Clinical trial • Phase IV • Endocrinology|Ophthalmology|Immunology

Atorvastatin for Graves ophthalmopathy|Graves' disease

Phase IV trial of Atorvastatin for Graves ophthalmopathy|Graves' disease. 554 participants.

Overview

Trial Therapeutic Area
Endocrinology|Ophthalmology|Immunology
Trial Disease
Graves ophthalmopathy|Graves' disease
Trial Stage
Phase IV
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
08-12-2025
First CTIS Authorization Date
04-02-2026

Trial design

Phase IV trial across 9 sites in Sweden.

Target Sample Size
554
Trial Duration For Participant
548

Eligibility

Recruits 554 Vulnerable populations are not selected for inclusion (isVulnerablePopulationSelected: false). Exclusion includes: 'Mental inability, reluctance or language difficulties that result in difficulty understanding the meaning of participation in the trial'. Subject information and informed consent forms are listed (documents L1_SIS and ICF)..

Pregnancy Exclusion
Pregnancy, planned pregnancy within 12 months or lactation
Vulnerable Population
Vulnerable populations are not selected for inclusion (isVulnerablePopulationSelected: false). Exclusion includes: 'Mental inability, reluctance or language difficulties that result in difficulty understanding the meaning of participation in the trial'. Subject information and informed consent forms are listed (documents L1_SIS and ICF).

Inclusion criteria

  • {"criterion_text":"- Age 18–85 years"}
  • {"criterion_text":"- Diagnosis of Graves' Disease (GD):TSH < 0.1 μU/L.\tElevated free T4 (fT4) and/or free T3 (fT3). \tPositive TSH receptor antibodies (TRAb)."}
  • {"criterion_text":"- Sufficient knowledge of Swedish to understand medical information and participate in telephone or video calls."}

Exclusion criteria

  • {"criterion_text":"- Pregnancy, planned pregnancy within 12 months or lactation"}
  • {"criterion_text":"- Concurrent use of medications that interact with statins, particularly CYP3A4 inhibitors or inducers."}
  • {"criterion_text":"- Need of corticosteroid protection for planned radioiodine therapy"}
  • {"criterion_text":"- Mental inability, reluctance or language difficulties that result in difficulty understanding the meaning of participation in the trial"}
  • {"criterion_text":"- Prior treatment with statins, selenium, corticosteroids, or other immunosuppressive medications for more than 7 days within the 3 months preceding GD diagnosis."}
  • {"criterion_text":"- Existing Graves' Ophthalmopathy (GO) at the time of GD diagnosis."}
  • {"criterion_text":"- Known hypersensitivity to atorvastatin or other statins."}
  • {"criterion_text":"- Active liver disease."}
  • {"criterion_text":"- Alcohol abuse."}
  • {"criterion_text":"- Elevated liver enzymes (ASAT/ALAT > 3 times the upper normal limit in two consecutive tests)."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- The proportion of patients developing active GO after 12 months, defined as a Clinical Activity Score (CAS) ≥3. CAS is a standardized method for assessing the activity of GO.","definition_or_measurement_approach":"Defined as Clinical Activity Score (CAS) ≥3; CAS is a standardized method for assessing activity of GO."}

Secondary endpoints

  • {"endpoint_text":"- Proportion of patients developing clinical GO at 3, 6, 9, 15, and 18 months.","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Time from GD diagnosis to GO onset.","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Highest CAS recorded during the study period.","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Proportion of patients requiring interventions such as corticosteroids, orbital irradiation, or biologics (e.g., rituximab or teprotumumab).","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Change in quality-of-life scores as measured by validated tools, including GO-QoL and Thyr-Pro questionnaires, at baseline, 12 months, and 18 months.","definition_or_measurement_approach":"Measured by validated tools GO-QoL and Thyr-Pro at baseline, 12 months, and 18 months."}
  • {"endpoint_text":"- Levels of TSH-receptor antibodies (TRAb) at 12 and 18 months","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Identification of new GO-related biomarkers using proteomics and microarray analysis.","definition_or_measurement_approach":""}
  • {"endpoint_text":"- Genetic differences between responders and non-responders to atorvastatin, identified via genome-wide association studies (GWAS) and analyses of relevant single nucleotide polymorphisms (SNPs).","definition_or_measurement_approach":""}

Recruitment

Planned Sample Size
554
Recruitment Window Months
56
Consent Approach
Informed consent to be obtained from adult participants (age 18–85). Participants must have sufficient knowledge of Swedish to understand medical information and participate in telephone or video calls. Subject information and informed consent form documents are listed (L1_SIS and ICF).

Geography

Total Number Of Sites
9
Total Number Of Participants
554

Sweden

Earliest CTIS Part Ii Submission Date
26-01-2026
Latest Decision Or Authorization Date
04-02-2026
Processing Time Days
9
Number Of Sites
9
Number Of Participants
554

Sites

Site Name
Region Skane Skanes Universitetssjukhus
Department Name
VE Endokrinologi SUS Lund, Lasarettsgatan 15, 221 85 Lund
Principal Investigator Name
Erik Uddman
Principal Investigator Email
erik.uddman@skane.se
Contact Person Name
Erik Uddman
Contact Person Email
erik.uddman@skane.se
Site Name
Sahlgrenska University Hospital-Vaestra Goetalandsregionen
Department Name
Invärtesmedicin och klinisk nutrition, Vita Stråket 11, Sahlgrenska Universitetssjukhuset, Göteborg
Principal Investigator Name
Helena Filipsson Nyström
Principal Investigator Email
helena.filipsson@medic.gu.se
Contact Person Name
Helena Filipsson Nyström
Contact Person Email
helena.filipsson@medic.gu.se
Site Name
S:t Eriks Oegonsjukhus AB
Department Name
KI, St Eriks ögonsjukhus, Eugeniavägen 12, 17141 Stockholm
Principal Investigator Name
Frank Träisk
Principal Investigator Email
frank.traisk@regionstockholm.se
Contact Person Name
Frank Träisk
Site Name
Region Skane Skanes Universitetssjukhus
Department Name
VE Endokrinologi, SUS Malmö, Tora Kjellgrens gata 17, 205 02 Malmö
Principal Investigator Name
Tereza Planck
Principal Investigator Email
tereza.planck@skane.se
Contact Person Name
Tereza Planck
Contact Person Email
tereza.planck@skane.se
Site Name
Region Oerebro Laen
Department Name
Endokrinologen, Örebro universitetssjukhus
Principal Investigator Name
Jeanette Wahlberg Hughes
Principal Investigator Email
jeanette.wahlberg@oru.se
Contact Person Name
Jeanette Wahlberg Hughes
Contact Person Email
jeanette.wahlberg@oru.se
Site Name
Region Vaesterbotten
Department Name
Norrlands universitetssjukhus, Daniel Naezéns väg, 907 37 Umeå, Medicincentrum
Principal Investigator Name
Marcus Imamovic
Principal Investigator Email
marcus.imamovic@umu.se
Contact Person Name
Marcus Imamovic
Contact Person Email
marcus.imamovic@umu.se
Site Name
Region Skane Skanes Universitetssjukhus
Department Name
VE Ögonsjukvård, Skånes Universitetssjukhus, Tora Kjellgrens gata 17, 20502 Malmö
Principal Investigator Name
Sabina Andersson Geimer
Principal Investigator Email
sabina.anderssongeimer@skane.se
Contact Person Name
Sabina Andersson Geimer
Site Name
Uppsala University Hospital
Department Name
Sektionen för endokrin och diabetes, Sjukhusvägen ingång 40, Akademiska sjukhuset
Principal Investigator Name
Selwan Khamisi
Principal Investigator Email
selwan.khamisi@medsci.uu.se
Contact Person Name
Selwan Khamisi
Contact Person Email
selwan.khamisi@medsci.uu.se
Site Name
Karolinska University Hospital
Department Name
ME Endokrinologi, Karolinska vägen 37A, 17176 Stockholm
Principal Investigator Name
Ileana Botusan
Principal Investigator Email
ileana.botusan@regionstockholm.se
Contact Person Name
Ileana Botusan

Sponsor

Primary sponsor

Full Name
Region Skane
Organisation Type
Hospital/Clinic/Other health care facility
Country Of Registered Address
Sweden

Investigational products

Investigational Product Name
Atorvastatin Viatris 40 mg Filmtabletten
Active Substance
Atorvastatin
Modality
Small molecule
Routes Of Administration
Oral
Route
Oral
Authorisation Status
Authorised (marketed product)
Starting Dose
40 mg
Dose Levels
40 mg
Maximum Dose
40 mg

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