Clinical trial • Not applicable • Neurology

apixaban for Intracerebral haemorrhage|Atrial fibrillation

Not applicable trial of apixaban for Intracerebral haemorrhage|Atrial fibrillation.

Overview

Trial Therapeutic Area
Neurology
Trial Disease
Intracerebral haemorrhage|Atrial fibrillation
Trial Stage
Not applicable
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
27-09-2024
First CTIS Authorization Date
24-10-2024

Trial design

Randomised, three strategies compared: direct oac (direct oral anticoagulant — apixaban (eliquis 2.5 mg film-coated tablets) is listed among medicinal products), left atrial appendage closure (laac) using devices (e.g. watchman, amplatzer_cardiac_plug as referenced in documents), and usual care (avoiding anticoagulation and laac). dose/schedule not specified in trial documents provided.-controlled Not applicable trial in France.

Randomised
Yes
Comparator
Three strategies compared: Direct OAC (direct oral anticoagulant — apixaban (Eliquis 2.5 mg film-coated tablets) is listed among medicinal products), Left Atrial Appendage Closure (LAAC) using devices (e.g. WATCHMAN, AMPLATZER_CARDIAC_PLUG as referenced in documents), and usual care (avoiding anticoagulation and LAAC). Dose/schedule not specified in trial documents provided.
Target Sample Size
300
Trial Duration For Participant
730

Eligibility

Recruits 300 People under guardianship, trusteeship, deprived of freedom are explicitly excluded. The trial enrols adults only (older than 18). Subject information and informed consent forms for patient and caregiver are listed in trial documents (L1_ICF_patient, L1_ICF_caregiver), indicating consent is provided by the adult participant; caregiver information/consent documents are available..

Pregnancy Exclusion
Pregnancy or breastfeeding
Vulnerable Population
People under guardianship, trusteeship, deprived of freedom are explicitly excluded. The trial enrols adults only (older than 18). Subject information and informed consent forms for patient and caregiver are listed in trial documents (L1_ICF_patient, L1_ICF_caregiver), indicating consent is provided by the adult participant; caregiver information/consent documents are available.

Inclusion criteria

  • {"criterion_text":"- Adult (older than 18 years old, no upper age limit)"}
  • {"criterion_text":"- With a history of paroxysmal, persistent or long-standin g non-valvular atrial fibrillation (documented on an electrocardiogram)"}
  • {"criterion_text":"- And a CHA2DS2VASc (22) score of 2 or more who have an indication for long-term anticoagulation"}
  • {"criterion_text":"- Who suffered from a spontaneous intracerebral haemorrhage (while being treated with oral anticoagulants or not) documented with brain CT or MRI"}
  • {"criterion_text":"- More than 1 month (more precisely 30 days) before randomization (no upper delay limit)"}
  • {"criterion_text":"- For whom there is a clinical equipoise regarding the choice of the best preventive strategy to avoid future vascular events."}
  • {"criterion_text":"- Being affiliated to the Sécurité Sociale"}

Exclusion criteria

  • {"criterion_text":"- Severe chronic renal insufficiency (clearance of creatinine < 15ml/min)"}
  • {"criterion_text":"- Pre-randomisation modified Rankin (2) score of 4 or 5"}
  • {"criterion_text":"- Conditions other than atrial fibrillation for which the patient requires long term anticoagulation (for example prosthetic mechanical heart valve)"}
  • {"criterion_text":"- Serious bleeding events within the 6 months before randomisation (except for intracerebral haemorrhage)"}
  • {"criterion_text":"- Life expectancy of less than 1 year"}
  • {"criterion_text":"- Pregnancy or breastfeeding"}
  • {"criterion_text":"- Woman of childbearing age not taking effective contraception"}
  • {"criterion_text":"- People under guardianship, trusteeship, deprive of freedom"}
  • {"criterion_text":"- Any other contraindication according to the health care team"}
  • {"criterion_text":"- (Exclusion criteria related to the LAAC only): Contraindications due to local, anatomical reasons (such as thrombus in the left atrial appendage, infection with a risk of endocarditis)"}
  • {"criterion_text":"- (Exclusion criteria related to the LAAC only): Patients older than 85 years"}
  • {"criterion_text":"- (Exclusion criteria related to the LAAC only): CHA2DS2VASc score of 2 or 3"}
  • {"criterion_text":"- (Exclusion criteria related to the LAAC only): Any other contraindication according to the health care team"}
  • {"criterion_text":"- (Exclusion criteria related to the Direct OAC only): Allergy to apixaban"}
  • {"criterion_text":"- (Exclusion criteria related to the Direct OAC only): Coexisting conditions predisposing to head trauma (e.g. gait disturbances, uncontrolled seizures disorders)"}
  • {"criterion_text":"- (Exclusion criteria related to the Direct OAC only): Any other contraindication according to the health care team"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- The primary endpoint is a composite criterion including all fatal or lifethreatening and major vascular events, i.e. cardiovascular/cerebrovascular ischaemic or haemorrhagic intracranial/extracranial events within 24 months after randomization","definition_or_measurement_approach":"Composite of all fatal or life‑threatening and major vascular events (cardiovascular/cerebrovascular ischaemic or haemorrhagic intracranial/extracranial events) assessed within 24 months after randomization."}

Secondary endpoints

  • {"endpoint_text":"- Each individual component of the composite outcome at 24 month after randomization (fatal or non-fatal major vascular events, i.e. cardiovascular/cerebrovascular ischaemic or haemorrhagic intracranial/extracranial events)","definition_or_measurement_approach":"Each component of the composite outcome assessed at 24 months after randomization (fatal or non-fatal major vascular events)."}
  • {"endpoint_text":"- Death of any cause at 24 months after randomization","definition_or_measurement_approach":"All-cause mortality measured at 24 months after randomization."}
  • {"endpoint_text":"- Functional dependence scored on the modified Rankin Scale at 24 months after randomization in a shift analysis","definition_or_measurement_approach":"Modified Rankin Scale score at 24 months; analyzed as shift in distribution."}
  • {"endpoint_text":"- Health-related quality of life measured by the EQ-5D (EuroQoL) at 24 months after randomization","definition_or_measurement_approach":"EQ-5D (EuroQoL) assessment at 24 months after randomization."}
  • {"endpoint_text":"- Baseline small-vessel diseases biomarkers on brain MRI (brain microbleeds, leukoaraiosis, superficial siderosis, perivascular spaces, territorial infarcts, silent macrohaemorrhages, cortical atrophy)","definition_or_measurement_approach":"Baseline brain MRI biomarkers assessment (listing of small-vessel disease features) to describe/predict risk."}
  • {"endpoint_text":"- Complications of endovascular treatment (up to 30 days)","definition_or_measurement_approach":"Procedural complications captured up to 30 days post-procedure."}
  • {"endpoint_text":"- Overall evaluation of the success of the procedure (at 30 days)","definition_or_measurement_approach":"Overall procedural success assessed at 30 days."}

Recruitment

Planned Sample Size
300
Recruitment Window Months
133
Consent Approach
Informed consent obtained from adult participants (study includes adults only). Subject information and informed consent forms for patients and caregivers are listed in the trial documents (L1_ICF_patient, L1_ICF_caregiver, L1_ICF_patient FU). Documents include French translations of titles; explicit languages available beyond French are not specified in the provided data.

Geography

Total Number Of Sites
36
Total Number Of Participants
300

France

Earliest CTIS Part Ii Submission Date
14-10-2024
Latest Decision Or Authorization Date
30-03-2026
Processing Time Days
532
Number Of Sites
36
Number Of Participants
300

Sites

Site Name
Assistance Publique Hopitaux De Paris
Department Name
Neurology
Principal Investigator Name
Christian Denier
Principal Investigator Email
christian.denier@aphp.fr
Contact Person Name
Christian Denier
Contact Person Email
christian.denier@aphp.fr
Site Name
Centre Hospitalier Universitaire Grenoble Alpes
Department Name
Neurology
Principal Investigator Name
Olivier Detante
Principal Investigator Email
odetante@chu-grenoble.fr
Contact Person Name
Olivier Detante
Contact Person Email
odetante@chu-grenoble.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Neurology
Principal Investigator Name
Eric Jouvent
Principal Investigator Email
eric.jouvent@aphp.fr
Contact Person Name
Eric Jouvent
Contact Person Email
eric.jouvent@aphp.fr
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Neurology
Principal Investigator Name
Aymeric WITTWER
Principal Investigator Email
aymeric.wittwer@aphp.fr
Contact Person Name
Aymeric WITTWER
Contact Person Email
aymeric.wittwer@aphp.fr
Site Name
Hospital Foch
Department Name
Neurology
Principal Investigator Name
David Weisenburger-Lile
Principal Investigator Email
d.weisenburger@hopital-foch.com
Contact Person Name
David Weisenburger-Lile
Site Name
Centre Hospitalier Universitaire Amiens Picardie
Department Name
Neurology
Principal Investigator Name
Sandrine Canaple
Principal Investigator Email
Canaple.Sandrine@chu-amiens.fr
Contact Person Name
Sandrine Canaple
Contact Person Email
Canaple.Sandrine@chu-amiens.fr
Site Name
Groupement Des Hopitaux De L'Institut Catholique De Lille
Department Name
Neurology
Principal Investigator Name
Marta Pasquini
Principal Investigator Email
pasquini.marta@ghicl.net
Contact Person Name
Marta Pasquini
Contact Person Email
pasquini.marta@ghicl.net
Site Name
Centre Hospitalier Universitaire D'Angers
Department Name
Neurology
Principal Investigator Name
Sophie Godard
Principal Investigator Email
SoGodard@chu-angers.fr
Contact Person Name
Sophie Godard
Contact Person Email
SoGodard@chu-angers.fr
Site Name
Fondation A De Rothschild
Department Name
Neurology
Principal Investigator Name
Michael Obadia
Principal Investigator Email
mobadia@for.paris
Contact Person Name
Michael Obadia
Contact Person Email
mobadia@for.paris
Site Name
Centre Hospitalier Sud Francilien
Department Name
Neurology
Principal Investigator Name
Yann L'Hermitte
Principal Investigator Email
yann.lhermitte@chsf.fr
Contact Person Name
Yann L'Hermitte
Contact Person Email
yann.lhermitte@chsf.fr
Site Name
Centre Hospitalier Regional Et Universitaire De Brest
Department Name
Neurology
Principal Investigator Name
Serge Timsit
Principal Investigator Email
serge.timsit@chu-brest.fr
Contact Person Name
Serge Timsit
Contact Person Email
serge.timsit@chu-brest.fr
Site Name
Centre Hospitalier Universitaire De Nice
Department Name
Neurology
Principal Investigator Name
Barbara Casolla
Principal Investigator Email
casolla.b@chu-nice.fr
Contact Person Name
Barbara Casolla
Contact Person Email
casolla.b@chu-nice.fr
Site Name
Centre Hospitalier Universitaire De Montpellier
Department Name
Service de neurologie, Unité Neurovasculaire
Principal Investigator Name
Lucas Corti
Principal Investigator Email
l-corti@chu-montpellier.fr
Contact Person Name
Lucas Corti
Contact Person Email
l-corti@chu-montpellier.fr
Site Name
Hospices Civils De Lyon
Department Name
Service de neurologie vasculaire
Principal Investigator Name
Elodie Ong
Principal Investigator Email
elodie.ong@chu-lyon.fr
Contact Person Name
Elodie Ong
Contact Person Email
elodie.ong@chu-lyon.fr
Site Name
Centre Hospitalier Universitaire De Bordeaux
Department Name
Unité Neuro-vasculaire
Principal Investigator Name
Igor Sibon
Principal Investigator Email
igor.sibon@chu-bordeaux.fr
Contact Person Name
Igor Sibon
Contact Person Email
igor.sibon@chu-bordeaux.fr
Site Name
Centre Hospitalier Universitaire De Caen Normandie
Department Name
Neurologt
Principal Investigator Name
Emmanuel Touze
Principal Investigator Email
touze-e@chu-caen.fr
Contact Person Name
Emmanuel Touze
Contact Person Email
touze-e@chu-caen.fr
Site Name
Centre Hospitalier Regional De Marseille
Department Name
Neurologie et Unité NeuroVasculaire
Principal Investigator Name
Emmanuelle Robinet-Borgomano
Principal Investigator Email
Emmanuelle.ROBINET-BORGOMANO@ap-hm.fr
Contact Person Name
Emmanuelle Robinet-Borgomano
Site Name
University Hospital Of Clermont-Ferrand
Department Name
Unité neurovasculaire
Principal Investigator Name
Anne Ferrier
Principal Investigator Email
aferrier@chu-clermontferrand.fr
Contact Person Name
Anne Ferrier
Site Name
Groupe Hospitalier Bretagne Sud
Department Name
Neurology
Principal Investigator Name
Claire Tourtier-Bellosta
Principal Investigator Email
c.tourtierbellosta@ghbs.bzh
Contact Person Name
Claire Tourtier-Bellosta
Contact Person Email
c.tourtierbellosta@ghbs.bzh
Site Name
Centre Hospitalier Universitaire De Rennes
Department Name
Neurology
Principal Investigator Name
Stéphane Vannier
Principal Investigator Email
stephane.vannier@chu-rennes.fr
Contact Person Name
Stéphane Vannier
Contact Person Email
stephane.vannier@chu-rennes.fr
Site Name
Les Hopitaux Universitaires De Strasbourg
Department Name
Neurology
Principal Investigator Name
Valérie Wolff
Principal Investigator Email
valerie.wolff@chru-strasbourg.fr
Contact Person Name
Valérie Wolff
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
Neurology
Principal Investigator Name
Nicolas Raposo
Principal Investigator Email
raposo.n@chu-toulouse.fr
Contact Person Name
Nicolas Raposo
Contact Person Email
raposo.n@chu-toulouse.fr
Site Name
GIE Groupe hospitalier Paris Saint-Joseph/Vinci
Department Name
Neurology
Principal Investigator Name
Mathieu Zuber
Principal Investigator Email
mzuber@hpsj.fr
Contact Person Name
Mathieu Zuber
Contact Person Email
mzuber@hpsj.fr
Site Name
Centre Hospitalier Universitaire Reims
Department Name
Neurology
Principal Investigator Name
Solène Moulin
Principal Investigator Email
smoulin@chu-reims.fr
Contact Person Name
Solène Moulin
Contact Person Email
smoulin@chu-reims.fr
Site Name
Centre Hospitalier De Versailles
Department Name
Neurology
Principal Investigator Name
Fernando Pico
Principal Investigator Email
fpico@ch-versailles.fr
Contact Person Name
Fernando Pico
Contact Person Email
fpico@ch-versailles.fr
Site Name
CHRU De Nancy
Department Name
Neurology
Principal Investigator Name
Vincent Richard
Principal Investigator Email
s.richard@chru-nancy.fr
Contact Person Name
Vincent Richard
Contact Person Email
s.richard@chru-nancy.fr
Site Name
Centre Hospitalier Saint Nazaire
Department Name
Neurology
Principal Investigator Name
Pierre Agius
Principal Investigator Email
p.agius@ch-saintnazaire.fr
Contact Person Name
Pierre Agius
Contact Person Email
p.agius@ch-saintnazaire.fr
Site Name
Centre Hospitalier Et Universitaire De Limoges
Department Name
Neurology
Principal Investigator Name
Francisco Macian Montoro
Principal Investigator Email
Francisco.Macian-Montoro@chu-limoges.fr
Contact Person Name
Francisco Macian Montoro
Site Name
Centre Hospitalier De Tourcoing
Department Name
Neurology
Principal Investigator Name
Sophie Delalande
Principal Investigator Email
sdelalande@ch-tourcoing.fr
Contact Person Name
Sophie Delalande
Contact Person Email
sdelalande@ch-tourcoing.fr
Site Name
Groupe Hospitalier Universitaire Paris Psychiatrie Et Neuroscience
Department Name
Neurology
Principal Investigator Name
David Calvet
Principal Investigator Email
D.CALVET@ghu-paris.fr
Contact Person Name
David Calvet
Contact Person Email
D.CALVET@ghu-paris.fr
Site Name
Centre Hospitalier Universitaire De Lille
Department Name
Neurology
Principal Investigator Name
Charlotte Cordonnier
Principal Investigator Email
charlotte.cordonnier@chru-lille.fr
Contact Person Name
Charlotte Cordonnier
Site Name
Centre Hospitalier Universitaire De Poitiers
Department Name
Neurology
Principal Investigator Name
Matthias Lamy
Principal Investigator Email
Matthias.LAMY@chu-poitiers.fr
Contact Person Name
Matthias Lamy
Contact Person Email
Matthias.LAMY@chu-poitiers.fr
Site Name
Centre Hospitalier Universitaire De Saint Etienne
Department Name
Unité Neurovasculaire
Principal Investigator Name
Pierre Garnier
Principal Investigator Email
pierre.garnier@chu-st-etienne.fr
Contact Person Name
Pierre Garnier
Site Name
Assistance Publique Hopitaux De Paris
Department Name
Service de neurologie et d'urgence Neurovasculaire
Principal Investigator Name
Sonia Alamowitch
Principal Investigator Email
sonia.alamowitch@aphp.fr
Contact Person Name
Sonia Alamowitch
Contact Person Email
sonia.alamowitch@aphp.fr
Site Name
Centre Hospitalier Universitaire De Nantes
Department Name
Neurology
Principal Investigator Name
Benoit Guillon
Principal Investigator Email
benoit.guillon@chu-nantes.fr
Contact Person Name
Benoit Guillon
Contact Person Email
benoit.guillon@chu-nantes.fr
Site Name
Centre Hospitalier Regional Universitaire De Tours
Department Name
Neurology
Principal Investigator Name
Marco Pasi
Principal Investigator Email
m.pasi@chu-tours.fr
Contact Person Name
Marco Pasi
Contact Person Email
m.pasi@chu-tours.fr

Sponsor

Primary sponsor

Full Name
Centre Hospitalier Universitaire De Lille
Organisation Type
Hospital/Clinic/Other health care facility
Country Of Registered Address
France

Investigational products

Investigational Product Name
Eliquis 2.5 mg film-coated tablets
Active Substance
apixaban
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
ORAL
Authorisation Status
Authorised (EU marketing authorisation EU/1/11/691/013)
Maximum Dose
10 mg

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