Clinical trial • Phase II • Musculoskeletal

CLOSTRIDIUM BOTULINUM, NEUROTOXIN SEROTYPE A/B for Cervical dystonia

Phase II trial of CLOSTRIDIUM BOTULINUM, NEUROTOXIN SEROTYPE A/B for Cervical dystonia.

Overview

Trial Therapeutic Area
Musculoskeletal
Trial Disease
Cervical dystonia
Trial Stage
Phase II
Drug Modality
Peptide/protein/enzyme

Key dates

Initial CTIS Submission Date
31-01-2025
First CTIS Authorization Date
12-05-2025

Trial design

Randomised, placebo of ipn10200 (placebo comparator). dose and schedule not specified in the ctis record.-controlled Phase II trial across 32 sites in France, Poland, Germany and others.

Randomised
Yes
Comparator
Placebo of IPN10200 (placebo comparator). Dose and schedule not specified in the CTIS record.
Target Sample Size
94
Trial Duration For Participant
252

Eligibility

Recruits 94 No vulnerable population selected (isVulnerablePopulationSelected=false). Informed consent is from adult participants; no assent arrangements are indicated..

Vulnerable Population
No vulnerable population selected (isVulnerablePopulationSelected=false). Informed consent is from adult participants; no assent arrangements are indicated.

Inclusion criteria

  • {"criterion_text":"- A clinical diagnosis of isolated Cervical Dystonia (CD) (idiopathic) characterized by dystonic symptoms localised to the head, neck, and shoulder areas with at least moderate severity at Screening and Baseline (Day 1) defined as: • (a) Toronto Western Spasmodic Torticollis Rating Scale (TWSTRS)- Total score ≥20 • (b) TWSTRS-Severity subscale score ≥15 • (c) TWSTRS-Disability subscale score ≥3 • (d) TWSTRS-Pain subscale score ≥ 1\n- Treatment naïve or non-naïve to BoNT therapy for CD"}

Exclusion criteria

  • {"criterion_text":"- Participants presenting with a swallowing disorder of any origin which might be exacerbated by BoNT treatment, such as: • (a) Grade 3 or 4 on the Dysphagia Severity Scale (severe dysphagia) with swallowing difficulties and requiring a change in diet.\n- Predominant anterocollis.\n- Predominant retrocollis.\n- Traumatic torticollis or tardive torticollis.\n- Marked limitation on passive range of motion that suggests cervical contractures or structural abnormality."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Change from Baseline in the Toronto Western Spasmodic Torticollis Rating Scale (TWSTRS) total score. [Time frame: at week 4]","definition_or_measurement_approach":"Change from baseline in the TWSTRS total score measured at Week 4."}

Secondary endpoints

  • {"endpoint_text":"- Change from Baseline in the TWSTRS total score at all other scheduled timepoints post injection until Week 36. [Time Frame: At all timepoints post injection until Week 36.]","definition_or_measurement_approach":"Change from baseline in TWSTRS total score measured at all scheduled post-injection timepoints up to Week 36."}
  • {"endpoint_text":"- Change from Baseline in the TWSTRS-Pain Subscale. The TWSTRS pain subscale consists of three patient-rated items that assess the participants usual, worst and best pain from the preceding week, and the subscore has a maximum of 20. [Time Frame: At all timepoints post injection until Week 36.]","definition_or_measurement_approach":"Change from baseline in TWSTRS pain subscale (three patient-rated items; max subscore 20) at scheduled timepoints up to Week 36."}
  • {"endpoint_text":"- Change from baseline in the daily Numerical Rating Scale (NRS) score [Time Frame: Averaged over every 7-day period until the Week 4 visit]","definition_or_measurement_approach":"Change from baseline in daily NRS score, averaged over each 7-day period until Week 4."}
  • {"endpoint_text":"- Time to onset of pain reduction Defined as the duration from the administration of the study injection to the first recorded instance of a minimum 2-point decrease in the Numeric Rating Scale (NRS) score. [Time Frame: From study injection to first timepoint at which at least 2-point reduction is observed in NRS score]","definition_or_measurement_approach":"Time from study injection to first recorded ≥2-point decrease in NRS score."}
  • {"endpoint_text":"- Time to return of symptoms in responders (time from treatment to loss of 80% of peak treatment effect) [Time Frame: From randomization until Week 36]","definition_or_measurement_approach":"Time from treatment to loss of 80% of peak treatment effect in responders, measured from randomization until Week 36."}
  • {"endpoint_text":"- Change from Baseline in the TWSTRS-Disability Subscale. The TWSTRS disability subscale assesses the effect that Cervical Dystonia (CD) has on the participant’s daily activities and the subscore has a maximum of 30 and consists of six items. [Time Frame: At all timepoints post injection until Week 36.]","definition_or_measurement_approach":"Change from baseline in TWSTRS disability subscale (6 items, max 30) at scheduled timepoints up to Week 36."}
  • {"endpoint_text":"- Change from Baseline in the TWSTRS-Severity Subscale. The TWSTRS severity subscale rates the maximal excursion of the torticollis (degree of tilt or rotation), elevation, range of motion, etc. This severity subscore has a maximum subtotal of 35 and consists of 11 items. [Time Frame: At all scheduled timepoints post injection until Week 36]","definition_or_measurement_approach":"Change from baseline in TWSTRS severity subscale (11 items, max subtotal 35) at scheduled timepoints up to Week 36."}
  • {"endpoint_text":"- Change from baseline in Clinical Global Impression of Severity (CGI-S) score. [Time Frame: At all timepoints post injection until Week 36.]","definition_or_measurement_approach":"Change from baseline in CGI-S score at scheduled timepoints up to Week 36."}
  • {"endpoint_text":"- Clinical Global Impression of Change (CGI-C) score [Time Frame: At all timepoints post injection until Week 36.]","definition_or_measurement_approach":"CGI-C assessed at scheduled timepoints up to Week 36."}
  • {"endpoint_text":"- Change from baseline in Patients' Global Impression of Severity (PGI-S) score [Time Frame: At all timepoints post injection until Week 36]","definition_or_measurement_approach":"Change from baseline in PGI-S score at scheduled timepoints up to Week 36."}
  • {"endpoint_text":"- Patients' Global Impression of Change (PGI-S) score [Time Frame: At all timepoints post injection until Week 36]","definition_or_measurement_approach":"PGI-C/PGI-S assessed at scheduled timepoints up to Week 36."}
  • {"endpoint_text":"- Change from Baseline in the Cervical Dystonia Impact Profile (CDIP-58) total score. [Time Frame: At all timepoints post injection until Week 36]","definition_or_measurement_approach":"Change from baseline in CDIP-58 total score at scheduled timepoints up to Week 36."}
  • {"endpoint_text":"- Percentage of participants experiencing any Adverse Event (AEs) including treatment emergent adverse events (TEAEs), serious adverse events (SAEs), adverse event of special interest (AESI) and AE leading to treatment discontinuation. [Time Frame: From baseline to Week 36.]","definition_or_measurement_approach":"Proportion of participants with any AE/TEAE/SAE/AESI/AEs leading to discontinuation from baseline to Week 36."}
  • {"endpoint_text":"- Percentage of participants with clinically significant changes from baseline in Laboratory Parameters Clinically significant change in laboratory parameters will be reported. The clinical significance will graded by the investigator. [Time Frame: At all timepoints post injection until Week 36]","definition_or_measurement_approach":"Proportion with clinically significant laboratory parameter changes as graded by investigator at scheduled timepoints up to Week 36."}
  • {"endpoint_text":"- Percentage of Participants With Clinically Significant Changes from baseline in Vital Signs Clinically significant changes in vital signs will be reported. The clinical significance will be graded by the investigator. [Time Frame: At all timepoints post injection until Week 36]","definition_or_measurement_approach":"Proportion with clinically significant vital sign changes as graded by investigator at scheduled timepoints up to Week 36."}
  • {"endpoint_text":"- Percentage of participants with clinically significant change from baseline in focused neurological/physical examinations. [Time Frame: At all timepoints post injection until Week 36]","definition_or_measurement_approach":"Proportion with clinically significant changes on focused neurological/physical exams at scheduled timepoints up to Week 36."}
  • {"endpoint_text":"- Percentage of participants with clinically significant change from baseline in 12-lead Electrocardiogram (ECG) readings. [Time Frame: At all timepoints post injection until Week 36]","definition_or_measurement_approach":"Proportion with clinically significant changes in 12-lead ECG readings at scheduled timepoints up to Week 36."}
  • {"endpoint_text":"- Treatment-emergence of suicidal ideation/suicidal behaviour. The Columbia Suicide Severity Rating Scale (C-SSRS) will be used in this study for the evaluation of suicidal ideation and behaviour. [Time Frame: From baseline to Week 36.]","definition_or_measurement_approach":"Treatment-emergent suicidal ideation/behaviour assessed using C-SSRS from baseline to Week 36."}
  • {"endpoint_text":"- Percentage of participants with Binding antibodies to IPN10200 [Time Frame: At all timepoints post injection until Week 36]","definition_or_measurement_approach":"Proportion with binding antibodies to IPN10200 at scheduled timepoints up to Week 36."}
  • {"endpoint_text":"- Percentage of participants with neutralising antibodies to IPN10200. [Time Frame: At all timepoints post injection until Week 36]","definition_or_measurement_approach":"Proportion with neutralising antibodies to IPN10200 at scheduled timepoints up to Week 36."}

Recruitment

Planned Sample Size
94
Recruitment Window Months
28
Consent Approach
Informed consent obtained from adult participants. Country-specific subject information and informed consent forms (ICFs) are provided (documents present for France, Poland, Germany, Spain, Italy, Czechia and English-language ICFs). Additional ICFs/materials for pregnant partners and data protection are present. No assent arrangements are indicated.

Geography

Total Number Of Sites
32
Total Number Of Participants
94

France

Earliest CTIS Part Ii Submission Date
11-03-2025
Latest Decision Or Authorization Date
20-04-2026
Processing Time Days
405
Number Of Sites
5
Number Of Participants
16

Sites

Site Name
Centre Hospitalier Universitaire De Nimes
Department Name
#250003
Principal Investigator Name
Giovanni Castelnovo
Principal Investigator Email
giovanni.castelnovo@chu-nimes.fr
Contact Person Name
Giovanni Castelnovo
Site Name
Les Hopitaux Universitaires De Strasbourg
Department Name
#250004
Principal Investigator Name
Christine Tranchant
Principal Investigator Email
Christine.Tranchant@chru-strasbourg.fr
Contact Person Name
Christine Tranchant
Site Name
Centre Hospitalier Regional De Marseille
Department Name
#250005
Principal Investigator Name
Frederique Fluchere
Principal Investigator Email
frederique.fluchere@ap-hm.fr
Contact Person Name
Frederique Fluchere
Contact Person Email
frederique.fluchere@ap-hm.fr
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
#250001
Principal Investigator Name
Marion Simonetta-Moreau
Principal Investigator Email
simonetta.m@chu-toulouse.fr
Contact Person Name
Marion Simonetta-Moreau
Contact Person Email
simonetta.m@chu-toulouse.fr
Site Name
Centre Hospitalier Universitaire Grenoble Alpes
Department Name
#250002
Principal Investigator Name
Elena Moro
Principal Investigator Email
emoro@chu-grenoble.fr
Contact Person Name
Elena Moro
Contact Person Email
emoro@chu-grenoble.fr

Poland

Earliest CTIS Part Ii Submission Date
12-05-2025
Latest Decision Or Authorization Date
21-04-2026
Processing Time Days
344
Number Of Sites
8
Number Of Participants
19

Sites

Site Name
Specjalistyczne Gabinety Sp. z o.o.
Department Name
#616008 Neurologia
Principal Investigator Name
Lucyna Horodecka-Wardega
Principal Investigator Email
lhwardega@specjalistycznegabinety.pl
Contact Person Name
Lucyna Horodecka-Wardega
Site Name
Instytut Zdrowia Dr Boczarska-Jedynak Sp. z o.o. S.K.
Department Name
#616003 Neurologia
Principal Investigator Name
Magdalena Boczarska-Jedynak
Principal Investigator Email
m.boczarskajedynak@gmail.com
Contact Person Name
Magdalena Boczarska-Jedynak
Contact Person Email
m.boczarskajedynak@gmail.com
Site Name
Samodzielny Publiczny Zaklad Opieki Zdrowotnej Szpital Uniwersytecki W Krakowie
Department Name
#616006 Zespol Poradni Specjal., Poradnia Neurologiczna
Principal Investigator Name
Agnieszka Slowik
Principal Investigator Email
slowik@cm-uj.krakow.pl
Contact Person Name
Agnieszka Slowik
Contact Person Email
slowik@cm-uj.krakow.pl
Site Name
Etg Neuroscience Sp. z o.o.
Department Name
#616001 Neurologia
Principal Investigator Name
Aleksandra Karbowniczek
Principal Investigator Email
a.karbowniczek@neuroscience.com.pl
Contact Person Name
Aleksandra Karbowniczek
Site Name
Eskulap Pabianice Sp z o.o.
Department Name
#616007 Neurologia
Principal Investigator Name
Malgorzata Tyslerowicz
Principal Investigator Email
m.tyslerowicz@eskulapbk.pl
Contact Person Name
Malgorzata Tyslerowicz
Contact Person Email
m.tyslerowicz@eskulapbk.pl
Site Name
Futuremeds Sp. z o.o.
Department Name
#616005 Neurologia
Principal Investigator Name
Karolina Porebska
Principal Investigator Email
karolina.porebska@futuremeds.com
Contact Person Name
Karolina Porebska
Site Name
Provincial Specialist Hospital Them. J. Gromkowski
Department Name
#616004 Oddzial Neurologii z Pododdzialem Udarowym
Principal Investigator Name
Katarzyna Marianska
Principal Investigator Email
marianskakatarzyna@gmail.com
Contact Person Name
Katarzyna Marianska
Contact Person Email
marianskakatarzyna@gmail.com
Site Name
Provincial Specialist Hospital Them. J. Gromkowski (additional listed site)

Germany

Earliest CTIS Part Ii Submission Date
23-04-2025
Latest Decision Or Authorization Date
15-04-2026
Processing Time Days
357
Number Of Sites
4
Number Of Participants
14

Sites

Site Name
St. Johannes Krankenhaus
Department Name
#276002: Neurologie
Principal Investigator Name
Sebastian Paus
Principal Investigator Email
sebastian.paus@gfo-kliniken-troisdorf.de
Contact Person Name
Sebastian Paus
Site Name
curiositas ad sanum Studien und Beratungs GmbH
Department Name
276003: Neurologie
Principal Investigator Name
Johannes Schwarz
Principal Investigator Email
j.schwarz@curiositas-ad-sanum.de
Contact Person Name
Johannes Schwarz
Site Name
University Medical Center Hamburg-Eppendorf
Department Name
#276004: Neurologie
Principal Investigator Name
Mathias Gelderblom
Principal Investigator Email
m.gelderblom@uke.de
Contact Person Name
Mathias Gelderblom
Contact Person Email
m.gelderblom@uke.de
Site Name
Universitaetsklinikum Tuebingen AöR
Department Name
#276001: Neurologie
Principal Investigator Name
Ebba Lohmann
Principal Investigator Email
ebba.lohmann@med.uni-tuebingen.de
Contact Person Name
Ebba Lohmann

Spain

Earliest CTIS Part Ii Submission Date
28-04-2025
Latest Decision Or Authorization Date
17-04-2026
Processing Time Days
354
Number Of Sites
4
Number Of Participants
14

Sites

Site Name
Hospital Universitario De La Princesa
Department Name
#724005: Neurologia
Principal Investigator Name
Lydia López Manzanares
Principal Investigator Email
lydia.lopez@salud.madrid.org
Contact Person Name
Lydia López Manzanares
Contact Person Email
lydia.lopez@salud.madrid.org
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
#724002: Neurofisiología Clínica
Principal Investigator Name
Pablo Mir Rivera
Principal Investigator Email
pmir@us.es
Contact Person Name
Pablo Mir Rivera
Contact Person Email
pmir@us.es
Site Name
Hospital De La Santa Creu I Sant Pau
Department Name
#724004: Neurología
Principal Investigator Name
Javier Pagonabarraga Mora
Principal Investigator Email
jpagonabarraga@santpau.cat
Contact Person Name
Javier Pagonabarraga Mora
Contact Person Email
jpagonabarraga@santpau.cat
Site Name
Hospital Universitario Puerta Del Mar
Department Name
#724003: Neurocirugía
Principal Investigator Name
Raul Espinosa Rosso
Principal Investigator Email
raul.espinosarosso@alum.uca.es
Contact Person Name
Raul Espinosa Rosso
Contact Person Email
raul.espinosarosso@alum.uca.es

Italy

Earliest CTIS Part Ii Submission Date
15-04-2025
Latest Decision Or Authorization Date
20-04-2026
Processing Time Days
370
Number Of Sites
6
Number Of Participants
14

Sites

Site Name
Azienda Unita Sanitaria Locale Di Bologna
Department Name
#380002: Sezione di Ricerca Neurofisiologia Traslazionale
Principal Investigator Name
Giulia Giannini
Principal Investigator Email
giannini.giulia3@gmail.com
Contact Person Name
Giulia Giannini
Contact Person Email
giannini.giulia3@gmail.com
Site Name
IRCCS Foundation Istituto Neurologico Carlo Besta
Department Name
#380003: Neurologia 1 - Malattia di Parkinson e Disturbi del Movimento
Principal Investigator Name
Roberto Eleopra
Principal Investigator Email
roberto.eleopra@istituto-besta.it
Contact Person Name
Roberto Eleopra
Site Name
Fondazione Istituto Neurologico Nazionale Casimiro Mondino
Department Name
#380005: Sezione di Ricerca Neurofisiologia Traslazionale
Principal Investigator Name
Giuseppe Cosentino
Principal Investigator Email
giuseppe.cosentino@mondino.it
Contact Person Name
Giuseppe Cosentino
Contact Person Email
giuseppe.cosentino@mondino.it
Site Name
Azienda USL IRCCS Di Reggio Emilia
Department Name
#380004: SOC di Neurologia
Principal Investigator Name
Francesco Cavallieri
Principal Investigator Email
francesco.cavallieri@ausl.re.it
Contact Person Name
Francesco Cavallieri
Site Name
Istituto Auxologico Italiano
Department Name
#380001: UO Neurologia
Principal Investigator Name
Alberto Doretti
Principal Investigator Email
a.doretti@auxologico.it
Contact Person Name
Alberto Doretti
Contact Person Email
a.doretti@auxologico.it
Site Name
Azienda Unita Sanitaria Locale Di Bologna (additional listed site)

Sponsor

Primary sponsor

Full Name
Ipsen Innovation
Organisation Type
Pharmaceutical company
Country Of Registered Address
France

Contract research organisations

Name
Parexel International (IRL) Limited
Responsibilities
1,10,11,12,13,14,2,5,6,8,9

Third parties

  • {"country":"France","full_name":"Eurofins BioPharma Product Testing Biologics","duties_or_roles":"4","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Ireland","full_name":"Parexel International (IRL) Limited","duties_or_roles":"1,10,11,12,13,14,2,5,6,8,9","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Clario Medical Imaging Inc.","duties_or_roles":"15 (PFT)","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Medidata Solutions Inc.","duties_or_roles":"7","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Scout Clinical","duties_or_roles":"15 (Patient expenses reimbursement)","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"United Kingdom","full_name":"Mapi Life Sciences UK Limited","duties_or_roles":"15 (patient questionnaires)","organisation_type":"Industry"}

Investigational products

Investigational Product Name
IPN10200
Active Substance
CLOSTRIDIUM BOTULINUM, NEUROTOXIN SEROTYPE A/B
Modality
Peptide/protein/enzyme
Routes Of Administration
Intramuscular
Route
INTRAMUSCULAR USE
Investigational Product Name
Placebo of IPN10200
Modality
Other

Related trials

Other published trials that may interest you.