Clinical trial • Phase III • Oncology

Cabozantinib for Hepatocellular carcinoma

Phase III trial of Cabozantinib for Hepatocellular carcinoma.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Hepatocellular carcinoma
Trial Stage
Phase III
Drug Modality
Small molecule|Monoclonal antibody
Orphan Drug
Yes

Key dates

Initial CTIS Submission Date
27-09-2024
First CTIS Authorization Date
14-10-2024

Trial design

Randomised, open-label, sorafenib (nexavar 200 mg film-coated tablets) — comparator arm; dosing schedule not specified in ctis record (product information shows nexavar 200 mg tablets, max daily dose 800 mg).-controlled Phase III trial across 6 sites in Belgium, France, Hungary and others.

Randomised
Yes
Open Label
Yes
Comparator
Sorafenib (Nexavar 200 mg film-coated tablets) — comparator arm; dosing schedule not specified in CTIS record (product information shows Nexavar 200 mg tablets, max daily dose 800 mg).
Target Sample Size
575

Eligibility

Recruits 575 No vulnerable population selected (isVulnerablePopulationSelected=false). Subject information and informed consent forms are provided for adults in multiple languages; no assent procedures or special consent for minors are specified in the CTIS record..

Vulnerable Population
No vulnerable population selected (isVulnerablePopulationSelected=false). Subject information and informed consent forms are provided for adults in multiple languages; no assent procedures or special consent for minors are specified in the CTIS record.

Inclusion criteria

  • {"criterion_text":"- Histological or cytological diagnosis of HCC or clinical diagnosis of HCC in cirrhotic patients by multiphase imaging using CT or MRI per the American Association for the Study of Liver Diseases (AASLD) guidelines or European Association for the Study of the Liver (EASL 2018)"}
  • {"criterion_text":"- The subject has disease that is not amenable to a curative treatment approach (eg, transplant, surgery, ablation therapy) or locoregional therapy (eg, TACE)."}
  • {"criterion_text":"- Measurable disease per RECIST 1.1 as determined by the Investigator. Barcelona Clinic Liver Cancer (BCLC) stage Category B or C."}
  • {"criterion_text":"- Child-Pugh Score of A."}
  • {"criterion_text":"- Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1."}

Exclusion criteria

  • {"criterion_text":"- Known fibrolamellar carcinoma, sarcomatoid HCC or mixed hepatocellular cholangiocarcinoma."}
  • {"criterion_text":"- Prior systemic anticancer therapy for advanced HCC including but not limited to chemotherapy, small molecule kinase inhibitors, and ICIs. Subjects who have received local intratumoral or arterial chemotherapy are eligible. Subjects who have received any local anticancer therapy within 28 days prior to randomization are ineligible"}
  • {"criterion_text":"- Radiation therapy for bone metastasis within 2 weeks, any other external beam radiation therapy within 8 weeks prior to randomization."}
  • {"criterion_text":"- Known brain metastases or cranial epidural disease unless adequately treated with radiotherapy and/or surgery (including radiosurgery) and stable for at least 8 weeks prior to randomization."}
  • {"criterion_text":"- Concomitant anticoagulation with oral anticoagulants."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Duration of Progression Free Survival (PFS) per RECIST 1.1, by Blinded Independent Radiology Committee (BIRC) for the experimental arm (cabozantinib+atezolizumab) vs the control arm ( sorafenib)","definition_or_measurement_approach":"Per RECIST 1.1 assessed by a Blinded Independent Radiology Committee (BIRC); compares PFS for cabozantinib+atezolizumab vs sorafenib."}
  • {"endpoint_text":"- Duration of Overall Survival (OS) for the experimental arm (cabozantinib+atezolizumab) vs the control arm (sorafenib)","definition_or_measurement_approach":"Duration of overall survival (OS) comparing experimental arm (cabozantinib+atezolizumab) versus control arm (sorafenib)."}

Secondary endpoints

  • {"endpoint_text":"- PFS per RECIST 1.1 by BIRC for the single-agent cabozantinib arm vs the control arm (sorafenib)","definition_or_measurement_approach":"PFS per RECIST 1.1 as assessed by a Blinded Independent Radiology Committee (BIRC) comparing single-agent cabozantinib versus sorafenib."}

Recruitment

Planned Sample Size
575
Recruitment Window Months
87
Consent Approach
Informed consent obtained from adult participants. Subject information and informed consent forms (SIS-ICF / ICF) are provided in multiple country-specific documents and languages (examples in CTIS: French, Dutch, Hungarian, Romanian, Spanish). There are specific ICF variants labelled for adults and for pregnant partners; no assent or minor-specific consent documents are listed in the CTIS record.

Geography

Total Number Of Sites
6
Total Number Of Participants
7

Belgium

Latest Decision Or Authorization Date
14-10-2024
Number Of Sites
1
Number Of Participants
1

Sites

Site Name
Centre Hospitalier Universitaire De Liege
Department Name
Gastroenterology Department
Principal Investigator Name
Jean Delwaide
Principal Investigator Email
jean.delwaide@chuliege.be
Contact Person Name
Jean Delwaide
Contact Person Email
jean.delwaide@chuliege.be

France

Latest Decision Or Authorization Date
14-10-2024
Number Of Sites
1
Number Of Participants
1

Sites

Site Name
CHRU De Nancy
Department Name
Hepato-Gastro-Enterology
Principal Investigator Name
Jean Pierre Bronowicki
Principal Investigator Email
jp.bronowicki@chru-nancy.fr
Contact Person Name
Jean Pierre Bronowicki
Contact Person Email
jp.bronowicki@chru-nancy.fr

Hungary

Latest Decision Or Authorization Date
14-10-2024
Number Of Sites
1
Number Of Participants
1

Sites

Site Name
University Of Debrecen
Department Name
Oncologiai Klinika
Principal Investigator Name
Peter Arkosy
Principal Investigator Email
arkosy.peter@med.unideb.hu
Contact Person Name
Peter Arkosy
Contact Person Email
arkosy.peter@med.unideb.hu

Romania

Latest Decision Or Authorization Date
21-10-2024
Number Of Sites
1
Number Of Participants
2

Sites

Site Name
Institute Of Oncology Prof. Dr. Ion Chiricuta Cluj-Napoca
Department Name
Oncologie Medicala
Principal Investigator Name
Tudor-Eliade Ciuleanu
Principal Investigator Email
office@iocn.ro
Contact Person Name
Tudor-Eliade Ciuleanu
Contact Person Email
office@iocn.ro

Spain

Latest Decision Or Authorization Date
14-10-2024
Number Of Sites
2
Number Of Participants
2

Sites

Site Name
Hospital Universitario Puerta De Hierro De Majadahonda
Department Name
Gastroenterology Department
Principal Investigator Name
Jose Luis Calleja Panero
Principal Investigator Email
joseluis.calleja@uam.es
Contact Person Name
Jose Luis Calleja Panero
Contact Person Email
joseluis.calleja@uam.es
Site Name
Institut Catala D'oncologia
Department Name
Gastroenterology Department
Principal Investigator Name
Mariona Calva Campos
Principal Investigator Email
mcalvo@idibell.cat
Contact Person Name
Mariona Calva Campos
Contact Person Email
mcalvo@idibell.cat

Sponsor

Primary sponsor

Full Name
Exelixis Inc.
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Contract research organisations

Name
Icon Clinical Research Limited
Responsibilities
sponsorDuties codes: 1,12,15 (15: 'Atezolizumab PK, immunogenicity, Receive local laboratory results without processing samples'),2,5

Third parties

  • {"country":"Ireland","full_name":"Icon Clinical Research Limited","duties_or_roles":"sponsorDuties codes: 1,12,15 (15: 'Atezolizumab PK, immunogenicity, Receive local laboratory results without processing samples'),2,5","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
CABOMETYX 60 mg film-coated tablets
Active Substance
Cabozantinib
Modality
Small molecule
Routes Of Administration
Oral use
Route
Oral
Authorisation Status
Authorised (EU marketing authorisation EU/1/16/1136/006)
Dose Levels
60 mg
Maximum Dose
60.00 mg (maxDailyDoseAmount reported for this product)
Investigational Product Name
CABOMETYX 20 mg film-coated tablets
Active Substance
Cabozantinib
Modality
Small molecule
Routes Of Administration
Oral use
Route
Oral
Authorisation Status
Authorised (EU marketing authorisation EU/1/16/1136/002)
Dose Levels
20 mg
Maximum Dose
40.00 mg (maxDailyDoseAmount reported for this product)
Investigational Product Name
Tecentriq 1 200 mg concentrate for solution for infusion
Active Substance
Atezolizumab
Modality
Monoclonal antibody
Routes Of Administration
Intravenous use
Route
Intravenous
Authorisation Status
Authorised (EU marketing authorisation EU/1/17/1220/001)
Dose Levels
Concentrate for solution for infusion (1200 mg vial)
Maximum Dose
Concentration 60.00 mg/ml (as reported)
Investigational Product Name
Nexavar 200 mg film-coated tablets
Active Substance
Sorafenib
Modality
Small molecule
Routes Of Administration
Oral use
Route
Oral
Authorisation Status
Authorised (EU marketing authorisation EU/1/06/342/001)
Orphan Designation
Yes
Dose Levels
200 mg tablets
Maximum Dose
800.00 mg (maxDailyDoseAmount reported)
Combination Treatment
Yes

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