Clinical trial • Phase II • Cardiology
CICLOSPORIN for Takotsubo syndrome
Phase II trial of CICLOSPORIN for Takotsubo syndrome.
Overview
- Trial Therapeutic Area
- Cardiology
- Trial Disease
- Takotsubo syndrome
- Trial Stage
- Phase II
- Drug Modality
- Small molecule
Key dates
- Initial CTIS Submission Date
- 20-06-2024
- First CTIS Authorization Date
- 30-08-2024
Trial design
Randomised, placebo (sodium chloride) intravenous bolus matching csa schedule. intervention arm: cyclosporine a 2.5 mg/kg intravenous bolus given at t0, t12 and t24; comparator arm: placebo (sodium chloride) intravenous bolus given at t0, t12 and t24 (matching schedule).-controlled Phase II trial across 24 sites in Germany.
- Randomised
- Yes
- Comparator
- Placebo (Sodium chloride) intravenous bolus matching CsA schedule. Intervention arm: Cyclosporine A 2.5 mg/kg intravenous bolus given at T0, T12 and T24; Comparator arm: placebo (sodium chloride) intravenous bolus given at T0, T12 and T24 (matching schedule).
- Target Sample Size
- 204
- Trial Duration For Participant
- 365
Eligibility
Recruits 204 Vulnerable population selected. Written informed consent is required from participants (patients aged over 18). Multiple informed consent forms and procedures are provided in the documentation including forms for legal authorised representative (LAR), spouse, oral consent, independent doctor, DZHK Heart Bank consent and subsequent consent versions, indicating processes to obtain consent where participants may be incapacitated or require alternative consenting routes..
- Pregnancy Exclusion
- Female patients currently pregnant or women of childbearing age without negative pregnancy test or without effective contraception
- Vulnerable Population
- Vulnerable population selected. Written informed consent is required from participants (patients aged over 18). Multiple informed consent forms and procedures are provided in the documentation including forms for legal authorised representative (LAR), spouse, oral consent, independent doctor, DZHK Heart Bank consent and subsequent consent versions, indicating processes to obtain consent where participants may be incapacitated or require alternative consenting routes.
Inclusion criteria
- {"criterion_text":"- Patients aged over 18"}
- {"criterion_text":"- Enrollment and first IMP administration within 24 hours after cardiac catheterization"}
- {"criterion_text":"- Regional Wall Motion Abnormality (WMA) consistent with TTS in angiography or echocardiography"}
- {"criterion_text":"- InterTAK prognostic score ≥ 9 or GEIST Score ≥ 9"}
- {"criterion_text":"- Written informed consent"}
Exclusion criteria
- {"criterion_text":"- Acute coronary syndrome (ACS) with significant coronary stenosis potentially associated with wall motion abnormalities (WMA) or percutaneous coronary intervention (PCI)"}
- {"criterion_text":"- History of chronic renal insufficiency (either creatinin clearance <30 ml/min/1.73m² or current medical care for severe renal insufficiency)"}
- {"criterion_text":"- History of liver insufficiency"}
- {"criterion_text":"- Uncontrolled hypertension at the time of screening for study inclusion (systolic blood pressure >180mmHg and/or diastolic blood pressure >110mmHg)"}
- {"criterion_text":"- Current medication with any compound containing Hypericum perforatum (St. John’s worth) or Stiripentol or Aliskiren or Bosentan or Rosuvastatine (Rosuvastatine > 5mg within 24h before IMP administration)"}
- {"criterion_text":"- Female patients currently pregnant or women of childbearing age without negative pregnancy test or without effective contraception"}
- {"criterion_text":"- Any disorder associated with immunological dysfunction ≤6 months prior to presentation (autoimmune disease, known positive serology for HIV or hepatitis)"}
- {"criterion_text":"- Immunosuppressive, chemotherapeutical, or antibody treatment"}
- {"criterion_text":"- Participation in other clinical trials except for non-interventional trials"}
- {"criterion_text":"- Neither male nor female at birth"}
- {"criterion_text":"- Infection (defined as concomitant infection with a positive blood culture at the time of study inclusion)"}
- {"criterion_text":"- History of hypersensitivity to cyclosporine"}
- {"criterion_text":"- History of hypersensitivity to egg, peanut or soybean proteins"}
Endpoints
Primary endpoints
- {"endpoint_text":"- Primary efficacy endpoint: Reduction of myocardial damage quantified by AUC of centrally measured highsensitive cardiac Troponin T (TnT) over 72 h.","definition_or_measurement_approach":"Centrally measured high-sensitive Troponin T area under the curve (AUC) over 72 hours with measurements at baseline, 3h, 12h, 24h, 36h, 48h, 60h and 72h."}
Secondary endpoints
- {"endpoint_text":"- Change in TnT/NTproBNP at T3/12/24/36/48/60/72/M1 and change in LVEF at T48/72/M1 (vs. baseline)","definition_or_measurement_approach":"Biomarker changes (TnT, NTproBNP) measured at specified timepoints (3h, 12h, 24h, 36h, 48h, 60h, 72h and Month1) and left ventricular ejection fraction (LVEF) assessed at 48h, 72h and Month1 vs baseline."}
- {"endpoint_text":"- Myocardial edema/inflammation at T48-72 (cMRI, T2 SIand EGE ratio (lake louise criteria))","definition_or_measurement_approach":"Cardiac MRI at 48–72 hours assessing T2 signal intensity and early gadolinium enhancement (EGE) ratio according to Lake Louise criteria to evaluate myocardial edema/inflammation."}
- {"endpoint_text":"- Length of stay on IMC/ICU and length of hospital stay","definition_or_measurement_approach":"Recorded duration of intermediate care/intensive care unit stay and total hospital length of stay."}
- {"endpoint_text":"- Composite cardiovascular outcome at 30d and 1year: mortality from any cause, stroke, myocardial infarction, heart failure, hospitalization, recurrent TTS, cardiac arrest / ventricular fibrillation, ventricular tachycardia, novel atrial fibrillation, thromboembolism, LV-Thrombus, AV-Block, ventricular rupture and new onset atrial fibrillation","definition_or_measurement_approach":"Composite event rate assessed at 30 days and 1 year including the listed cardiovascular events and outcomes."}
- {"endpoint_text":"- Psychosocial and quality of life assessments between groups at M1 vs. M12","definition_or_measurement_approach":"Validated psychosocial and quality-of-life instruments assessed at Month 1 and Month 12 comparing groups."}
Recruitment
- Planned Sample Size
- 204
- Recruitment Window Months
- 43
- Consent Approach
- Written informed consent from the participant is required. Multiple consent variants and supporting documents are provided (subject information and informed consent form, oral consent form, consent by independent doctor, LAR (legal authorised representative) consent, spouse consent, DZHK Heart Bank consent, subsequent consent versions), indicating procedures for obtaining consent where participants may be unable to consent themselves. Study population restricted to adults (>18 years). No languages explicitly listed in the available metadata.
Geography
- Total Number Of Sites
- 24
- Total Number Of Participants
- 204
Germany
- Earliest CTIS Part Ii Submission Date
- 06-08-2024
- Latest Decision Or Authorization Date
- 04-12-2025
- Processing Time Days
- 485
- Number Of Sites
- 24
- Number Of Participants
- 204
Sites
- Site Name
- Universitaetsklinikum Duesseldorf AöR
- Department Name
- Division of Cardiology, Pneumology, and Vascular Diseases
- Contact Person Name
- Fabian Voß
- Contact Person Email
- Fabian.voss@med.uni-duesseldorf.de
- Site Name
- Klinikum rechts der Isar der TU Muenchen AöR
- Department Name
- Medizinische Klinik und Poiliklinik der Inneren Medizin I, Studienzentrum Kardiologie
- Contact Person Name
- Karl-Ludwig Laugwitz
- Contact Person Email
- sabrina.doering@mri.tum.de
- Site Name
- Universitaetsklinikum Frankfurt AöR
- Department Name
- Med. Klinik 3 – Kardiologie, Angiologie
- Contact Person Name
- Maria Papathanasiou
- Contact Person Email
- papathanasiou@med.uni-frankfurt.de
- Site Name
- Rostock University Medical Center
- Department Name
- Department für Innere Medizin, Klinik und Poliklinik für Kardiologie
- Contact Person Name
- Hüseyin Ince
- Contact Person Email
- Hueseyin.Ince@med.uni-rostock.de
- Site Name
- Universitaetsklinikum Magdeburg AöR
- Department Name
- Klinik für Kardiologie und Angiologie
- Contact Person Name
- Rüdiger Braun-Dullaeus
- Contact Person Email
- r.braun.dullaeus@med.ovgu.de
- Site Name
- Universitaetsklinikum Mannheim GmbH
- Department Name
- Medizinische Klinik I
- Contact Person Name
- Ibrahim Akin
- Contact Person Email
- ibrahim.akin@umm.de
- Site Name
- Universitaetsklinikum Bonn AöR
- Department Name
- Medizinische Klinik und Poliklinik II, Herzzentrum
- Contact Person Name
- Georg Nickenig
- Contact Person Email
- Georg.Nickenig@ukbonn.de
- Site Name
- Helios Universitaetsklinikum Wuppertal
- Department Name
- Kardiologie
- Contact Person Name
- Melchior Seyfarth
- Contact Person Email
- nadine.abandor@helios-gesundheit.de
- Site Name
- Charite Universitaetsmedizin Berlin KöR
- Department Name
- Deutsches Herzzentrum der Charité, Klinik für Kardiologie, Angiologie und Intensivmedizin
- Contact Person Name
- Frank Edelmann
- Contact Person Email
- frank.edelmann@dhzc-charite.de
- Site Name
- Universitaetsmedizin Goettingen
- Department Name
- Heart Center Göttingen
- Contact Person Name
- Stephan von Haehling
- Contact Person Email
- stephan.von.haehling@med.uni-goettingen.de
- Site Name
- Martin-Luther-Universitaet Halle-Wittenberg
- Department Name
- Universitätsklinik und Poliklinik für Innere Medizin III
- Contact Person Name
- Daniel Sedding
- Contact Person Email
- direktion-kardiologie@uk-halle.de
- Site Name
- Herzzentrum Leipzig GmbH
- Department Name
- Leipzig Heart Center
- Contact Person Name
- Holger Thiele
- Contact Person Email
- Holger.Thiele@medizin.uni-leipzig.de
- Site Name
- Universitaetsklinikum Heidelberg AöR
- Department Name
- Internal Medicine 3
- Contact Person Name
- Norbert Frey
- Contact Person Email
- norbert.frey@med.uni-heidelberg.de
- Site Name
- Charite Universitaetsmedizin Berlin KöR
- Department Name
- Klinik für Kardiologie, Angiologie und Intensivmedizin, Campus Benjamin Franklin
- Contact Person Name
- Christian Oeing
- Contact Person Email
- christian.oeing@dhzc-charite.de
- Site Name
- Kerckhoff-Klinik GmbH
- Department Name
- Kardiologie
- Contact Person Name
- Samuel Sossalla
- Contact Person Email
- kardiologie@kerckhoff-klinik.de
- Site Name
- Universitaetsklinikum Schleswig-Holstein AöR
- Department Name
- Medizinische Klinik II, Universitäres Herzzentrum Lübeck
- Contact Person Name
- Ingo Eitel
- Contact Person Email
- Ingo.Eitel@uksh.de
- Site Name
- University Hospital Cologne AöR
- Department Name
- Herzzentrum der Universität zu Köln
- Contact Person Name
- Roman Pfister
- Contact Person Email
- roman.pfister@uk-koeln.de
- Site Name
- Herzzentrum Dresden GmbH Universitaetsklinik
- Department Name
- Klinik für Innere Medizin und Kardiologie
- Contact Person Name
- Stefanie Jellinghaus
- Contact Person Email
- Stefanie.Jellinghaus@mailbox.tu-dresden.de
- Site Name
- Universitaet Leipzig
- Department Name
- Klinik und Poliklinik für Kardiologie
- Contact Person Name
- Rolf Wachter
- Contact Person Email
- studien.kardiologie@medizin.uni-leipzig.de
- Site Name
- Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz KöR
- Department Name
- Zentrum für Kardiologie
- Contact Person Name
- Maike Knorr
- Contact Person Email
- maike.knorr@unimedizin-mainz.de
- Site Name
- Universitaetsklinikum Ulm AöR
- Department Name
- Klinik für Innere Medizin II
- Contact Person Name
- Wolfgang Rottbauer
- Contact Person Email
- uta.dichristin@uniklinik-ulm.de
- Site Name
- University Medical Center Hamburg-Eppendorf
- Department Name
- Klinik für Kardiologie
- Contact Person Name
- Christina Magnussen
- Contact Person Email
- c.magnussen@uke.de
- Site Name
- Universitaetsklinikum Essen AöR
- Department Name
- Klinik für Kardiologie und Angiologie
- Contact Person Name
- Tienush Rassaf
- Contact Person Email
- tienush.rassaf@uk-essen.de
- Site Name
- Klinikum der Universitaet Muenchen AöR
- Department Name
- Medizinische Klinik und Poliklinik I, Standort Großhadern
- Contact Person Name
- Ludwig Weckbach
- Contact Person Email
- Ludwig.weckbach@med.uni-muenchen.de
Sponsor
Primary sponsor
- Full Name
- Universitaetsklinikum Heidelberg AöR
- Organisation Type
- Hospital/Clinic/Other health care facility
- Country Of Registered Address
- Germany
Third parties
- {"country":"Germany","full_name":"Universitaetsklinikum Heidelberg AöR","duties_or_roles":"[1,10,12,5,6,8]","organisation_type":"Hospital/Clinic/Other health care facility"}
Investigational products
- Investigational Product Name
- Sandimmun® 50 mg/ml Konzentrat zur Herstellung einer Infusionslösung
- Active Substance
- CICLOSPORIN
- Modality
- Small molecule
- Routes Of Administration
- INTRAVENOUS BOLUS USE
- Route
- Intravenous bolus
- Authorisation Status
- Authorised in Germany (marketing authorisation number 3123.00.00)
- Starting Dose
- 2.5 mg/kg
- Dose Levels
- 2.5 mg/kg (single planned dose per administration)
- Frequency
- At T0, T12 and T24 (three administrations)
- Investigational Product Name
- SODIUM CHLORIDE
- Active Substance
- SODIUM CHLORIDE
- Modality
- Small molecule
- Routes Of Administration
- INTRAVENOUS BOLUS USE
- Route
- Intravenous bolus
- Authorisation Status
- Authorised / pharmaceutical aid (used as placebo/diluent)
- Frequency
- At T0, T12 and T24 (matching placebo schedule)
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