Clinical trial • Not applicable • Respiratory

BI 1015550 for Interstitial lung disease | Familial pulmonary fibrosis | Pulmonary fibrosis

Not applicable trial of BI 1015550 for Interstitial lung disease | Familial pulmonary fibrosis | Pulmonary fibrosis.

Overview

Trial Therapeutic Area
Respiratory
Trial Disease
Interstitial lung disease | Familial pulmonary fibrosis | Pulmonary fibrosis
Trial Stage
Not applicable
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
29-10-2025
First CTIS Authorization Date
03-03-2026

Trial design

Randomised, placebo matching bi 1015550 (oral matching placebo). dose/schedule for placebo not specified.-controlled Not applicable trial in Belgium, France, Germany and others.

Randomised
Yes
Comparator
Placebo matching BI 1015550 (oral matching placebo). Dose/schedule for placebo not specified.
Target Sample Size
49
Trial Duration For Participant
730

Eligibility

Recruits 49 No vulnerable population selected (isVulnerablePopulationSelected=false). Informed consent is to be provided by participants (adults); no assent or parental consent procedures are described in the CTIS record..

Vulnerable Population
No vulnerable population selected (isVulnerablePopulationSelected=false). Informed consent is to be provided by participants (adults); no assent or parental consent procedures are described in the CTIS record.

Inclusion criteria

  • {"criterion_text":"- 1. Individuals ≥40 years of age at the time of first signed informed consent at Visit 1a\n- 2. Participants must have at least 1 first-degree relative (biological parent, sibling, or child) with confirmed pulmonary fibrosis (idiopathic pulmonary fibrosis [IPF], idiopathic nonspecific interstitial pneumonia [NSIP], and/or pulmonary fibrosis due to known genetic cause [e.g. short telomere syndrome, MUC5B mutation, surfactant protein mutations])\n- 3. HRCT scan with evidence of interstitial lung abnormalities involving at least 5% of a single lung zone, or ILD, based on central evaluation.\n- 4. FVC ≥80% of predicted normal at Visit 1b\n- 5. Diffusing capacity of the lungs for carbon monoxide (DLCO) corrected for hemoglobin ≥70% of predicted normal at Visit 1b\n- 6. Further inclusion criteria apply."}

Exclusion criteria

  • {"criterion_text":"- 1. Prior known pulmonary fibrosis that, in the opinion of the Investigator, requires treatment with approved therapies\n- 2. Prebronchodilator FEV1/FVC <0.7 at Visit 1b\n- 3. HRCT findings consistent with probable or definite usual interstitial pneumonia (UIP) pattern\n- 4. Any medical condition that is known to predispose to the development of pulmonary fibrosis (e.g. known connective tissue disease)\n- 5. Prior or current use of nerandomilast, nintedanib, or pirfenidone\n- 6. Further exclusion criteria apply."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Time to physiologic or radiologic worsening of ILA/ILD (defined as: relative decline in FVC % predicted of >10% from baseline; or absolute decline in DLCO % predicted >10% from baseline; or absolute increase in weighted reticulovascular score (wRVS) >2% and total disease extent (TDE) >2.5% on chest HRCT, as measured by e-Lung Quantitative HRCT scoring, from baseline) over the whole trial","definition_or_measurement_approach":"Defined/measured as: relative decline in FVC % predicted >10% from baseline; or absolute decline in DLCO % predicted >10% from baseline; or absolute increase in wRVS >2% and TDE >2.5% on chest HRCT measured by e-Lung Quantitative HRCT scoring, from baseline, over the whole trial."}

Secondary endpoints

  • {"endpoint_text":"- Absolute change from baseline in wRVS on e-Lung Quantitative HRCT scoring at weeks 26, 52, and 104","definition_or_measurement_approach":"Measured by e-Lung Quantitative HRCT scoring at weeks 26, 52, and 104; absolute change from baseline."}
  • {"endpoint_text":"- Absolute change from baseline in TDE on e-Lung Quantitative HRCT scoring at weeks 26, 52, and 104","definition_or_measurement_approach":"Measured by e-Lung Quantitative HRCT scoring at weeks 26, 52, and 104; absolute change from baseline."}
  • {"endpoint_text":"- Absolute change from baseline in FVC (% predicted) at weeks 26, 52, and 104","definition_or_measurement_approach":"Forced vital capacity (% predicted) measured at weeks 26, 52, and 104; absolute change from baseline."}
  • {"endpoint_text":"- Absolute change from baseline in DLCO (% predicted) at weeks 26, 52, and 104","definition_or_measurement_approach":"DLCO (% predicted) measured at weeks 26, 52, and 104; absolute change from baseline."}
  • {"endpoint_text":"- Time to relative decline from baseline in FVC (% predicted) of >10% over 52 weeks and over the whole trial","definition_or_measurement_approach":"Time-to-event endpoint using relative decline in FVC % predicted >10% from baseline, assessed over 52 weeks and over the whole trial."}
  • {"endpoint_text":"- Time to absolute decline from baseline in FVC (% predicted) of >5% over 52 weeks and over the whole trial","definition_or_measurement_approach":"Time-to-event endpoint using absolute decline in FVC % predicted >5% from baseline, assessed over 52 weeks and over the whole trial."}
  • {"endpoint_text":"- Time to absolute decline from baseline in DLCO (% predicted) of >10% over 52 weeks and over the whole trial","definition_or_measurement_approach":"Time-to-event endpoint using absolute decline in DLCO % predicted >10% from baseline, assessed over 52 weeks and over the whole trial."}
  • {"endpoint_text":"- Time to absolute increase in wRVS >2% and TDE >2.5% on chest HRCT, as measured by e-Lung Quantitative HRCT scoring over 52 weeks and over the whole trial","definition_or_measurement_approach":"Time-to-event endpoint defined by absolute increase in wRVS >2% and TDE >2.5% on chest HRCT measured by e-Lung Quantitative HRCT scoring, over 52 weeks and over the whole trial."}
  • {"endpoint_text":"- Time to physiologic or radiologic worsening of ILA/ILD over 52 weeks","definition_or_measurement_approach":"As defined for the primary endpoint (decline in FVC, decline in DLCO, or increase in HRCT scores), assessed over 52 weeks."}

Recruitment

Digital Remote Recruitment
Yes
Planned Sample Size
49
Recruitment Window Months
40
Consent Approach
Informed consent is obtained from participants (adults ≥40 years). Participant information and informed consent forms are provided in multiple languages (English, Dutch, French, German, Spanish, Italian as evidenced by l1_icf-main-*.pdf documents). No assent or parental consent processes are described in the CTIS record.

Methods

  • Belgium: Recruitment materials including posters and information brochures (documents titled k2_recruitment-material-poster-be-eng, k2_recruitment-material-info-brochure-be, k1_recruitment-arrangements-icf-prr-be) — channel: printed posters and brochures; target audience: individuals with interstitial lung abnormalities and family history of pulmonary fibrosis.
  • France: Recruitment arrangements and information brochures (documents associated with entity 272889 such as k1_recruitment-arrangements-icf-pr-fr, k2_recruitment-material-information-brochure-fr) — channel: clinical-site materials and brochures; target audience: eligible high-risk individuals.
  • Germany: Advertisement visuals, digital and print, and information brochures (documents such as k2_recruitment-material-adv-poster-de, k1_recruitment-arrangements-adv-visuals-digital-de) — channel: digital and print advertising; target audience: potential participants with family history of pulmonary fibrosis.
  • Italy: GP letter and recruitment brochures (documents associated with entity 277342 such as k1_recruitment-arrangements-adv-gp-letter-it, k2_recruitment-material-info-brochure-it) — channel: general practitioner outreach and brochures; target audience: patients identified via GPs and clinical sites.
  • Spain: Recruitment posters, digital visuals and brochures (documents such as k2_recruitment-material-poster-es, k1_recruitment-arrangements-visuals-digital-es, k2_recruitment-material-info-brochure-es) — channel: posters, digital adverts and brochures; target audience: eligible individuals at clinical sites and via digital adverts.
  • Netherlands: Recruitment information brochure and local recruitment arrangements (documents associated with entity 293698 such as k2_recruitment-material-information-brochure-nl, k1_recruitment-arrangements-nl) — channel: brochures and site-level recruitment arrangements; target audience: eligible high-risk individuals.

Geography

Total Number Of Sites
20
Total Number Of Participants
28

Belgium

Earliest CTIS Part Ii Submission Date
03-02-2026
Latest Decision Or Authorization Date
04-03-2026
Processing Time Days
29
Number Of Sites
2
Number Of Participants
2

Sites

Site Name
UZ Leuven
Department Name
Department of Respiratory Medicine
Principal Investigator Name
Wim Wuyts
Principal Investigator Email
wim.wuyts@uzleuven.be
Contact Person Name
Wim Wuyts
Contact Person Email
wim.wuyts@uzleuven.be
Site Name
Cliniques Universitaires Saint-Luc
Department Name
Pulmonary Medicine
Principal Investigator Name
Antoine Froidure
Principal Investigator Email
antoine.froidure@saintluc.uclouvain.be
Contact Person Name
Antoine Froidure

France

Earliest CTIS Part Ii Submission Date
19-01-2026
Latest Decision Or Authorization Date
03-03-2026
Processing Time Days
43
Number Of Sites
5
Number Of Participants
7

Sites

Site Name
Hospices Civils De Lyon
Department Name
Service de Pneumologie
Principal Investigator Name
Vincent Cottin
Principal Investigator Email
vincent.cottin@chu-lyon.fr
Contact Person Name
Vincent Cottin
Contact Person Email
vincent.cottin@chu-lyon.fr
Site Name
Centre Hospitalier Universitaire De Lille
Department Name
Service Pneumo Immuno Allergologie
Principal Investigator Name
Lidwine Wemeau
Principal Investigator Email
lidwine.wemeau@chu-lille.fr
Contact Person Name
Lidwine Wemeau
Contact Person Email
lidwine.wemeau@chu-lille.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Centre d’Investigation Clinique - Pneumologie
Principal Investigator Name
Raphaël Borie
Principal Investigator Email
raphael.borie@aphp.fr
Contact Person Name
Raphaël Borie
Contact Person Email
raphael.borie@aphp.fr
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
Département de Pneumologie
Principal Investigator Name
Grégoire Prevot
Principal Investigator Email
prevotinvestigateur31@gmail.com
Contact Person Name
Grégoire Prevot
Site Name
Centre Hospitalier Universitaire De Rennes
Department Name
Centre Cardio-Pneumologique - Service de Pneumologie
Principal Investigator Name
Stephane Jouneau
Principal Investigator Email
stephane.jouneau@chu-rennes.fr
Contact Person Name
Stephane Jouneau
Contact Person Email
stephane.jouneau@chu-rennes.fr

Germany

Earliest CTIS Part Ii Submission Date
30-01-2026
Latest Decision Or Authorization Date
04-03-2026
Processing Time Days
33
Number Of Sites
4
Number Of Participants
4

Sites

Site Name
Krankenhaus Bethanien gGmbH
Department Name
Innere Medizin und Pneumologie, Allergologie, Schlafmedizin
Principal Investigator Name
Lars Hagmeyer
Principal Investigator Email
lars.hagmeyer@klinik-bethanien.de
Contact Person Name
Lars Hagmeyer
Site Name
Ruhrlandklinik Westdeutsches Lungenzentrum Am Universitaetsklinikum Essen gGmbH
Department Name
am Universitätsklinikum Essen gGmbH, Abteilung Pneumologie und Allergologie
Principal Investigator Name
Francesco Bonella
Principal Investigator Email
francesco.bonella@rlk.uk-essen.de
Contact Person Name
Francesco Bonella
Site Name
Lungenfachklinik
Department Name
Fachklinik für Lungenerkrankungen
Principal Investigator Name
Peter Hammerl
Principal Investigator Email
hammerl@lungenfachklinik-immenhausen.de
Contact Person Name
Peter Hammerl
Site Name
Medizinische Hochschule Hannover
Department Name
Klinik für Pneumologie/Studienzentrum
Principal Investigator Name
Jonas Christian Schupp
Principal Investigator Email
schupp.jonas@mh-hannover.de
Contact Person Name
Jonas Christian Schupp
Contact Person Email
schupp.jonas@mh-hannover.de

Italy

Earliest CTIS Part Ii Submission Date
03-02-2026
Latest Decision Or Authorization Date
03-03-2026
Processing Time Days
28
Number Of Sites
3
Number Of Participants
5

Sites

Site Name
Azienda Ospedaliera di Padova
Department Name
U.O. Pneumologia
Principal Investigator Name
Elisabetta Balestro
Principal Investigator Email
elisabetta.balestro@aopd.veneto.it
Contact Person Name
Elisabetta Balestro
Site Name
Multimedica S.p.A.
Department Name
U.O. pneumologia
Principal Investigator Name
Sergio Harari
Principal Investigator Email
sergioharari0@gmail.com
Contact Person Name
Sergio Harari
Contact Person Email
sergioharari0@gmail.com
Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
UOC di Pneumologia
Principal Investigator Name
Luca Richeldi
Principal Investigator Email
luca.richeldi@policlinicogemelli.it
Contact Person Name
Luca Richeldi

Spain

Earliest CTIS Part Ii Submission Date
20-11-2025
Latest Decision Or Authorization Date
04-03-2026
Processing Time Days
104
Number Of Sites
4
Number Of Participants
6

Sites

Site Name
Bellvitge University Hospital
Department Name
Servicio de Neumología
Principal Investigator Name
Maria Molina Molina
Principal Investigator Email
mariamolinamolina@hotmail.com
Contact Person Name
Maria Molina Molina
Contact Person Email
mariamolinamolina@hotmail.com
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Servicio Neumología
Principal Investigator Name
José Antonio Rodríguez Portal
Principal Investigator Email
josearportal@gmail.com
Contact Person Name
José Antonio Rodríguez Portal
Contact Person Email
josearportal@gmail.com
Site Name
Hospital De Galdakao Usansolo
Department Name
Servicio de Neumología
Principal Investigator Name
Myriam Aburto Barrenetxea
Principal Investigator Email
myriam.aburtobarreneche@osakidetza.eus
Contact Person Name
Myriam Aburto Barrenetxea
Site Name
Hospital Universitario De La Princesa
Department Name
Servicio Neumología
Principal Investigator Name
Claudia Valenzuela
Principal Investigator Email
claudiavale@hotmail.com
Contact Person Name
Claudia Valenzuela
Contact Person Email
claudiavale@hotmail.com

Netherlands

Earliest CTIS Part Ii Submission Date
12-02-2026
Latest Decision Or Authorization Date
03-04-2026
Processing Time Days
50
Number Of Sites
2
Number Of Participants
4

Sites

Site Name
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Department Name
Department of ILD
Principal Investigator Name
Marlies Wijsenbeek-Lourens
Principal Investigator Email
m.wijsenbeek-lourens@erasmusmc.nl
Contact Person Name
Marlies Wijsenbeek-Lourens
Site Name
Sint Antonius Ziekenhuis Stichting
Department Name
Polikliniek Longziekten
Principal Investigator Name
Marcel Veltkamp
Principal Investigator Email
m.veltkamp@antoniusziekenhuis.nl
Contact Person Name
Marcel Veltkamp

Sponsor

Primary sponsor

Full Name
Boehringer Ingelheim International GmbH
Organisation Type
Pharmaceutical company
Country Of Registered Address
Germany

Investigational products

Investigational Product Name
BI 1015550
Active Substance
BI 1015550
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
Oral
Authorisation Status
Authorised (prodAuthStatus=1)
Dose Levels
max daily dose amounts recorded: 36 mg (product PRD10442862) and 18 mg (product PRD10855744); maxTotalDoseAmount values 41328 mg and 20664 mg respectively
Maximum Dose
36 mg (one product record); 18 mg (alternative product record) - max daily dose amounts provided in product records
Investigational Product Name
Placebo matching BI 1015550
Modality
Other

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