Clinical trial • Phase II/III • Immunology|Dermatology

BELIMUMAB for Systemic sclerosis-associated interstitial lung disease

Phase II/III trial of BELIMUMAB for Systemic sclerosis-associated interstitial lung disease.

Overview

Trial Therapeutic Area
Immunology|Dermatology
Trial Disease
Systemic sclerosis-associated interstitial lung disease
Trial Stage
Phase II/III
Drug Modality
Monoclonal antibody

Key dates

Initial CTIS Submission Date
01-11-2023
First CTIS Authorization Date
04-03-2024

Trial design

Randomised, treatment arm 1: belimumab 200 mg sc via syringe safety device every 7 days (±3 days). treatment arm 2: placebo sc via syringe safety device every 7 days (±3 days).-controlled, adaptive Phase II/III trial in Greece, Denmark, Finland and others.

Randomised
Yes
Comparator
Treatment arm 1: belimumab 200 mg SC via syringe safety device every 7 days (±3 days). Treatment arm 2: placebo SC via syringe safety device every 7 days (±3 days).
Adaptive
True (Independent Data Monitoring Committee (IDMC) will conduct periodic reviews of unblinded data including a futility interim analysis; controlled early access to unblinded PK/PD for model development; emergency unblinding procedures specified.)
Target Sample Size
177
Trial Duration For Participant
364

Eligibility

Recruits 177 No vulnerable population selected. Participants must be capable of giving signed informed consent. A caregiver may administer study medication if the participant is unable to self-administer. Optional sub-study consents (e.g., genetic) are handled via separate ICFs..

Pregnancy Exclusion
Female participants: A female participant is eligible to participate if she is not pregnant or breastfeeding, and one of the following conditions applies: • Is a WONCBP as defined in Appendix 4: Contraceptive and Barrier Guidance. OR • Is a WOCBP and using a contraceptive method that is highly effective, with a failure rate of <1%.
Vulnerable Population
No vulnerable population selected. Participants must be capable of giving signed informed consent. A caregiver may administer study medication if the participant is unable to self-administer. Optional sub-study consents (e.g., genetic) are handled via separate ICFs.

Inclusion criteria

  • {"criterion_text":"- 1.\t18 years of age or old1.\t18 years of age or older.\n- 2.\tDocumented diagnosis of SSc as defined by the ACR/EULAR 2013 SSc classification criteria.\n- 3.\tDiffuse cutaneous disease, defined as presence of thickened skin with mRSS >0 over at least one skin area proximal to elbows and/or knees in addition to distal areas.\n- 4.\tPresence of interstitial lung disease.\n- 5.\tEvidence for active or progressive disease\n- 6.\tParticipant has an area of uninvolved or mildly thickened skin that, in the opinion of the investigator, would allow SC injection at the abdomen or the front, middle region of the thigh.\n- 7.\tParticipant is capable and willing to self-administer the study medication or has a caregiver who is capable and willing to administer the study medication throughout the study.\n- 8.\tFemale participants: A female participant is eligible to participate if she is not pregnant or breastfeeding, and one of the following conditions applies: •\tIs a WONCBP as defined in Appendix 4: Contraceptive and Barrier Guidance. OR •\tIs a WOCBP and using a contraceptive method that is highly effective, with a failure rate of <1%.\n- 9.\tCapable of giving signed informed consent which includes compliance with the requirements and restrictions listed in the ICF and in this protocol.er."}

Exclusion criteria

  • {"criterion_text":"- 1.\tSystemic sclerosis-like illness.\n- 2.\tPulmonary arterial hypertension.\n- 3.\tSSc renal crisis within 6 months .\n- 4.\tHistory or presence of cardiovascular, respiratory, hepatic, renal, gastrointestinal, endocrine, hematologic, or neurological disorders capable of significantly altering the absorption, metabolism, or elimination of drugs; constituting a risk when taking the study intervention or interfering with the interpretation of data.\n- 5.\tObstructive pulmonary disease (pre-bronchodilator FEV1/FVC <0.7).\n- 6.\tSignificant allergies to human or murine proteins, humanized monoclonal antibodies, or contrast agents.\n- 7.\tClinically significant multiple or severe drug allergies.\n- 8.\tLymphoma, leukemia, or any malignancy within the past 5 years except for basal cell or squamous epithelial carcinomas of the skin that have been resected with no evidence of metastatic disease for 3 years.\n- 9.\tBreast cancer within the past 10 years.\n- 10.\tALT>2 x ULN.\n- 11.\tTotal bilirubin >1.5 x ULN (isolated total bilirubin >1.5 x ULN is acceptable if total bilirubin is fractionated and direct bilirubin <35%).\n- 12.\tCirrhosis or current unstable liver or biliary disease.\n- 13.\tQTc >450 msec or QTc >480 msec in participants with bundle branch block.\n- 14.\tMajor surgery (including joint surgery) within 3 months or planned during the duration of the study.\n- 15.\tAn active infection, or a history of serious infections\n- 16.\tSymptomatic herpes zoster within 3 months.\n- 17.\tConfirmed diagnosis of active TB or untreated latent TB infection.\n- 18.\tConfirmed PML or unexplained new-onset or deteriorating neurologic signs and symptoms.\n- 19.\tParticipants with PHQ-9 score ≥10 that in the opinion of a mental healthcare professional pose a serious suicide risk, or have any history of suicidal behavior in the last 6 months and/or any suicidal ideation in the last 2 months, or who in the investigator's judgment, pose a significant suicide risk.\n- 20.\tPrevious or planned major organ transplant.\n- 21.\tCytotoxic drugs such as, chlorambucil, nitrogen mustard, or other alkylating agents within 6 months.\n- 22.\tLive vaccine(s) within 30 days or plans to receive such vaccines during the study.\n- 23.\tPositive HIV antibody test.\n- 24. Serologic evidence of Hepatitis B infection based on the results of testing for HBsAg, Anti-HBc and Anti-HBs as follows: •\tPatients positive for HBsAg are excluded. •\tPatients negative for HBsAg but positive for Anti-HBc, regardless of Anti-HBs antibody status, will require clarification of their status by testing for HBV DNA. o\tif HBV DNA is detectable, patients will be excluded from participation. o\tif HBV DNA is not detectable, patients will be eligible to enroll.\n- 25.\tPositive hepatitis C antibody .\n- 26.\tHistory of a primary immunodeficiency, or hypogammaglobulinaemia (IgG <400 mg/dL), or IgA deficiency (IgA <10 mg/dL).\n- 27.\tHave a Grade 3 or greater neutropenia, defined as absolute neutrophil count <1000/mm3 (<1.0x10e9/L) based on the CTCAE v5.0."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Absolute change from baseline in FVC (mL) at Week 52.","definition_or_measurement_approach":"Absolute change from baseline in forced vital capacity (FVC) measured in mL at Week 52; change from baseline measurement of FVC."}

Secondary endpoints

  • {"endpoint_text":"- 1. Absolute change from baseline in mRSS at Week 52.\n- 2. Absolute change from baseline in FACIT-Fatigue score at Week 52.\n- 3. Time to SSc progression or death.","definition_or_measurement_approach":"1) Change from baseline in modified Rodnan skin score (mRSS) at Week 52. 2) Change from baseline in FACIT-Fatigue patient-reported score at Week 52. 3) Time-to-event endpoint measuring time to systemic sclerosis (SSc) progression or death."}

Recruitment

Registry Or Advocacy Recruitment
True (patient advocacy group mentioned: 'patient advocacy group' in K2_content for website or social medial patient advocacy group; no specific group name provided)
Digital Remote Recruitment
True (digital methods include Facebook and Instagram adverts, website/web text, online videos and eConsent/on-screen materials, study website layout and online recruitment materials).
Planned Sample Size
177
Recruitment Window Months
42
Consent Approach
Informed consent obtained via signed ICF from each participant capable of giving consent. ICFs available in multiple languages (English, French, German, Spanish, Italian, Greek, Dutch/BE variants as indicated by document translations). Optional separate consent forms for genetic and optional substudies are provided. eConsent and educational videos/onscreen text are available as part of the consent process.

Methods

  • Facebook advertisement (Advertisement for Subject Recruitment_Facebook_No CCI PI)
  • Instagram advertisement (Advertisement for Subject Recruitment_Instagram_No CCI PI)
  • Website and web text (K2_Recruitment_Study Website; K2_content for website or social medial patient advocacy group; K2_Website_No CCI PI)
  • Posters, trifold and brochures (K2_Poster; K2_Trifold; K2_Brochure website; K2_Multifold)
  • Patient letters and referral letters (K2_Patient Letter; K2_Recruitment_Referral Letter)
  • Flipcharts and welcome guides for site use (K2_Recruitment_Flipchart; K2_Flipchart; K2_Welcome Guide)
  • Videos and on-screen eConsent/educational materials (K2_Recruitment_Video Understanding Clinical Trials; UYS Video; Understanding Informed Consent and eConsent 2D Animation)
  • Recruitment arrangements and informed consent procedures documents for sites (Recruitment and Informed Consent Procedure; K1_Recruitment and Informed Consent Procedure)

Geography

Total Number Of Sites
49
Total Number Of Participants
123

Greece

Earliest CTIS Part Ii Submission Date
20-11-2023
Latest Decision Or Authorization Date
07-03-2024
Processing Time Days
108
Number Of Sites
5
Number Of Participants
15

Sites

Site Name
424 Military General Training Hospital
Department Name
Rheumatology Department
Principal Investigator Name
Periklis Vounotrypidis
Principal Investigator Email
perivoun@email.com
Contact Person Name
Periklis Vounotrypidis
Contact Person Email
perivoun@email.com
Site Name
University General Hospital Attikon
Department Name
4th Department of Internal Medicine
Principal Investigator Name
Dimitrios Boumpas
Principal Investigator Email
boumpasd@uoc.gr
Contact Person Name
Dimitrios Boumpas
Contact Person Email
boumpasd@uoc.gr
Site Name
Ippokratio General Hospital Of Thessaloniki
Department Name
4th Internal Medicine Clinic
Principal Investigator Name
Theodoros Dimitroulas
Principal Investigator Email
dimitroul@hotmail.com
Contact Person Name
Theodoros Dimitroulas
Contact Person Email
dimitroul@hotmail.com
Site Name
General University Hospital Of Larissa
Department Name
Rheumatology and Clinical Immunology
Principal Investigator Name
Dimitrios Bogdanos
Principal Investigator Email
bogdanos@med.uth.gr
Contact Person Name
Dimitrios Bogdanos
Contact Person Email
bogdanos@med.uth.gr
Site Name
University General Hospital Of Heraklion
Department Name
Pulmonology Clinic
Principal Investigator Name
Katerina Antoniou
Principal Investigator Email
kantoniou@med.uoc.gr
Contact Person Name
Katerina Antoniou
Contact Person Email
kantoniou@med.uoc.gr

Denmark

Earliest CTIS Part Ii Submission Date
20-11-2023
Latest Decision Or Authorization Date
04-03-2024
Processing Time Days
105
Number Of Sites
1
Number Of Participants
6

Sites

Site Name
Region Midtjylland
Department Name
Reumatologisk Afdeling
Principal Investigator Name
Esben Naeser
Principal Investigator Email
auhhov@rm.dk
Contact Person Name
Esben Naeser
Contact Person Email
auhhov@rm.dk

Finland

Earliest CTIS Part Ii Submission Date
05-02-2024
Latest Decision Or Authorization Date
04-03-2024
Processing Time Days
28
Number Of Sites
1
Number Of Participants
2

Sites

Site Name
Turku University Hospital
Department Name
Reumatologian ja kliinisen immunologian keskus
Principal Investigator Name
Laura Pirilä
Principal Investigator Email
etunimi.sukunimi@varha.fi
Contact Person Name
Laura Pirilä
Contact Person Email
etunimi.sukunimi@varha.fi

Belgium

Earliest CTIS Part Ii Submission Date
06-02-2024
Latest Decision Or Authorization Date
05-03-2024
Processing Time Days
28
Number Of Sites
2
Number Of Participants
10

Sites

Site Name
Universitair Ziekenhuis Gent
Department Name
Systeem Sclerose Unit
Principal Investigator Name
Vanessa Smith
Principal Investigator Email
vanessa.smith@ugent.be
Contact Person Name
Vanessa Smith
Contact Person Email
vanessa.smith@ugent.be
Site Name
Centre hospitalier universitaire de Liege
Department Name
Respiratory Medicine
Principal Investigator Name
Julien Guiot
Principal Investigator Email
j.guiot@chuliege.be
Contact Person Name
Julien Guiot
Contact Person Email
j.guiot@chuliege.be

Spain

Earliest CTIS Part Ii Submission Date
19-12-2023
Latest Decision Or Authorization Date
04-03-2024
Processing Time Days
76
Number Of Sites
10
Number Of Participants
20

Sites

Site Name
Hospital Universitario Basurto
Department Name
Reumatologia
Principal Investigator Name
María Esther Ruiz Lucea
Principal Investigator Email
MARIAESTHER.RUIZLUCEA@osakidetza.eus
Contact Person Name
María Esther Ruiz Lucea
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Medicina Interna
Principal Investigator Name
Salvador García Morillo
Principal Investigator Email
salvaymar@gmail.com
Contact Person Name
Salvador García Morillo
Contact Person Email
salvaymar@gmail.com
Site Name
Hospital Universitario Y Politecnico La Fe
Department Name
Reumatologia
Principal Investigator Name
José Andrés Román Ivorra
Principal Investigator Email
roman_jan@gva.es
Contact Person Name
José Andrés Román Ivorra
Contact Person Email
roman_jan@gva.es
Site Name
Hospital Universitario Clinico San Cecilio
Department Name
Enfermedades Autoinmunes Sistémicas
Principal Investigator Name
José Luis Callejas Rubio
Principal Investigator Email
jlcalleja@telefonica.net
Contact Person Name
José Luis Callejas Rubio
Contact Person Email
jlcalleja@telefonica.net
Site Name
Hospital De La Santa Creu I Sant Pau
Department Name
Reumatología
Principal Investigator Name
José Luis Tandaipan Jaime
Principal Investigator Email
jtandaipan@santpau.cat
Contact Person Name
José Luis Tandaipan Jaime
Contact Person Email
jtandaipan@santpau.cat
Site Name
Hospital Clinic De Barcelona
Department Name
Enfermedades Autoinmunes
Principal Investigator Name
Gerard Espinosa Garriga
Principal Investigator Email
GESPINO@clinic.cat
Contact Person Name
Gerard Espinosa Garriga
Contact Person Email
GESPINO@clinic.cat
Site Name
Hospital Universitari Vall D Hebron
Department Name
Medicina Interna
Principal Investigator Name
Alfredo Guillén del Castillo
Principal Investigator Email
alguillen@vhebron.net
Contact Person Name
Alfredo Guillén del Castillo
Contact Person Email
alguillen@vhebron.net
Site Name
Hospital Universitario La Paz
Department Name
Enfermedades Autoinmunes Sistémicas
Principal Investigator Name
Clara Itziar Soto Abánades
Principal Investigator Email
clarasoto27@gmail.com
Contact Person Name
Clara Itziar Soto Abánades
Contact Person Email
clarasoto27@gmail.com
Site Name
Complexo Hospitalario Universitario De Vigo
Department Name
Reumatologia
Principal Investigator Name
José María Pego Reigosa
Principal Investigator Email
jose.maria.pego.reigosa@sergas.es
Contact Person Name
José María Pego Reigosa
Site Name
Hospital General Universitario Gregorio Maranon
Department Name
Reumatologia
Principal Investigator Name
Julia Martínez Barrio
Principal Investigator Email
jmbarrio@salud.madrid.org
Contact Person Name
Julia Martínez Barrio
Contact Person Email
jmbarrio@salud.madrid.org

Germany

Earliest CTIS Part Ii Submission Date
19-12-2023
Latest Decision Or Authorization Date
07-03-2024
Processing Time Days
79
Number Of Sites
8
Number Of Participants
15

Sites

Site Name
Universitaetsklinikum Duesseldorf AöR
Department Name
Klinik für Rheumatologie
Principal Investigator Name
Joerg Distler
Principal Investigator Email
joerg.distler@med.uni-duesseldorf.de
Contact Person Name
Joerg Distler
Site Name
Muhlenkreiskliniken AöR
Department Name
Johannes Wesling Klinikum-Klinik für Rheumatologie und klinische Immunologie
Principal Investigator Name
Gunter Assmann
Principal Investigator Email
Gunter.Assmann@muehlenkreiskliniken.de
Contact Person Name
Gunter Assmann
Site Name
Thermalsole und Schwefelbad Bentheim GmbH
Department Name
Dermatology
Principal Investigator Name
Athanasios Tsianakas
Principal Investigator Email
a.tsianakas@fk-bentheim.de
Contact Person Name
Athanasios Tsianakas
Contact Person Email
a.tsianakas@fk-bentheim.de
Site Name
Krankenhaus Porz Am Rhein gGmbH
Department Name
Rheumatology
Principal Investigator Name
Johannes Strunk
Principal Investigator Email
j.strunk@khporz.de
Contact Person Name
Johannes Strunk
Contact Person Email
j.strunk@khporz.de
Site Name
Klinikverbund St. Antonius und St. Josef GmbH
Department Name
Innere Medizin II - Internistische Rheumatologie
Principal Investigator Name
Annette Alberding
Principal Investigator Email
annette.alberding@cellitinnen.de
Contact Person Name
Annette Alberding
Site Name
Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz KöR
Department Name
Internal Medicine |
Principal Investigator Name
Andreas Schwarting
Principal Investigator Email
schwarting@uni-mainz.de
Contact Person Name
Andreas Schwarting
Contact Person Email
schwarting@uni-mainz.de
Site Name
Universitaetsklinikum Tuebingen AöR
Department Name
Medizinische Klinik II - Rheumatologie
Principal Investigator Name
Joerg Henes
Principal Investigator Email
joerg.henes@med.uni-tuebingen.de
Contact Person Name
Joerg Henes
Site Name
Klinikverbund St. Antonius und St. Josef GmbH (additional entry)
Department Name
see site record
Principal Investigator Name
Annette Alberding
Principal Investigator Email
annette.alberding@cellitinnen.de
Contact Person Name
Annette Alberding

France

Earliest CTIS Part Ii Submission Date
20-11-2023
Latest Decision Or Authorization Date
04-03-2024
Processing Time Days
105
Number Of Sites
7
Number Of Participants
10

Sites

Site Name
Assistance Publique Hopitaux De Paris (Hôpital Cochin, service de Rhumatologie)
Department Name
Hôpital Cochin, service de Rhumatologie
Principal Investigator Name
Yannick Allanore
Principal Investigator Email
yannick.allanore@cch.aphp.fr
Contact Person Name
Yannick Allanore
Contact Person Email
yannick.allanore@cch.aphp.fr
Site Name
Centre Hospitalier Regional Et Universitaire De Brest
Department Name
Hôpital La Cavale Blanche, Service de Médecine Interne
Principal Investigator Name
Claire De Moreuil
Principal Investigator Email
claire.demoreuil@chu-brest.fr
Contact Person Name
Claire De Moreuil
Contact Person Email
claire.demoreuil@chu-brest.fr
Site Name
Assistance Publique Hopitaux De Paris (Cochin, Service de Médecine Interne)
Department Name
Hôpital Cochin, Service de Médecine Interne
Principal Investigator Name
Benjamin Chaigne
Principal Investigator Email
benjamin.chaigne@aphp.fr
Contact Person Name
Benjamin Chaigne
Contact Person Email
benjamin.chaigne@aphp.fr
Site Name
Assistance Publique Hopitaux De Paris (Hôpital pitié-salpétrière)
Department Name
Hôpital pitié-salpétrière, Service de Médecine maladies auto-immunes et systémiques
Principal Investigator Name
Zahir Amoura
Principal Investigator Email
zahir.amoura@aphp.fr
Contact Person Name
Zahir Amoura
Contact Person Email
zahir.amoura@aphp.fr
Site Name
Assistance Publique Hopitaux De Paris (Hôpital Avicenne, service de pneumologie)
Department Name
Hôpital Avicenne, service de pneumologie
Principal Investigator Name
Yurdagul Uzunhan
Principal Investigator Email
yurdagul.uzunhan@aphp.fr
Contact Person Name
Yurdagul Uzunhan
Contact Person Email
yurdagul.uzunhan@aphp.fr
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
Hôpital Rangueil, CHU Toulouse, service de médecine interne et immunologie clinique
Principal Investigator Name
Grégory Pugnet
Principal Investigator Email
pugnet.g@chu-toulouse.fr
Contact Person Name
Grégory Pugnet
Contact Person Email
pugnet.g@chu-toulouse.fr
Site Name
Assistance Publique Hopitaux De Paris (other site entry)
Department Name
see site record
Contact Person Name
other contact

Italy

Earliest CTIS Part Ii Submission Date
29-02-2024
Latest Decision Or Authorization Date
11-03-2024
Processing Time Days
11
Number Of Sites
15
Number Of Participants
45

Sites

Site Name
University Hospital Of Ferrara
Department Name
UO Reumatologia
Principal Investigator Name
Marcello Govoni
Principal Investigator Email
gvl@unife.it
Contact Person Name
Marcello Govoni
Contact Person Email
gvl@unife.it
Site Name
Fondazione IRCCS Policlinico San Matteo
Department Name
S.C. Reumatologia
Principal Investigator Name
Veronica Codullo
Principal Investigator Email
v.codullo@smatteo.pv.it
Contact Person Name
Veronica Codullo
Contact Person Email
v.codullo@smatteo.pv.it
Site Name
Asst Centro Specialistico Ortopedico Traumatologico Gaetano Pini Cto
Department Name
Day Hospital UOC Reumatologia
Principal Investigator Name
Nicoletta Del Papa
Principal Investigator Email
nicoletta.delpapa@asst-pini-cto.it
Contact Person Name
Nicoletta Del Papa
Site Name
Azienda Ospedaliero Universitaria Policlinico G Rodolico San Marco Di Catania
Department Name
Reumatologia
Principal Investigator Name
Rosario Foti
Principal Investigator Email
rosfoti5@gmail.com
Contact Person Name
Rosario Foti
Contact Person Email
rosfoti5@gmail.com
Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
UOC Reumatologia
Principal Investigator Name
Maria Antonietta D'Agostino
Contact Person Name
Maria Antonietta D'Agostino
Site Name
University Hospital Consorziale Policlinico
Department Name
UOC Reumatologia
Principal Investigator Name
Florenzo Iannone
Principal Investigator Email
florenzo.iannone@uniba.it
Contact Person Name
Florenzo Iannone
Contact Person Email
florenzo.iannone@uniba.it
Site Name
Azienda Ospedale-Universita Padova
Department Name
UOC Reumatologia
Principal Investigator Name
Elisabetta Zanatta
Principal Investigator Email
elisabetta.zanatta@unipd.it
Contact Person Name
Elisabetta Zanatta
Contact Person Email
elisabetta.zanatta@unipd.it
Site Name
Careggi University Hospital
Department Name
SODc di Reumatologia
Principal Investigator Name
Serena Guiducci
Principal Investigator Email
guiduccis@aou-careggi.toscana.it
Contact Person Name
Serena Guiducci
Site Name
Azienda Ospedaliero-Universitaria San Luigi Gonzaga
Department Name
Dipartimento Reumatologia
Principal Investigator Name
Renato Carignola
Principal Investigator Email
renatocarigno@gmail.com
Contact Person Name
Renato Carignola
Contact Person Email
renatocarigno@gmail.com
Site Name
Azienda Ospedaliero-Universitaria Di Cagliari
Department Name
UOC Reumatologia
Principal Investigator Name
Alberto Cauli
Principal Investigator Email
cauli@unica.it
Contact Person Name
Alberto Cauli
Contact Person Email
cauli@unica.it
Site Name
Azienda Ospedaliero Universitaria Integrata Verona
Department Name
Medicina Generale B
Principal Investigator Name
Elisa Tinazzi
Principal Investigator Email
elisa.tinazzi@univr.it
Contact Person Name
Elisa Tinazzi
Contact Person Email
elisa.tinazzi@univr.it
Site Name
Azienda Ospedaliera Universitaria Universita' Degli Studi Della Campania Luigi Vanvitelli
Department Name
UO Reumatologia
Principal Investigator Name
Francesco Ciccia
Principal Investigator Email
f.ciccia.napoli@gmail.com
Contact Person Name
Francesco Ciccia
Contact Person Email
f.ciccia.napoli@gmail.com
Site Name
Azienda Ospedaliero Universitaria Di Modena
Department Name
UOC Reumatologia
Principal Investigator Name
Dilia Giuggioli
Principal Investigator Email
dilia.giuggioli@unimore.it
Contact Person Name
Dilia Giuggioli
Contact Person Email
dilia.giuggioli@unimore.it
Site Name
Azienda Ospealiero Universitaria Policlinico Umberto I
Department Name
UOC Reumatologia
Principal Investigator Name
Simona Truglia
Principal Investigator Email
s.truglia@policlinicoumberto1.it
Contact Person Name
Simona Truglia
Site Name
Azienda Ospedaliero Universitaria Delle Marche
Department Name
SOD Clinica Medica
Principal Investigator Name
Gianluca Moroncini
Principal Investigator Email
g.moroncini@staff.univpm.it
Contact Person Name
Gianluca Moroncini
Contact Person Email
g.moroncini@staff.univpm.it

Sponsor

Primary sponsor

Full Name
Glaxosmithkline Research & Development Limited
Organisation Type
Pharmaceutical company
Country Of Registered Address
United Kingdom

Contract research organisations

Name
Sermes CRO
Responsibilities
patient fee reimbursement

Third parties

  • {"country":"United States","full_name":"Medqia LLC","duties_or_roles":"Imaging","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Marken LLP","duties_or_roles":"Courier for drug deliver to patient’s home","organisation_type":"Pharmaceutical company"}
  • {"country":"Germany","full_name":"Clariness GmbH","duties_or_roles":"Recruitment Support","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"Spain","full_name":"Srcl Consenur S.L.","duties_or_roles":"sharp destruction","organisation_type":"Pharmaceutical company"}
  • {"country":"Spain","full_name":"Trial Form Support S.L.","duties_or_roles":"Site Coordination Services, including data management","organisation_type":"Pharmaceutical company"}
  • {"country":"Spain","full_name":"Alcura Health Espana S.A.","duties_or_roles":"medicine product destruction","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Corevitas LLC","duties_or_roles":"Study Participant Feedback Questionaire","organisation_type":"Pharmaceutical company"}
  • {"country":"Greece","full_name":"Affidea Piraeus Biopathological","duties_or_roles":"Other (for some sites only) - HRCT + ECG + local lab assessments (if specifically required by protocol)","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"United States","full_name":"Medable Inc.","duties_or_roles":"","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Spain","full_name":"Sermes CRO","duties_or_roles":"patient fee reimbursement","organisation_type":"Pharmaceutical company"}
  • {"country":"Greece","full_name":"Bioiatriki Private Medical Polyclinic S.A.","duties_or_roles":"Other (for some sites only) - HRCT + ECG + local lab assessments (if specifically required by protocol)","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"Italy","full_name":"Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico","duties_or_roles":"study-specific assessment (pulmonary function tests) on behalf of Site “Asst Centro Specialistico Ortopedico Traumatologico Gaetano Pini Cto” in Milan (Italy)","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"United States","full_name":"WCG Clinical Inc.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"Germany","full_name":"ZALARIS Deutschland GmbH","duties_or_roles":"Reimbursement of patient fees and compensation","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"France","full_name":"Creapharm Clinical Supplies","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Greenphire LLC","duties_or_roles":"Participant travel and reimbursement","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"France","full_name":"Fm Richard Et Associes","duties_or_roles":"Reimbursement of patient fees","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United Kingdom","full_name":"Drug Development Solutions Limited","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Infinity Biologix LLC","duties_or_roles":"Study Participant Feedback Questionaire / long term storage for biological samples","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Medable Inc. (additional entry)","duties_or_roles":"","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United Kingdom","full_name":"Biocair International Limited","duties_or_roles":"Malfunction syringe return kit","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Advarra Inc.","duties_or_roles":"Adjudication committee","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"Germany","full_name":"IL-CSM Clinical Supplies Management GmbH","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"Germany","full_name":"Azenta Germany GmbH","duties_or_roles":"long term storage for biological samples","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Labcorp Early Development Laboratories Inc.","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Q2 Solutions LLC","duties_or_roles":"","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"Germany","full_name":"Azenta Germany GmbH (additional entry)","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Smithers PDS LLC","duties_or_roles":"","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Jumo Health USA Inc.","duties_or_roles":"","organisation_type":"Hospital/Clinic/Other health care facility"}
  • {"country":"United States","full_name":"Eresearchtechnology Inc.","duties_or_roles":"Spirometry","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
Benlysta 200 mg solution for injection in pre-filled syringe.
Active Substance
BELIMUMAB
Modality
Monoclonal antibody
Routes Of Administration
Subcutaneous
Route
Subcutaneous
Authorisation Status
Marketing authorisation available (EU/1/11/700/006)
Starting Dose
200 mg
Dose Levels
200 mg
Frequency
Every 7 days (±3 days)
Maximum Dose
200 mg
Investigational Product Name
Placebo for Belimumab Solution for Injection, 200 mg/mL
Modality
Other
Frequency
Every 7 days (±3 days) (matching belimumab schedule)

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