Clinical trial • Phase I • Neurology
AP-2 for Amyotrophic lateral sclerosis | Frontotemporal dementia | Alexander disease
Phase I trial of AP-2 for Amyotrophic lateral sclerosis | Frontotemporal dementia | Alexander disease. 72 participants.
Overview
- Trial Therapeutic Area
- Neurology
- Trial Disease
- Amyotrophic lateral sclerosis | Frontotemporal dementia | Alexander disease
- Trial Stage
- Phase I
Key dates
- Initial CTIS Submission Date
- 15-11-2025
- First CTIS Authorization Date
- 10-03-2026
Trial design
Phase I trial across 1 site in Spain.
- Target Sample Size
- 72
Eligibility
Recruits 72 No vulnerable populations selected; population includes Healthy volunteers; isVulnerablePopulationSelected=false.
- Vulnerable Population
- No vulnerable populations selected; population includes Healthy volunteers; isVulnerablePopulationSelected=false
Recruitment
- Planned Sample Size
- 72
- Recruitment Window Months
- 5
Geography
- Total Number Of Sites
- 1
- Total Number Of Participants
- 72
Spain
- Earliest CTIS Part Ii Submission Date
- 24-11-2025
- Latest Decision Or Authorization Date
- 24-04-2026
- Processing Time Days
- 151
- Number Of Sites
- 1
- Number Of Participants
- 72
Sites
- Site Name
- Hospital Universitario De La Princesa
- Department Name
- Clinical pharmacology
- Principal Investigator Name
- Dolores Ochoa Mazarro
- Principal Investigator Email
- mdolores.ochoa@salud.madrid.org
- Contact Person Name
- Dolores Ochoa Mazarro
- Contact Person Email
- mdolores.ochoa@salud.madrid.org
Sponsor
Primary sponsor
- Full Name
- Molefy Pharma S.L.
- Organisation Type
- Pharmaceutical company
- Country Of Registered Address
- Spain
Investigational products
- Investigational Product Name
- AP-2
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