Clinical trial • Phase II/III • Oncology

CAPECITABINE for Locally advanced rectal cancer (stage II/III)

Phase II/III trial of CAPECITABINE for Locally advanced rectal cancer (stage II/III).

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Locally advanced rectal cancer (stage II/III)
Trial Stage
Phase II/III
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
29-11-2024
First CTIS Authorization Date
10-01-2025

Trial design

Randomised, open-label, oxaliplatin (intravenous; product record: oxaliplatin; max daily dose amount listed as 130 mg/m2) and capecitabine (oral; product record: capecitabine; max daily dose amount listed as 2000 mg). specific schedules not specified in ctis record.-controlled Phase II/III trial across 29 sites in Italy.

Randomised
Yes
Open Label
Yes
Comparator
Oxaliplatin (intravenous; product record: OXALIPLATIN; max daily dose amount listed as 130 mg/m2) and Capecitabine (oral; product record: CAPECITABINE; max daily dose amount listed as 2000 mg). Specific schedules not specified in CTIS record.
Target Sample Size
340

Eligibility

Recruits 340 Vulnerable population selected in CTIS record. Subject information and informed consent forms are listed in the documents (e.g. 'Informativa e consenso NeoAspMet vers 1 del 29 06 2020', 'Consenso tratt dati pers NeoAspMet vers 1 del 7 10 2024 for publication'). No further specific consent/assent handling details provided in the CTIS data..

Vulnerable Population
Vulnerable population selected in CTIS record. Subject information and informed consent forms are listed in the documents (e.g. 'Informativa e consenso NeoAspMet vers 1 del 29 06 2020', 'Consenso tratt dati pers NeoAspMet vers 1 del 7 10 2024 for publication'). No further specific consent/assent handling details provided in the CTIS data.

Inclusion criteria

  • {"criterion_text":"- Pathologically proven diagnosis of adenocarcinoma of the rectum by endoscopic biopsy within 56 days prior to randomisation. Locally advanced tumour (defined as TNM Stage II or III) based upon the following minimum diagnostic workup: MRI of the pelvis, contrast-enhanced CT of abdomen and chest. Able to undergo induction chemotherapy, chemoradiotherapy and total mesorectal excision (TME). For further information please refer to the protocol"}

Exclusion criteria

  • {"criterion_text":"- Prior treatment for LARC (recurrent rectal tumours are excluded) or previous pelvic radiotherapy. Unequivocal evidence of established metastatic disease based on minimum diagnostic workup. Patients with equivocal lesions are eligible. Patients already taking daily aspirin and/or metformin for more than 4 weeks prior to randomisation. Hypersensitivity to salicylic acid compounds or prostaglandin synthetase inhibitors and to any of the excipients. Hypersensitivity to metformin or to any of the excipients. For further information please see protocol"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Good Pathological Response (GPR) defined as Tumour downstaging (ypT0 or ypT1) irrespective of the pathological N stage","definition_or_measurement_approach":"Good Pathological Response (GPR) defined as Tumour downstaging (ypT0 or ypT1) irrespective of the pathological N stage"}

Secondary endpoints

  • {"endpoint_text":"- Tumor Regression Rate\n- Pathological complete responses (pCR)\n- NeoAdjuvant Rectal (NAR) score\n- MRI Tumor Downstaging (mr TGR) rate\n- Event-Free Survival (EFS)\n- Overall Survival (OS)\n- Time to Distant Recurrence (TDR)\n- Rate of local recurrence at 3 years\n- Abdominal Perineal Resection (APR) rate\n- Organ preservation rate at 3 years\n- Post-operative complications\n- Treatment-related toxicity\n- Quality of Life (QoL)","definition_or_measurement_approach":"For further information please see protocol"}

Recruitment

Planned Sample Size
340
Recruitment Window Months
70
Consent Approach
Subject information and informed consent forms available (document titles in CTIS: 'Informativa e consenso NeoAspMet vers 1 del 29 06 2020', 'Consenso tratt dati pers NeoAspMet vers 1 del 7 10 2024 for publication', 'Lettera medico di base NeoAspMet vers 1 del 29 06 2020'). No further details on who provides consent, age-specific documents or languages are provided in the CTIS data.

Geography

Total Number Of Sites
29
Total Number Of Participants
340

Italy

Earliest CTIS Part Ii Submission Date
16-10-2024
Latest Decision Or Authorization Date
05-12-2025
Processing Time Days
415
Number Of Sites
29
Number Of Participants
340

Sites

Site Name
Azienda Ospedaliero-Universitaria San Luigi Gonzaga
Department Name
SCDU Chirurgia Generale
Contact Person Name
Maurizio Degiuli
Site Name
Centro Di Riferimento Oncologico Di Aviano
Department Name
SOC Oncologia Medica e Prevenzione Oncologica
Contact Person Name
Angela Buonadonna
Contact Person Email
abuonadonna@cro.it
Site Name
IRCCS Istituto Nazionale Tumori Fondazione Pascale
Department Name
UOC Oncologia Chirurgica Colorettale
Contact Person Name
Paolo Del Rio
Contact Person Email
p.delrio@istitutotumori.na.it
Site Name
Casa Di Cura Macchiarella S.p.A.
Department Name
Oncologia Medica
Contact Person Name
Concetta Maria Porretto
Contact Person Email
69cp@libero.it
Site Name
Azienda USL IRCCS Di Reggio Emilia
Department Name
Oncologia Medica, A.U.S.L. di Reggio Emilia - IRCCS - Presidio Arcispedale S. Maria Nuova
Contact Person Name
Maria Banzi
Contact Person Email
maria.banzi@ausl.re.it
Site Name
Istituto Oncologico Veneto
Department Name
U. O. di Oncologia Medica 1
Contact Person Name
Sara Lonardi
Contact Person Email
sara.lonardi@iov.veneto.it
Site Name
Ospedale San Raffaele S.r.l.
Department Name
Chirurgia gastro-enterologica
Contact Person Name
Ugo Elmore
Contact Person Email
elmore.ugo@hsr.it
Site Name
Sant Andrea Hospital
Department Name
Oncologia
Contact Person Name
carlo Aschele
Contact Person Email
carlo.aschele@asl5.liguria.it
Site Name
Azienda Ospedaliera Regionale San Carlo
Department Name
Unità Operativa di Oncologia Medica - Azienda Ospedaliera S.Carlo
Contact Person Name
Domenico Bilancia
Contact Person Email
domenicobilancia@gmail.com
Site Name
Azienda Socio Sanitaria Territoriale Di Bergamo Ovest
Department Name
U.O. Oncologia Medica Osp. Treviglio
Contact Person Name
Petrelli Fausto
Contact Person Email
faustopetrelli@gmail.com
Site Name
Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
Department Name
UO Chirurgia tratto alimentare e urgenza
Contact Person Name
Gilberto Poggioli
Contact Person Email
cuicchidajana@gmail.com
Site Name
Azienda Ospedaliero-Universitaria Di Cagliari
Department Name
Oncologia Medica -AOU Cagliari - Policlinico Universitario "Duilio Casula Monserrato"
Contact Person Name
Mario Scartozzi
Contact Person Email
marioscartozzi@gmail.com
Site Name
Fondazione IRCCS San Gerardo Dei Tintori
Department Name
Oncologia Medica
Contact Person Name
Alessandro Guidi
Contact Person Email
alessandro.guidi@asst-monza.it
Site Name
Azienda Ospedaliero Universitaria Di Modena
Department Name
SSD DH Oncologico Policlinico di Modena -AOU Modena
Contact Person Name
Fabio Gelsomino
Contact Person Email
gelsomino.fabio@aou.mo.it
Site Name
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico
Department Name
Oncologia Medica IRCCS Ca' Granda Osp. Maggiore
Contact Person Name
Angela Damato
Site Name
Ospedale San Giovanni Bosco
Department Name
SC Oncologia Medica
Contact Person Name
Cristiano Oliva
Contact Person Email
cristiano.oliva@gmail.com
Site Name
Ospedale Isola Tiberina Gemelli Isola
Department Name
UOC di Oncologia
Contact Person Name
Domenico Cristiano Corsi
Contact Person Email
domenico.corsi@libero.it
Site Name
Azienda Ospedaliero-Universitaria Maggiore Della Carita
Department Name
SCDU Oncologia - AOU Maggiore della Carità - Novara
Contact Person Name
Alessandra Gennari
Contact Person Email
alessandra.gennari@uniupo.it
Site Name
Azienda Socio Sanitaria Territoriale Della Valtellina E Dell Alto Lario
Department Name
Oncologia Medica - Ospedale di Sondrio
Contact Person Name
Alessandro Bertolini
Site Name
Ospedale Santa Maria della Misericordia
Department Name
Dipartimento di Oncologia - ASU FC S. Maria della Misericordia -Udine
Contact Person Name
Nicoletta Pella
Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
UOC Servizio di Radioterapia Oncologica Gemelli
Contact Person Name
Maria Antonietta Gambacorta
Site Name
Ospedale San Vincenzo Taormina
Department Name
Oncologia Medica
Contact Person Name
Francesco Ferrau'
Contact Person Email
ferrau@oncologiataormina.it
Site Name
Azienda Sanitaria Locale Della Provincia Di Biella
Department Name
SC Oncologia
Contact Person Name
Myriam Katja Paris
Site Name
Fondazione IRCCS Istituto Nazionale Dei Tumori
Department Name
Tumori ereditari dell'apparato digerente
Contact Person Name
Marco Vitellaro
Site Name
Istituto Tumori Bari Giovanni Paolo II
Department Name
Chirurgia Generale
Contact Person Name
Raffaele De Luca
Contact Person Email
dr.raffaele.deluca@gmail.com
Site Name
Azienda Sanitaria Locale TO3
Department Name
Chirugia Generale Ospedale Agnelli
Contact Person Name
Andrea Muratore
Contact Person Email
amuratore67@gmail.com
Site Name
Ospedale ' Civile Maria Paterno' Arezzo
Department Name
Oncologia Medica P.O. Maria Paternò Arezzo dell’ASP di Ragusa
Contact Person Name
Stefano Cordio
Contact Person Email
stefano.cordio@asp.rg.it
Site Name
Ospedale S G Moscati
Department Name
Oncologia
Contact Person Name
Salvatore Pisconti
Site Name
IRCCS Istituto Nazionale Tumori Fondazione Pascale (SSD Chirurgia robotica addominale)
Department Name
SSD Chirurgia robotica addominale_
Contact Person Name
Ugo Pace
Contact Person Email
u.pace@istitutotumori.na.it

Sponsor

Primary sponsor

Full Name
IRCCS Istituto Nazionale Tumori Fondazione Pascale
Organisation Type
Hospital/Clinic/Other health care facility
Country Of Registered Address
Italy

Investigational products

Investigational Product Name
CAPECITABINE
Active Substance
CAPECITABINE
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
ORAL
Maximum Dose
2000 mg (maxDailyDoseAmount)
Investigational Product Name
METFORMIN
Active Substance
METFORMIN EMBONATE
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
ORAL
Maximum Dose
1700 mg (maxDailyDoseAmount)
Investigational Product Name
ACETYLSALICYLIC ACID (CARBASALATE CALCIUM)
Active Substance
CARBASALATE CALCIUM
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
ORAL
Maximum Dose
100 mg (maxDailyDoseAmount)
Investigational Product Name
OXALIPLATIN
Active Substance
OXALIPLATIN
Modality
Small molecule
Routes Of Administration
INTRAVENOUS USE
Route
INTRAVENOUS
Maximum Dose
130 mg/m2 (maxDailyDoseAmount)
Combination Treatment
Yes

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