Clinical trial • Phase II • Oncology

(3S,3'S,3A'S,10A'S)-6-CHLORO-3'-(3-CHLORO-2-FLUOROPHENYL)-1'-(CYCLOPROPYLMETHYL)-6'-METHYL-2-OXO-1,2,3',3A',10',10A'-HEXAHYDRO-1'H-SPIRO[INDOLE-3,2'-PYRROLO[2',3':4,5]PYRROLO[1,2-B]INDAZOLE]-7'-CARBOXYLIC ACID for Solid tumours

Phase II trial of (3S,3'S,3A'S,10A'S)-6-CHLORO-3'-(3-CHLORO-2-FLUOROPHENYL)-1'-(CYCLOPROPYLMETHYL)-6'-METHYL-2-OXO-1,2,3',3A',10',10A'-HEXAHYDRO-1'H-SPIRO…

Overview

Trial Therapeutic Area
Oncology
Trial Disease
Solid tumours
Trial Stage
Phase II
Drug Modality
Small molecule
Orphan Drug
Yes

Key dates

Initial CTIS Submission Date
19-07-2024
First CTIS Authorization Date
23-10-2024

Trial design

open-label Phase II trial in Norway, Czechia, Poland and others.

Open Label
Yes
Target Sample Size
62

Eligibility

Recruits 62 Vulnerable population not selected. Informed consent is required: "Provision of signed and dated, written informed consent form (ICF) in accordance with International Council for Harmonisation of Technical Requirements for Pharmaceuticals for Human Use - Good Clinical Practice (ICH-GCP) and local legislation prior to any trial-specific procedures, sampling, or analyses." No specific assent/parental consent provisions for minors are indicated..

Pregnancy Exclusion
Women who are pregnant, nursing, or who plan to become pregnant while in the trial. Female patients who do not agree to the interruption of breastfeeding from the start of study treatment until 6 months and 12 days after the last dose of study treatment.
Vulnerable Population
Vulnerable population not selected. Informed consent is required: "Provision of signed and dated, written informed consent form (ICF) in accordance with International Council for Harmonisation of Technical Requirements for Pharmaceuticals for Human Use - Good Clinical Practice (ICH-GCP) and local legislation prior to any trial-specific procedures, sampling, or analyses." No specific assent/parental consent provisions for minors are indicated.

Inclusion criteria

  • {"criterion_text":"- Patient is ongoing on brigimadlin treatment in any trial sponsored by Boehringer Ingelheim (hereafter referred to as the ‘parent trial')."}
  • {"criterion_text":"- Provision of signed and dated, written informed consent form (ICF) in accordance with International Council for Harmonisation of Technical Requirements for Pharmaceuticals for Human Use - Good Clinical Practice (ICH-GCP) and local legislation prior to any trial-specific procedures, sampling, or analyses."}
  • {"criterion_text":"- Women of childbearing potential (WOCBP) and men able to father a child must be ready and able to use 2 medically acceptable methods of birth control per ICH M3 (R2) that result in a low failure rate of <1% per year when used consistently and correctly beginning at Screening, during trial participation, and until 6 months and 12 days after the last dose for women and 102 days after the last dose for men. A list of contraception methods meeting these criteria and instructions on the duration of use is provided in the participant information."}
  • {"criterion_text":"- Participants must be willing and able to comply with the scheduled visits, treatment plan, lifestyle, laboratory tests, contraceptive guidelines, and other study procedures."}
  • {"criterion_text":"- Adequate organ function."}
  • {"criterion_text":"- Patient is eligible to receive continued treatment according to the clinical trial protocol of the parent trial they are currently participating in. Patients currently experiencing a dose delay in the parent trial due to adverse events are eligible if recovery from the adverse event takes place within the allowed time window in the parent trial."}

Exclusion criteria

  • {"criterion_text":"- Any medical condition which in the opinion of the investigator should exclude the patient from receiving treatment with brigimadlin."}
  • {"criterion_text":"- Participants who must receive or intend to receive restricted medications or any drug considered likely to interfere with the safe conduct of the trial."}
  • {"criterion_text":"- Patient unable to swallow the trial medication."}
  • {"criterion_text":"- Women who are pregnant, nursing, or who plan to become pregnant while in the trial. Female patients who do not agree to the interruption of breastfeeding from the start of study treatment until 6 months and 12 days after the last dose of study treatment."}
  • {"criterion_text":"- Patient has unacceptable toxicity on brigimadlin at the time of transition into this trial."}
  • {"criterion_text":"- Patient has an AE which has caused a dose delay and has not recovered within the allowed time window in the parent trial."}
  • {"criterion_text":"- Patient who has already required 2 dose reductions and would require a third dose reduction at trial entry, unless the investigator deems treatment continuation beneficial, and the third dose reduction is agreed in writing between the investigator and the sponsor."}
  • {"criterion_text":"- Further exclusion criteria apply."}

Endpoints

Primary endpoints

  • {"endpoint_text":"- Occurrence of treatment-emergent AEs according to CTCAE Version 5.0 during the entire treatment period","definition_or_measurement_approach":"Occurrence of treatment-emergent adverse events assessed according to CTCAE Version 5.0 during the entire treatment period."}

Recruitment

Planned Sample Size
62
Recruitment Window Months
144
Consent Approach
Provision of signed and dated, written informed consent form (ICF) in accordance with ICH-GCP and local legislation prior to any trial-specific procedures, sampling, or analyses. Multiple country-specific ICF documents and language versions are provided (local language ICFs and re-consent documents are listed in the trial documents).

Geography

Total Number Of Sites
27
Total Number Of Participants
31

Norway

Earliest CTIS Part Ii Submission Date
09-05-2025
Latest Decision Or Authorization Date
14-05-2025
Processing Time Days
5
Number Of Sites
1
Number Of Participants
1

Sites

Site Name
Oslo University Hospital HF
Department Name
Radiumhospitalet
Principal Investigator Name
Kjetil Boye
Principal Investigator Email
pbk@ous-hf.no
Contact Person Name
Kjetil Boye
Contact Person Email
pbk@ous-hf.no

Czechia

Earliest CTIS Part Ii Submission Date
26-05-2025
Latest Decision Or Authorization Date
16-06-2025
Processing Time Days
21
Number Of Sites
1
Number Of Participants
1

Sites

Site Name
University Hospital Olomouc
Department Name
Department of Comprehensive Oncology Care
Principal Investigator Name
Bohuslav Melichar
Principal Investigator Email
bohuslav.melichar@fnol.cz
Contact Person Name
Bohuslav Melichar
Contact Person Email
bohuslav.melichar@fnol.cz

Poland

Earliest CTIS Part Ii Submission Date
28-05-2025
Latest Decision Or Authorization Date
30-06-2025
Processing Time Days
33
Number Of Sites
1
Number Of Participants
2

Sites

Site Name
Narodowy Instytut Onkologii Im. Marii Sklodowskiej-Curie Panstwowy Instytut Badawczy
Department Name
Department of Early Phase Trials
Principal Investigator Name
Iwona Lugowska
Principal Investigator Email
iwona.lugowska@coi.pl
Contact Person Name
Iwona Lugowska
Contact Person Email
iwona.lugowska@coi.pl

Belgium

Earliest CTIS Part Ii Submission Date
07-10-2024
Latest Decision Or Authorization Date
29-10-2024
Processing Time Days
22
Number Of Sites
3
Number Of Participants
2

Sites

Site Name
Cliniques Universitaires Saint-Luc
Department Name
Service d'oncologie medicale
Principal Investigator Name
Rachel Galot
Principal Investigator Email
rachel.galot@saintluc.uclouvain.be
Contact Person Name
Rachel Galot
Site Name
Antwerp University Hospital
Principal Investigator Name
Hans Prenen
Principal Investigator Email
Hans.Prenen@uza.be
Contact Person Name
Hans Prenen
Contact Person Email
Hans.Prenen@uza.be
Site Name
UZ Leuven
Department Name
Department of General Medical Oncology
Principal Investigator Name
Patrick Schöffski
Principal Investigator Email
patrick.schoffski@uzleuven.be
Contact Person Name
Patrick Schöffski
Contact Person Email
patrick.schoffski@uzleuven.be

France

Earliest CTIS Part Ii Submission Date
11-06-2025
Latest Decision Or Authorization Date
18-06-2025
Processing Time Days
7
Number Of Sites
2
Number Of Participants
3

Sites

Site Name
Centre Leon Berard
Department Name
Oncologie Médicale
Principal Investigator Name
Jean-Yves Blay
Principal Investigator Email
jean-yves.blay@lyon.unicancer.fr
Contact Person Name
Jean-Yves Blay
Site Name
Centre De Lutte Contre Le Cancer Eugene Marquis
Department Name
Service d'Oncologie Médicale
Principal Investigator Name
Christophe Perrin
Principal Investigator Email
c.perrin@rennes.unicancer.fr
Contact Person Name
Christophe Perrin
Contact Person Email
c.perrin@rennes.unicancer.fr

Denmark

Earliest CTIS Part Ii Submission Date
19-06-2025
Latest Decision Or Authorization Date
24-06-2025
Processing Time Days
5
Number Of Sites
1
Number Of Participants
2

Sites

Site Name
Rigshospitalet
Department Name
Department of Oncology
Principal Investigator Name
Martin Hojgaard
Principal Investigator Email
martin.hojgaard@regionh.dk
Contact Person Name
Martin Hojgaard
Contact Person Email
martin.hojgaard@regionh.dk

Spain

Earliest CTIS Part Ii Submission Date
06-08-2024
Latest Decision Or Authorization Date
23-10-2024
Processing Time Days
78
Number Of Sites
12
Number Of Participants
8

Sites

Site Name
Hospital Clinico San Carlos
Department Name
Servicio de Oncología Médica
Principal Investigator Name
Jorge Bartolomé
Principal Investigator Email
jorgebart@msn.com
Contact Person Name
Jorge Bartolomé
Contact Person Email
jorgebart@msn.com
Site Name
Hospital Universitario Quironsalud Madrid
Department Name
Unidad Fases I Next Oncology
Principal Investigator Name
Valentina Boni
Principal Investigator Email
vboni@nextoncology.eu
Contact Person Name
Valentina Boni
Contact Person Email
vboni@nextoncology.eu
Site Name
Institut Catala D'oncologia
Department Name
Unidad de Sarcoma y Cáncer Genitourinario
Principal Investigator Name
Laura Jiménez Colomo
Principal Investigator Email
ljcolomo@iconcologia.net
Contact Person Name
Laura Jiménez Colomo
Contact Person Email
ljcolomo@iconcologia.net
Site Name
Hospital Clinico Universitario De Valencia
Department Name
Servicio de Oncología Médica
Principal Investigator Name
Desamparados Roda
Principal Investigator Email
derope@hotmail.com
Contact Person Name
Desamparados Roda
Contact Person Email
derope@hotmail.com
Site Name
Hospital Quironsalud Barcelona
Department Name
Medicina Interna
Principal Investigator Name
Fabricio Racca Bussano
Principal Investigator Email
fracca@nextoncology.eu
Contact Person Name
Fabricio Racca Bussano
Contact Person Email
fracca@nextoncology.eu
Site Name
Hospital Universitario Miguel Servet
Department Name
Servicio Oncología
Principal Investigator Name
Javier Martínez Trufero
Principal Investigator Email
jmtrufero@seom.org
Contact Person Name
Javier Martínez Trufero
Contact Person Email
jmtrufero@seom.org
Site Name
Hospital Universitario 12 De Octubre
Department Name
Servicio de Oncologia
Principal Investigator Name
Jorge Adeva
Principal Investigator Email
jorge.adeva@salud.madrid.org
Contact Person Name
Jorge Adeva
Contact Person Email
jorge.adeva@salud.madrid.org
Site Name
Hospital Universitario Fundacion Jimenez Diaz
Department Name
Servicio de Oncología
Principal Investigator Name
Javier Martín Broto
Principal Investigator Email
jmartin@atbsarc.org
Contact Person Name
Javier Martín Broto
Contact Person Email
jmartin@atbsarc.org
Site Name
Hospital Del Mar
Department Name
Servicio de Oncologia
Principal Investigator Name
María Martínez García
Principal Investigator Email
mariamartinezgarcia@psmar.cat
Contact Person Name
María Martínez García
Contact Person Email
mariamartinezgarcia@psmar.cat
Site Name
Complexo Hospitalario Universitario De Santiago
Department Name
Servicio de Oncología Médica
Principal Investigator Name
Vanesa Varela
Principal Investigator Email
vanesa.varela.pose@sergas.es
Contact Person Name
Vanesa Varela
Contact Person Email
vanesa.varela.pose@sergas.es
Site Name
Hospital Universitari Vall D Hebron
Department Name
Oncologia
Principal Investigator Name
Teresa Macarulla
Principal Investigator Email
tmacarulla@vhio.net
Contact Person Name
Teresa Macarulla
Contact Person Email
tmacarulla@vhio.net
Site Name
Hospital Universitario Hm Sanchinarro
Department Name
Centro Integral Oncologico Clara Campal
Principal Investigator Name
Gema García Ledo
Principal Investigator Email
gmgarcialedo@hmhospitales.com
Contact Person Name
Gema García Ledo
Contact Person Email
gmgarcialedo@hmhospitales.com

Italy

Earliest CTIS Part Ii Submission Date
25-04-2025
Latest Decision Or Authorization Date
13-06-2025
Processing Time Days
49
Number Of Sites
2
Number Of Participants
3

Sites

Site Name
Fondazione IRCCS Istituto Nazionale Dei Tumori
Department Name
Not applicable
Principal Investigator Name
Roberta Sanfilippo
Principal Investigator Email
roberta.sanfilippo@istitutotumori.mi.it
Contact Person Name
Roberta Sanfilippo
Site Name
Istituto Oncologico Veneto
Department Name
Not applicable
Principal Investigator Name
Antonella Brunello
Principal Investigator Email
antonella.brunello@iov.veneto.it
Contact Person Name
Antonella Brunello

Sweden

Earliest CTIS Part Ii Submission Date
22-05-2025
Latest Decision Or Authorization Date
13-06-2025
Processing Time Days
22
Number Of Sites
1
Number Of Participants
1

Sites

Site Name
Karolinska University Hospital
Department Name
Comprehensive Cancer Center
Principal Investigator Name
Christina Linder-Stragliotto
Principal Investigator Email
christina.linder-stragliotto@sll.se
Contact Person Name
Christina Linder-Stragliotto

Germany

Earliest CTIS Part Ii Submission Date
02-06-2025
Latest Decision Or Authorization Date
25-06-2025
Processing Time Days
23
Number Of Sites
2
Number Of Participants
5

Sites

Site Name
HELIOS Klinikum Berlin-Buch GmbH
Department Name
Onkologie und Palliativmedizin
Principal Investigator Name
Peter Reichardt
Principal Investigator Email
peter.reichardt@helios-gesundheit.de
Contact Person Name
Peter Reichardt
Site Name
Universitaetsklinikum Tuebingen AöR
Department Name
Innere Medizin VIII - Medizinische Onkologie und Pneumologie
Principal Investigator Name
Ulrich Lauer
Principal Investigator Email
ulrich.lauer@uni-tuebingen.de
Contact Person Name
Ulrich Lauer
Contact Person Email
ulrich.lauer@uni-tuebingen.de

Hungary

Earliest CTIS Part Ii Submission Date
19-09-2024
Latest Decision Or Authorization Date
06-11-2024
Processing Time Days
48
Number Of Sites
1
Number Of Participants
3

Sites

Site Name
Clinexpert Kft.
Department Name
Dept of Oncology
Principal Investigator Name
Zsuzsanna Papai
Principal Investigator Email
trial.zspapai@gmail.com
Contact Person Name
Zsuzsanna Papai
Contact Person Email
trial.zspapai@gmail.com

Sponsor

Primary sponsor

Full Name
Boehringer Ingelheim International GmbH
Organisation Type
Pharmaceutical company
Country Of Registered Address
Germany

Investigational products

Investigational Product Name
BI 907828
Active Substance
(3S,3'S,3A'S,10A'S)-6-CHLORO-3'-(3-CHLORO-2-FLUOROPHENYL)-1'-(CYCLOPROPYLMETHYL)-6'-METHYL-2-OXO-1,2,3',3A',10',10A'-HEXAHYDRO-1'H-SPIRO[INDOLE-3,2'-PYRROLO[2',3':4,5]PYRROLO[1,2-B]INDAZOLE]-7'-CARBOXYLIC ACID
Modality
Small molecule
Routes Of Administration
ORAL USE
Route
oral
Orphan Designation
Yes
Dose Levels
30 mg | 45 mg
Maximum Dose
45 mg

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