivity to the active substance or to any of the excipients)"}
  • {"criterion_text":"- Long term requirement for colchicine for another clinical indication"}
  • {"criterion_text":"- Active diarrhoea"}
  • {"criterion_text":"- eGFR < 30 mL/min/1.73 m2"}
  • {"criterion_text":"- Cirrhosis or severe chronic liver disease"}
  • {"criterion_text":"- Woman who is pregnant, or breast-feeding or of child-bearing potential not protected by reliable contraception or is planning conception during the study"}
  • {"criterion_text":"- Current or planned long term use of cyclosporine, verapamil, HIV protease inhibitors, azole antifungals, or macrolide antibiotics (with the exception of azithromycin)"}
  • {"criterion_text":"- Patients who are deemed unlikely to return for follow-up"}
  • {"criterion_text":"- Patients with life expectancy < 1 year"}
  • {"criterion_text":"- Patients with blood dyscrasias"}
  • {"criterion_text":"- Patients with severe heart failure (NYHA class IV)"}
  • {"criterion_text":"- Patients with severe gastrointestinal insufficiency"}
  • {"criterion_text":"- Participation in a clinical trial in which an investigational drug was administered within 30 days of screening, or within the 5 half-lives of the study drug, whichever is longer"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Rate of major adverse cardiovascular and limb events (MACE or MALE). This composite outcome consists of cardiovascular deaths, myocardial infarction, stroke, and severe limb ischemia that requires a vascular intervention (i.e., pharmacological reperfusion, endovascular or surgical revascularization) or a major vascular amputation (defined as ankle/transtibial amputation or higher).","definition_or_measurement_approach":"Composite endpoint defined as cardiovascular deaths, myocardial infarction, stroke, and severe limb ischemia requiring vascular intervention or major vascular amputation (ankle/transtibial amputation or higher). Measurement approach not further specified in the provided extract."}

Secondary endpoints

  • {"endpoint_text":"- Extended MALE; This composite outcome includes major adverse limb events (MALE) as well as revascularization for new or worsening claudication of new stenosis or occlusion detected on screening after a previous intervention","definition_or_measurement_approach":"Composite endpoint including MALE plus revascularization for new/worsening claudication or new stenosis/occlusion detected on screening after prior intervention."}
  • {"endpoint_text":"- Cardiovascular death","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Myocardial infarction","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Stroke","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Hospitalization","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Acute or chronic limb-threatening ischemia","definition_or_measurement_approach":""}
  • {"endpoint_text":"- All revascularization (coronary or cerebrovascular or lower limb or other peripheral revascularization)","definition_or_measurement_approach":"Includes coronary, cerebrovascular, lower limb or other peripheral revascularization procedures."}
  • {"endpoint_text":"- Total vascular amputation","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Overall mortality","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Any thrombosis or thromboembolism (arterial and venous)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Fontaine Stage","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Standard Assessment of Global Everyday Activities (SAGEA)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Vascular Quality of Life Questionnaire-6 (VascQOL-6)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- EuroQol 5 Dimension 5 Level (EQ-5D-5L)","definition_or_measurement_approach":""}

Recruitment

Digital Remote Recruitment
Yes
Planned Sample Size
5852
Recruitment Window Months
60
Consent Approach
Written informed consent from the patient is required. Subject information and informed consent forms are available in country-specific versions: Belgium (DE, NL, FR), Italy (IT), Netherlands (NL), Germany (DE). No paediatric assent or guardian consent provisions are specified in the provided documentation.

Methods

  • Site-based recruitment via participating hospitals/vascular surgery and cardiology clinics (documented in site-specific 'Recruitment and Informed Consent Procedures' K1 PDFs)
  • Study website (document: K2_Recruitment Material_Study Website_NL) used for recruitment materials
  • Letters to general practitioners (documents: L2_Letter to GP_IT and L2_Letter to GP_NL) documented as part of subject information/invitation materials

Geography

Total Number Of Sites
19
Total Number Of Participants
1898

Belgium

Earliest CTIS Part Ii Submission Date
06-11-2024
Latest Decision Or Authorization Date
27-02-2025
Processing Time Days
113
Number Of Sites
1
Number Of Participants
48

Sites

Site Name
UZ Leuven
Department Name
Cardiology
Contact Person Name
Thomas Vanassche
Contact Person Email
thomas.vanassche@uzleuven.be

Italy

Earliest CTIS Part Ii Submission Date
24-01-2025
Latest Decision Or Authorization Date
01-07-2025
Processing Time Days
158
Number Of Sites
7
Number Of Participants
250

Sites

Site Name
Universita' Degli Studi G. D'Annunzio Di Chieti
Department Name
Vascular Surgery
Contact Person Name
Marcello Di Nisio
Contact Person Email
mdinisio@unich.it
Site Name
Azienda Ulss 6 Euganea
Department Name
Internal Medicine-Thrombosis
Contact Person Name
Sofia Barbar
Contact Person Email
sofia.barbar@aulss6.veneto.it
Site Name
Azienda Unita' Locale Socio Sanitaria N. 2 Marca Trevigiana
Department Name
Cardiology
Contact Person Name
Beniamino Zalunardo
Site Name
Ospedale Ss. Giovanni E Paolo
Department Name
Cardiology
Contact Person Name
Cristiano Bortoluzzi
Contact Person Email
crisbort@libero.it
Site Name
Azienda Unita Locale Socio Sanitaria N. 1 Dolomiti
Department Name
Cardiology
Contact Person Name
Romeo Martini
Contact Person Email
romeo.martini@aulss1.veneto.it
Site Name
AULSS 5 POLESANA, PRESIDIO OSPEDALIERO DI ROVIGO
Department Name
Cardiology
Contact Person Name
Marco Marzolo
Contact Person Email
marco.marzolo@aulss5.veneto.it
Site Name
Azienda Ospedaliera di Padova
Department Name
Cardiology
Contact Person Name
Paolo Simioni
Contact Person Email
paolo.simioni@unipd.it

Netherlands

Earliest CTIS Part Ii Submission Date
03-06-2025
Latest Decision Or Authorization Date
26-11-2025
Processing Time Days
176
Number Of Sites
10
Number Of Participants
1500

Sites

Site Name
Alrijne Zorggroep Stichting
Department Name
Vascular Surgery
Contact Person Name
Borger van der Burg
Contact Person Email
blsborgervanderburg@alrijne.nl
Site Name
Slingeland Ziekenhuis
Department Name
Vascular Surgery
Contact Person Name
D.M. Scharn
Contact Person Email
d.scharn@slingeland.nl
Site Name
Stichting Elisabeth-Tweesteden Ziekenhuis
Department Name
Vascular Surgery
Contact Person Name
M.K. Dinkelman
Contact Person Email
m.dinkelman@etz.nl
Site Name
Meander Medisch Centrum
Department Name
Vascular Surgery
Contact Person Name
Hidde Jongsma
Contact Person Email
h.jongsma@meandermc.nl
Site Name
Universitair Medisch Centrum Utrecht
Department Name
Vascular Surgery
Contact Person Name
Martin Teraa
Contact Person Email
M.Teraa@umcutrecht.nl
Site Name
Universitair Medisch Centrum Groningen
Department Name
Vascular Surgery
Contact Person Name
Ben Saleem
Contact Person Email
b.r.saleem@umcg.nl
Site Name
Academisch Ziekenhuis Maastricht
Department Name
Vascular Surgery
Contact Person Name
Barend Mees
Contact Person Email
barend.mees@mumc.nl
Site Name
Deventer Ziekenhuis
Department Name
Vascular Surgery
Contact Person Name
Bob van Tongeren
Contact Person Email
r.b.m.vantongeren@dz.nl
Site Name
Groene Hart Ziekenhuis
Department Name
Vascular Surgery
Contact Person Name
Joris Blok
Contact Person Email
Joris.Blok@ghz.nl
Site Name
Jeroen Bosch Ziekenhuis Stichting
Department Name
Vascular Surgery
Contact Person Name
Olivier Koning
Contact Person Email
a.v.asseldonk@jbz.nl

Germany

Earliest CTIS Part Ii Submission Date
12-03-2026
Latest Decision Or Authorization Date
24-03-2026
Processing Time Days
12
Number Of Sites
1
Number Of Participants
100

Sites

Site Name
Universitaetsklinikum Essen AöR
Department Name
Cardiology and Angiology
Contact Person Name
Christos Rammos
Contact Person Email
christos.rammos@uk-essen.de

Sponsor

Primary sponsor

Full Name
Hamilton Health Sciences Corporation
Organisation Type
Hospital/Clinic/Other health care facility
Country Of Registered Address
Canada

Investigational products

Investigational Product Name
Colchicine Tiofarma 500 microgram Tablets
Active Substance
Colchicine
Modality
Small molecule
Routes Of Administration
ORAL
Route
oral
Authorisation Status
Marketing authorisation PL 17299/0003 (prodAuthStatus 2)
Starting Dose
0.5 mg daily
Dose Levels
0.5 mg
Frequency
daily
Maximum Dose
0.5 mg
Investigational Product Name
Placebo matching Tiofarma colchicine 500 mcg tablets
Modality
Other
Frequency
daily

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