Clinical trial • Phase III • Oncology

ALECTINIB for ALK-positive non-small cell lung cancer | Resected stage Ib–IIIa non-small cell lung cancer

Phase III trial of ALECTINIB for ALK-positive non-small cell lung cancer | Resected stage Ib–IIIa non-small cell lung cancer.

Overview

Trial Therapeutic Area
Oncology
Trial Disease
ALK-positive non-small cell lung cancer | Resected stage Ib–IIIa non-small cell lung cancer
Trial Stage
Phase III
Drug Modality
Small molecule

Key dates

Initial CTIS Submission Date
19-04-2024
First CTIS Authorization Date
21-05-2024

Trial design

Randomised, open-label, experimental arm: alectinib 600 mg orally twice daily (bid) with food for 24 months. control arm 1: cisplatin 75 mg/m2 on day 1 plus vinorelbine 25 mg/m2 on days 1 and 8. control arm 2: cisplatin 75 mg/m2 on day 1 plus gemcitabine 1250 mg/m2 on days 1 and 8. control arm 3: cisplatin 75 mg/m2 on day 1 plus pemetrexed 500 mg/m2 on day 1. Phase III trial in Romania, Denmark, Spain and others.

Randomised
Yes
Open Label
Yes
Comparator
Experimental arm: Alectinib 600 mg orally twice daily (BID) with food for 24 months. Control arm 1: Cisplatin 75 mg/m2 on Day 1 plus vinorelbine 25 mg/m2 on Days 1 and 8. Control arm 2: Cisplatin 75 mg/m2 on Day 1 plus gemcitabine 1250 mg/m2 on Days 1 and 8. Control arm 3: Cisplatin 75 mg/m2 on Day 1 plus pemetrexed 500 mg/m2 on Day 1.
Target Sample Size
202
Trial Duration For Participant
730

Eligibility

Recruits 202 Vulnerable population flag selected in the trial record (populationOfTrialSubjects.isVulnerablePopulationSelected = true). Informed consent is to be obtained using the Subject Information and Informed Consent Forms (multiple ICF documents and language versions are provided). No explicit assent or age-specific parental consent procedures are detailed in the available CTIS data..

Pregnancy Exclusion
Pregnant or breastfeeding, or intending to become pregnant during the study and for at least 5 weeks after the last dose of alectinib or according to local labels or guidelines for chemotherapy
Vulnerable Population
Vulnerable population flag selected in the trial record (populationOfTrialSubjects.isVulnerablePopulationSelected = true). Informed consent is to be obtained using the Subject Information and Informed Consent Forms (multiple ICF documents and language versions are provided). No explicit assent or age-specific parental consent procedures are detailed in the available CTIS data.

Inclusion criteria

  • {"criterion_text":"- Complete resection of histologically-confirmed Stage Ib (tumor ≥ 4 cm) to Stage IIIa (T2-3 N0, T1-3 N1, T1-3 N2, T4 N0-1) NSCLC as per UICC/AJCC, 7th edition, with negative margins, at 4-12 weeks before enrollment"}
  • {"criterion_text":"- Documented ALK-positive disease according to an FDA-approved and CE-marked test"}
  • {"criterion_text":"- Eligible to receive a platinum-based chemotherapy regimen according to the local labels or guidelines"}
  • {"criterion_text":"- Eastern Cooperative Oncology Group Performance Status of Grade 0 or 1"}
  • {"criterion_text":"- Adequate hematologic and renal function"}
  • {"criterion_text":"- Willingness and ability to comply with scheduled visits, treatment plans, laboratory tests, and other study procedures"}

Exclusion criteria

  • {"criterion_text":"- Pregnant or breastfeeding, or intending to become pregnant during the study and for at least 5 weeks after the last dose of alectinib or according to local labels or guidelines for chemotherapy"}
  • {"criterion_text":"- Prior adjuvant radiotherapy for NSCLC Prior exposure to systemic anti-cancer therapy and ALK inhibitors"}
  • {"criterion_text":"- Stage IIIA N2 patients that, in the investigator's opinion, should receive post-operative radiotherapy treatment are excluded from the study"}
  • {"criterion_text":"- Known sensitivity to any component of study drug to which the patient may be randomized. This includes, but is not limited to, patients with galactose intolerance, a congenital lactase deficiency or glucose-galactose malabsorption."}
  • {"criterion_text":"- Significant liver disease or impaired liver transaminase enzymes levels, symptomatic bradycardia, any GI disorder that may affect absorption of oral medications, such as malabsorption syndrome or status post-major bowel resection, HIV positivity"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- 1. Disease-free survival per investigator’s assessment","definition_or_measurement_approach":"Disease-free survival assessed by the investigator (investigator-assessed DFS as stated in the main objective/endpoints)."}

Secondary endpoints

  • {"endpoint_text":"- 1. Overall survival","definition_or_measurement_approach":"Overall survival (time from randomisation to death from any cause)."}
  • {"endpoint_text":"- 2. Incidence of adverse events, with severity determined through use of National Cancer Institute Common Terminology Criteria for Adverse Events version 5.0","definition_or_measurement_approach":"Incidence and severity of adverse events graded using NCI CTCAE v5.0."}
  • {"endpoint_text":"- 3. Incidence of abnormal laboratory findings","definition_or_measurement_approach":"Incidence of clinically relevant abnormal laboratory results (laboratory assessments per protocol)."}
  • {"endpoint_text":"- 4. Changes in vital signs and electrocardiograms","definition_or_measurement_approach":"Changes in vital signs and ECG parameters measured at protocol-specified timepoints."}
  • {"endpoint_text":"- 5. Plasma concentrations of alectinib and its major metabolite(s) at specified timepoints for alectinib","definition_or_measurement_approach":"Plasma pharmacokinetic sampling for alectinib and major metabolites at specified timepoints (PK characterization)."}

Recruitment

Planned Sample Size
202
Recruitment Window Months
95
Consent Approach
Informed consent obtained via subject information sheets and informed consent forms (multiple ICF documents present in the dossier). Multiple language versions and addenda exist (examples: EN, DE, FR, ES, IT, PL, GR, HU, RO). No explicit description of assent or separate parental consent for minors is provided in the available CTIS data.

Geography

Total Number Of Sites
31
Total Number Of Participants
55

Romania

Earliest CTIS Part Ii Submission Date
06-05-2024
Latest Decision Or Authorization Date
06-04-2026
Processing Time Days
700
Number Of Sites
2
Number Of Participants
2

Sites

Site Name
Institute Of Oncology Prof. Dr. Ion Chiricuta Cluj-Napoca
Department Name
Oncology
Principal Investigator Name
Tudor Ciuleanu
Principal Investigator Email
office@iocn.ro
Contact Person Name
Tudor Ciuleanu
Contact Person Email
office@iocn.ro
Site Name
Oncomed S.R.L.
Department Name
Oncology
Principal Investigator Name
Dorel Popovici
Principal Investigator Email
office@oncohelp.ro
Contact Person Name
Dorel Popovici
Contact Person Email
office@oncohelp.ro

Denmark

Earliest CTIS Part Ii Submission Date
06-05-2024
Latest Decision Or Authorization Date
20-02-2026
Processing Time Days
655
Number Of Sites
1
Number Of Participants
2

Sites

Site Name
Odense University Hospital
Department Name
Onkologisk afdeling R
Principal Investigator Name
Lise Eckhoff
Principal Investigator Email
ouh.ode.r.ctis@rsyd.dk
Contact Person Name
Lise Eckhoff
Contact Person Email
ouh.ode.r.ctis@rsyd.dk

Spain

Earliest CTIS Part Ii Submission Date
06-05-2024
Latest Decision Or Authorization Date
04-03-2026
Processing Time Days
667
Number Of Sites
7
Number Of Participants
7

Sites

Site Name
Hospital Universitari Vall D Hebron
Department Name
Oncología
Principal Investigator Name
Aleix Martí
Principal Investigator Email
amartinezmarti@vhio.net
Contact Person Name
Aleix Martí
Contact Person Email
amartinezmarti@vhio.net
Site Name
Hospital Germans Trias I Pujol
Department Name
Oncología
Principal Investigator Name
Enric Carcereny
Principal Investigator Email
ecarcereny@iconcologia.net
Contact Person Name
Enric Carcereny
Contact Person Email
ecarcereny@iconcologia.net
Site Name
University Hospital Virgen Del Rocio S.L.
Department Name
Oncología
Principal Investigator Name
Reyes Bernabe
Principal Investigator Email
reyesbernab@yahoo.es
Contact Person Name
Reyes Bernabe
Contact Person Email
reyesbernab@yahoo.es
Site Name
Hospital Clinico Universitario De Valencia
Department Name
Oncología
Principal Investigator Name
Amelia Insa
Principal Investigator Email
ameliainsamolla@gmail.com
Contact Person Name
Amelia Insa
Contact Person Email
ameliainsamolla@gmail.com
Site Name
Hospital Universitario La Paz
Department Name
Oncología
Principal Investigator Name
Javier De Castro
Principal Investigator Email
javier.decastro@salud.madrid.org
Contact Person Name
Javier De Castro
Site Name
Hospital De La Santa Creu I Sant Pau
Department Name
Oncología
Principal Investigator Name
Margarita Magem
Principal Investigator Email
mmajem@santpau.cat
Contact Person Name
Margarita Magem
Contact Person Email
mmajem@santpau.cat
Site Name
Hospital Universitari Vall D Hebron (duplicate entry in CTIS list)
Department Name
Oncología
Principal Investigator Name
Aleix Martí
Principal Investigator Email
amartinezmarti@vhio.net
Contact Person Name
Aleix Martí
Contact Person Email
amartinezmarti@vhio.net

Austria

Earliest CTIS Part Ii Submission Date
06-05-2024
Latest Decision Or Authorization Date
26-02-2026
Processing Time Days
661
Number Of Sites
1
Number Of Participants
5

Sites

Site Name
Krankenhaus Nord Klinik Floridsdorf
Department Name
Department for Respiratory and Critical Care Medicine
Principal Investigator Name
Maximilian Hochmair
Principal Investigator Email
maximilian.hochmair@gesundheitsverbund.at
Contact Person Name
Maximilian Hochmair

Hungary

Earliest CTIS Part Ii Submission Date
06-05-2024
Latest Decision Or Authorization Date
25-02-2026
Processing Time Days
660
Number Of Sites
2
Number Of Participants
2

Sites

Site Name
Orszagos Onkologiai Intezet
Department Name
Belgyógyászati-Onkológiai Osztály és Klinikai Farmakológiai Osztály
Principal Investigator Name
Tünde Nagy
Principal Investigator Email
drnt@freemail.hu
Contact Person Name
Tünde Nagy
Contact Person Email
drnt@freemail.hu
Site Name
Jasz-Nagykun-Szolnok Varmegyei Hetenyi Geza Korhaz-Rendelointezet
Department Name
Onkológiai központ
Principal Investigator Name
Hajnalka Nemeth
Principal Investigator Email
nemethhajnalka@hotmail.com
Contact Person Name
Hajnalka Nemeth
Contact Person Email
nemethhajnalka@hotmail.com

France

Earliest CTIS Part Ii Submission Date
06-05-2024
Latest Decision Or Authorization Date
25-02-2026
Processing Time Days
660
Number Of Sites
3
Number Of Participants
6

Sites

Site Name
Institut Gustave Roussy
Department Name
Service d'Oncologie Thoracique
Principal Investigator Name
David PLANCHARD
Principal Investigator Email
david.planchard@gustaveroussy.fr
Contact Person Name
David PLANCHARD
Site Name
Centre Hospitalier Universitaire D'Angers
Department Name
Service de Pneumologie
Principal Investigator Name
José HUREAUX
Principal Investigator Email
jose.hureaux@chu-angers.fr
Contact Person Name
José HUREAUX
Contact Person Email
jose.hureaux@chu-angers.fr
Site Name
Centre Hospitalier Regional De Marseille
Department Name
Oncologie Multidisciplinaire et Innovations thérapeutiques
Principal Investigator Name
Pascale TOMASINI
Principal Investigator Email
pascale.tomasini@ap-hm.fr
Contact Person Name
Pascale TOMASINI
Contact Person Email
pascale.tomasini@ap-hm.fr

Germany

Earliest CTIS Part Ii Submission Date
06-05-2024
Latest Decision Or Authorization Date
10-03-2026
Processing Time Days
673
Number Of Sites
4
Number Of Participants
6

Sites

Site Name
Thoraxklinik Heidelberg gGmbH
Department Name
Thoraxklinik
Principal Investigator Name
Helge Bischoff
Principal Investigator Email
helge.bischoff@med.uni-heidelberg.de
Contact Person Name
Helge Bischoff
Site Name
Klinikum Chemnitz gGmbH
Department Name
Innere Medizin IV
Principal Investigator Name
Stefan Hammerschmidt
Principal Investigator Email
S.Hammerschmidt@skc.de
Contact Person Name
Stefan Hammerschmidt
Contact Person Email
S.Hammerschmidt@skc.de
Site Name
Franziskus Hospital Harderberg
Department Name
Klinik für Thoraxonkologie
Principal Investigator Name
Petra Hoffknecht
Principal Investigator Email
petra.hoffknecht@niels-stensen-kliniken.de
Contact Person Name
Petra Hoffknecht
Site Name
Lungenfachklinik Immenhausen
Principal Investigator Name
Achim Rittmeyer
Contact Person Name
Achim Rittmeyer

Poland

Earliest CTIS Part Ii Submission Date
06-05-2024
Latest Decision Or Authorization Date
26-02-2026
Processing Time Days
662
Number Of Sites
4
Number Of Participants
8

Sites

Site Name
Warminsko-Mazurskie Centrum Chorob Pluc W Olsztynie
Department Name
Oddział onkologii z pododdziałem chemioterapii
Principal Investigator Name
Andrzej Każarnowicz
Principal Investigator Email
sekretariat@pulmonologia.olsztyn.pl
Contact Person Name
Andrzej Każarnowicz
Site Name
Wielkopolskie Centrum Pulmonologii I Torakochirurgii Im. Eugenii I Janusza Zeylandow
Department Name
Oddział Onkologii Klinicznej z Pododdziałem Dziennej Chemioterapii
Principal Investigator Name
Katarzyna Stencel
Principal Investigator Email
poznan@wcpit.org
Contact Person Name
Katarzyna Stencel
Contact Person Email
poznan@wcpit.org
Site Name
Uniwersyteckie Centrum Kliniczne
Department Name
Klinika Onkologii i Radioterapii
Principal Investigator Name
Rafał Dziadziuszko
Principal Investigator Email
onkologia@uck.gda.pl
Contact Person Name
Rafał Dziadziuszko
Contact Person Email
onkologia@uck.gda.pl
Site Name
Narodowy Instytut Onkologii Im. Marii Sklodowskiej-Curie Panstwowy Instytut Badawczy
Department Name
Klinika Nowotworów Płuca i Klatki Piersiowej
Principal Investigator Name
Maciej Głogowski
Principal Investigator Email
malgorzata.falgowska@nio.gov.pl
Contact Person Name
Maciej Głogowski

Italy

Earliest CTIS Part Ii Submission Date
06-05-2024
Latest Decision Or Authorization Date
23-02-2026
Processing Time Days
658
Number Of Sites
5
Number Of Participants
15

Sites

Site Name
Azienda Ospedaliera Dei Colli
Department Name
Pneumologia Oncologica
Principal Investigator Name
Fabiana Vitiello
Principal Investigator Email
fabianavitiello@libero.it
Contact Person Name
Fabiana Vitiello
Contact Person Email
fabianavitiello@libero.it
Site Name
Hospital Santa Maria Della Misericordia
Department Name
Oncologia Medica
Principal Investigator Name
Giulio Metro
Principal Investigator Email
giulio.metro@ospedale.perugia.it
Contact Person Name
Giulio Metro
Site Name
Azienda Ospedaliero-Universitaria San Luigi Gonzaga
Department Name
Malattie Apparato Respiratorio 5 ad Indirizzo Oncologico
Principal Investigator Name
Silvia Novello
Principal Investigator Email
silvia.novello@unito.it
Contact Person Name
Silvia Novello
Contact Person Email
silvia.novello@unito.it
Site Name
Istituto Europeo Di Oncologia S.r.l.
Department Name
Divisione di Oncologia
Principal Investigator Name
Gianluca Spitaleri
Principal Investigator Email
gianluca.spitaleri@ieo.it
Contact Person Name
Gianluca Spitaleri
Contact Person Email
gianluca.spitaleri@ieo.it
Site Name
San Camillo Forlanini Hospital
Department Name
Unità Operativa Complessa di Pneumologia Oncologica 1
Principal Investigator Name
Serena Ricciardi
Principal Investigator Email
sricciardi@scamilloforlanini.rm.it
Contact Person Name
Serena Ricciardi

Greece

Earliest CTIS Part Ii Submission Date
04-07-2024
Latest Decision Or Authorization Date
24-02-2026
Processing Time Days
600
Number Of Sites
2
Number Of Participants
2

Sites

Site Name
Metropolitan Hospital
Department Name
Β΄ Oncology Department
Principal Investigator Name
Epaminondas Samantas
Principal Investigator Email
epsam@otenet.gr
Contact Person Name
Epaminondas Samantas
Contact Person Email
epsam@otenet.gr
Site Name
Theageneio Cancer Hospital
Department Name
Oncology Clinic
Principal Investigator Name
Theodora Tsiouda
Principal Investigator Email
doratsiouda@yahoo.gr
Contact Person Name
Theodora Tsiouda
Contact Person Email
doratsiouda@yahoo.gr

Sponsor

Primary sponsor

Full Name
F. Hoffmann-La Roche AG
Organisation Type
Pharmaceutical company
Country Of Registered Address
Switzerland

Contract research organisations

Name
Almac Clinical Technologies LLC
Responsibilities
Randomization
Name
Bioclinica Inc.
Responsibilities
Other Third Party Duty
Name
Greenphire LLC
Responsibilities
Other Third Party Duty
Name
Fortrea Inc.
Responsibilities
Other Third Party Duty
Name
Labcorp Central Laboratory Services SARL
Responsibilities
code:4
Name
CellCarta
Responsibilities
code:4
Name
Foundation Medicine Inc.
Responsibilities
Other Third Party Duty

Third parties

  • {"country":"United States","full_name":"Foundation Medicine Inc.","duties_or_roles":"Other Third Party Duty","organisation_type":"Pharmaceutical company"}
  • {"country":"Canada","full_name":"Axon Communications Inc.","duties_or_roles":"Meeting Organizer","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Greenphire LLC","duties_or_roles":"Other Third Party Duty","organisation_type":"Non-Pharmaceutical company"}
  • {"country":"United States","full_name":"Bioclinica Inc.","duties_or_roles":"Other Third Party Duty","organisation_type":"Laboratory/Research/Testing facility"}
  • {"country":"United States","full_name":"Fortrea Inc.","duties_or_roles":"Other Third Party Duty","organisation_type":"Pharmaceutical company"}
  • {"country":"Switzerland","full_name":"Labcorp Central Laboratory Services SARL","duties_or_roles":"code:4","organisation_type":"Pharmaceutical company"}
  • {"country":"United States","full_name":"Almac Clinical Technologies LLC","duties_or_roles":"Randomization","organisation_type":"Pharmaceutical company"}
  • {"country":"Belgium","full_name":"CellCarta","duties_or_roles":"code:4","organisation_type":"Laboratory/Research/Testing facility"}

Investigational products

Investigational Product Name
Alecensa 150 mg hard capsules
Active Substance
ALECTINIB
Modality
Small molecule
Routes Of Administration
ORAL
Route
Oral
Authorisation Status
Authorised
Starting Dose
600 mg orally twice daily (BID) with food (per protocol experimental arm)
Dose Levels
600 mg BID (fixed)
Frequency
Twice daily (BID)
Maximum Dose
1200 mg/day
Investigational Product Name
VINORELBINE
Active Substance
VINORELBINE
Modality
Small molecule
Routes Of Administration
IV INFUSION
Route
IV infusion
Authorisation Status
Authorised
Starting Dose
25 mg/m2 on Days 1 and 8 (when used with cisplatin)
Dose Levels
25 mg/m2
Frequency
Days 1 and 8 of cycle
Maximum Dose
25 mg/m2 (per dosing information provided)
Investigational Product Name
Gemcitabin-GRY 1000 mg Pulver zur Herstellung einer Infusionslösung
Active Substance
GEMCITABINE HYDROCHLORIDE
Modality
Small molecule
Routes Of Administration
IV INFUSION
Route
IV infusion
Authorisation Status
Authorised
Starting Dose
1250 mg/m2 on Days 1 and 8 (when used with cisplatin)
Dose Levels
1250 mg/m2
Frequency
Days 1 and 8 of cycle
Maximum Dose
1250 mg/m2
Investigational Product Name
Cisplatin NeoCorp 1 mg/ml - Konzentrat zur Herstellung einer Infusionslösung
Active Substance
CISPLATIN
Modality
Small molecule
Routes Of Administration
IV INFUSION
Route
IV infusion
Authorisation Status
Authorised
Starting Dose
75 mg/m2 on Day 1 (used in control arms)
Dose Levels
75 mg/m2
Frequency
Day 1 of cycle
Maximum Dose
75 mg/m2
Investigational Product Name
Carboplatin ACTAVIS 10 mg/ml concentrat pentru soluţie perfuzabilă / Carboplatin-GRY® 10 mg/ml Konzentrat zur Herstellung einer Infusionslösung
Active Substance
CARBOPLATIN
Modality
Small molecule
Routes Of Administration
IV INFUSION
Route
IV infusion
Authorisation Status
Authorised
Investigational Product Name
ALIMTA 500 mg powder for concentrate for solution for infusion
Active Substance
PEMETREXED
Modality
Small molecule
Routes Of Administration
IV INFUSION
Route
IV infusion
Authorisation Status
Authorised
Starting Dose
500 mg/m2 on Day 1 (when used with cisplatin according to one control arm)
Dose Levels
500 mg/m2
Frequency
Day 1 of cycle
Maximum Dose
500 mg/m2

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