Clinical trial • Phase III • Oncology

CAMIZESTRANT for Estrogen receptor-positive, HER2-negative advanced breast cancer

Phase III trial of CAMIZESTRANT for Estrogen receptor-positive, HER2-negative advanced breast cancer.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Estrogen receptor-positive, HER2-negative advanced breast cancer
Trial Stage
Phase III
Drug Modality
Small molecule | Peptide/protein/enzyme

Key dates

Initial CTIS Submission Date
31-01-2024
First CTIS Authorization Date
13-03-2024

Trial design

Randomised, test arm: azd9833 (camizestrant) oral (max daily dose indicated 75 mg) plus palbociclib (oral; max daily dose indicated 125 mg). comparator arm: anastrozole (arimidex®) 1 mg oral daily plus palbociclib (oral; max daily dose indicated 125 mg). placebo to match camizestrant and placebo to match arimidex are listed for blinding.-controlled Phase III trial in Norway, Belgium, Czechia and others.

Randomised
Yes
Comparator
Test arm: AZD9833 (camizestrant) oral (max daily dose indicated 75 mg) plus palbociclib (oral; max daily dose indicated 125 mg). Comparator arm: Anastrozole (Arimidex®) 1 mg oral daily plus palbociclib (oral; max daily dose indicated 125 mg). Placebo to match camizestrant and placebo to match Arimidex are listed for blinding.
Target Sample Size
822

Eligibility

Recruits 822 adults.

Pregnancy Exclusion
Currently pregnant (confirmed with positive pregnancy test) or breastfeeding.

Inclusion criteria

  • {"criterion_text":"- Pre-/peri-menopausal women or men can be enrolled if amenable to be treated with concomitant, approved LHRH agonists for the duration of the study treatment."}
  • {"criterion_text":"- De novo Stage 4 disease, or recurrence from early stage disease after at least 24 months of standard adjuvant endocrine therapy. Note that at least 12 months must have elapsed since the patient's last dose of adjuvant AI therapy without disease progression on treatment. Note that a 2-week washout period is required after the last dose of tamoxifen prior to randomisation."}
  • {"criterion_text":"- Histologically or cytologically documented diagnosis of ER+, HER2- negative breast cancer based on local laboratory results."}
  • {"criterion_text":"- Previously untreated with any systemic anti-cancer therapy for their locoregionally recurrent or metastatic ER+ disease."}
  • {"criterion_text":"- Measurable disease as defined per RECIST v.1.1 OR at least one lytic or mixed (lytic + sclerotic) bone lesion with a soft tissue component that can be assessed by CT or MRI."}
  • {"criterion_text":"- Eastern Cooperative Oncology Group performance status of 0 or 1."}
  • {"criterion_text":"- Adequate organ and marrow function."}
  • {"criterion_text":"- Willingness and ability to comply with scheduled visits, treatment plan, laboratory tests, and other study procedures."}

Exclusion criteria

  • {"criterion_text":"- \"Previous neoadjuvant or adjuvant treatment with an AI treatment +/- CDK4/6 inhibitor with disease recurrence while on or within 12 months of completing treatment. \""}
  • {"criterion_text":"- Prior exposure to AZD9833, other investigational SERDs/endocrine agents or fulvestrant."}
  • {"criterion_text":"- Participation in another clinical study with a study treatment or investigational medicinal device administered in the last 4 weeks prior to randomization or concurrent enrollment in another clinical study, unless it is an observational (non-interventional) clinical study or during the follow-up period of an interventional study."}
  • {"criterion_text":"- Advanced, symptomatic, visceral spread, that are at risk of lifethreatening complications in the short term and/or impending visceral crisis"}
  • {"criterion_text":"- Known active uncontrolled or symptomatic CNS metastases, carcinomatous meningitis, or leptomeningeal disease."}
  • {"criterion_text":"- Any clinically important and symptomatic heart disease."}
  • {"criterion_text":"- Currently pregnant (confirmed with positive pregnancy test) or breastfeeding."}
  • {"criterion_text":"- As judged by the investigator, any evidence of diseases (such as severe or uncontrolled systemic diseases, renal transplant and active bleeding diseases) which, in the investigator's opinion, makes it undesirable for the participant to participate in the study or that would jeopardize compliance with the protocol."}
  • {"criterion_text":"- Any concurrent anti-cancer treatment."}
  • {"criterion_text":"- Active infection including tuberculosis, HBV and HCV."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Progression-free survival (PFS) assessed by the Investigator as defined by response evaluation criteria in solid tumors (RECIST) version 1.1.","definition_or_measurement_approach":"Assessed by the Investigator per RECIST version 1.1"}

Secondary endpoints

  • {"endpoint_text":"- \"Overall survival (OS) \"","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Progression-free survival 2 (PFS2)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- \"Objective response rate (ORR) assessed by the Investigator as defined by RECIST version 1.1 \"","definition_or_measurement_approach":"Assessed by the Investigator per RECIST v1.1"}
  • {"endpoint_text":"- \"Duration of response (DoR) assessed by the Investigator as defined by RECIST version 1.1 \"","definition_or_measurement_approach":"Assessed by the Investigator per RECIST v1.1"}
  • {"endpoint_text":"- Time to second subsequent therapy (TSST)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Time to chemotherapy (TTC)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Time to first subsequent anti-cancer therapy (TFST)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Clinical benefit rate at 24 weeks (CBR24)","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Plasma concentration of AZD9833 at specified timepoints","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Change from baseline in EORTC QLQ-C30 and EORTC QLQ-BR45 scales","definition_or_measurement_approach":""}

Recruitment

Planned Sample Size
822
Recruitment Window Months
93
Consent Approach
Informed consent is obtained using subject information and informed consent forms (documents listed in the CTIS record). Country-specific ICFs and addenda are provided (adult ICFs, pregnant partner ICFs, genetic and biological sample addenda). No explicit text about assent or minor consent handling is available in the provided record.

Geography

Total Number Of Sites
101
Total Number Of Participants
499

Norway

Earliest CTIS Part Ii Submission Date
14-02-2024
Latest Decision Or Authorization Date
14-03-2024
Processing Time Days
29
Number Of Sites
1
Number Of Participants
10

Sites

Site Name
Vestre Viken HF
Department Name
Onkologisk Poliklinikk
Principal Investigator Name
Alina Porojnicu
Principal Investigator Email
alinacp@vestreviken.no
Contact Person Name
Alina Porojnicu
Contact Person Email
alinacp@vestreviken.no

Belgium

Earliest CTIS Part Ii Submission Date
14-02-2024
Latest Decision Or Authorization Date
22-03-2024
Processing Time Days
37
Number Of Sites
6
Number Of Participants
34

Sites

Site Name
Centre Hospitalier Universitaire Dinant Godinne Sainte-Elisabeth-UCL-Namur
Department Name
Medical Oncology
Principal Investigator Name
Stéphanie Henry
Principal Investigator Email
stephanie.henry@chuuclnamur.uclouvain.be
Contact Person Name
Stéphanie Henry

Czechia

Earliest CTIS Part Ii Submission Date
14-02-2024
Latest Decision Or Authorization Date
13-03-2024
Processing Time Days
28
Number Of Sites
6
Number Of Participants
35

Sites

Site Name
Fakultni Nemocnice V Motole
Department Name
Onkologická klinika
Principal Investigator Name
Kateřina Kopečková
Principal Investigator Email
katerina.kopeckova@fnmotol.cz
Contact Person Name
Kateřina Kopečková
Contact Person Email
katerina.kopeckova@fnmotol.cz

Germany

Earliest CTIS Part Ii Submission Date
14-02-2024
Latest Decision Or Authorization Date
15-03-2024
Processing Time Days
30
Number Of Sites
9
Number Of Participants
40

Sites

Site Name
MVZ Onkologie Velbert GbR
Department Name
Gemeinschaftspraxis Dres. Naser Kalhori Arnd Nusch Werner Langer
Principal Investigator Name
Arnd Nusch
Principal Investigator Email
nusch@aol.com
Contact Person Name
Arnd Nusch
Contact Person Email
nusch@aol.com

Poland

Earliest CTIS Part Ii Submission Date
14-02-2024
Latest Decision Or Authorization Date
25-03-2024
Processing Time Days
40
Number Of Sites
6
Number Of Participants
37

Sites

Site Name
Centrum Onkologii Ziemi Lubelskiej Im. Sw. Jana Z Dukli
Department Name
Oddzial Onkologii Klinicznej z Pododdzialem Chemioterapii Dziennej
Principal Investigator Name
Bozena Kukielka-Budny
Principal Investigator Email
bozena-budny@wp.pl
Contact Person Name
Bozena Kukielka-Budny
Contact Person Email
bozena-budny@wp.pl

Spain

Earliest CTIS Part Ii Submission Date
14-02-2024
Latest Decision Or Authorization Date
13-03-2024
Processing Time Days
28
Number Of Sites
11
Number Of Participants
66

Sites

Site Name
Hospital Universitario Marques De Valdecilla
Department Name
Oncology department
Principal Investigator Name
Carmen Hinojo Gonzalez
Principal Investigator Email
carmen.hinojo@scsalud.es
Contact Person Name
Carmen Hinojo Gonzalez
Contact Person Email
carmen.hinojo@scsalud.es

Italy

Earliest CTIS Part Ii Submission Date
14-02-2024
Latest Decision Or Authorization Date
25-03-2024
Processing Time Days
40
Number Of Sites
16
Number Of Participants
55

Sites

Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
Department of Medical Oncology
Principal Investigator Name
Ida Paris
Principal Investigator Email
ida_paris@yahoo.it
Contact Person Name
Ida Paris
Contact Person Email
ida_paris@yahoo.it

Austria

Earliest CTIS Part Ii Submission Date
14-02-2024
Latest Decision Or Authorization Date
27-03-2024
Processing Time Days
42
Number Of Sites
3
Number Of Participants
20

Sites

Site Name
Vorarlberger Krankenhaus-Betriebsgesellschaft mbH
Department Name
Department of Internal Medicine III
Principal Investigator Name
Margit Sandholzer
Principal Investigator Email
margit.sandholzer@lkhf.at
Contact Person Name
Margit Sandholzer
Contact Person Email
margit.sandholzer@lkhf.at

Hungary

Earliest CTIS Part Ii Submission Date
14-02-2024
Latest Decision Or Authorization Date
18-03-2024
Processing Time Days
33
Number Of Sites
9
Number Of Participants
35

Sites

Site Name
Central Hospital Of Northern Pest Military Hospital
Department Name
Onkologiai Osztaly
Principal Investigator Name
Zsuzsanna Papai
Principal Investigator Email
trial.zspapai@gmail.com
Contact Person Name
Zsuzsanna Papai
Contact Person Email
trial.zspapai@gmail.com

Bulgaria

Earliest CTIS Part Ii Submission Date
14-02-2024
Latest Decision Or Authorization Date
04-04-2024
Processing Time Days
50
Number Of Sites
6
Number Of Participants
20

Sites

Site Name
MC Nadezhda Clinical
Principal Investigator Name
Mila Petrova
Principal Investigator Email
milllapetrova@gmail.com
Contact Person Name
Mila Petrova
Contact Person Email
milllapetrova@gmail.com

France

Earliest CTIS Part Ii Submission Date
14-02-2024
Latest Decision Or Authorization Date
15-03-2024
Processing Time Days
30
Number Of Sites
12
Number Of Participants
42

Sites

Site Name
Medipole De Nancy
Department Name
Oncologie Médicale
Principal Investigator Name
Laurene Gavoille
Principal Investigator Email
l.gavoille@ilcgroupe.fr
Contact Person Name
Laurene Gavoille
Contact Person Email
l.gavoille@ilcgroupe.fr

Slovakia

Earliest CTIS Part Ii Submission Date
14-02-2024
Latest Decision Or Authorization Date
13-03-2024
Processing Time Days
28
Number Of Sites
5
Number Of Participants
45

Sites

Site Name
Fakultna Nemocnica S Poliklinikou J. A. Reimana Presov
Department Name
Outpatient care of clinical oncology
Principal Investigator Name
Jaroslava Lešková
Principal Investigator Email
leskova.j@fnsppresov.sk
Contact Person Name
Jaroslava Lešková
Contact Person Email
leskova.j@fnsppresov.sk

Portugal

Earliest CTIS Part Ii Submission Date
14-02-2024
Latest Decision Or Authorization Date
13-03-2024
Processing Time Days
29
Number Of Sites
11
Number Of Participants
60

Sites

Site Name
CCAB Centro Clinico Academico Braga Associacao
Department Name
Oncology Department
Principal Investigator Name
Marta Almeida
Principal Investigator Email
marta.almeida@hb.min-saude.pt
Contact Person Name
Marta Almeida
Contact Person Email
marta.almeida@hb.min-saude.pt

Sponsor

Primary sponsor

Full Name
AstraZeneca AB
Organisation Type
Pharmaceutical company
Country Of Registered Address
Sweden

Investigational products

Investigational Product Name
Camizestrant
Active Substance
CAMIZESTRANT
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Authorisation Status
prodAuthStatus 1
Maximum Dose
75 mg (maxDailyDoseAmount 75)
Investigational Product Name
IBRANCE (palbociclib) formulations
Active Substance
PALBOCICLIB
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Authorisation Status
prodAuthStatus 2
Dose Levels
75 mg / 100 mg / 125 mg formulations listed
Maximum Dose
125 mg (maxDailyDoseAmount 125)
Investigational Product Name
Arimidex® (anastrozole)
Active Substance
ANASTROZOLE
Modality
Small molecule
Routes Of Administration
ORAL
Route
ORAL
Authorisation Status
prodAuthStatus 2
Frequency
Daily (maxDailyDoseAmount 1 mg)
Maximum Dose
1 mg (maxDailyDoseAmount 1)
Investigational Product Name
LEUPRORELIN ACETATE
Active Substance
LEUPRORELIN ACETATE
Modality
Peptide/protein/enzyme
Routes Of Administration
INTRAMUSCULAR
Route
INTRAMUSCULAR
Authorisation Status
prodAuthStatus 2
Maximum Dose
0.13 mg (maxDailyDoseAmount 0.13)
Investigational Product Name
GOSERELIN ACETATE
Active Substance
GOSERELIN ACETATE
Modality
Peptide/protein/enzyme
Routes Of Administration
SUBCUTANEOUS
Route
SUBCUTANEOUS
Authorisation Status
prodAuthStatus 2
Maximum Dose
0.12 mg (maxDailyDoseAmount 0.12)
Investigational Product Name
Placebo to match camizestrant
Modality
Other
Investigational Product Name
Placebo to match Arimidex
Modality
Other
Combination Treatment
Yes

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