Clinical trial • Phase III • Immunology

ABATACEPT for Rheumatoid arthritis

Phase III trial of ABATACEPT for Rheumatoid arthritis.

Overview

Trial Therapeutic Area
Immunology
Trial Disease
Rheumatoid arthritis
Trial Stage
Phase III
Drug Modality
Peptide/protein/enzyme | Monoclonal antibody

Key dates

Initial CTIS Submission Date
08-12-2023
First CTIS Authorization Date
26-01-2024

Trial design

Randomised, abatacept (test; active substance: abatacept; subcutaneous solution for injection; max daily dose listed as 125 mg in record) versus adalimumab (humira 40 mg solution for injection in pre-filled syringe; active substance: adalimumab; subcutaneous; 40 mg specified). both given on background methotrexate. specific schedules not stated in the ctis record.-controlled Phase III trial across 19 sites in Czechia, France, Germany and others.

Randomised
Yes
Comparator
Abatacept (test; active substance: ABATACEPT; subcutaneous solution for injection; max daily dose listed as 125 mg in record) versus Adalimumab (Humira 40 mg solution for injection in pre-filled syringe; active substance: ADALIMUMAB; subcutaneous; 40 mg specified). Both given on background methotrexate. Specific schedules not stated in the CTIS record.
Biomarker Stratified
True, biomarker: SE HLA Class II risk alleles ("Shared Epitope") — primary analyses focused on SE+ subset (SE+) and whole population included as additional strata
Target Sample Size
259
Trial Duration For Participant
728

Eligibility

Recruits 259 Vulnerable population selected in the record. Subject information and informed consent form documents are available (L1_SIS and ICF documents listed), but no detailed description of consent/assent handling for vulnerable participants is provided in the record..

Pregnancy Exclusion
Women who are breastfeeding
Vulnerable Population
Vulnerable population selected in the record. Subject information and informed consent form documents are available (L1_SIS and ICF documents listed), but no detailed description of consent/assent handling for vulnerable participants is provided in the record.

Inclusion criteria

  • {"criterion_text":"- Early rheumatoid arthritis (RA), defined as symptoms of RA that started ≤ 12 months prior to screening and satisfied the American College of Rheumatology/European League Against Rheumatism (ACR/EULAR) 2010 criteria for the classification of RA at some point during the 12-month period"}
  • {"criterion_text":"- Naïve to any targeted (biologic or nonbiologic) disease-modifying antirheumatic drugs (DMARDs), conventional synthetic DMARDs other than methotrexate (MTX), or investigational therapies for RA"}
  • {"criterion_text":"- Treated with MTX for at least 12 weeks, with a stable dose of oral or parenteral MTX for at least 4 weeks prior to randomization"}
  • {"criterion_text":"- Anti-cyclic citrullinated peptide-2 (Anti-CCP-2) test that is > 3× the upper limit of normal and are positive for rheumatoid factor (RF) according to central lab testing during screening"}
  • {"criterion_text":"- At least a Disease Activity Score 28-joint count calculated using Creactive protein (DAS28-CRP) ≥ 3.2 at screening"}
  • {"criterion_text":"- At least 3 tender and at least 3 swollen joints at screening and at randomization."}

Exclusion criteria

  • {"criterion_text":"- Women who are breastfeeding"}
  • {"criterion_text":"- Current clinical findings or a history of a demyelinating disorder"}
  • {"criterion_text":"- 5 or more joints cannot be assessed for tenderness or swelling"}
  • {"criterion_text":"- Autoimmune disease other than RA (e.g., psoriasis, systemic lupus erythematosus [SLE], vasculitis, seronegative spondyloarthritis, inflammatory bowel disease, Sjogren's syndrome) or currently active fibromyalgia"}
  • {"criterion_text":"- History of or current inflammatory joint disease other than RA (e.g., psoriatic arthritis, gout, reactive arthritis, Lyme disease)"}
  • {"criterion_text":"- At risk for tuberculosis"}
  • {"criterion_text":"- Recent acute infection"}
  • {"criterion_text":"- History of chronic or recurrent bacterial infection (e.g., chronic pyelonephritis, osteomyelitis, bronchiectasis)"}
  • {"criterion_text":"- History of infection of a joint prosthesis or artificial joint"}
  • {"criterion_text":"- History of systemic fungal infections (such as histoplasmosis, blastomycosis, or coccidiomycosis)"}
  • {"criterion_text":"- History of primary immunodeficiency"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Proportion of SE+ participants meeting ACR50 response at Week 24","definition_or_measurement_approach":"Measured as the proportion of participants positive for the Shared Epitope (SE+) meeting ACR50 response at Week 24."}

Secondary endpoints

  • {"endpoint_text":"- Proportion of SE+ participants achieving DAS28-CRP remission (DAS28-CRP < 2.6) at Week 24","definition_or_measurement_approach":"DAS28-CRP remission defined as DAS28-CRP < 2.6 at Week 24 in SE+ participants."}
  • {"endpoint_text":"- Proportion of whole study population participants meeting ACR50 response at Week 24","definition_or_measurement_approach":"Measured as the proportion of all randomized participants meeting ACR50 response at Week 24."}
  • {"endpoint_text":"- Proportion of SE+ participants achieving CDAI remission (CDAI ≤ 2.8) at Week 24","definition_or_measurement_approach":"CDAI remission defined as CDAI ≤ 2.8 at Week 24 in SE+ participants."}
  • {"endpoint_text":"- Mean change from baseline in SE+ participant-reported pain (VAS) at Week 24","definition_or_measurement_approach":"Mean change from baseline in patient-reported pain using a visual analogue scale (VAS) at Week 24 for SE+ participants."}
  • {"endpoint_text":"- Proportion of SE+ subset and whole population achieving ACR20/50/70 responses, DAS remission, CDAI remission, SDAI remission over the SBTP and OLTP; mean changes from baseline in DAS28-CRP, CDAI, SDAI over the SBTP and OLTP; mean changes from baseline in the 7 ACR core components over the SBTP and OLTP","definition_or_measurement_approach":"Composite and multiple efficacy measures assessed over the single-blind treatment period (SBTP) and open-label treatment period (OLTP); includes ACR20/50/70, remission criteria (DAS, CDAI, SDAI), and mean changes in core scores."}
  • {"endpoint_text":"- Mean change from baseline in SF-36 in SE+ subset and whole population at Week 24 and Week 104 (4 physical and 4 mental subscales and the physical component and mental component summary)","definition_or_measurement_approach":"Mean change from baseline in SF-36 quality-of-life scores assessed at Week 24 and Week 104 for SE+ subset and whole population."}

Recruitment

Planned Sample Size
259
Recruitment Window Months
46
Consent Approach
Subject information and informed consent form documents are listed (L1_SIS and ICF documents, redacted versions present). Patient-facing documents are available in multiple languages (documents in PL, DE, FR, IT etc. are present in the record). No further explicit details on assent, age-specific consent handling, or specific consent procedures are provided in the CTIS record.

Geography

Total Number Of Sites
19
Total Number Of Participants
141

Czechia

Latest Decision Or Authorization Date
30-01-2024
Number Of Sites
2
Number Of Participants
18

Sites

Site Name
Revmatologicky Ustav
Department Name
Oddeleni experimentalni revmatologie
Principal Investigator Name
Ladislav Senolt
Principal Investigator Email
senolt@revma.cz
Contact Person Name
Ladislav Senolt
Contact Person Email
senolt@revma.cz
Site Name
Revmatologie s.r.o.
Principal Investigator Name
Petr Nemec
Principal Investigator Email
revmatologie.nemec@seznam.cz
Contact Person Name
Petr Nemec
Contact Person Email
revmatologie.nemec@seznam.cz

France

Latest Decision Or Authorization Date
26-01-2024
Number Of Sites
2
Number Of Participants
11

Sites

Site Name
Centre Hospitalier Universitaire De Montpellier
Department Name
Département de Rhumatologie
Principal Investigator Name
Jacques MOREL
Principal Investigator Email
j-morel@chu-montpellier.fr
Contact Person Name
Jacques MOREL
Contact Person Email
j-morel@chu-montpellier.fr
Site Name
Centre Hospitalier Universitaire De Toulouse
Department Name
Centre de Rhumatologie
Principal Investigator Name
Arnaud CONSTANTIN
Principal Investigator Email
constantin.a@chu-toulouse.fr
Contact Person Name
Arnaud CONSTANTIN
Contact Person Email
constantin.a@chu-toulouse.fr

Germany

Latest Decision Or Authorization Date
30-01-2024
Number Of Sites
5
Number Of Participants
24

Sites

Site Name
Klinische Forschung Im Medizinischen Versorgungsalltag GbR
Department Name
Rheumatologie
Principal Investigator Name
Patrizia Maria Sternad
Principal Investigator Email
patrizia.sternad@rheumatologie-welcker.de
Contact Person Name
Patrizia Maria Sternad
Site Name
Medical Center - University Of Freiburg
Department Name
Department Innere Medizin Klinik f. Rheumatologie und Klinische Immunologie
Principal Investigator Name
Stephanie Finzel
Principal Investigator Email
stephanie.finzel@uniklinik-freiburg.de
Contact Person Name
Stephanie Finzel
Site Name
MVZ Rheumatologie und Autoimmunmedizin Hamburg GmbH
Department Name
Rheumatologie und Autoimmunmedizin
Principal Investigator Name
Andrea Everding
Principal Investigator Email
everding@hotmail.de
Contact Person Name
Andrea Everding
Contact Person Email
everding@hotmail.de
Site Name
Universitaetsklinikum Bonn AöR
Department Name
Medizinische Klinik und Poliklinik III, Klinik f. Onkologie, Haematologie, Immunonkologie u Rheumato
Principal Investigator Name
Valentin Schaefer
Principal Investigator Email
valentin.schaefer@ukbonn.de
Contact Person Name
Valentin Schaefer
Contact Person Email
valentin.schaefer@ukbonn.de
Site Name
Charite Universitaetsmedizin Berlin KöR
Department Name
Department of Rheumatology and Clinical Immunology
Principal Investigator Name
Gerd Burmester
Principal Investigator Email
gerd.burmester@charite.de
Contact Person Name
Gerd Burmester
Contact Person Email
gerd.burmester@charite.de

Italy

Latest Decision Or Authorization Date
26-02-2024
Number Of Sites
4
Number Of Participants
11

Sites

Site Name
Azienda Ospedaliero Universitaria Policlinico G Rodolico San Marco Di Catania
Department Name
Rheumatology
Principal Investigator Name
Rosario Foti
Principal Investigator Email
rosfoti5@gmail.com
Contact Person Name
Rosario Foti
Contact Person Email
rosfoti5@gmail.com
Site Name
Fondazione IRCCS Policlinico San Matteo
Department Name
Rheumatology
Principal Investigator Name
Francesca Bobbio Pallavicini
Principal Investigator Email
f.bobbiopallavicini@smatteo.pv.it
Contact Person Name
Francesca Bobbio Pallavicini
Site Name
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Department Name
Rheumatology
Principal Investigator Name
Maria Antonietta D'agostino
Contact Person Name
Maria Antonietta D'agostino
Site Name
Hospital Santa Maria Della Misericordia
Department Name
Rheumatology
Principal Investigator Name
Roberto Gerli
Principal Investigator Email
roberto.gerli@unipg.it
Contact Person Name
Roberto Gerli
Contact Person Email
roberto.gerli@unipg.it

Spain

Latest Decision Or Authorization Date
29-01-2024
Number Of Sites
3
Number Of Participants
7

Sites

Site Name
Complexo Hospitalario Universitario A Coruna
Department Name
Rheumatology
Principal Investigator Name
Francisco Javier Blanco Garcia
Principal Investigator Email
fblagar@sergas.es
Contact Person Name
Francisco Javier Blanco Garcia
Contact Person Email
fblagar@sergas.es
Site Name
Hospital Universitario La Paz
Department Name
Rheumatology
Principal Investigator Name
Alejandro Balsa Criado
Principal Investigator Email
alejandro.balsa@salud.madrid.org
Contact Person Name
Alejandro Balsa Criado
Site Name
Hospital Universitario Marques De Valdecilla
Department Name
Rheumatology
Principal Investigator Name
Ricardo Blanco
Principal Investigator Email
rblanco@humv.es
Contact Person Name
Ricardo Blanco
Contact Person Email
rblanco@humv.es

Poland

Latest Decision Or Authorization Date
18-03-2025
Number Of Sites
3
Number Of Participants
70

Sites

Site Name
Centrum Kliniczno-Badawcze J.Brzezicki B.Gornikiewicz-Brzezicka Lekarze sp.p.
Principal Investigator Name
Jan Brzezicki
Principal Investigator Email
janisb@poczta.onet.pl
Contact Person Name
Jan Brzezicki
Contact Person Email
janisb@poczta.onet.pl
Site Name
MICS Centrum Medyczne Torun
Principal Investigator Name
Piotr Kalmus
Principal Investigator Email
p.kalmus@naszlekarz.pl
Contact Person Name
Piotr Kalmus
Contact Person Email
p.kalmus@naszlekarz.pl
Site Name
Szpital Uniwersytecki Nr 2 Im Dr Jana Biziela W Bydgoszczy
Department Name
Klinika Reumatologii i Układowych Chorób Tkanki Łącznej
Principal Investigator Name
Iwona Dankiewicz-Fares
Principal Investigator Email
iwonadankiewiczfares@gmail.com
Contact Person Name
Iwona Dankiewicz-Fares
Contact Person Email
iwonadankiewiczfares@gmail.com

Sponsor

Primary sponsor

Full Name
Bristol-Myers Squibb Services Unlimited Company
Organisation Type
Pharmaceutical company
Country Of Registered Address
Ireland

Contract research organisations

Name
Q2 Solutions Europe
Responsibilities
Sample mgmt, Kit building, Storage and distribution of samples to other vendors for analysis
Name
Accenture Services Pvt. Ltd.
Responsibilities
Pharmacovigilance duties: Medical review and Cases Data Entry; submission administrative support

Third parties

  • {"country":"United Kingdom","full_name":"Q2 Solutions Europe","duties_or_roles":"Sample mgmt, Kit building, Storage and distribution of samples to other vendors for analysis","organisation_type":"Health care"}
  • {"country":"India","full_name":"Accenture Services Pvt. Ltd.","duties_or_roles":"Pharmacovigilance duties: Medical review and Cases Data Entry","organisation_type":"SME"}
  • {"country":"India","full_name":"Accenture Services Pvt. Ltd.","duties_or_roles":"submission administrative support","organisation_type":"SME"}

Investigational products

Investigational Product Name
Abatacept
Active Substance
ABATACEPT
Modality
Peptide/protein/enzyme
Routes Of Administration
Subcutaneous
Route
Subcutaneous
Maximum Dose
125 mg
Investigational Product Name
Humira 40 mg solution for injection in pre-filled syringe
Active Substance
ADALIMUMAB
Modality
Monoclonal antibody
Routes Of Administration
Subcutaneous
Route
Subcutaneous
Authorisation Status
Marketing authorisation present (marketingAuthNumber: EU/1/03/256/013)
Maximum Dose
40 mg
Combination Treatment
Yes

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