Clinical trial • Phase III • Haematology|Rare Disease
ANSELAMIMAB for Amyloid light-chain (AL) amyloidosis | Cardiac amyloidosis (Mayo stage IIIa)
Phase III trial of ANSELAMIMAB for Amyloid light-chain (AL) amyloidosis | Cardiac amyloidosis (Mayo stage IIIa).
Overview
- Trial Therapeutic Area
- Haematology|Rare Disease
- Trial Disease
- Amyloid light-chain (AL) amyloidosis | Cardiac amyloidosis (Mayo stage IIIa)
- Trial Stage
- Phase III
- Drug Modality
- Monoclonal antibody|Other
- Orphan Drug
- Yes
Key dates
- Initial CTIS Submission Date
- 30-04-2024
- First CTIS Authorization Date
- 13-06-2024
Trial design
Randomised, placebo: sodium chloride intravenous infusion (0.9% nacl) plus plasma cell dyscrasia treatment (cybord-based soc). active arm: cael-101 (anselamimab) intravenous infusion plus plasma cell dyscrasia treatment (cybord-based soc). dose and schedule not specified in provided documents.-controlled Phase III trial in Poland, Italy, Greece and others.
- Randomised
- Yes
- Comparator
- Placebo: SODIUM CHLORIDE intravenous infusion (0.9% NaCl) plus plasma cell dyscrasia treatment (CyBorD-based SoC). Active arm: CAEL-101 (anselamimab) intravenous infusion plus plasma cell dyscrasia treatment (CyBorD-based SoC). Dose and schedule not specified in provided documents.
- Target Sample Size
- 198
- Trial Duration For Participant
- 350
Eligibility
Recruits 198 The trial has vulnerable population selected (populationOfTrialSubjects.isVulnerablePopulationSelected = true). Informed consent is required: "Each patient will be assigned a unique identifier after signing the Informed Consent Form (ICF). Patient numbers will not be reassigned. Any patient records or datasets transferred to the Sponsor must contain only the unique identifier and must not include patient names or any information which would make the patient identifiable. Patients will be informed that their personal study-related data will be used by the Sponsor in accordance with local data protection laws and that their medical records may be examined by representatives of the Sponsor, Institutional Review Board (IRB)/Independent Ethics Committee (IEC) members and by inspectors from regulatory authorities. Study monitors will inspect all documents and records that are required to be maintained by the Investigator for this study.' Consent is provided by adult patients via the ICF; multiple language ICFs are provided (see consent languages). No separate assent procedure for minors is described in the available documents..
- Pregnancy Exclusion
- Women of childbearing potential must have a negative pregnancy test during Screening and must agree to use highly effective contraception from Screening to at least 5 months following the last study drug administration or 12 months following the last dose of her PCD therapy, whichever is longer
- Vulnerable Population
- The trial has vulnerable population selected (populationOfTrialSubjects.isVulnerablePopulationSelected = true). Informed consent is required: "Each patient will be assigned a unique identifier after signing the Informed Consent Form (ICF). Patient numbers will not be reassigned. Any patient records or datasets transferred to the Sponsor must contain only the unique identifier and must not include patient names or any information which would make the patient identifiable. Patients will be informed that their personal study-related data will be used by the Sponsor in accordance with local data protection laws and that their medical records may be examined by representatives of the Sponsor, Institutional Review Board (IRB)/Independent Ethics Committee (IEC) members and by inspectors from regulatory authorities. Study monitors will inspect all documents and records that are required to be maintained by the Investigator for this study.' Consent is provided by adult patients via the ICF; multiple language ICFs are provided (see consent languages). No separate assent procedure for minors is described in the available documents.
Inclusion criteria
- {"criterion_text":"- AL amyloidosis stage IIIa based on the European Modification of the 2004 Standard Mayo Clinic Staging who also have NT-proBNP ≥ 650 ng/L at the time of Screening\n- Measurable hematologic disease at Screening as defined by at least one of the following: a. Involved/uninvolved free light chain difference (dFLC) > 4 mg/dL OR b. Involved free light chain (iFLC) > 4 mg/dL with abnormal Kappa/Lambda ratio OR c. Serum protein electrophoresis (SPEP) m-spike > 0.5 g/dL\n- Histopathological diagnosis of amyloidosis based on polarizing light microscopy of green bi-refringent material in Congo red stained tissue specimens AND confirmation of AL derived amyloid deposits by at least one of the following: a. Immunohistochemistry/Immunofluorescence OR b. Mass spectrometry OR c. Characteristic electron microscopy appearance/Immunoelectron microscopy\n- Cardiac involvement as defined by: a. Documented clinical signs and symptoms supportive of a diagnosis of heart failure in the setting of a confirmed diagnosis of AL amyloidosis in the absence of an alternative explanation for heart failure AND b. At least one of the following: I. Endomyocardial biopsy demonstrating AL cardiac amyloidosis OR ii. Echocardiogram demonstrating a mean left ventricular wall thickness (calculated as [IVSd+LPWd]/2) of > 12 mm at diastole in the absence of other causes (e.g., severe hypertension, aortic stenosis), which would adequately explain the degree of wall thickening OR iii. Cardiac magnetic resonance imaging (MRI) with gadolinium contrast agent diagnostic of cardiac amyloidosis\n- Planned first-line treatment for plasma cell dyscrasia is cyclophosphamide-bortezomib-dexamethasone (CyBorD)-based regimen administered as SoC.\n- Women of childbearing potential must have a negative pregnancy test during Screening and must agree to use highly effective contraception from Screening to at least 5 months following the last study drug administration or 12 months following the last dose of her PCD therapy, whichever is longer\n- Men must be surgically sterile or must agree to use highly effective contraception and refrain from donating sperm from Screening to at least 5 months following the last study drug administration or 12 months following the last dose of their PCD therapy, whichever is longer"}
Exclusion criteria
- {"criterion_text":"- Have any other form of amyloidosis other than AL amyloidosis\n- Received prior therapy for AL amyloidosis or multiple myeloma. A maximum exposure of 2 weeks of a CyBorD-based PCD treatment after Screening laboratory samples are obtained and prior to randomization is allowed.\n- Has POEMS syndrome OR multiple myeloma defined as clonal bone marrow plasma cells > 10% from a bone marrow biopsy (performed ≤ 3 months prior to signing the ICF or during Screening) OR biopsy-proven (performed ≤ 3 months prior to signing the ICF or during Screening) bony or extramedullary plasmacytoma AND any one or more of the following CRAB features: a. Evidence of end organ damage that can be attributed to the underlying plasma cell proliferative disorder, (eg, multiple myeloma and POEMS syndrome), specifically: i. Hypercalcemia: serum calcium > 0.25 mmol/L (> 1 mg/dL) higher than the ULN or > 2.75 mmol/L (> 11 mg/dL) OR ii. Renal insufficiency: creatinine clearance < 40 mL per minute or serum creatinine > 177 μmol/L (> 2 mg/dL) OR iii. Anemia: hemoglobin value of > 20 g/L below the lowest limit of normal, or a hemoglobin value < 100 g/L OR iv. Bone lesions: one or more osteolytic lesion on imaging tests (performed ≤ 3 months prior to signing the ICF or during Screening): skeletal radiography, CT, or PET/CT, or MRI. If bone marrow has < 10% clonal plasma cells, more than one bone lesion is required to distinguish from solitary plasmacytoma with minimal marrow involvement OR b. Any one of the following biomarkers of malignancy: i. 60% or greater clonal plasma cells on bone marrow examination OR ii. More than one focal lesion on MRI that is at least 5mm or greater in size\n- Have supine systolic blood pressure < 90 mmHg or symptomatic orthostatic hypotension, defined as a decrease in systolic blood pressure upon standing of > 30 mmHg despite medical management (e.g., midodrine, fludrocortisones) in the absence of volume depletion"}
Endpoints
Primary endpoints
- {"endpoint_text":"- A hierarchical combination of time to all-cause Mortality (ACM) and the frequency of cardiovascular hospitalizations (CVH). Incidence of treatment emergent adverse events (TEAEs) and serious adverse events (SAEs). Changes from baseline in vital signs, weight, clinical laboratory tests, and 12lead electrocardiograms (ECGs).","definition_or_measurement_approach":"Hierarchical combination: time-to-event assessment for all-cause mortality (ACM) and count/frequency assessment of cardiovascular hospitalizations (CVH). Safety assessed by incidence of TEAEs and SAEs. Additional measures: changes from baseline in vital signs, weight, clinical laboratory tests, and 12-lead ECGs as recorded in clinic assessments."}
Secondary endpoints
- {"endpoint_text":"- Time to ACM in Primary Evaluation Treatment Period (PETP)","definition_or_measurement_approach":"Time-to-event analysis for all-cause mortality during the Primary Evaluation Treatment Period (PETP)."}
- {"endpoint_text":"- Frequency of CVH in PETP","definition_or_measurement_approach":"Frequency/count of cardiovascular-related hospitalizations during the PETP."}
- {"endpoint_text":"- Changes from baseline to Week 50 in the KCCQ-OS.","definition_or_measurement_approach":"Change from baseline to Week 50 in Kansas City Cardiomyopathy Questionnaire Overall Score (KCCQ-OS)."}
- {"endpoint_text":"- Change from baseline to Week 50 in NTproBNP","definition_or_measurement_approach":"Change from baseline to Week 50 in NT-proBNP biomarker levels."}
- {"endpoint_text":"- Changes from baseline to Week 50 in GLS%.","definition_or_measurement_approach":"Change from baseline to Week 50 in global longitudinal strain (GLS%)."}
- {"endpoint_text":"- Changes from baseline to Week 50 in the 6MWT","definition_or_measurement_approach":"Change from baseline to Week 50 in distance walked in the six-minute walk test (6MWT)."}
- {"endpoint_text":"- Change from baseline to Week 50 in the SF-36v2 PCS","definition_or_measurement_approach":"Change from baseline to Week 50 in the Short Form 36 Health Survey Physical Component Score (SF-36v2 PCS)."}
Recruitment
- Planned Sample Size
- 198
- Recruitment Window Months
- 77
- Consent Approach
- Informed consent is required and obtained via a signed Informed Consent Form (ICF). "Each patient will be assigned a unique identifier after signing the Informed Consent Form (ICF). Patient numbers will not be reassigned. Any patient records or datasets transferred to the Sponsor must contain only the unique identifier and must not include patient names or any information which would make the patient identifiable. Patients will be informed that their personal study-related data will be used by the Sponsor in accordance with local data protection laws and that their medical records may be examined by representatives of the Sponsor, Institutional Review Board (IRB)/Independent Ethics Committee (IEC) members and by inspectors from regulatory authorities. Study monitors will inspect all documents and records that are required to be maintained by the Investigator for this study.' ICFs and patient information are provided in multiple languages (examples in the dossier: English, German, Greek, Polish, Spanish, French, Italian, Czech). No separate assent process for minors is described in the available documents.
Geography
- Total Number Of Sites
- 37
- Total Number Of Participants
- 83
Poland
- Earliest CTIS Part Ii Submission Date
- 05-02-2024
- Latest Decision Or Authorization Date
- 14-06-2024
- Processing Time Days
- 130
- Number Of Sites
- 2
- Number Of Participants
- 2
Sites
- Site Name
- Uniwersyteckie Centrum Kliniczne
- Department Name
- Klinika Hematologii i Transplantologii
- Principal Investigator Name
- Monika Szarejko
- Principal Investigator Email
- monasza1@gumed.edu.pl
- Contact Person Name
- Monika Szarejko
- Contact Person Email
- monasza1@gumed.edu.pl
- Site Name
- Uniwersyteckie Centrum Kliniczne Warszawskiego Uniwersytetu Medycznego
- Department Name
- Klinika Hematologii, Transplantologii i Chorób Wewnętrznych
- Principal Investigator Name
- Krzysztof Jamroziak
- Principal Investigator Email
- k.m.jamroziak@gmail.com
- Contact Person Name
- Krzysztof Jamroziak
- Contact Person Email
- k.m.jamroziak@gmail.com
Italy
- Earliest CTIS Part Ii Submission Date
- 05-02-2024
- Latest Decision Or Authorization Date
- 24-06-2024
- Processing Time Days
- 140
- Number Of Sites
- 2
- Number Of Participants
- 1
Sites
- Site Name
- Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia
- Department Name
- UOS DH Ematologico
- Principal Investigator Name
- Alessandra Tucci
- Principal Investigator Email
- alessandra.tucci@asst-spedalicivili.it
- Contact Person Name
- Alessandra Tucci
- Contact Person Email
- alessandra.tucci@asst-spedalicivili.it
- Site Name
- Fondazione IRCCS Policlinico San Matteo
- Department Name
- UOC Medicina generale 2
- Principal Investigator Name
- Giovanni Palladini
- Principal Investigator Email
- giovanni.palladini@unipv.it
- Contact Person Name
- Giovanni Palladini
- Contact Person Email
- giovanni.palladini@unipv.it
Greece
- Earliest CTIS Part Ii Submission Date
- 05-02-2024
- Latest Decision Or Authorization Date
- 04-07-2024
- Processing Time Days
- 150
- Number Of Sites
- 3
- Number Of Participants
- 13
Sites
- Site Name
- General University Hospital Of Patras
- Department Name
- Hematology Department of the Department of Internal Medicine of the General Hospital of Patras
- Principal Investigator Name
- Alexandros Spyridonidis
- Principal Investigator Email
- spyridonidis@upatras.gr
- Contact Person Name
- Alexandros Spyridonidis
- Contact Person Email
- spyridonidis@upatras.gr
- Site Name
- University General Hospital Of Thessaloniki Ahepa
- Department Name
- Hematology Department, First Department of Internal Medicine
- Principal Investigator Name
- Evdoxia Hatjiharissi
- Principal Investigator Email
- ehatjiharissi@gmail.com
- Contact Person Name
- Evdoxia Hatjiharissi
- Contact Person Email
- ehatjiharissi@gmail.com
- Site Name
- Alexandra Hospital
- Department Name
- Plasma Cell Dyscrasia Unit/ Therapeutic Clinic, Medical School
- Principal Investigator Name
- Efstathios Kastritis
- Principal Investigator Email
- ekastritis@med.uoa.gr
- Contact Person Name
- Efstathios Kastritis
- Contact Person Email
- ekastritis@med.uoa.gr
Czechia
- Earliest CTIS Part Ii Submission Date
- 05-02-2024
- Latest Decision Or Authorization Date
- 17-06-2024
- Processing Time Days
- 133
- Number Of Sites
- 2
- Number Of Participants
- 2
Sites
- Site Name
- Fakultni Nemocnice Ostrava
- Department Name
- Klinika hematoonkologie FNO a LF OU
- Principal Investigator Name
- Roman Hájek
- Principal Investigator Email
- roman.hajek@fno.cz
- Contact Person Name
- Roman Hájek
- Contact Person Email
- roman.hajek@fno.cz
- Site Name
- Vseobecna Fakultni Nemocnice V Praze
- Department Name
- Interní klinika - klinika hematologie 1.LF a VFN
- Principal Investigator Name
- František Sedlák
- Principal Investigator Email
- frantisek.sedlak@vfn.cz
- Contact Person Name
- František Sedlák
- Contact Person Email
- frantisek.sedlak@vfn.cz
Austria
- Earliest CTIS Part Ii Submission Date
- 05-02-2024
- Latest Decision Or Authorization Date
- 18-06-2024
- Processing Time Days
- 134
- Number Of Sites
- 2
- Number Of Participants
- 2
Sites
- Site Name
- Medical University Of Vienna
- Department Name
- Department of Medicine I, Division of Hematology and Hemostaseology
- Principal Investigator Name
- Hermine Agis
- Principal Investigator Email
- hermine.agis@meduniwien.ac.at
- Contact Person Name
- Hermine Agis
- Contact Person Email
- hermine.agis@meduniwien.ac.at
- Site Name
- Ordensklinikum Linz GmbH
- Department Name
- Internal 1 - Hematology with stem cell transplantation, hemostaseology and medical oncology
- Principal Investigator Name
- Irene Strassl
- Principal Investigator Email
- irene.strassl@ordensklinikum.at
- Contact Person Name
- Irene Strassl
- Contact Person Email
- irene.strassl@ordensklinikum.at
Spain
- Earliest CTIS Part Ii Submission Date
- 05-02-2024
- Latest Decision Or Authorization Date
- 13-06-2024
- Processing Time Days
- 129
- Number Of Sites
- 11
- Number Of Participants
- 22
Sites
- Site Name
- Hospital Universitario De Cabuenes
- Department Name
- Hematology
- Principal Investigator Name
- Maria Esther Gonzalez García
- Principal Investigator Email
- gonzalezesther@uniovi.es
- Contact Person Name
- Maria Esther Gonzalez García
- Contact Person Email
- gonzalezesther@uniovi.es
- Site Name
- University Hospital Virgen Del Rocio S.L.
- Department Name
- Hematology
- Principal Investigator Name
- Eusebio Narciso Martín Chacón
- Principal Investigator Email
- eusebion.martin.sspa@juntadeandalucia.es
- Contact Person Name
- Eusebio Narciso Martín Chacón
- Contact Person Email
- eusebion.martin.sspa@juntadeandalucia.es
- Site Name
- Hospital Universitario Fundacion Jimenez Diaz
- Department Name
- Hematology
- Principal Investigator Name
- Elham Askari
- Principal Investigator Email
- EAskari@quironsalud.es
- Contact Person Name
- Elham Askari
- Contact Person Email
- EAskari@quironsalud.es
- Site Name
- Hospital Universitario Y Politecnico La Fe
- Department Name
- Hematology
- Principal Investigator Name
- Francisco Javier de la Rubia Comos
- Principal Investigator Email
- delarubia_jav@gva.es
- Contact Person Name
- Francisco Javier de la Rubia Comos
- Contact Person Email
- delarubia_jav@gva.es
- Site Name
- Hospital Clinic De Barcelona
- Department Name
- Hematology
- Principal Investigator Name
- Maria Teresa Cibeira Lopez
- Principal Investigator Email
- mcibeira@clinic.cat
- Contact Person Name
- Maria Teresa Cibeira Lopez
- Contact Person Email
- mcibeira@clinic.cat
- Site Name
- Hospital Universitario Virgen De Las Nieves
- Department Name
- Hematology
- Principal Investigator Name
- María Esther Clavero Sánchez
- Principal Investigator Email
- mariaeclavero@juntadeandalucia.es
- Contact Person Name
- María Esther Clavero Sánchez
- Contact Person Email
- mariaeclavero@juntadeandalucia.es
- Site Name
- Hospital Universitario De Salamanca
- Department Name
- Hematology
- Principal Investigator Name
- Verónica González de la Calle
- Principal Investigator Email
- vgcalle@saludcastillayleon.com
- Contact Person Name
- Verónica González de la Calle
- Contact Person Email
- vgcalle@saludcastillayleon.com
- Site Name
- Hospital Universitari Vall D Hebron
- Department Name
- Hematology
- Principal Investigator Name
- Mercedes Gironella Mesa
- Principal Investigator Email
- mgironel@vhebron.net
- Contact Person Name
- Mercedes Gironella Mesa
- Contact Person Email
- mgironel@vhebron.net
- Site Name
- Hospital Universitario Puerta De Hierro De Majadahonda
- Department Name
- Hematology
- Principal Investigator Name
- Irene Romera Martinez
- Principal Investigator Email
- irene.romera@salud.madrid.org
- Contact Person Name
- Irene Romera Martinez
- Contact Person Email
- irene.romera@salud.madrid.org
- Site Name
- Clinica Universidad De Navarra
- Department Name
- Hematology
- Principal Investigator Name
- Ramon Lecumberri Villamediana
- Principal Investigator Email
- rlecumber@unav.es
- Contact Person Name
- Ramon Lecumberri Villamediana
- Contact Person Email
- rlecumber@unav.es
- Site Name
- Hospital La Luz Grupo Quironsalud
- Department Name
- Cardiology
- Principal Investigator Name
- Roberto Martín Reyes
- Principal Investigator Email
- RmartinR@quironsalud.es
- Contact Person Name
- Roberto Martín Reyes
- Contact Person Email
- RmartinR@quironsalud.es
Germany
- Earliest CTIS Part Ii Submission Date
- 05-02-2024
- Latest Decision Or Authorization Date
- 14-06-2024
- Processing Time Days
- 130
- Number Of Sites
- 6
- Number Of Participants
- 16
Sites
- Site Name
- Universitaetsklinikum Heidelberg AöR
- Department Name
- Intern
- Principal Investigator Name
- Stefan Schönland
- Principal Investigator Email
- Stefan.Schoenland@med.uni-heidelberg.de
- Contact Person Name
- Stefan Schönland
- Contact Person Email
- Stefan.Schoenland@med.uni-heidelberg.de
- Site Name
- Universitaetsklinikum Duesseldorf AöR
- Department Name
- Oncology and clinical immunology
- Principal Investigator Name
- Roland Fenk
- Principal Investigator Email
- fenk@med.uni-duesseldorf.de
- Contact Person Name
- Roland Fenk
- Contact Person Email
- fenk@med.uni-duesseldorf.de
- Site Name
- HOPA MVZ GmbH
- Department Name
- Hematology and Oncology
- Principal Investigator Name
- Timo Hansen
- Principal Investigator Email
- timon.hansen@hopa.de
- Contact Person Name
- Timo Hansen
- Contact Person Email
- timon.hansen@hopa.de
- Site Name
- Universitaetsklinikum Wuerzburg AöR
- Department Name
- Medical Clinic and Polyclinic II
- Principal Investigator Name
- Maximilian Johannes Steinhardt
- Principal Investigator Email
- steinhardt_M@ukw.de
- Contact Person Name
- Maximilian Johannes Steinhardt
- Contact Person Email
- steinhardt_M@ukw.de
- Site Name
- Universitaetsklinikum Essen AöR
- Department Name
- Hematology
- Principal Investigator Name
- Alexander Carpinteiro
- Principal Investigator Email
- alexander.carpinteiro@uk-essen.de
- Contact Person Name
- Alexander Carpinteiro
- Contact Person Email
- alexander.carpinteiro@uk-essen.de
- Site Name
- Charite Universitaetsmedizin Berlin KöR
- Department Name
- Hematology, Oncology and Tumor Immunology (CBF)
- Principal Investigator Name
- Stephan Bohl
- Principal Investigator Email
- Stephan.Bohl@charite.de
- Contact Person Name
- Stephan Bohl
- Contact Person Email
- Stephan.Bohl@charite.de
France
- Earliest CTIS Part Ii Submission Date
- 05-02-2024
- Latest Decision Or Authorization Date
- 18-06-2024
- Processing Time Days
- 134
- Number Of Sites
- 9
- Number Of Participants
- 25
Sites
- Site Name
- Centre Hospitalier Universitaire De Dijon
- Department Name
- Service d’Hématologie Clinique
- Principal Investigator Name
- Jean-Noël BASTIE
- Principal Investigator Email
- jean-noel.bastie@chu-dijon.fr
- Contact Person Name
- Jean-Noël BASTIE
- Contact Person Email
- jean-noel.bastie@chu-dijon.fr
- Site Name
- Centre Hospitalier Universitaire De Bordeaux
- Department Name
- Service de médecine interne et maladies infectieuses
- Principal Investigator Name
- Jean-François VIALLARD
- Principal Investigator Email
- jean-fracois.viallard@chu-bordeaux.fr
- Contact Person Name
- Jean-François VIALLARD
- Contact Person Email
- jean-fracois.viallard@chu-bordeaux.fr
- Site Name
- Institut Paoli Calmettes
- Department Name
- Département d'hématologie
- Principal Investigator Name
- Jean-Marc SCHIANO DE COLELLA
- Principal Investigator Email
- schianojm@ipc.unicancer.fr
- Contact Person Name
- Jean-Marc SCHIANO DE COLELLA
- Contact Person Email
- schianojm@ipc.unicancer.fr
- Site Name
- Centre Hospitalier Et Universitaire De Limoges
- Department Name
- Service d’Hématologie Clinique et Thérapie Cellulaire
- Principal Investigator Name
- Arnaud JACCARD
- Principal Investigator Email
- arnaud.jaccard@chu-limoges.fr
- Contact Person Name
- Arnaud JACCARD
- Contact Person Email
- arnaud.jaccard@chu-limoges.fr
- Site Name
- Centre Hospitalier Universitaire De Toulouse
- Department Name
- Service de Néphrologie-Transplantation
- Principal Investigator Name
- Antoine HUART
- Principal Investigator Email
- huart.a@chu-toulouse.fr
- Contact Person Name
- Antoine HUART
- Contact Person Email
- huart.a@chu-toulouse.fr
- Site Name
- Assistance Publique Hopitaux De Paris
- Department Name
- Unité Hémopathies Lymphoïdes
- Principal Investigator Name
- Karim BELHADJ
- Principal Investigator Email
- karim.belhadj@aphp.fr
- Contact Person Name
- Karim BELHADJ
- Contact Person Email
- karim.belhadj@aphp.fr
- Site Name
- Hospices Civils De Lyon
- Department Name
- Service d'hematologie clinique
- Principal Investigator Name
- Lionel KARLIN
- Principal Investigator Email
- lionel.karlin@chu-lyon.fr
- Contact Person Name
- Lionel KARLIN
- Contact Person Email
- lionel.karlin@chu-lyon.fr
- Site Name
- Centre Hospitalier Universitaire De Caen Normandie
- Department Name
- Hématologie Clinique
- Principal Investigator Name
- Caroline BAUGE
- Principal Investigator Email
- bauge-c@chu-caen.fr
- Contact Person Name
- Caroline BAUGE
- Contact Person Email
- bauge-c@chu-caen.fr
- Site Name
- Centre Hospitalier Universitaire De Poitiers
- Department Name
- Service de Néphrologie et transplantation rénale
- Principal Investigator Name
- Estelle DESPORT
- Principal Investigator Email
- estelle.desport@chu-poitiers.fr
- Contact Person Name
- Estelle DESPORT
- Contact Person Email
- estelle.desport@chu-poitiers.fr
Sponsor
Primary sponsor
- Full Name
- Alexion Pharmaceuticals Inc.
- Organisation Type
- Pharmaceutical company
- Country Of Registered Address
- United States
Contract research organisations
- Name
- IQVIA Limited
- Responsibilities
- Maintain eTMF, manage ePRO and Central Lab, periodic safety reporting responsibilities to Investigators in France; other operational/statistical responsibilities (multiple sponsorDuties entries).
- Name
- Almac Clinical Services LLC
- Responsibilities
- Duties code 14 (clinical supply/ logistics or similar as listed).
- Name
- Labcorp Central Laboratory Services SARL
- Responsibilities
- Statistical programming, biostatistical support and lab services.
- Name
- Biotel Research LLC
- Responsibilities
- ECG analysis/review, medical image analysis/review.
- Name
- Signant Health LLC
- Responsibilities
- Electronic patient-reported outcome (ePRO) management.
Third parties
- {"country":"United States","full_name":"Biotel Research LLC","duties_or_roles":"ECG analysis/ review, Medical image analysis/ review (listed under sponsorDuties)","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Signant Health LLC","duties_or_roles":"Electronic patient-reported outcome (ePRO)","organisation_type":"Pharmaceutical company"}
- {"country":"United Kingdom","full_name":"IQVIA Limited","duties_or_roles":"Multiple duties including e.g., maintain eTMF, manage ePRO and Central Lab, periodic safety reporting to Investigators in France, statistical and operational support (multiple sponsorDuties codes)","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Almac Clinical Services LLC","duties_or_roles":"Duties code 14 (as listed in sponsorDuties)","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"The Brigham And Women’s Hospital Inc.","duties_or_roles":"Echocardiogram (GLS%)","organisation_type":"Hospital/Clinic/Other health care facility"}
- {"country":"Switzerland","full_name":"Labcorp Central Laboratory Services SARL","duties_or_roles":"Statistical programming, biostatistical support; and code 4","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Resolian Bioanalytics","duties_or_roles":"Duties code 4","organisation_type":"Industry"}
- {"country":"United States","full_name":"Yourway Transport Inc.","duties_or_roles":"Management/Shipment of standard of care CyBorD for those sites that require it; duties codes 14 and 15","organisation_type":"Pharmaceutical company"}
- {"country":"United States","full_name":"Medidata Solutions Inc.","duties_or_roles":"Duties code 7","organisation_type":"Non-Pharmaceutical company"}
- {"country":"United States","full_name":"4g Clinical LLC","duties_or_roles":"Duties code 3","organisation_type":"Non-Pharmaceutical company"}
- {"country":"Greece","full_name":"IQVIA RDS Hellas Single Member S.A.","duties_or_roles":"Duties including code 1, 12, 2 (local country responsibilities)","organisation_type":"Non-Pharmaceutical company"}
Investigational products
- Investigational Product Name
- CAEL-101
- Active Substance
- ANSELAMIMAB
- Modality
- Monoclonal antibody
- Routes Of Administration
- Intravenous
- Route
- Intravenous
- Authorisation Status
- Not authorised (investigational product)
- Orphan Designation
- Yes
- Investigational Product Name
- SODIUM CHLORIDE
- Active Substance
- potassium chloride ph. eur.; sodium hydrogen carbonate pheur; sodium chloride ph. eur.
- Modality
- Other
- Routes Of Administration
- Intravenous
- Route
- Intravenous
- Authorisation Status
- Authorised (marketing authorised as an isotonic solution/placebo comparator)
- Combination Treatment
- Yes
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