Clinical trial • Phase III • Oncology

CAPECITABINE for Metastatic colorectal cancer | Advanced colorectal cancer

Phase III trial of CAPECITABINE for Metastatic colorectal cancer | Advanced colorectal cancer.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Metastatic colorectal cancer | Advanced colorectal cancer
Trial Stage
Phase III
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
07-03-2024
First CTIS Authorization Date
17-05-2024

Trial design

Randomised, open-label, four randomized arms: fluoropyrimidine monotherapy, full dose (standard dosage) vs fluoropyrimidine monotherapy, upfront dose-reduced (upfront reduction of 25% [75% of standard dosage]); fluoropyrimidine + oxaliplatin, full dose (standard dosage) vs fluoropyrimidine + oxaliplatin, upfront dose-reduced (upfront reduction of 25% [75% of standard dosage]). specific mg/m2 dosing not stated in arm descriptions.-controlled Phase III trial in Netherlands.

Randomised
Yes
Open Label
Yes
Comparator
Four randomized arms: Fluoropyrimidine monotherapy, full dose (standard dosage) vs Fluoropyrimidine monotherapy, upfront dose-reduced (Upfront reduction of 25% [75% of standard dosage]); Fluoropyrimidine + oxaliplatin, full dose (standard dosage) vs Fluoropyrimidine + oxaliplatin, upfront dose-reduced (Upfront reduction of 25% [75% of standard dosage]). Specific mg/m2 dosing not stated in arm descriptions.
Target Sample Size
587

Stratification factors

  • Mono-chemotherapy versus doublet chemotherapy (stratification based on individual risk of toxicity)

Eligibility

Recruits 587 Vulnerable population not selected. The trial requires written informed consent and excludes "Patients with severe cognitive deficits making informed consent not possible". Participants must be able to understand the Dutch language (language requirement). Consent is provided by the adult participant (no pediatric/assent procedures described)..

Vulnerable Population
Vulnerable population not selected. The trial requires written informed consent and excludes "Patients with severe cognitive deficits making informed consent not possible". Participants must be able to understand the Dutch language (language requirement). Consent is provided by the adult participant (no pediatric/assent procedures described).

Inclusion criteria

  • {"criterion_text":"- Patients aged 70 years or older with colorectal cancer and distant metastases without localized treatment options."}
  • {"criterion_text":"- Patients who are candidates for first-line palliative chemotherapy as judged by their treating oncologist"}
  • {"criterion_text":"- Being able to understand the Dutch language"}
  • {"criterion_text":"- Written informed consent"}
  • {"criterion_text":"- Adequate bone marrow and organ function as defined by following laboratory values: Absolute neutrophil count (ANC) > 1.5 x 10^9 mmol/L, Hemoglobin (Hb) > 6.0 mmol/L, Platelets >100 x 109 / L, Serum bilirubin ≤ 2 x upper limit of normal (ULN), serum transaminases ≤ 3 x ULN without presence of liver metastases or ≤ 5x ULN with presence of liver metastases."}

Exclusion criteria

  • {"criterion_text":"- Patients who received prior palliative chemotherapy"}
  • {"criterion_text":"- Patients in whom local treatment of metastases with curative intent is scheduled (i.e. liver surgery or stereotactic radiotherapy)"}
  • {"criterion_text":"- Patients who received prior adjuvant chemotherapy in the one year before inclusion in the study (chemotherapy before that time is allowed)"}
  • {"criterion_text":"- Patients with complete or incomplete dihydropyrimidine dehydrogenase (DPD) deficiency"}
  • {"criterion_text":"- Patients with Microsatellite instable (MSI)-high colorectal cancer"}
  • {"criterion_text":"- Patients with known HIV or active hepatitis infection"}
  • {"criterion_text":"- Patients with severe kidney failure (defined as GFR ≤30ml/min)"}
  • {"criterion_text":"- Patients with severe cognitive deficits making informed consent not possible"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Progression-free survival","definition_or_measurement_approach":""}

Secondary endpoints

  • {"endpoint_text":"- Quality of Life","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Physical Functioning","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Grade 3-5 chemotherapy-related toxicity","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Overall Survival","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Number of completed treatment cycles","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Dose reductions during treatment","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Unplanned hospitalizations","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Cumulative received dosage","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Cost-effectiveness","definition_or_measurement_approach":""}

Recruitment

Planned Sample Size
587
Recruitment Window Months
54
Consent Approach
Written informed consent is required from each participant. Participants must be able to understand the Dutch language. Subject information and informed consent forms for adults are provided (documents listed). No pediatric assent procedures described.

Geography

Total Number Of Sites
40
Total Number Of Participants
587

Netherlands

Earliest CTIS Part Ii Submission Date
29-04-2024
Latest Decision Or Authorization Date
31-03-2025
Processing Time Days
336
Number Of Sites
40
Number Of Participants
587

Sites

Site Name
Laurentius Ziekenhuis Roermond
Department Name
Oncologie
Contact Person Name
Loes Verhoeven
Contact Person Email
loes.verhoeven@lzr.nl
Site Name
Stichting Viecuri Medisch Centrum voor Noord-Limburg
Department Name
Interne geneeskunde oncologie
Contact Person Name
H. Vestjens
Contact Person Email
hvestjens@viecuri.nl
Site Name
Medisch Centrum Leeuwarden B.V.
Department Name
Polikliniek en Dagcentrum OCL
Contact Person Name
J.A.J. Douma
Contact Person Email
Wetenschap@mclacademie.nl
Site Name
Amsterdam UMC Stichting
Department Name
Medische Oncologie
Contact Person Name
K. Versteeg
Contact Person Email
k.versteeg@amsterdamumc.nl
Site Name
Sint Franciscus Vlietland Groep Stichting
Department Name
Oncologie
Contact Person Name
Danielle Mathijssen-van Stein
Site Name
Isala Klinieken Stichting
Department Name
Oncologie
Contact Person Name
R.T. Lugtenberg
Contact Person Email
r.t.lugtenberg@isala.nl
Site Name
Noordwest Ziekenhuisgroep Stichting
Department Name
Oncologie
Contact Person Name
I.G.C. Hermsen
Contact Person Email
igc.hermsen@nwz.nl
Site Name
Medisch Spectrum Twente
Department Name
Oncologie
Contact Person Name
A.N.M. Wymenga
Contact Person Email
A.Wymenga@mst.nl
Site Name
Ziekenhuis Amstelland
Department Name
Oncologie
Contact Person Name
A. van Zweeden
Contact Person Email
a.vanzweeden@zha.nl
Site Name
Catharina Ziekenhuis Stichting
Department Name
Oncologie
Contact Person Name
I.E.G. van Hellemond
Site Name
ZorgSaam Ziekenhuis
Department Name
Oncologie
Contact Person Name
M.A. van Dijk
Contact Person Email
m.vandijk@zzv.nl
Site Name
Diakonessenhuis Stichting
Department Name
Interne Oncologie
Contact Person Name
T. Oostergo
Contact Person Email
wetenschapsbureau@diakhuis.nl
Site Name
Wilhelmina Ziekenhuis Assen
Department Name
Inwendige geneeskunde, interne oncologie
Contact Person Name
Titia Lamberts
Contact Person Email
researchbureau@wza.nl
Site Name
Meander Medisch Centrum
Department Name
Oncologie
Contact Person Name
Hans-Martin Otten
Contact Person Email
jmmb.otten@meandermc.nl
Site Name
Admiraal De Ruyter Ziekenhuis B.V.
Department Name
Interne Geneeskunde/oncologie
Contact Person Name
H. van Halteren
Contact Person Email
hk.vanhalteren@adrz.nl
Site Name
Elkerliek Ziekenhuis
Department Name
Interne Geneeskunde - Hemato-oncologie
Contact Person Name
M.M. Teeuwen - van Genderen
Contact Person Email
mm.vangenderen@elkerliek.nl
Site Name
Ziekenhuis St Jansdal
Department Name
Interne Geneeskunde
Contact Person Name
J.A. Ropela
Contact Person Email
ja.ropela@stjansdal.nl
Site Name
Ziekenhuis Gelderse Vallei Stichting
Department Name
Oncologisch Centrum
Contact Person Name
A. Baars
Contact Person Email
BaarsA@zgv.nl
Site Name
Deventer Ziekenhuis
Department Name
Oncologie
Contact Person Name
Lonneke Kessels
Contact Person Email
L.Kessels@dz.nl
Site Name
Ziekenhuisgroep Twente Stichting
Department Name
Interne Geneeskunde
Contact Person Name
R de Jong- Wever
Contact Person Email
J.Coes@zgt.nl
Site Name
Alrijne Zorggroep Stichting
Department Name
Medische Oncologie
Contact Person Name
L. Spierings
Contact Person Email
leaspierings@alrijne.nl
Site Name
Haga Hospital
Department Name
Medische Oncologie
Contact Person Name
D. Houtsma
Contact Person Email
d.houtsma@hagaziekenhuis.nl
Site Name
Jeroen Bosch Ziekenhuis
Department Name
Oncologie
Contact Person Name
H. Pruijt
Contact Person Email
H.Pruijt@jbz.nl
Site Name
Rode Kruis Ziekenhuis B.V.
Department Name
Interne Geneeskunde
Contact Person Name
A. Goosens
Contact Person Email
agoosens@rkz.nl
Site Name
Treant Ziekenhuiszorg Stichting
Department Name
Interne Geneeskunde
Contact Person Name
M. Tent
Contact Person Email
m.tent@treant.nl
Site Name
Sint Antonius Ziekenhuis Stichting
Department Name
Interne Geneeskunde
Contact Person Name
M. Los
Contact Person Email
m.los@antoniusziekenhuis.nl
Site Name
Rijnstate Ziekenhuis Stichting
Department Name
Medische Oncologie
Contact Person Name
Inge Werter
Contact Person Email
iwerter@rijnstate.nl
Site Name
Streekziekenhuis Koningin Beatrix
Department Name
Oncologie/poli Interne
Contact Person Name
M. Duizer
Contact Person Email
m.duizer@skbwinterswijk.nl
Site Name
Tergooiziekenhuizen
Department Name
Interne Geneeskunde
Contact Person Name
A. van der Velden
Contact Person Email
avandervelden@tergooi.nl
Site Name
Leids Universitair Medisch Centrum (LUMC)
Department Name
Medical Oncology
Contact Person Name
Johanneke Portielje
Contact Person Email
J.E.A.Portielje@lumc.nl
Site Name
Reinier de Graaf Groep
Department Name
Research Unit Oncology
Contact Person Name
Arjan Verschoor
Contact Person Email
wetenschapsbureau@rdgg.nl
Site Name
Ommelander Ziekenhuis Groningen B.V.
Department Name
Medische Oncologie
Contact Person Name
T. Osinga
Contact Person Email
t.osinga@ozg.nl
Site Name
Bravis Ziekenhuis
Department Name
Oncologie
Contact Person Name
F Terheggen
Contact Person Email
f.terheggen@bravis.nl
Site Name
Medical Center Haaglanden
Department Name
Oncologie
Contact Person Name
A. Jochems
Contact Person Email
a.jochems@haaglandenmc.nl
Site Name
Canisius Wilhelmina Ziekenhuis
Department Name
Oncologie
Contact Person Name
Johan Janssen
Contact Person Email
Johan.janssen@cwz.nl
Site Name
Spaarne Gasthuis Stichting
Department Name
Oncologie
Contact Person Name
J. Schrama
Contact Person Email
jschrama@spaarnegasthuis.nl
Site Name
Bernhoven B.V.
Department Name
Interne Geneeskunde
Contact Person Name
M. Janssen
Contact Person Email
mar.janssen@bernhoven.nl
Site Name
Beatrix Ziekenhuis
Department Name
Interne oncologie
Contact Person Name
M.A. Davidis
Contact Person Email
m.davidis@rivas.nl
Site Name
Maxima Medisch Centrum
Department Name
Oncologie
Contact Person Name
Lieke Simkens
Contact Person Email
l.simkens@mmc.nl
Site Name
Slingeland Ziekenhuis
Department Name
Interne Geneeskunde
Contact Person Name
C. van Arkel
Contact Person Email
c.van.arkel@slingeland.nl
Site Name
Maasstad Ziekenhuis Stichting
Department Name
Oncologie
Contact Person Name
B.C.M. Haberkorn
Site Name
Zaans Medisch Centrum Stichting
Department Name
Oncologie
Contact Person Name
A.S.B. Conijn
Contact Person Email
Conijn.A@zaansmc.nl
Site Name
Ikazia Ziekenhuis
Department Name
Oncologie
Contact Person Name
F.E. de Jongh
Contact Person Email
fe.de.jongh@ikazia.nl
Site Name
Groene Hart Ziekenhuis
Department Name
Medische Oncologie
Contact Person Name
Marissa Cloos-van Baalen
Contact Person Email
Marissa.Cloos@ghz.nl
Site Name
IJsselland Ziekenhuis
Department Name
Oncologie
Contact Person Name
Laura Poppe-Manenschijn
Contact Person Email
dkehrer@ysl.nl

Sponsor

Primary sponsor

Full Name
Academisch Ziekenhuis Leiden
Organisation Type
Hospital/Clinic/Other health care facility
Country Of Registered Address
Netherlands

Investigational products

Investigational Product Name
Capecitabine 500 mg Film-coated Tablets
Active Substance
CAPECITABINE
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Authorisation Status
Authorised
Maximum Dose
1000 mg/m2 per day
Investigational Product Name
Fluorouracil 50 mg/ml Solution for injection/infusion
Active Substance
FLUOROURACIL
Modality
Small molecule
Routes Of Administration
INTRAVENOUS
Route
INTRAVENOUS
Authorisation Status
Authorised
Maximum Dose
1200 mg/m2 per day
Investigational Product Name
Calcium Folinate 10 mg/ml Solution for injection or infusion
Active Substance
FOLINIC ACID
Modality
Small molecule
Routes Of Administration
INTRAVENOUS INFUSION
Route
INTRAVENOUS INFUSION
Authorisation Status
Authorised
Maximum Dose
400 mg/m2 per day
Investigational Product Name
Oxaliplatin 5 mg/ml Concentrate for Solution for infusion
Active Substance
OXALIPLATIN
Modality
Small molecule
Routes Of Administration
INTRAVENOUS
Route
INTRAVENOUS
Authorisation Status
Authorised
Maximum Dose
130 mg/m2 per day
Combination Treatment
Yes

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