Clinical trial • Phase III • Immunology|Rare Disease
BELUMOSUDIL MESILATE for Chronic graft versus host disease
Phase III trial of BELUMOSUDIL MESILATE for Chronic graft versus host disease.
Overview
- Trial Therapeutic Area
- Immunology|Rare Disease
- Trial Disease
- Chronic graft versus host disease
- Trial Stage
- Phase III
- Drug Modality
- Small molecule
- Paediatric Trial
- Yes
- Orphan Drug
- Yes
Key dates
- Initial CTIS Submission Date
- 05-10-2023
- First CTIS Authorization Date
- 12-02-2024
Trial design
Randomised, belumosudil in combination with corticosteroids versus placebo in combination with corticosteroids (comparator described as placebo + corticosteroids); no specific belumosudil dose/schedule stated in the ctis record for the randomized comparison-controlled Phase III trial across 70 sites in Denmark, Portugal, Germany and others.
- Randomised
- Yes
- Comparator
- Belumosudil in combination with corticosteroids versus placebo in combination with corticosteroids (comparator described as placebo + corticosteroids); no specific belumosudil dose/schedule stated in the CTIS record for the randomized comparison
- Target Sample Size
- 193
Eligibility
Recruits 193 paediatric patients.
- Pregnancy Exclusion
- Female participants who are pregnant or breastfeeding
- Vulnerable Population
- The study includes adolescents (minimum age 12 years). Consent requirements state: 'Participants or their legally authorized representative must be capable of giving signed informed consent.' Age-specific information and consent/assent documents are provided (e.g. L1-sis-icf-children, L1-sis-icf-parents, adolescent/assent forms) in multiple language versions.
Inclusion criteria
- {"criterion_text":"- Patients must be at least 12 years of age inclusive, at the time of signing the informed consent\n- Participants who have undergone allogenic HCT with newly diagnosed moderate to severe cGVHD according to NIH consensus diagnosis and staging criteria (2014)\n- Participants who require systemic treatment with corticosteroids for cGVHD\n- Participants who have not received any prior systemic treatment for cGVHD (including ECP)\n- If participants are receiving other immunosuppressive agents for the prophylaxis or treatment of acute GVHD, the dose should be under the threshold pre-defined in protocol\n- For adult participants, the body weight should be ≥40 kg. For adolescent participants, the body weight should be ≥30 kg.\n- Contraceptive use by men and women should be consistent with local regulations regarding the methods of contraception for those participating in clinical studies.\n- Participants or their legally authorized representative must be capable of giving signed informed consent"}
Exclusion criteria
- {"criterion_text":"- Active uncontrolled cytomegalovirus (CMV) and Epstein-Barr virus (EBV) infection. Infections are considered controlled if appropriate therapy has been instituted and, at the time of screening, no signs of infection worsening are present according to Investigator’s judgement\n- Received any investigational agents, or any investigational device or procedure, or prohibited therapy for this study within 28 days or 5 elimination half-lives prior to randomization, whichever is longer\n- -\tAbsolute neutrophil count (ANC) <0.5 x 109/L. The use of granulocyte-colony stimulating factor (G-CSF) is not allowed to reach this level during screening\n- Karnofsky (if aged ≥16 years)/Lansky (if aged <16 years) Performance Score of < 60\n- -\tPlatelets <25 x 109/L. Platelet transfusion is not allowed within 3 days before the screening hematological test\n- Any active, uncontrolled infections assessed to be clinically significant by the Investigator\n- Estimated Glomerular Filtration Rate (eGFR) <30 mL/min/1.73 m2 using the MDRD-4 variable formula (if aged ≥18 years) or using the Bedside Schwartz formula (if aged <18 years)\n- -\tAspartate aminotransferase (AST) and/or alanine aminotransferase (ALT) >3 x ULN without liver cGVHD or>5 × ULN with liver) cGVHD\n- Total bilirubin >1.5 × (ULN) (>3 × ULN if Gilbert syndrome)\n- Participant has forced expiratory volume in 1 second (FEV1) of predicted ≤39% or has lung score of 3 according to NIH consensus diagnostic and staging criteria (2014)\n- History or other evidence of severe illness or any other conditions that would make the participant, in the opinion of the Investigator, unsuitable for the study (such as malabsorption syndromes, poorly controlled psychiatric disease or coronary artery disease)\n- Diagnosed or treated for another malignancy other than the underlying disease allogeneic HCT was indicated for, within 3 years prior to randomization with the exception of complete resection of basal cell carcinoma or squamous cell carcinoma of the skin, an in-situ malignancy, or low risk prostate cancer after curative therapy\n- Known history of human immunodeficiency virus (HIV)\n- Active viral disease including hepatitis B virus (HBV) or hepatitis C virus (HCV)\n- -\tAny evidence (histologic, cytogenetic, molecular, hematologic, or mixed) of progressive or relapsed underlying disease after the most recent allogeneic HCT\n- Post-transplant lymphoproliferative disease within 4 weeks prior to randomization\n- Unable to swallow tablets\n- Participant not suitable for participation, whatever the reason, as judged by the Investigator, including medical or clinical conditions, or participants potentially at risk of noncompliance to study procedures\n- Female participants who are pregnant or breastfeeding\n- Unable to tolerate a prednisone equivalent dose of corticosteroids ≥ 1 mg/kg/day\n- Participant has had previous exposure to belumosudil.\n- Received any previous systemic treatment for cGVHD with the following exception: Corticosteroids for cGVHD received within 7 days prior to the planned administration of IMP only if in the interest of participant."}
Endpoints
Primary endpoints
- {"endpoint_text":"- Event-Free Survival (EFS) from the date of randomization to the date of any predefined event, whichever occurs first","definition_or_measurement_approach":"EFS measured from date of randomization to the date of any predefined event (whichever occurs first) as stated in the protocol."}
Secondary endpoints
- {"endpoint_text":"- Proportion of participants who achieve a clinically relevant reduction in mLSS of at least 6 points from baseline (Only in participants at least 18 years of age)","definition_or_measurement_approach":"Measured as proportion achieving ≥6-point reduction in modified Lee Symptom Scale (mLSS) from baseline; applicable only to participants ≥18 years."}
- {"endpoint_text":"- Demonstrate the superiority of belumosudil in combination with prednisone vs prednisone alone in durable overall response rate (ORR)","definition_or_measurement_approach":"Overall response rate (ORR) per 2014 NIH consensus response criteria; durability defined in protocol (e.g., maintained for at least 6 months as specified in other endpoints)."}
- {"endpoint_text":"- Demonstrate the superiority of belumosudil in combination with prednisone vs prednisone alone in the rate of corticosteroid withdrawal","definition_or_measurement_approach":"Proportion of participants who successfully discontinue all systemic corticosteroids for cGVHD for at least 30 days before cGVHD progression, start of new systemic treatment for cGVHD, relapse/recurrence of underlying disease, or unacceptable toxicity."}
- {"endpoint_text":"- Overall response rate (ORR)","definition_or_measurement_approach":"ORR determined according to 2014 NIH consensus response criteria (PR or CR)."}
- {"endpoint_text":"- ORR by 24 weeks","definition_or_measurement_approach":"Proportion achieving ORR within 24 weeks."}
- {"endpoint_text":"- Duration of response (DOR)","definition_or_measurement_approach":"Time from date of first response to date of cGVHD progression, start of new systemic treatment for cGVHD, or death, whichever occurs first; determined only for participants who achieved overall response (PR or CR) per 2014 NIH criteria."}
- {"endpoint_text":"- Dose reduction in corticosteroids","definition_or_measurement_approach":"Proportion or extent of reduction in daily corticosteroid dose (as defined in protocol)."}
- {"endpoint_text":"- Failure Free Survival (FFS)","definition_or_measurement_approach":"FFS defined as time from randomization to start of a new systemic treatment for cGVHD, relapse/recurrence of underlying disease, or death, whichever occurs first."}
- {"endpoint_text":"- Change in patient reported outcome (PRO)","definition_or_measurement_approach":"Change from baseline in PROMIS-GH (only participants ≥18 years) and EQ-5D-5L as specified in protocol."}
- {"endpoint_text":"- Number of participants with treatment-emergent adverse events [TEAEs], serious TEAEs, and adverse events of special interest (AESIs)","definition_or_measurement_approach":"Counts and summaries of TEAEs, serious TEAEs and AESIs per safety reporting procedures."}
- {"endpoint_text":"- The time from the date of randomization to the date of death due to any cause","definition_or_measurement_approach":"Overall survival measured from randomization to death from any cause."}
- {"endpoint_text":"- Time to Response is defined as the time from randomization to the date the patient has first response (CR or PR).","definition_or_measurement_approach":"Measured as time from randomization to first documented CR or PR per 2014 NIH criteria."}
- {"endpoint_text":"- Proportion of participants who achieve CR or PR as per NIH consensus response criteria (2014) at any time point in each involved organ and before the start of a new systemic therapy for cGVHD.","definition_or_measurement_approach":"Organ-specific response rates per 2014 NIH consensus response criteria, assessed prior to initiation of new systemic therapy for cGVHD."}
Recruitment
- Planned Sample Size
- 193
- Recruitment Window Months
- 40
- Consent Approach
- Informed consent must be signed by the participant or their legally authorized representative ('Participants or their legally authorized representative must be capable of giving signed informed consent'). Age-specific information and consent/assent materials are provided (e.g. L1-sis-icf-children, L1-sis-icf-parents, adolescent/assent forms) and multiple language versions of ICFs are included in the documents list.
Methods
- K1 recruitment arrangements and K2 recruitment materials are provided (leaflets/infographics, doctor-to-doctor referral letters); materials available in multiple languages per country-specific documentation (documents titled K1-recruitment-arrangements and K2-recruitment-material-... in the document list).
Geography
- Total Number Of Sites
- 70
- Total Number Of Participants
- 157
Denmark
- Latest Decision Or Authorization Date
- 12-02-2024
- Number Of Sites
- 3
- Number Of Participants
- 5
Sites
- Site Name
- Aarhus Universitetshospital
- Department Name
- Oncology
- Contact Person Name
- Gitte Olesen
- Contact Person Email
- gitolese@rm.dk
- Site Name
- Odense University Hospital
- Department Name
- Oncology
- Contact Person Name
- Duruta Weber
- Contact Person Email
- Duruta.Weber@rsyd.dk
- Site Name
- Rigshospitalet
- Department Name
- Oncology
- Contact Person Name
- Brian Kornblit
- Contact Person Email
- brian.thomas.kornblit@regionh.dk
Portugal
- Latest Decision Or Authorization Date
- 04-06-2024
- Number Of Sites
- 2
- Number Of Participants
- 4
Sites
- Site Name
- Hospital De Santa Maria E.P.E.
- Department Name
- Centro Hospitalar Universitario Lisboa Norte- Hospital Santa Maria (#1)
- Contact Person Name
- Joao Forjaz De Lacerda
- Contact Person Email
- jlacerda@medicina.ulisboa.pt
- Site Name
- Instituto Portugues De Oncologia Do Porto Francisco Gentil E.P.E.
- Department Name
- INSTITUITO PORTUGUES DE ONCOLOGIA DO PORTO CLIN. ONCOL. IV( #22)
- Contact Person Name
- Gil Paiva Brás
- Contact Person Email
- gil.paiva.bras@ipoporto.min-saude.pt
Germany
- Latest Decision Or Authorization Date
- 13-02-2024
- Number Of Sites
- 9
- Number Of Participants
- 20
Sites
- Site Name
- Charite Universitaetsmedizin Berlin KöR
- Department Name
- Charite-Campus Virchow-Klinikum - Universitatsmedizin Berlin / Klinik fur Padiatrie
- Contact Person Name
- Olaf Penack
- Contact Person Email
- olaf.penack@charite.de
- Site Name
- Universitaetsklinikum Tuebingen AöR
- Department Name
- Hamatologie, Onkologie, Immunologie, Rheumatologie und Pulmonologie
- Contact Person Name
- Wolfgang Bethge
- Contact Person Email
- wolfgang.bethge@med.uni-tuebingen.de
- Site Name
- Universitaetsklinikum Muenster AöR
- Department Name
- Medizinische Klinik und Poliklinik A Hamatologie, Hamostaseologie, Onkologie, Pneumologie
- Contact Person Name
- Matthias Stelljes
- Contact Person Email
- matthias.stelljes@ukmuenster.de
- Site Name
- Medical Center - University Of Freiburg
- Department Name
- Cardiology
- Contact Person Name
- Robert Zeiser
- Contact Person Email
- robert.zeiser@uniklinik-freiburg.de
- Site Name
- Universitaetsklinikum Carl Gustav Carus Dresden an der Technischen Universitaet Dresden AöR
- Department Name
- Medizinische Klinik und Poliklinik I Hamatologie, Zelltherapie und Medizinische Onkologie
- Contact Person Name
- Katharina Egger-Heidrich
- Contact Person Email
- Katharina.Heidrich@ukdd.de
- Site Name
- Universitaetsklinikum Schleswig-Holstein
- Department Name
- Klinik für Innere Medizin II / Sektion für Stammzelltransplatation und zelluläre Immuntherapie
- Contact Person Name
- Friedrich Stölzel
- Contact Person Email
- friedrich.stoelzel@uksh.de
- Site Name
- Universitaetsklinikum Regensburg AöR
- Department Name
- Innere Medizin III: Hamatologie/Onkologie
- Contact Person Name
- Daniel Wolff
- Contact Person Email
- daniel.wolff@ukr.de
- Site Name
- University Hospital Cologne AöR
- Department Name
- Klinik I - Innere Medizin
- Contact Person Name
- Udo Holtick
- Contact Person Email
- udo.holtick@uk-koeln.de
- Site Name
- University Medical Center Hamburg-Eppendorf
- Department Name
- Zentrum für Onkologie Interdisziplinäre Klinik und Poliklinik für Stammzelltransplantation
- Contact Person Name
- Silke Heidenreich
- Contact Person Email
- s.heidenreich@uke.de
Czechia
- Latest Decision Or Authorization Date
- 13-02-2024
- Number Of Sites
- 4
- Number Of Participants
- 5
Sites
- Site Name
- Fakultni Nemocnice Hradec Kralove
- Department Name
- IV. interni hematologicka klinika
- Contact Person Name
- Pavel Zak
- Contact Person Email
- pavel.zak@fnhk.cz
- Site Name
- Fakultni Nemocnice Ostrava
- Department Name
- Klinika hematoonkologie
- Contact Person Name
- Zdenek Koristek
- Contact Person Email
- zdenek.koristek@fno.cz
- Site Name
- Fakultni Nemocnice Brno
- Department Name
- Interní hematologická a onkologická klinika
- Contact Person Name
- Jiří Mayer
- Contact Person Email
- mayer.jiri@fnbrno.cz
- Site Name
- Institute Of Hematology And Blood Transfusion
- Department Name
- Ustav hematologie a krevni transfuze (#1)
- Contact Person Name
- Veronika Valkova
- Contact Person Email
- veronika.valkova@uhkt.cz
Austria
- Latest Decision Or Authorization Date
- 19-02-2024
- Number Of Sites
- 3
- Number Of Participants
- 8
Sites
- Site Name
- Ordensklinikum Linz GmbH
- Department Name
- Interne 1 - Hämatologie mit Stammzelltransplantation, Hämostaseologie und medizinische Onkologie
- Contact Person Name
- Johannes Clausen
- Contact Person Email
- johannes.clausen@ordensklinikum.at
- Site Name
- St. Anna Kinderspital GmbH
- Department Name
- Zentrum für Kinder- und Jugendheilkunde, Stammzelltransplantations-Station (1A)
- Contact Person Name
- Anita Lawitschka
- Contact Person Email
- anita.lawitschka@stanna.at
- Site Name
- Medical University Of Graz
- Department Name
- Klinische Abteilung fur Hamatologie
- Contact Person Name
- Bianca Huber-Kraßnitzer
- Contact Person Email
- bianca.huber-krassnitzer@uniklinikum.kages.at
Sweden
- Latest Decision Or Authorization Date
- 16-02-2024
- Number Of Sites
- 3
- Number Of Participants
- 7
Sites
- Site Name
- Region Skane Skanes Universitetssjukhus
- Department Name
- Department of Hematology
- Contact Person Name
- Beata Tomaszewska-Toporska
- Contact Person Email
- Beata.Tomaszewska-Toporska@skane.se
- Site Name
- Sahlgrenska University Hospital-Vastra Gotalandsregionen
- Department Name
- Department of Hematology
- Contact Person Name
- Krista Vaht
- Contact Person Email
- krista.vaht@vgregion.se
- Site Name
- Karolinska University Hospital
- Department Name
- Karolinska Comprehensive Cancer Center
- Contact Person Name
- Johan Torlen
- Contact Person Email
- johan.karlsson-torlen@regionstockholm.se
France
- Latest Decision Or Authorization Date
- 07-06-2024
- Number Of Sites
- 8
- Number Of Participants
- 20
Sites
- Site Name
- Centre Hospitalier Universitaire De Nantes
- Department Name
- Service d'Hematologie
- Contact Person Name
- Patrice Chevallier
- Contact Person Email
- patrice.chevallier@chu-nantes.fr
- Site Name
- Centre Hospitalier Universitaire De Bordeaux
- Department Name
- Hematologie clinique et Therapie cellulaire
- Contact Person Name
- Edouard Forcade
- Contact Person Email
- edouard.forcade@chu-bordeaux.fr
- Site Name
- Assistance Publique Hopitaux De Paris
- Department Name
- Département d'Hématologie Clinique et de Thérapie Cellulaire
- Contact Person Name
- Florent Malard
- Contact Person Email
- florent.malard@inserm.fr
- Site Name
- Hospices Civils De Lyon
- Department Name
- Service Hematologie Clinique
- Contact Person Name
- Helene Labussiere Wallet
- Contact Person Email
- helene.labussiere-wallet@chu-lyon.fr
- Site Name
- CHRU De Nancy
- Department Name
- Département d'hématologie
- Contact Person Name
- Maud Daveni-Piney
- Contact Person Email
- m.daveni-piney@chru-nancy.fr
- Site Name
- Assistance Publique Hopitaux De Paris (Claude Vellefaux)
- Department Name
- Service hematologie
- Contact Person Name
- David Michonneau
- Contact Person Email
- david.michonneau@aphp.fr
- Site Name
- Institut Paoli-Calmettes
- Department Name
- Departement Hematologie
- Contact Person Name
- Raynier Devillier
- Contact Person Email
- DEVILLIERR@ipc.unicancer.fr
- Site Name
- Centre Hospitalier Universitaire De Rennes
- Department Name
- Service Hematologie
- Contact Person Name
- Jean-Baptiste Mear
- Contact Person Email
- jean-baptiste.mear@chu-rennes.fr
Belgium
- Latest Decision Or Authorization Date
- 13-02-2024
- Number Of Sites
- 6
- Number Of Participants
- 15
Sites
- Site Name
- Algemeen Ziekenhuis Delta
- Department Name
- Hematology
- Contact Person Name
- Dries Deeren
- Contact Person Email
- Dries.Deeren@azdelta.be
- Site Name
- Az St-Jan Brugge-Oostende A.V.
- Contact Person Name
- Alexander Schauwvlieghe
- Contact Person Email
- Alexander.Schauwvlieghe@azsintjan.be
- Site Name
- Universitair Ziekenhuis Gent
- Department Name
- Hematology
- Contact Person Name
- Anke Delie
- Contact Person Email
- anke.delie@uzgent.be
- Site Name
- CHU De Liege
- Department Name
- Hematology
- Contact Person Name
- Evelyne Willems
- Contact Person Email
- ewillems@chuliege.be
- Site Name
- Cliniques Universitaires Saint-Luc
- Department Name
- Hematology
- Contact Person Name
- Xavier Poire
- Contact Person Email
- xavier.poire@saintluc.uclouvain.be
- Site Name
- UZ Leuven
- Department Name
- Hematology
- Contact Person Name
- Helene Schoemans
- Contact Person Email
- helene.schoemans@uzleuven.be
Italy
- Latest Decision Or Authorization Date
- 15-02-2024
- Number Of Sites
- 12
- Number Of Participants
- 27
Sites
- Site Name
- Grande Ospedale Metropolitano Bianchi Melacrino Morelli
- Department Name
- Onco-ematologico e radioterapico
- Contact Person Name
- Massimo Martino
- Contact Person Email
- massimo.martino@ospedalerc.it
- Site Name
- IRCCS Ospedale Policlinico San Martino
- Department Name
- U.O. Clinica Ematologica
- Contact Person Name
- Anna Maria Raiola
- Contact Person Email
- annamaria.raiola@hsanmartino.it
- Site Name
- Azienda Sanitaria Universitaria Friuli Centrale
- Department Name
- Ematologia
- Contact Person Name
- Francesca Patriarca
- Contact Person Email
- francesca.patriarca@asuiud.sanita.fvg.it
- Site Name
- Hospital Santa Maria Della Misericordia
- Department Name
- Ematologia
- Contact Person Name
- Antonio Pierini
- Contact Person Email
- antonio.pierini@unipg.it
- Site Name
- Azienda Ospedaliero-Universitaria Di Bologna IRCCS
- Department Name
- Ematologia
- Contact Person Name
- Francesca Bonifazi
- Contact Person Email
- francesca.bonifazi@unibo.it
- Site Name
- Ospedale San Raffaele S.r.l.
- Department Name
- Oncologia
- Contact Person Name
- Maria Teresa Lupo Stanghellini
- Contact Person Email
- lupostanghellini.mariateresa@hsr.it
- Site Name
- Azienda Ospedaliero Universitaria Delle Marche
- Department Name
- Clinica Ematologica
- Contact Person Name
- Giorgia Mancini
- Contact Person Email
- giorgia.mancini@ospedaliriuniti.marche.it
- Site Name
- Fondazione Policlinico Universitario Agostino Gemelli IRCCS
- Department Name
- Ematologia e Trapianto di cellule staminali emopoietiche
- Contact Person Name
- Simona Sica
- Contact Person Email
- simona.sica@unicatt.it
- Site Name
- Fondazione IRCCS Policlinico San Matteo
- Department Name
- SC Ematologia I
- Contact Person Name
- Nicola Polverelli
- Contact Person Email
- n.polverelli@smatteo.pv.it
- Site Name
- Humanitas Research Hospital
- Department Name
- Ematologia
- Contact Person Name
- Stefania Bramanti
- Contact Person Email
- stefania.bramanti@cancercenter.humanitas.it
- Site Name
- Azienda Ospedaliera Papa Giovanni XXIII
- Department Name
- Oncologia
- Contact Person Name
- Alessandro Rambaldi
- Contact Person Email
- arambaldi@asst-pg23.it
- Site Name
- Azienda Ospedaliera Universitaria Citta' Della Salute E Della Scienza Di Torino
- Department Name
- Ematologia
- Contact Person Name
- Benedetto Bruno
- Contact Person Email
- benedetto.bruno@unito.it
Spain
- Latest Decision Or Authorization Date
- 13-02-2024
- Number Of Sites
- 10
- Number Of Participants
- 27
Sites
- Site Name
- Hospital Universitario Y Politecnico La Fe
- Department Name
- Servicio de Hematología
- Contact Person Name
- Jaime Sanz
- Contact Person Email
- jaime.sanz@uv.es
- Site Name
- Institut Catala D'oncologia
- Department Name
- Servicio de Hematología
- Contact Person Name
- Alberto Mussetti
- Contact Person Email
- amussetti@iconcologia.net
- Site Name
- Hospital Universitario De Salamanca
- Department Name
- Servicio de Hematología
- Contact Person Name
- Lucia Lopez Corral
- Contact Person Email
- lucialopezcorral@usal.es
- Site Name
- Hospital Infantil Universitario Nino Jesus
- Department Name
- Servicio de Hematología
- Contact Person Name
- Marta Gonzalez-Vicent
- Contact Person Email
- martagonzalezvicent@gmail.com
- Site Name
- Hospital Clinic De Barcelona
- Department Name
- Servicio de Hematología
- Contact Person Name
- Carmen Martinez Muñoz
- Contact Person Email
- cmarti@clinic.cat
- Site Name
- Hospital Universitario Marques De Valdecilla
- Department Name
- Hematology Service
- Contact Person Name
- Maria Aranzazu Bermudez Rodriguez
- Contact Person Email
- maranzazu.bermudez@scsalud.es
- Site Name
- University Hospital Virgen Del Rocio S.L.
- Department Name
- Servicio de Hematología
- Contact Person Name
- Jose Antonio Perez Simon
- Contact Person Email
- josea.perez.simon.sspa@juntadeandalucia.es
- Site Name
- Hospital Universitario Regional De Malaga
- Department Name
- Servicio de Hematología
- Contact Person Name
- Maria Jesus Pascual
- Contact Person Email
- mariaj.pascual.sspa@juntadeandalucia.es
- Site Name
- Hospital Clinico Universitario De Valencia
- Department Name
- Hematology Service
- Contact Person Name
- Carlos Solano Vercet
- Contact Person Email
- carlos.solano@uv.es
- Site Name
- Hospital General Universitario Gregorio Maranon
- Department Name
- Servicio Hematología
- Contact Person Name
- Mi Kwon
- Contact Person Email
- m.kwon@salud.madrid.org
Greece
- Latest Decision Or Authorization Date
- 16-02-2024
- Number Of Sites
- 1
- Number Of Participants
- 7
Sites
- Site Name
- Geniko Nosokomeio Thessalonikis George Papanikolaou
- Department Name
- Hematology Department -BMT Unit
- Contact Person Name
- Ioanna Sakellari
- Contact Person Email
- ioannamarilena@gmail.com
Poland
- Latest Decision Or Authorization Date
- 16-02-2024
- Number Of Sites
- 5
- Number Of Participants
- 7
Sites
- Site Name
- Narodowy Instytut Onkologii Im. Marii Sklodowskiej-Curie Panstwowy Instytut Badawczy
- Department Name
- Klinika Transplantacji Szpiku i Onkohematologii
- Contact Person Name
- Sebastian Giebel
- Contact Person Email
- ktsbadaniakliniczne@io.gliwice.pl
- Site Name
- Uniwersyteckie Centrum Kliniczne
- Department Name
- Klinika Hematologii i Transplantologii
- Contact Person Name
- Agnieszka Piekarska
- Contact Person Email
- babajaga@gumed.edu.pl
- Site Name
- Uniwersytecki Szpital Dzieciecy W Krakowie
- Department Name
- Osrodek Transplantacji, Uniwersytecki Szpital Dzieciecy( #1)
- Contact Person Name
- Jolanta Gozdzik
- Contact Person Email
- jgozdzik@cm-uj.krakow.pl
- Site Name
- Samodzielny Publiczny Szpital Kliniczny Im.Adrzeja Mieleckiego Slaskiego Uniwersytetu Medycznego
- Department Name
- Oddzial Hematologii i Transplantacji Szpiku
- Contact Person Name
- Anna Koclega
- Contact Person Email
- ohits@spskm.katowice.pl
- Site Name
- Samodzielny Publiczny Szpital Kliniczny Nr 1 Im Prof. Tadeusza Sokolowskiego Pomorskiego Uniwersytetu Medycznego W Szczecinie
- Department Name
- Klinika Hematologii z Oddzialem Transplantacji Szpiku
- Contact Person Name
- Boguslaw Machalinski
- Contact Person Email
- boguslaw.machalinski@pum.edu.pl
Netherlands
- Latest Decision Or Authorization Date
- 19-02-2024
- Number Of Sites
- 4
- Number Of Participants
- 5
Sites
- Site Name
- Universitair Medisch Centrum Groningen
- Department Name
- Afdeling Hematologie
- Contact Person Name
- Goda Choi
- Contact Person Email
- c.w.choi@umcg.nl
- Site Name
- Amsterdam UMC
- Department Name
- Department of Hematology
- Contact Person Name
- Man Wai Tang
- Contact Person Email
- m.w.tang@amsterdamumc.nl
- Site Name
- Prinses Maxima Centrum voor Kinderoncologie B.V.
- Department Name
- Afdeling hematologie
- Contact Person Name
- Caroline Lindemans
- Contact Person Email
- c.a.lindemans@prinsesmaximacentrum.nl
- Site Name
- Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
- Department Name
- Afdeling hematologie
- Contact Person Name
- Annoek BROERS
- Contact Person Email
- a.broers@erasmusmc.nl
Sponsor
Primary sponsor
- Full Name
- Sanofi-Aventis Research & Development
- Organisation Type
- Pharmaceutical company
- Country Of Registered Address
- France
Contract research organisations
- Name
- Endpoint Clinical Inc.
- Responsibilities
- sponsorDuties codes: ["3"]
- Name
- Eresearchtechnology Inc.
- Responsibilities
- sponsorDuties codes: ["7"]
- Name
- ESMS Global Limited
- Responsibilities
- Centralized 24-Hour Emergency System: eSMS (sponsorDuties code: 15)
- Name
- Precision for Medicine GmbH
- Responsibilities
- sponsorDuties codes: ["4"]
- Name
- Labcorp Central Laboratory Services LP
- Responsibilities
- sponsorDuties codes: ["4"]
- Name
- Labcorp Early Development Laboratories Inc.
- Responsibilities
- sponsorDuties codes: ["4"]
Third parties
- {"country":"United States","full_name":"Endpoint Clinical Inc.","duties_or_roles":"sponsorDuties codes: [\"3\"]","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Eresearchtechnology Inc.","duties_or_roles":"sponsorDuties codes: [\"7\"]","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"ESMS Global Limited","duties_or_roles":"Centralized 24-Hour Emergency System: eSMS (sponsorDuties code: 15)","organisation_type":"Pharmaceutical company"}
- {"country":"Greece","full_name":"Bioiatriki Private Medical Polyclinic S.A.","duties_or_roles":"sponsorDuties codes: [\"4\"]","organisation_type":"Hospital/Clinic/Other health care facility"}
- {"country":"Poland","full_name":"Centrala Farmaceutyczna Cefarm S.A.","duties_or_roles":"sponsorDuties codes: [\"14\"]","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Labcorp Early Development Laboratories Inc.","duties_or_roles":"sponsorDuties codes: [\"4\"]","organisation_type":"Pharmaceutical company"}
- {"country":"Germany","full_name":"Azenta Germany GmbH","duties_or_roles":"sponsorDuties codes: [\"4\"]","organisation_type":"Pharmaceutical company"}
- {"country":"Italy","full_name":"Depo-pack S.r.l.","duties_or_roles":"sponsorDuties codes: [\"14\"]","organisation_type":"Pharmaceutical company"}
- {"country":"Spain","full_name":"Alcura Health Espana S.A.","duties_or_roles":"sponsorDuties codes: [\"14\"]","organisation_type":"Pharmaceutical company"}
- {"country":"Germany","full_name":"Precision for Medicine GmbH","duties_or_roles":"sponsorDuties codes: [\"4\"]","organisation_type":"Laboratory/Research/Testing facility"}
- {"country":"United States","full_name":"Labcorp Central Laboratory Services LP","duties_or_roles":"sponsorDuties codes: [\"4\"]","organisation_type":"Pharmaceutical company"}
- {"country":"Poland","full_name":"Centrala Farmaceutyczna Cefarm S.A. (Warsaw address)","duties_or_roles":"sponsorDuties codes: [\"14\"]","organisation_type":"Pharmaceutical company"}
- {"country":"Greece","full_name":"Peifasyn Pharmaceutical Coop Of Piraeus Ltd.","duties_or_roles":"sponsorDuties codes: [\"14\"]","organisation_type":"Pharmaceutical company"}
Investigational products
- Investigational Product Name
- SAR445761 - belumosudil
- Active Substance
- BELUMOSUDIL MESILATE
- Modality
- Small molecule
- Routes Of Administration
- ORAL
- Route
- ORAL
- Authorisation Status
- prodAuthStatus: 1
- Orphan Designation
- Yes
- Maximum Dose
- 400 mg per day (maxDailyDoseAmount: 400 mg)
- Investigational Product Name
- same excipients except no hypromellose (placebo)
- Modality
- Other
- Investigational Product Name
- PREDNISONE / PREDNISOLONE (auxiliary corticosteroid)
- Active Substance
- PREDNISOLONE
- Modality
- Small molecule
- Routes Of Administration
- ORAL
- Route
- ORAL
- Authorisation Status
- prodAuthStatus: 2 (listed as auxiliary medicinal product)
- Maximum Dose
- 1 mg/kg per day (maxDailyDoseAmount: 1; doseUom mg/Kg)
- Combination Treatment
- Yes
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