Clinical trial • Phase II • Cardiology

AB-1002 for Congestive heart failure | Non-ischaemic cardiomyopathy

Phase II trial of AB-1002 for Congestive heart failure | Non-ischaemic cardiomyopathy.

Overview

Trial Therapeutic Area
Cardiology
Trial Disease
Congestive heart failure | Non-ischaemic cardiomyopathy
Trial Stage
Phase II
Drug Modality
Gene therapy

Key dates

Initial CTIS Submission Date
16-05-2024
First CTIS Authorization Date
10-09-2024

Trial design

Randomised, placebo infusion (ab-1002 placebo) administered as comparator to single antegrade intracoronary infusion of ab-1002; specific dose and schedule not specified in the provided record.-controlled, adaptive Phase II trial in Hungary, Bulgaria, Romania and others.

Randomised
Yes
Comparator
Placebo infusion (AB-1002 Placebo) administered as comparator to single antegrade intracoronary infusion of AB-1002; specific dose and schedule not specified in the provided record.
Adaptive
True, adaptive design is stated (Phase 2 adaptive). No detailed adaptive elements (e.g., explicit dose-escalation rules, interim analysis timing, or stopping rules) are described in the provided record.
Target Sample Size
80
Trial Duration For Participant
364

Eligibility

Recruits 80 Vulnerable population selected. Participants must be adults (≥18 years) and provide informed consent. Country-specific subject information and informed consent forms are provided (multiple languages/countries). No mention of assent for minors (minors are excluded)..

Pregnancy Exclusion
Pregnancy or breastfeeding or plans to become pregnant within the next 12 months at the time of screening
Vulnerable Population
Vulnerable population selected. Participants must be adults (≥18 years) and provide informed consent. Country-specific subject information and informed consent forms are provided (multiple languages/countries). No mention of assent for minors (minors are excluded).

Inclusion criteria

  • {"criterion_text":"- Subject must be age ≥18 years of age, at the time of signing the informed consent\n- Chronic non-ischemic cardiomyopathy\n- 15% ≤ LVEF ≤ 35% by transthoracic echocardiography (TTE) at screening\n- 6MWT >50 meters\n- Medically stable, NYHA Class III HF for a minimum of 4 weeks while on appropriate medical therapy (defined below) including, but not limited to: a.\tAngiotensin-converting enzyme inhibitor (ACE-I), angiotensin receptor-neprilysin inhibitor (ARNI), angiotensin receptor blocker (ARB), sacubitril/valsartan combination therapy (Entresto), beta blocker therapy, mineralocorticoid receptor antagonist (MRA), sodium-glucose co-transporter 2 inhibitor (SGLT2i) for ≥ 90 days prior to enrollment. Doses of the above medications must be stable for ≥ 30 days prior to enrollment. b.\tCardiac resynchronization therapy (Zareba et al., 2011), if clinically indicated, must have been implanted ≥ 90 days prior to enrollment. ICD must be implanted, if clinically indicated ≥ 30 days prior to enrollment.\n- Women of childbearing potentia (for definition see also Section 9.4.1)l must use at least one of the following highly effective birth control methods throughout the study: - Intrauterine device in place at least 90 days prior receiving SI - Abstinence (the subject must be willing to remain abstinent from screening to 6 months after receiving SI). Females are allowed to claim abstinence as their method of contraception only when it is the preferred and usual lifestyle of the subject - Surgical sterilization of the partner(s) (vasectomy) for >180 days prior to SI administration - Hormonal contraceptives associated with the inhibition of ovulation starting > 90 days prior to SI. If hormonal contraceptives are started less than 90 days prior to receiving SI, subjects must agree to use a barrier method (diaphragm plus spermicide or condom) from screening through 90 days after initiation of hormonal contraceptives\n- Males subjects capable of fathering a child: - Must agree not to donate sperm for 6 months (in Belgium: 12 months) after time of receiving SI - Documented evidence of vasectomy in males for 180 days minimum prior to receiving SI is an acceptable form of contraception - Males who claim abstinence as their method of contraception are allowed, provided they agree to use barrier methods should they become sexually active from screening through 6 months (in Belgium: 12 months) after receiving IP. Males are allowed to claim abstinence as their method of contraception only when it is the preferred and usual lifestyle of the subject\n- Appropriate candidate for protocol-specified intracoronary infusion in the judgment of the infusing interventional cardiologist\n- To protect partners of study subjects from potential viral shedding, sexually active subjects and their partners must agree to use barrier methods of contraception (condoms, female condoms, and dams) for a minimum of 6 months (in Belgium: 12 months) after SI administration; barrier methods should be used regardless of any other applied birth control methods."}

Exclusion criteria

  • {"criterion_text":"- Chronic ischemic cardiomyopathy secondary to obstructive coronary artery disease\n- known hypersensivity to SI or to any of the exipients or to the placebo\n- Expected survival < 1 year in the judgment of the investigator\n- Clinicially relevant infection 48 hours prior to intracoronary infusion\n- Known intrinsic liver disease (e.g., cirrhosis, hepatitis A, chronic hepatitis B or hepatitis C virus infection). If serology is positive and polymerase chain reaction (PCR) is known to be negative, the subject may be eligible (confirm with medical monitor)\n- Liver function tests (alanine aminotransferase [ALT], aspartate aminotransferase [AST], alkaline phosphatase or total bilirubin) > 2x upper limit of normal (ULN) within 30 days prior to enrollment. In the case that patients have a confirmed diagnosis of benign liver dysfunction (e.g. Gilbert’s syndrome with unconjugated bilirubin not exceeding 4 mg/dL), patients may be eligible for inclusion into the study).\n- Chronic Kidney Disease Stage 5, dialysis dependent or eGFR<15 within 30 days prior to enrollment\n- Bleeding diathesis or thrombocytopenia defined as platelets <50,000 platelets/μL within 30 days prior to enrollment\n- Anemia is defined as hemoglobin <10 g/dL or transfusion dependent within 30 days prior to enrollment\n- Neutropenia is defined as absolute neutrophils <1500 mm3 within 30 days prior to enrollment\n- Known AIDS or HIV-positive status, or a previous diagnosis of immunodeficiency with an absolute neutrophil count <1000 cells/mm3\n- Intravenous (IV) inotropic therapy, intra-aortic balloon pump (IABP) or percutaneous cardiac assist device therapy within 30 days prior to enrollment\n- Previous participation in a study of gene transfer\n- Receiving investigational intervention or participating in another clinical study within 30 days of another investigational drug administration prior to administration of AB-1002 that may impact the therapeutic potential of AB-1002\n- Pregnancy or breastfeeding or plans to become pregnant within the next 12 months at the time of screening\n- Subjects with any other condition which in the opinion of the investigator would preclude participation in the study (including risk for noncompliance and any intercurrent conditions that pose an undue medical hazard, or which could interfere with the interpretation of the study results)\n- Malignant neoplasm within 5 years of dosing, with the exception of those with negligible risk of metastasis or death (such as adequately treated carcinoma in situs of the cervix, basal or squamous cell skin cancer, localized prostate cancer or ductal carcinoma in situ)\n- Any documented history of noncompliance with medications; illicit drug use or laboratory evidence of illicit drug use during screen period\n- Restrictive cardiomyopathy, obstructive cardiomyopathy, pericardial disease, amyloidosis, infiltrative cardiomyopathy, uncorrected thyroid disease, or dyskinetic LV aneurysm\n- Cardiac surgery or PCI within 30 days prior to enrollment\n- Uncorrected third degree heart block\n- Clinically significant MI in the judgment of the subject’s physician (e.g., ST elevation MI [STEMI] or large non-STEMI) within 6 months prior to enrollment\n- Prior heart transplantation, left ventricular reduction surgery (LVRS), cardiomyoplasty, passive restraint device (e.g., CorCap™ Cardiac Support Device), surgically implanted LVAD or cardiac shunt\n- Likely to receive cardiac resynchronization therapy, cardiomyoplasty, LV reduction surgery, heart transplant, conventional revascularization procedure, or valvular repair within 3 months of SI dosing in the judgment of the investigator\n- Known hypersensitivity to contrast dyes (not easily controlled by antihistamines) used for angiography; history of, or likely need for, high dose steroid pretreatment prior to contrast angiography"}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Modified Win Ratio at 52-weeks as defined by hierarchical evaluation of the following assessments in the given order: - Cardiovascular related death (Binary) - NYHA Classification change from baseline (Ordinal) - LVEF change from baseline (Binary, >=5% increase for responders) - six-minute walk test (6MWT) change from baseline (Binary >30m increase for responders)","definition_or_measurement_approach":"Modified Win Ratio at 52 weeks defined by hierarchical evaluation: (1) cardiovascular related death (binary); (2) NYHA classification change from baseline (ordinal); (3) LVEF change from baseline (binary; responder if >=5% increase); (4) 6MWT change from baseline (binary; responder if >30m increase)."}
  • {"endpoint_text":"- The safety endpoints will be assessed over the 52-week Observation Period as indicated in the Schedule of Activities: - Treatment-Emergent Adverse Events (AEs) and Serious Adverse Events (SAEs) - Observed value and change from baseline in clinical laboratory tests - Observed value and change from baseline in vital signs - Observed value and change from baseline in electrocardiograms (ECGs)","definition_or_measurement_approach":"Safety endpoints assessed over 52-week observation: collection and assessment of treatment-emergent AEs and SAEs; observed values and change from baseline in clinical laboratory tests, vital signs, and ECGs as per schedule of activities."}

Secondary endpoints

  • {"endpoint_text":"- Cardiovascular related death","definition_or_measurement_approach":"Event of cardiovascular-related death as recorded during follow-up."}
  • {"endpoint_text":"- Functional Status and Hospitalizations at 24 and 52 weeks","definition_or_measurement_approach":"Assessment of functional status and recording of hospitalizations at 24 and 52 weeks."}
  • {"endpoint_text":"- Observed value and change from baseline in NYHA Classification","definition_or_measurement_approach":"NYHA classification recorded and compared to baseline."}
  • {"endpoint_text":"- Observed value and change from baseline in LVEF","definition_or_measurement_approach":"Left ventricular ejection fraction measured (echocardiography) and change from baseline evaluated."}
  • {"endpoint_text":"- Observed value and change from baseline in 6MWT","definition_or_measurement_approach":"Six-minute walk test distance measured and change from baseline evaluated."}
  • {"endpoint_text":"- Number of HF hospitalizations","definition_or_measurement_approach":"Count of heart failure-related hospital admissions during follow-up."}
  • {"endpoint_text":"- Time to first HF hospitalization","definition_or_measurement_approach":"Time (e.g., days) from randomization to first heart failure hospitalization."}
  • {"endpoint_text":"- Physiologic Assessments","definition_or_measurement_approach":"Physiologic assessments as defined in schedule (unspecified in summary)."}
  • {"endpoint_text":"- Observed value and change from baseline in Echocardiographic assessments of: - LVEF (at 4, 12 and 36 weeks) - LV volumes: end systolic and end diastolic volumes - LVEDV and left ventricular end diastolic index (LVEDVI) - LVESV and LVESVI - sphericity index (SpI) - GLS and - degree of mitral regurgitation","definition_or_measurement_approach":"Echocardiographic measures (LVEF at weeks 4, 12, 36; LV volumes; LVEDV/LVEDVI; LVESV/LVESVI; sphericity index; global longitudinal strain (GLS); mitral regurgitation grade) and change from baseline."}
  • {"endpoint_text":"- Observed value and change from baseline in cardiac biomarker NT-proBNP","definition_or_measurement_approach":"NT-proBNP concentration measured and change from baseline recorded."}
  • {"endpoint_text":"- Observed value and change from baseline in the KCCQ as assessed by a 15-item, self-administered instrument that quantifies physical function, symptoms (frequency, severity, and recent change), social function, self-efficacy and knowledge, and QOL","definition_or_measurement_approach":"Kansas City Cardiomyopathy Questionnaire (KCCQ) 15-item self-administered score and change from baseline."}

Recruitment

Planned Sample Size
80
Recruitment Window Months
72
Consent Approach
Informed consent is required from each participant (must be ≥18 years). Country-specific subject information and informed consent form (ICF) documents are provided in multiple languages/countries (examples: HU, BG, RO, PL, DE, NL, ES, BE). Additional ICFs address pregnancy information, biopsy/heart tissue donation, and study updates. No assent procedures for minors are provided (minors excluded).

Methods

  • Use of site-level recruitment materials (flyers, patient brochures, gene therapy sheets) and patient-facing materials (tabletop flip charts, visit schemes) tailored by country (documents listed for HU, BG, RO, PL, AT, DE, NL, ES, BE).
  • Use of multimedia materials (gene therapy video and storyboard) for patient information and recruitment (country-specific video/storyboard documents present).
  • Site recruitment procedures and templates (K1 Recruitment arrangements / Procedure Template) for country-specific recruitment and ICF procedure (documents exist for multiple countries).

Geography

Total Number Of Sites
54
Total Number Of Participants
243

Hungary

Earliest CTIS Part Ii Submission Date
18-11-2024
Latest Decision Or Authorization Date
11-12-2024
Processing Time Days
23
Number Of Sites
6
Number Of Participants
38

Sites

Site Name
Semmelweis University
Department Name
Varosmajori Sziv- es Ergyogyaszati Klinika
Principal Investigator Name
Bela Peter Merkely
Principal Investigator Email
merkely.bela@kardio.sote.hu
Contact Person Name
Bela Peter Merkely
Contact Person Email
merkely.bela@kardio.sote.hu
Site Name
Central Hospital Of Northern Pest Military Hospital
Department Name
Kardiologiai Osztaly
Principal Investigator Name
Gabor Zoltan Duray
Principal Investigator Email
duray.gabor@epc-honvedkorhaz.hu
Contact Person Name
Gabor Zoltan Duray
Site Name
University Of Szeged
Department Name
Belgyogyaszati Klinika
Principal Investigator Name
Tamas Szili-Torok
Principal Investigator Email
szili-torok.tamas@med.u-szeged.hu
Contact Person Name
Tamas Szili-Torok
Site Name
University Of Pecs
Department Name
Szivgyogyaszati Klinika, Intervencios Kardiologia
Principal Investigator Name
Ivan Gabor Horvath
Principal Investigator Email
ivan.g.horvath@pte.hu
Contact Person Name
Ivan Gabor Horvath
Contact Person Email
ivan.g.horvath@pte.hu
Site Name
Somogy Varmegyei Kaposi Mor Oktato Korhaz
Department Name
Kardiologiai Osztaly, Klinikai Vizsgalati Egyseg
Principal Investigator Name
Andras Vorobcsuk
Principal Investigator Email
vorobcsuk.andras@kmmk.hu
Contact Person Name
Andras Vorobcsuk
Contact Person Email
vorobcsuk.andras@kmmk.hu
Site Name
Budapesti Uzsoki Utcai Korhaz
Department Name
Kardiologiai Osztaly
Principal Investigator Name
Balazs Sarman
Principal Investigator Email
sarman.balazs@uzsoki.hu
Contact Person Name
Balazs Sarman
Contact Person Email
sarman.balazs@uzsoki.hu

Bulgaria

Earliest CTIS Part Ii Submission Date
06-08-2025
Latest Decision Or Authorization Date
21-08-2025
Processing Time Days
15
Number Of Sites
9
Number Of Participants
30

Sites

Site Name
University Multiprofile Hospital For Active Treatment And Emergency Medicine N I Pirogov
Department Name
Department of Invasive Cardiology at Clinic of Cardiology
Principal Investigator Name
Ivan Martinov
Principal Investigator Email
pirogov@pirogov.bg
Contact Person Name
Ivan Martinov
Contact Person Email
pirogov@pirogov.bg
Site Name
South West Hospital Ltd.
Department Name
Department of Cardiology
Principal Investigator Name
Boris Zehirov
Principal Investigator Email
mbal_st_vrach@abv.bg
Contact Person Name
Boris Zehirov
Contact Person Email
mbal_st_vrach@abv.bg
Site Name
University Multiprofile Hospital For Active Treatment Sofiamed OOD
Department Name
Clinic of Cardiology
Principal Investigator Name
Iveta Tasheva
Principal Investigator Email
hospitalsofiamed@bulpharma.bg
Contact Person Name
Iveta Tasheva
Contact Person Email
hospitalsofiamed@bulpharma.bg
Site Name
University Multidisciplinary Hospital For Active Treatment Sveta Ekaterina EAD
Department Name
Clinic of Cardiology
Principal Investigator Name
Diana Trendafilova - Lazarova
Principal Investigator Email
info@uhsek.com
Contact Person Name
Diana Trendafilova - Lazarova
Contact Person Email
info@uhsek.com
Site Name
Мultidisciplinary hospital for active treatment Saint George Pernik OOD
Department Name
Department of Cardiology
Principal Investigator Name
Kostadin Kichukov
Principal Investigator Email
sbalk.svetigeorgi@gmail.com
Contact Person Name
Kostadin Kichukov
Contact Person Email
sbalk.svetigeorgi@gmail.com
Site Name
Specialized Hospital For Active Cardiology Treatement Cardiolife OOD
Department Name
Department of Cardiology
Principal Investigator Name
Trayan Tsvetkov
Principal Investigator Email
mbal_kardiolife@abv.bg
Contact Person Name
Trayan Tsvetkov
Contact Person Email
mbal_kardiolife@abv.bg
Site Name
Specialized Hospital For Active Cardiology Treatment Medica Kor EAD
Department Name
Department of Cardiology
Principal Investigator Name
Dobrin Vasilev
Principal Investigator Email
info@medica-core.com
Contact Person Name
Dobrin Vasilev
Contact Person Email
info@medica-core.com
Site Name
MHAT National Heart Hospital EAD
Department Name
Clinic of Cardiology
Principal Investigator Name
Alexander Alexandrov
Principal Investigator Email
nkb@hearthospital.bg
Contact Person Name
Alexander Alexandrov
Contact Person Email
nkb@hearthospital.bg
Site Name
Acibadem City Clinic Tokuda University Hospital EAD
Department Name
Clinic of Cardiology
Principal Investigator Name
Valeri Gelev
Principal Investigator Email
tcrc@acibademcityclinic.bg
Contact Person Name
Valeri Gelev
Contact Person Email
tcrc@acibademcityclinic.bg

Romania

Earliest CTIS Part Ii Submission Date
23-06-2025
Latest Decision Or Authorization Date
25-08-2025
Processing Time Days
63
Number Of Sites
6
Number Of Participants
25

Sites

Site Name
Institutul De Boli Cardiovasculare Timisoara
Department Name
Cardiology
Principal Investigator Name
Dan Gaita
Principal Investigator Email
office@cardiologie.ro
Contact Person Name
Dan Gaita
Contact Person Email
office@cardiologie.ro
Site Name
Spitalul Clinic Judetean De Urgenta Targu Mures
Department Name
Cardiology
Principal Investigator Name
Theodora Benedek
Principal Investigator Email
secretariat@spitalmures.ro
Contact Person Name
Theodora Benedek
Contact Person Email
secretariat@spitalmures.ro
Site Name
Spitalul Clinic Judetean De Urgenta Brasov
Department Name
Cardiology
Principal Investigator Name
Florin Ortan
Principal Investigator Email
secretariat@spitaluljudeteanbrasov.ro
Contact Person Name
Florin Ortan
Site Name
Spitalul Universitar De Urgenta Bucuresti
Department Name
Cardiology
Principal Investigator Name
Dragos Vinereanu
Principal Investigator Email
secretariat@suub.ro
Contact Person Name
Dragos Vinereanu
Contact Person Email
secretariat@suub.ro
Site Name
Spitalul Clinic Judetean De Urgenta Craiova
Department Name
Cardiology
Principal Investigator Name
Constantin Militaru
Principal Investigator Email
info@scjuc.ro
Contact Person Name
Constantin Militaru
Contact Person Email
info@scjuc.ro
Site Name
Spitalul Clinic Judetean De Urgenta Militar Central Dr. Carol Davila
Department Name
Cardiology
Principal Investigator Name
Silviu Dumitrescu
Principal Investigator Email
secretariat@scumc.ro
Contact Person Name
Silviu Dumitrescu
Contact Person Email
secretariat@scumc.ro

Poland

Earliest CTIS Part Ii Submission Date
22-07-2025
Latest Decision Or Authorization Date
22-08-2025
Processing Time Days
31
Number Of Sites
9
Number Of Participants
25

Sites

Site Name
Uniwersytecki Szpital Kliniczny Nr 4 W Lublinie
Department Name
Cardiology
Principal Investigator Name
Michał Tomaszewski
Principal Investigator Email
cwbk@umlub.pl
Contact Person Name
Michał Tomaszewski
Contact Person Email
cwbk@umlub.pl
Site Name
Narodowy Instytut Kardiologii Stefana Kardynala Wyszynskiego Panstwowy Instytut Badawczy
Department Name
Cardiology
Principal Investigator Name
Przemyslaw Leszek
Principal Investigator Email
kns@ikard.pl
Contact Person Name
Przemyslaw Leszek
Contact Person Email
kns@ikard.pl
Site Name
American Heart Of Poland S.A. (Chrzanow)
Department Name
Cardiology
Principal Investigator Name
Aleksander Zurakowski
Principal Investigator Email
clinicaltrial@ahop.pl
Contact Person Name
Aleksander Zurakowski
Contact Person Email
clinicaltrial@ahop.pl
Site Name
1 Wojskowy Szpital Kliniczny Z Poliklinika samodzielny publiczny zakład opieki zdrowotnej W Lublinie
Department Name
Cardiology
Principal Investigator Name
Grzegorz Sobieszek
Principal Investigator Email
cwbk@1wszk.pl
Contact Person Name
Grzegorz Sobieszek
Contact Person Email
cwbk@1wszk.pl
Site Name
American Heart Of Poland S.A. (Bielsko-Biala)
Department Name
Cardiology
Principal Investigator Name
Krzysztof Milewski
Principal Investigator Email
clinicaltrial@ahop.pl
Contact Person Name
Krzysztof Milewski
Contact Person Email
clinicaltrial@ahop.pl
Site Name
Gornoslaskie Centrum Medyczne Im Prof. Leszka Gieca Sląskiego Uniwersytetu Medycznego W Katowicach
Department Name
Cardiology
Principal Investigator Name
Krzysztof Golba
Principal Investigator Email
ekk@gcm.pl
Contact Person Name
Krzysztof Golba
Contact Person Email
ekk@gcm.pl
Site Name
American Heart Of Poland S.A. (Tychy)
Department Name
Cardiology
Principal Investigator Name
Adam Janas
Principal Investigator Email
clinicaltrial@ahop.pl
Contact Person Name
Adam Janas
Contact Person Email
clinicaltrial@ahop.pl
Site Name
Krakowski Szpital Specjalistyczny Im. Sw. Jana Pawla II
Department Name
Cardiology
Principal Investigator Name
Grzegorz Kopec
Principal Investigator Email
sekr_kard@szpitaljp2.krakow.pl
Contact Person Name
Grzegorz Kopec
Contact Person Email
sekr_kard@szpitaljp2.krakow.pl
Site Name
Wojewodzki Szpital Zespolony Im.L.Rydygiera W Toruniu
Department Name
Cardiology
Principal Investigator Name
Grzegorz Skonieczny
Principal Investigator Email
kardiologia@wszz.torun.pl
Contact Person Name
Grzegorz Skonieczny
Contact Person Email
kardiologia@wszz.torun.pl

Austria

Earliest CTIS Part Ii Submission Date
26-06-2024
Latest Decision Or Authorization Date
15-09-2024
Processing Time Days
81
Number Of Sites
4
Number Of Participants
25

Sites

Site Name
Medical University Of Graz
Department Name
Universitaetsklinik fuer Innere Medizin, Klin. Abt. fuer Kardiologie
Principal Investigator Name
Markus Wallner
Principal Investigator Email
markus.wallner@medunigraz.at
Contact Person Name
Markus Wallner
Contact Person Email
markus.wallner@medunigraz.at
Site Name
Noe LGA Gesundheit Region Mitte GmbH
Department Name
Innere Med III
Principal Investigator Name
Deddo Moertl
Principal Investigator Email
deddo.moertl@stpoelten.lknoe.at
Contact Person Name
Deddo Moertl
Site Name
Gemeinnutzige Salzburger Landes kliniken Betriebsgesellschaft mbH
Department Name
Innere Medizin II, Kardiologie, Internistische Intensivmedizin
Principal Investigator Name
Michael Lichtenauer
Principal Investigator Email
m.lichtenauer@salk.at
Contact Person Name
Michael Lichtenauer
Contact Person Email
m.lichtenauer@salk.at
Site Name
Kepler Universitaetsklinikum GmbH
Department Name
Klinik fuer Kardiologie und Internistische Intensivmedizin; Med Campus III
Principal Investigator Name
Clemens Steinwender
Principal Investigator Email
clemens.steinwender@kepleruniklinikum.at
Contact Person Name
Clemens Steinwender

Germany

Earliest CTIS Part Ii Submission Date
16-08-2024
Latest Decision Or Authorization Date
27-09-2024
Processing Time Days
42
Number Of Sites
6
Number Of Participants
25

Sites

Site Name
Universitaetsklinikum Heidelberg AöR
Department Name
Klinik für Kardiologie, Angiologie, Pneumologie (Innere Medizin III)
Principal Investigator Name
Philipp Schlegel
Principal Investigator Email
philipp.schlegel@med.uni-heidelberg.de
Contact Person Name
Philipp Schlegel
Site Name
Medizinische Hochschule Hannover
Department Name
Klinik fuer Kardiologie und Angiologie
Principal Investigator Name
Johann Bauersachs
Principal Investigator Email
bauersachs.johann@mh-hannover.de
Contact Person Name
Johann Bauersachs
Site Name
Charite Universitaetsmedizin Berlin KöR
Department Name
Klinik fuer Kardiologie, Angiologie und Intensivmedizin
Principal Investigator Name
Frank Edelmann
Principal Investigator Email
frank.edelmann@dhzc-charite.de
Contact Person Name
Frank Edelmann
Contact Person Email
frank.edelmann@dhzc-charite.de
Site Name
Klinikum rechts der Isar der TU Muenchen AöR
Department Name
Klinik und Poliklinik fuer Innere Medizin I
Principal Investigator Name
Christian Kupatt
Principal Investigator Email
christian.kupatt@tum.de
Contact Person Name
Christian Kupatt
Contact Person Email
christian.kupatt@tum.de
Site Name
Universitaetsklinikum Schleswig-Holstein AöR
Department Name
Klinik fuer Kardiologie, Angiologie und internistische Intensivmedizin
Principal Investigator Name
Derk Frank
Principal Investigator Email
derk.frank@uksh.de
Contact Person Name
Derk Frank
Contact Person Email
derk.frank@uksh.de
Site Name
Medical Center - University Of Freiburg
Department Name
Klinik fuer Kardiologie und Angiologie
Principal Investigator Name
Markus Welzel
Principal Investigator Email
markus.welzel@uniklinik-freiburg.de
Contact Person Name
Markus Welzel

Netherlands

Earliest CTIS Part Ii Submission Date
28-08-2024
Latest Decision Or Authorization Date
16-09-2024
Processing Time Days
19
Number Of Sites
4
Number Of Participants
25

Sites

Site Name
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Department Name
Cardiology
Principal Investigator Name
Olivier Manintveld
Principal Investigator Email
o.manintveld@erasmusmc.nl
Contact Person Name
Olivier Manintveld
Contact Person Email
o.manintveld@erasmusmc.nl
Site Name
Stichting Radboud universitair medisch centrum
Department Name
Cardiology
Principal Investigator Name
Carlijne Hassing
Principal Investigator Email
Carlijne.Hassing@radboudumc.nl
Contact Person Name
Carlijne Hassing
Contact Person Email
Carlijne.Hassing@radboudumc.nl
Site Name
Amsterdam UMC Stichting
Department Name
Cardiology
Principal Investigator Name
Ahmad Shoaib Amin
Principal Investigator Email
a.s.amin@amsterdamumc.nl
Contact Person Name
Ahmad Shoaib Amin
Contact Person Email
a.s.amin@amsterdamumc.nl
Site Name
Universitair Medisch Centrum Utrecht
Department Name
Cardiology
Principal Investigator Name
Linda van Laake
Principal Investigator Email
researchdhl@umcutrecht.nl
Contact Person Name
Linda van Laake
Contact Person Email
researchdhl@umcutrecht.nl

Spain

Earliest CTIS Part Ii Submission Date
26-08-2024
Latest Decision Or Authorization Date
10-09-2024
Processing Time Days
15
Number Of Sites
6
Number Of Participants
25

Sites

Site Name
Clinica Universidad De Navarra
Department Name
Cardiology
Principal Investigator Name
Juan Jose Gavira Gomez
Principal Investigator Email
jjgavira@unav.es
Contact Person Name
Juan Jose Gavira Gomez
Contact Person Email
jjgavira@unav.es
Site Name
Bellvitge University Hospital
Department Name
Cardiology
Principal Investigator Name
Lidia Alcoberro Torres
Principal Investigator Email
lalcoberro@bellvitgehospital.cat
Contact Person Name
Lidia Alcoberro Torres
Site Name
Hospital Universitario La Paz
Department Name
Cardiology
Principal Investigator Name
Jose Raul Moreno Gomez
Principal Investigator Email
joseraul.moreno@salud.madrid.org
Contact Person Name
Jose Raul Moreno Gomez
Site Name
Hospital Clinico Universitario De Valencia
Department Name
Cardiology
Principal Investigator Name
Julio Eduardo Nuñez Villota
Principal Investigator Email
juenuvi@uv.es
Contact Person Name
Julio Eduardo Nuñez Villota
Contact Person Email
juenuvi@uv.es
Site Name
Hospital Universitario Ramon Y Cajal
Department Name
Cardiology
Principal Investigator Name
Marcelo Sanmartin Fernandez
Principal Investigator Email
marcelo.sanmartin@salud.madrid.org
Contact Person Name
Marcelo Sanmartin Fernandez
Site Name
Complexo Hospitalario Universitario De Santiago
Department Name
Cardiology
Principal Investigator Name
Jose Ramon Gonzalez Juanatey
Principal Investigator Email
Jose.Ramon.Gonzalez.Juanatey@sergas.es
Contact Person Name
Jose Ramon Gonzalez Juanatey

Belgium

Earliest CTIS Part Ii Submission Date
16-07-2025
Latest Decision Or Authorization Date
08-08-2025
Processing Time Days
23
Number Of Sites
4
Number Of Participants
25

Sites

Site Name
Universitair Ziekenhuis Gent
Department Name
Cardiology
Principal Investigator Name
Frank Timmermans
Principal Investigator Email
cardiologie@uzgent.be
Contact Person Name
Frank Timmermans
Contact Person Email
cardiologie@uzgent.be
Site Name
Onze-Lieve-Vrouwziekenhuis
Department Name
Cardiology
Principal Investigator Name
Marc Vanderheyden
Principal Investigator Email
cardio.studie.aalst@azorg.be
Contact Person Name
Marc Vanderheyden
Contact Person Email
cardio.studie.aalst@azorg.be
Site Name
Algemeen Ziekenhuis Delta
Department Name
Cardiology
Principal Investigator Name
Karl Dujardin
Principal Investigator Email
ctc.cardio@azdelta.be
Contact Person Name
Karl Dujardin
Contact Person Email
ctc.cardio@azdelta.be
Site Name
Universitair Ziekenhuis Antwerpen
Department Name
Cardiology
Principal Investigator Name
Emeline Van Craenenbroeck
Principal Investigator Email
Studies.cardiologie@uza.be
Contact Person Name
Emeline Van Craenenbroeck
Contact Person Email
Studies.cardiologie@uza.be

Sponsor

Primary sponsor

Full Name
Askbio Inc.
Organisation Type
Pharmaceutical company
Country Of Registered Address
United States

Third parties

  • {"country":"Germany","full_name":"Bayer AG","duties_or_roles":"sponsorDuties codes: [1,10,11,13,2,3,4,5,6,7,8]; contact: clinical-trials-contact@bayer.com","organisation_type":"Pharmaceutical company"}

Investigational products

Investigational Product Name
AB-1002
Active Substance
AB-1002
Modality
Gene therapy
Routes Of Administration
INTRACORONARY USE
Route
Intracoronary
Authorisation Status
prodAuthStatus: 1
Frequency
Single antegrade intracoronary infusion
Maximum Dose
143000000000000.00 (doseUom: Other, maxDailyDoseAmount/maxTotalDoseAmount provided in record)
Investigational Product Name
AB-1002 Placebo
Modality
Other

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