Clinical trial • Phase I • Oncology

Azacitidine for Acute myeloid leukemia|Myelodysplastic syndrome

Phase I trial of Azacitidine for Acute myeloid leukemia|Myelodysplastic syndrome. 70 participants.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Acute myeloid leukemia|Myelodysplastic syndrome
Trial Stage
Phase I
Drug Modality
Other|Small molecule|Small molecule

Key dates

Initial CTIS Submission Date
12-06-2025
First CTIS Authorization Date
26-09-2025

Trial design

Phase I trial across 5 sites in France, Spain.

Target Sample Size
70

Recruitment

Planned Sample Size
70
Recruitment Window Months
37

Geography

Total Number Of Sites
5
Total Number Of Participants
35

France

Earliest CTIS Part Ii Submission Date
19-09-2025
Latest Decision Or Authorization Date
20-04-2026
Processing Time Days
213
Number Of Sites
3
Number Of Participants
21

Sites

Site Name
Assistance Publique Hopitaux De Paris
Department Name
Hématologie
Principal Investigator Name
Emmanuel RAFFOUX
Principal Investigator Email
emmanuel.raffoux@aphp.fr
Contact Person Name
Emmanuel RAFFOUX
Contact Person Email
emmanuel.raffoux@aphp.fr
Site Name
Oncopole Claudius Regaud
Department Name
Hématologie
Principal Investigator Name
Christian RECHER
Principal Investigator Email
recher.christian@iuct-oncopole.fr
Contact Person Name
Christian RECHER
Site Name
Institut Paoli Calmettes
Department Name
Hématologie IPC4
Principal Investigator Name
Sylvain GARCIAZ
Principal Investigator Email
garciazs@ipc.unicancer.fr
Contact Person Name
Sylvain GARCIAZ
Contact Person Email
garciazs@ipc.unicancer.fr

Spain

Earliest CTIS Part Ii Submission Date
04-09-2025
Latest Decision Or Authorization Date
17-12-2025
Processing Time Days
104
Number Of Sites
2
Number Of Participants
14

Sites

Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Hematology
Principal Investigator Name
Eduardo Rodriguez Arboli
Principal Investigator Email
XXXX@XXXX.XX
Contact Person Name
Eduardo Rodriguez Arboli
Contact Person Email
XXXX@XXXX.XX
Site Name
Hospital Clinic De Barcelona
Department Name
Hematology
Principal Investigator Name
Jordi Esteve Reyner
Principal Investigator Email
jesteve@clinic.cat
Contact Person Name
Jordi Esteve Reyner
Contact Person Email
jesteve@clinic.cat

Sponsor

Primary sponsor

Full Name
Bristol-Myers Squibb Services Unlimited Company
Organisation Type
Pharmaceutical company
Country Of Registered Address
Ireland

Investigational products

Investigational Product Name
BMS-986497
Modality
Other
Investigational Product Name
Azacitidine
Active Substance
Azacitidine
Modality
Small molecule
Investigational Product Name
Venetoclax
Active Substance
Venetoclax
Modality
Small molecule
Combination Treatment
Yes

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